NCT07225504

Brief Summary

The purpose of this study is to provide efficacy and safety data for remibrutinib in patients with secondary progressive multiple sclerosis (SPMS)

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,275

participants targeted

Target at P75+ for phase_3

Timeline
90mo left

Started Nov 2025

Longer than P75 for phase_3

Geographic Reach
30 countries

231 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress9%
Nov 2025Jan 2034

First Submitted

Initial submission to the registry

November 4, 2025

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 6, 2025

Completed
5 days until next milestone

Study Start

First participant enrolled

November 11, 2025

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 3, 2030

Expected
3.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 2, 2034

Last Updated

July 29, 2026

Status Verified

July 1, 2026

Enrollment Period

5.1 years

First QC Date

November 4, 2025

Last Update Submit

July 28, 2026

Conditions

Keywords

MSMultiple sclerosissecondary progressive multiple sclerosisSPMSremibrutinibLOU064adultExpanded Disability Status ScaleEDSSMcDonald diagnostic criteria

Outcome Measures

Primary Outcomes (1)

  • Time to 6-month confirmed disability progression (6mCDP) on Expanded Disability Status Scale (EDSS)

    The EDSS is an ordinal scale used for assessing neurologic impairment in MS based on a neurological examination. It consists of scores in each of seven functional systems and an ambulation score that are then combined to determine the EDSS steps (ranging from 0 (normal) to 10 (death due to MS)). 6mCDP is defined as an increase from baseline in EDSS sustained for at least 6 months.

    From baseline up to approximately 5 years

Secondary Outcomes (8)

  • Time to 3-month confirmed disability progression (3mCDP) on EDSS

    From baseline up to approximately 5 years

  • Time to 6-month confirmed disability improvement (6mCDI) on EDSS

    From baseline up to approximately 5 years

  • Time to 3-month worsening by at least 20% in Timed 25-Foot Walk (T25FW)

    From baseline up to approximately 5 years

  • Time to 3-month worsening by at least 20% in 9-Hole Peg Test (9-HPT)

    From baseline up to approximately 5 years

  • Annualized rate of new or enlarging T2 lesions

    From baseline up to approximately 5 years

  • +3 more secondary outcomes

Study Arms (2)

Remibrutinib (LOU064)

EXPERIMENTAL

Core Part: Remibrutinib film-coated tablet taken orally \[Extension Part: Open-label remibrutinib film-coated tablet taken orally\]

Drug: Remibrutinib (blinded)Drug: Remibrutinib (Open label)

Placebo

PLACEBO COMPARATOR

Core Part: Matching placebo film-coated tablet taken orally \[Extension Part: Open-label remibrutinib film-coated tablet taken orally\]

Drug: PlaceboDrug: Remibrutinib (Open label)

Interventions

Remibrutinib (Blinded) active treatment, oral tablet

Also known as: LOU064
Remibrutinib (LOU064)

Remibrutinib (Open Label), oral tablet

Also known as: LOU064
PlaceboRemibrutinib (LOU064)

Matching placebo (binded), oral tablet

Placebo

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Signed informed consent must be obtained prior to any assessment performed.
  • Male or female participants aged 18-65 (inclusive) at Screening.
  • Diagnosis of MS according to the 2017 revised McDonald criteria (Thompson et al 2018), with current SPMS in accordance with the revised clinical course (Lublin et al 2014) at Screening
  • Absence of documented clinical relapses in the 24 months before Screening and randomization.
  • EDSS score of 3.0 to 6.0 (inclusive) at Screening.
  • Documented evidence of disability progression in the 12 months before Screening.

You may not qualify if:

  • Unwilling or unable to undergo MRI scans as per protocol (for example, claustrophobia, or presents absolute contraindications to MRI (e.g., metallic implants, metallic foreign bodies, pacemaker, defibrillator)).
  • History of clinically significant central nervous system (CNS) disease (e.g. stroke, traumatic brain or spinal injury, history or presence of myelopathy) or neurological disorders which may mimic multiple sclerosis (MS).
  • Ongoing substance abuse (drug or alcohol) or any other factor (e.g. serious psychiatric condition) that may interfere with the participant's ability to cooperate and comply with the study procedures.
  • Participants with history of confirmed Progressive Multifocal Leukoencephalopathy (PML) or neurological symptoms consistent with PML.
  • Women of childbearing potential (WOCBP), unless they are using highly effective methods of contraception (failure rate \< 1% per year) while taking study treatment and for at least 1 week after stopping study treatment.
  • Significant bleeding risk or coagulation disorders, at Screening.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (256)

Alabama Neurology Associates PC

Birmingham, Alabama, 35209, United States

RECRUITING

Ctr for Neurology and Spine

Phoenix, Arizona, 85018, United States

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AZ Integrated Neuro and Spine

Phoenix, Arizona, 85037, United States

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Center for Neurosciences

Tucson, Arizona, 85718, United States

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Fullerton Neuro and Headache Ctr

Fullerton, California, 92835, United States

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Regina Berkovich MD PhD Inc

West Hollywood, California, 90048, United States

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UC Health Neuroscience Ctr

Aurora, Colorado, 80045, United States

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Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

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Medstar Washington Hosp Ctr

Washington D.C., District of Columbia, 20010, United States

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Neurology of Central FL Res Ctr

Altamonte Springs, Florida, 32714, United States

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UF Health Cancer Center

Gainesville, Florida, 32610, United States

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Homestead Assoc In Research Inc

Homestead, Florida, 33033, United States

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Neurology Associates PA

Maitland, Florida, 32751, United States

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Miami NS Ins Baptist Health S FL

Miami, Florida, 33176, United States

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Aqualane Clinical Research

Naples, Florida, 34105, United States

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Orlando Health Clinical Trials

Orlando, Florida, 32806, United States

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Comprehensive Neurology Clinic

Orlando, Florida, 32825, United States

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Neurology Associates of Ormond Beach

Ormond Beach, Florida, 32174, United States

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Axiom Brain Health

Tampa, Florida, 33609, United States

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University Of South Florida

Tampa, Florida, 33612, United States

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Joi Life Wellness Group LLC

Smyrna, Georgia, 30080, United States

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Hawaii Pacific Neuroscience LLC

Honolulu, Hawaii, 96817, United States

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Northwestern Memorial Hospital

Chicago, Illinois, 60611, United States

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University of Kansas Hospital

Kansas City, Kansas, 66160, United States

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Mid Atlantic Epilepsy and Sleep Ctr

Bethesda, Maryland, 20817-1807, United States

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Neuro Institute of New England P C

Foxborough, Massachusetts, 02035, United States

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Elliot Lewis MS Center

Wellesley, Massachusetts, 02481, United States

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U Mass Memorial Medical Center

Worchester, Massachusetts, 01605, United States

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Michigan Institute of Neurological

Farmington Hills, Michigan, 48334, United States

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University of New Mexico Hospital

Albuquerque, New Mexico, 87106, United States

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Premier Neurology

Greenville, South Carolina, 29605, United States

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Neurology Clinic PC

Cordova, Tennessee, 38018, United States

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Carum Research

Dallas, Texas, 75231, United States

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Saturn Research Solution

Plano, Texas, 75024, United States

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Citta Clinical Research

Spokane, Washington, 99202, United States

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Novartis Investigative Site

CABA, Buenos Aires, C1428AQK, Argentina

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Novartis Investigative Site

Capital Federal, Buenos Aires, 1424, Argentina

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Buenos Aires, Buenos Aires F.D., 1221, Argentina

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Bombal, Mendoza Province, M5500DXO, Argentina

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San Juan, San Juan Province, J5402DIL, Argentina

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Rosario, Santa Fe Province, 2000, Argentina

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Rosario, Santa Fe Province, S2000DSW, Argentina

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Santiago del Estero, Santiago del Estero Province, G4200AIR, Argentina

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San Miguel de, Tucumán Province, T4000, Argentina

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Buenos Aires, C1012AAR, Argentina

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Caba, C1055AAF, Argentina

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CABA, C1181ACH, Argentina

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Caba, C1182, Argentina

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Caba, C1424BYD, Argentina

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Kogarah, New South Wales, 2217, Australia

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New Lambton Heights, New South Wales, 2305, Australia

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Westmead, New South Wales, 2145, Australia

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Clayton, Victoria, 3168, Australia

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Heidelberg, Victoria, 3084, Australia

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Murdoch, Western Australia, 6150, Australia

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Southport, 4215, Australia

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Innsbruck, Tyrol, 6020, Austria

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Linz, Upper Austria, 4020, Austria

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Linz, 4020, Austria

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Vienna, 1180, Austria

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Leuven, Vlaams Brabant, 3000, Belgium

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Roeselare, West-Vlaanderen, 8800, Belgium

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Bonheiden, 2820, Belgium

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Brussels, 1070, Belgium

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Porto Alegre, Rio Grande do Sul, 90430-001, Brazil

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Porto Alegre, Rio Grande do Sul, 90560-032, Brazil

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Porto Alegre, Rio Grande do Sul, 90620-130, Brazil

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Joinville, Santa Catarina, 89202-165, Brazil

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Santo André, São Paulo, 09040 010, Brazil

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São Paulo, São Paulo, 04076-004, Brazil

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Pleven, 5800, Bulgaria

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Sofia, 1113, Bulgaria

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Sofia, 1309, Bulgaria

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Sofia, 1407, Bulgaria

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Novartis Investigative Site

Sofia, 1408, Bulgaria

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Novartis Investigative Site

Sofia, 1431, Bulgaria

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Sofia, 1510, Bulgaria

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Sofia, 1606, Bulgaria

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Vancouver, British Columbia, V6T 2A1, Canada

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Halifax, Nova Scotia, B3H 4K4, Canada

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Ottawa, Ontario, K1H 8L6, Canada

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Lévis, Quebec, G6W 0M5, Canada

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Montreal, Quebec, H2X 1R9, Canada

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Montreal, Quebec, H3A 2B4, Canada

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Montreal, Quebec, H4A 3T2, Canada

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Québec, Quebec, G1J 1Z4, Canada

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Sherbrooke, Quebec, J1H 5N4, Canada

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Guangzhou, Guangdong, 510080, China

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Zhengzhou, Henan, 450003, China

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Wuhan, Hubei, 430030, China

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Wuhan, Hubei, 430060, China

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Hohhot, Inner Mongolia, 010017, China

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Suzhou, Jiangsu, 215004, China

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Changchun, Jilin, 130021, China

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Shenyang, Liaoning, 110011, China

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Yinchuan, Ningxia, 750004, China

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Xianyang, Shaanxi, 712000, China

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Taiyuan, Shanxi, 030001, China

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Hangzhou, Zhejiang, 310002, China

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Hangzhou, Zhejiang, 310016, China

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Wenzhou, Zhejiang, 325000, China

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Beijing, 100034, China

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Beijing, 100070, China

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Chongqing, 400016, China

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Shanghai, 200040, China

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Tianjin, 300052, China

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Barranquilla, Atlántico, 080020, Colombia

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Bogotá, 111321, Colombia

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Medellín, 050001, Colombia

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Medellín, 050034, Colombia

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Varaždin, Varaždin County, 42000, Croatia

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Brno, 602 00, Czechia

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Hradec Králové, 500 05, Czechia

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Jihlava, 586 01, Czechia

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Prague, 140 59, Czechia

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Prague, 150 06, Czechia

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Teplice, 415029, Czechia

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Novartis Investigative Site

Aarhus N, 8200, Denmark

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Esbjerg, 6700, Denmark

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Tallinn, 11315, Estonia

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Tartu, 51014, Estonia

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Limoges, Haute Vienne, 87000, France

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Ajaccio, 20090, France

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Amiens, 80054, France

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Clermont-Ferrand, 63003, France

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Gonesse, 95500, France

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Grenoble, 38043, France

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Lille, 59000, France

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Lille, 59037, France

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Montpellier, 34090, France

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Nancy, 54035, France

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Nice, 06000, France

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Nîmes, 30029, France

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Orsay, 91400, France

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Paris, 75013, France

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Paris, 75940, France

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Poitiers, 86021, France

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Rennes, 35033, France

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Rouen, 76031, France

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Strasbourg, 67000, France

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Toulouse, 31059, France

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Tours, 37044, France

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Freiburg im Breisgau, Baden-Wurttemberg, 79106, Germany

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Mannheim, Baden-Wurttemberg, 68167, Germany

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Munich, Bavaria, 81377, Germany

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Unterhaching, Bavaria, 82008, Germany

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Cottbus, Brandenburg, 03048, Germany

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Halle, Saxony-Anhalt, 06120, Germany

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Erfurt, 99089, Germany

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Giessen, 35392, Germany

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Greifswald, 17475, Germany

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Heidelberg, 69120, Germany

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Ibbenbueren, 49477, Germany

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Itzehoe, 25524, Germany

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Tübingen, 72076, Germany

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Ulm, 89073, Germany

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Novartis Investigative Site

Athens, 115 28, Greece

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Chaïdári, 124 62, Greece

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Ioannina, 455 00, Greece

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Pécs, Baranya, 7623, Hungary

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Budapest, 1033, Hungary

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Novartis Investigative Site

Budapest, 1044, Hungary

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Novartis Investigative Site

Budapest, 1106, Hungary

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Kistarcsa, 2143, Hungary

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Tatabánya, H 2800, Hungary

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Gurugram, Haryana, 122011, India

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Mangalore, Karnataka, 575003, India

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Novartis Investigative Site

Kochi, Kerala, 682025, India

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New Delhi, National Capital Territory of Delhi, 110029, India

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Novartis Investigative Site

New Delhi, National Capital Territory of Delhi, 110060, India

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Chandigarh, Punjab, 160012, India

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Vellore, Tamil Nadu, 632 004, India

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Hyderabad, Telangana, 500082, India

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Novartis Investigative Site

Ashkelon, 7830604, Israel

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Hadera, 3820302, Israel

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Haifa, 3436212, Israel

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Jerusalem, 9112001, Israel

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Ramat Gan, 5265601, Israel

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Rehovot, 7661041, Israel

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Tel Aviv, 6423906, Israel

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Ẕerifin, 7030000, Israel

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Ancona, AN, 60020, Italy

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Bergamo, BG, 24127, Italy

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Foggia, FG, 71122, Italy

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Pozzilli, IS, 86077, Italy

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Pavia, PV, 27100, Italy

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Roma, RM, 00133, Italy

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Roma, RM, 00189, Italy

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Gallarate, VA, 21013, Italy

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Naples, 80138, Italy

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Novartis Investigative Site

Kaunas, 3007, Lithuania

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Chihuahua City, Chihuahua, 31203, Mexico

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Benito Juárez, Mexico City, 03100, Mexico

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Mexico City, Mexico City, 06700, Mexico

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San Luis Potosí City, 78216, Mexico

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Arnhem, Gelderland, 6815 AD, Netherlands

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's-Hertogenbosch, North Brabant, 5223 GZ, Netherlands

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Amsterdam, North Holland, 1081 HV, Netherlands

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Leiden, 2334 CN, Netherlands

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Krakow, Lesser Poland Voivodeship, 30-727, Poland

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Krakow, Poland, 31 531, Poland

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Bydgoszcz, Woj Kujawsko Pomorskie, 85-796, Poland

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Chojnice, 89-600, Poland

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Katowice, 40-081, Poland

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Katowice, 40-686, Poland

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Lodz, 93-113, Poland

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Lublin, 20-410, Poland

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Rzeszów, 35-323, Poland

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Skorzewo, 60-185, Poland

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Warsaw, 01-684, Poland

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Zabrze, 41-800, Poland

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Żory, 44-240, Poland

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Braga, 4710243, Portugal

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Lisbon, 1169-050, Portugal

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Lisbon, 1349-019, Portugal

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Lisbon, 1649-035, Portugal

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Porto, 4200 319, Portugal

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Constanța, ROM, 900123, Romania

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Bucharest, 040215, Romania

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Campulung Muscel, 115100, Romania

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Bratislava, Slovakia, 826 06, Slovakia

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Trnava, Slovakia, 917 02, Slovakia

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Bratislava, 851 01, Slovakia

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Komárno, 945 05, Slovakia

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Nitra, 950 01, Slovakia

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Cape Town, Western Cape, 7405, South Africa

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Barcelona, Barcelona, 08035, Spain

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L'Hospitalet de Llobregat, Barcelona, 08907, Spain

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Jerez de la Frontera, Cadiz, 11407, Spain

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Albacete, Castille-La Mancha, 02006, Spain

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Logroño, La Rioja, 26006, Spain

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Pozuelo de Alarcón, Madrid, 28223, Spain

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Torrejón de Ardoz, Madrid, 28850, Spain

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El Palmar, Murcia, 30120, Spain

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Castilleja de la Cuesta, Sevilla, 41950, Spain

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Valencia, Valencia, 46017, Spain

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Barakaldo, Vizcaya, 48903, Spain

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Alicante, 03010, Spain

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Las Palmas GC, 35010, Spain

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Lleida, 25198, Spain

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Madrid, 28006, Spain

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Madrid, 28009, Spain

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Madrid, 28034, Spain

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Madrid, 28040, Spain

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Málaga, 29010, Spain

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Salamanca, 37007, Spain

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Valencia, 46026, Spain

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Bern, 3010, Switzerland

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Lausanne, 1011, Switzerland

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Brighton, East Sussex, BN2 5BE, United Kingdom

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Romford, Essex, RM7 0AG, United Kingdom

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Coventry, CV2 2DX, United Kingdom

RECRUITING

Novartis Investigative Site

Glasgow, EH9 1LF, United Kingdom

RECRUITING

Novartis Investigative Site

Leeds, LS1 3EX, United Kingdom

RECRUITING

Novartis Investigative Site

London, E1 2AT, United Kingdom

RECRUITING

Novartis Investigative Site

Nottingham, NG7 2UH, United Kingdom

RECRUITING

MeSH Terms

Conditions

Multiple Sclerosis, Chronic ProgressiveMultiple Sclerosis

Interventions

remibrutinib

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Central Study Contacts

Novartis Pharmaceuticals

CONTACT

Novartis Pharmaceuticals

CONTACT

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Double blind on Core part and Open label on Extension part
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

November 4, 2025

First Posted

November 6, 2025

Study Start

November 11, 2025

Primary Completion (Estimated)

December 3, 2030

Study Completion (Estimated)

January 2, 2034

Last Updated

July 29, 2026

Record last verified: 2026-07

Data Sharing

IPD Sharing
Will share

Novartis is committed to sharing with qualified external researchers, access to patient-level data and supporting clinical documents from eligible studies. These requests are reviewed and approved by an independent review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. This trial data availability is according to the criteria and process described on www.clinicalstudydatarequest.com

Locations