NCT00063479

Brief Summary

The primary purpose of this trial is to evaluate whether the investigational medication is safe, effective and has the ability to increase spine bone density in osteogenesis imperfecta (OI) patients.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
158

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jun 2003

Typical duration for phase_2

Geographic Reach
1 country

10 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2003

Completed
26 days until next milestone

First Submitted

Initial submission to the registry

June 27, 2003

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 30, 2003

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2007

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2007

Completed
Last Updated

June 1, 2017

Status Verified

May 1, 2017

Enrollment Period

3.9 years

First QC Date

June 27, 2003

Last Update Submit

May 31, 2017

Conditions

Keywords

Osteogenesis ImperfectaOIbone markersfracturebone losspediatricbisphosphonatebrittle bone diseasepamidronate

Outcome Measures

Primary Outcomes (1)

  • Change in lumbar spine bone mineral density at month 12 relative to baseline

Secondary Outcomes (1)

  • Change in Z score of the lumbar spine at month 12 relative to baseline

Interventions

Eligibility Criteria

Age3 Months - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Male or Female children between 3 months and 17 years old
  • OI type I, III or IV

You may not qualify if:

  • Deformity or abnormality which would prevent spine bone density from being done
  • Any surgical bone-lengthening procedure
  • Any kidney diseases or abnormalities
  • Low calcium or vitamin D levels in the blood

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

UCLA - Division of Pediatric Nephrology

Los Angeles, California, 90024, United States

Location

Alfred I. DuPont Hospital for Children

Wilmington, Delaware, 19899, United States

Location

Intermountain Orthopedics

Boise, Idaho, 83702, United States

Location

St. Jude Children's Research Hospital

Peoria, Illinois, 61637, United States

Location

Children's Hospital

Omaha, Nebraska, 68198, United States

Location

Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Children's Hospital

Columbus, Ohio, 43205, United States

Location

Oregon Health Sciences University

Portland, Oregon, 97201, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Texas Children's Hosptial

Houston, Texas, 77030, United States

Location

MeSH Terms

Conditions

Osteogenesis ImperfectaFractures, BoneBone Diseases, Metabolic

Interventions

Zoledronic Acid

Condition Hierarchy (Ancestors)

OsteochondrodysplasiasBone Diseases, DevelopmentalBone DiseasesMusculoskeletal DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCollagen DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesWounds and InjuriesMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

DiphosphonatesOrganophosphonatesOrganophosphorus CompoundsOrganic ChemicalsImidazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

June 27, 2003

First Posted

June 30, 2003

Study Start

June 1, 2003

Primary Completion

May 1, 2007

Study Completion

May 1, 2007

Last Updated

June 1, 2017

Record last verified: 2017-05

Locations