NCT00091715

Brief Summary

The present trial investigates a possible use of oral bosentan, which is currently approved for the treatment of symptoms of pulmonary arterial hypertension (PAH) Class III and IV, to patients suffering from PAH Class II.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
185

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Apr 2004

Longer than P75 for phase_3

Geographic Reach
13 countries

31 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2004

Completed
6 months until next milestone

First Submitted

Initial submission to the registry

September 16, 2004

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 20, 2004

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2006

Completed
4.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2011

Completed
Last Updated

August 30, 2011

Status Verified

August 1, 2011

Enrollment Period

2.6 years

First QC Date

September 16, 2004

Last Update Submit

August 26, 2011

Conditions

Keywords

Pulmonary arterial hypertensionPAHPPHbosentanearly

Outcome Measures

Primary Outcomes (2)

  • exercise capacity

    Baseline to end of study

  • cardiac hemodynamics

    Baseline to end of study

Study Arms (2)

1

EXPERIMENTAL

62.5 mg table twice a day for 4 weeks followed by 125 mg tablet twice a day for 6 months followed by an open label period until end of study.

Drug: bosentan

2

PLACEBO COMPARATOR

placebo for 6 months followed by an open label period

Drug: placebo

Interventions

65 mg tablet twice a day for 4 weeks followed by 125 mg tablet twice a day until end of study

Also known as: Tracleer
1

placebo for 6 months followed by an open-label period

2

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • PAH NYHA Class II
  • Significant elevation of mean pulmonary arterial pressure
  • Significant elevation of pulmonary vascular resistance at rest
  • Limited 6-minute walk distance

You may not qualify if:

  • PAH secondary to portal hypertension, complex congenital heart disease or reverse shunt
  • Restrictive or obstructive lung disease
  • Significant vasoreactivity
  • Treatments for PAH (within 4 weeks of randomization)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (34)

University of Alabama-Birmingham

Birmingham, Alabama, 35294, United States

Location

Harbor UCLA Medical Center

Torrance, California, 90509, United States

Location

Tufts- New England Medical Center

Boston, Massachusetts, 02111, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

St. Paul University Hospital

Dallas, Texas, 75390, United States

Location

The Prince Charles Hospital

Brisbane, 4032, Australia

Location

Royal Prince Albert Hospital

Camperdown, Australia

Location

St. Vincent's Hospital

Darlinghurst, Australia

Location

General Hospital of Vienna

Vienna, 1180, Austria

Location

UZ Gasthuisberg

Leuven, Belgium

Location

University of Calgary

Calgary, Alberta, T1Y 6J4, Canada

Location

University of Alberta

Edmonton, Alberta, T6G 2B7, Canada

Location

Halifax Infirmary

Halifax, Nova Scotia, B3H 3A7, Canada

Location

Victoria Medical Centre

Hamilton, Ontario, L8L 5G4, Canada

Location

Toronto General Hospital

Toronto, Ontario, M5G 2N2, Canada

Location

Centre de Pneumologie de L'Hospital Laval

Sainte-Foy, Quebec, G1V 4G5, Canada

Location

Queen Mary Hospital

Hong Kong, China

Location

Interni klinika VFN

Prague, Czechia

Location

Marseille-Timone

Marseille, 13005, France

Location

Universitat Greifswald

Greifswald, 17487, Germany

Location

Universitat Greifswald

Greifswald, Germany

Location

Universitarsklinikum Hamburg-Eppendorf

Hamburg, Germany

Location

Medizinische Universitatsklinik

Heidelberg, Germany

Location

Universitatsklinikim Leipzig

Leipzig, Germany

Location

Klinikum der Universitat Regensburg

Regensburg, Germany

Location

Policlinico S. Orsola-Malpighi

Bologna, Italy

Location

VU Medisch Centrum

Amsterdam, Netherlands

Location

University Hospital Maastricht

Maastricht, Netherlands

Location

Hospital Clinic

Barcelona, Spain

Location

Hospital Valle d'Hebron

Barcelona, Spain

Location

Hospital 12 de Octubre

Madrid, Spain

Location

Zurich University Hospital

Zurich, Switzerland

Location

Papworth Hospital

Cambridge, CB3 8RE, United Kingdom

Location

Related Publications (1)

  • Galie N, Rubin Lj, Hoeper M, Jansa P, Al-Hiti H, Meyer G, Chiossi E, Kusic-Pajic A, Simonneau G. Treatment of patients with mildly symptomatic pulmonary arterial hypertension with bosentan (EARLY study): a double-blind, randomised controlled trial. Lancet. 2008 Jun 21;371(9630):2093-100. doi: 10.1016/S0140-6736(08)60919-8.

MeSH Terms

Conditions

Hypertension, PulmonaryPulmonary Arterial Hypertension

Interventions

Bosentan

Condition Hierarchy (Ancestors)

Lung DiseasesRespiratory Tract DiseasesHypertensionVascular DiseasesCardiovascular Diseases

Intervention Hierarchy (Ancestors)

BenzenesulfonamidesSulfonamidesAmidesOrganic ChemicalsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsSulfonesSulfur CompoundsPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 16, 2004

First Posted

September 20, 2004

Study Start

April 1, 2004

Primary Completion

November 1, 2006

Study Completion

February 1, 2011

Last Updated

August 30, 2011

Record last verified: 2011-08

Locations