NCT07044336

Brief Summary

This is a Phase III, 2-arm, randomized, open label, multicenter, global study assessing the efficacy and safety of puxitatug samrotecan compared to physician's choice of chemotherapy (doxorubicin or paclitaxel) in participants with B7-H4 selected advanced/metastatic EC that progressed following platinum based chemotherapy and anti-PD-1/anti-PD-L1 therapy.

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
700

participants targeted

Target at P75+ for phase_3

Timeline
39mo left

Started Aug 2025

Typical duration for phase_3

Geographic Reach
27 countries

301 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress19%
Aug 2025Jul 2029

First Submitted

Initial submission to the registry

June 23, 2025

Completed
7 days until next milestone

First Posted

Study publicly available on registry

June 30, 2025

Completed
1 month until next milestone

Study Start

First participant enrolled

August 1, 2025

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 20, 2028

Expected
1.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 17, 2029

Last Updated

April 13, 2026

Status Verified

April 1, 2026

Enrollment Period

2.5 years

First QC Date

June 23, 2025

Last Update Submit

April 9, 2026

Conditions

Keywords

Bluestar-Endometrial01AZD8205Puxitatug SamrotecanPuxi-SamPlatinum-based chemotherapyB7-H4advanced/metastaticEndometrial CancerAnti-PD-1Anti-PD-L1antibody-drug conjugateTopoisomerase 1 Inhibitorsuterine neoplasmfemale urogenital neoplasm

Outcome Measures

Primary Outcomes (2)

  • Progression Free Survival (PFS) for Arm A vs Arm B

    PFS is defined as the time from randomization until progression per RECIST 1.1 as assessed by BICR or death due to any cause.

    Approximately 3 years

  • Overall survival (OS) for Arm A vs Arm B

    OS is defined as the time from randomization until the date of death due to any cause.

    Approximately 3 years

Secondary Outcomes (7)

  • Assessment of Overall Response Rate (ORR) for Arm A vs Arm B

    Approximately 3 years

  • Assessment of Duration of response (DoR) for Arm A vs Arm B

    Approximately 3 years

  • Assessment of progression-free survival 2 (PFS2) for Arm A vs Arm B

    Approximately 3 years

  • Time until first subsequent anticancer therapy after discontinuation of the randomized treatment, or death (TFST) for Arm A vs Arm B

    Approximately 3 years

  • Time until the second subsequent anticancer therapy after discontinuation of the first subsequent treatment, or death (TSST) for Arm A vs Arm B

    Approximately 3 years

  • +2 more secondary outcomes

Study Arms (2)

Puxitatug Samrotecan

EXPERIMENTAL

Puxi-Sam IV (intravenous) Q3W .

Drug: Puxitatug Samrotecan

Chemotherapy

ACTIVE COMPARATOR

Physician's choice of chemotherapy Doxorubicin IV Q3W or Paclitaxel IV on Days 1, 8, and 15 in 28 day cycles.

Drug: DoxorubicinDrug: Paclitaxel

Interventions

2.4 mg/kg on Day 1 Q3W Route of administration: IV infusion

Also known as: Puxi-Sam
Puxitatug Samrotecan

60 mg/m2 on Day 1 Q3W Route of administration: IV

Also known as: ADRIAMYCIN®
Chemotherapy

80 mg/m2 on Days 1, 8, and 15 in 28-day cycle Route of Administration: IV

Also known as: TAXOL®
Chemotherapy

Eligibility Criteria

Age18 Years+
Sexfemale(Gender-based eligibility)
Gender Eligibility DetailsFemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed diagnosis of endometrial carcinoma or carcinosarcoma.
  • Recurrent/metastatic EC ie, with radiological or objective evidence of recurrence or progression.
  • Has received prior platinum-based chemotherapy and anti-programmed cell death 1 protein (PD-1)/anti- programmed cell death ligand 1 (PD-L1) therapy, either separately or in combination.
  • A WHO/ECOG performance status of 0 or 1 at Screening.
  • Has radiographically measurable disease by RECIST 1.1

You may not qualify if:

  • Had uterine sarcomas or uterine neuroendocrine carcinoma.
  • Has had a recurrence of endometrial carcinoma or carcinosarcoma more than \> 12 months after completing platinum-based therapy administered in the curative-intent setting without any additional platinum-based therapy received in the recurrent setting.
  • Had previously received treatment with any therapy (approved or investigational) that contained a TOP1i including ADCs .
  • Had previously received treatment with Puxi-Sam or another B7-H4 targeting agent.
  • History of (non-infectious) ILD/pneumonitis that required steroids, has current ILD/pneumonitis, or where suspected ILD/pneumonitis cannot be ruled out by imaging at screening.
  • Has clinically severe pulmonary compromise resulting from intercurrent pulmonary illnesses.
  • Active or previously documented autoimmune or inflammatory disorders

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (307)

Research Site

Tucson, Arizona, 85719, United States

NOT YET RECRUITING

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La Jolla, California, 92037, United States

RECRUITING

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Los Angeles, California, 90095, United States

NOT YET RECRUITING

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Orange, California, 92868, United States

RECRUITING

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Jupiter, Florida, 33458, United States

RECRUITING

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Miami, Florida, 33136, United States

NOT YET RECRUITING

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Miami, Florida, 33176, United States

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Miami Beach, Florida, 33140, United States

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Orlando, Florida, 32806, United States

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West Palm Beach, Florida, 33401, United States

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Honolulu, Hawaii, 96826, United States

NOT YET RECRUITING

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Chicago, Illinois, 60607, United States

NOT YET RECRUITING

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Peoria, Illinois, 61637, United States

RECRUITING

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Urbana, Illinois, 61801, United States

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Fort Wayne, Indiana, 46845, United States

NOT YET RECRUITING

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Indianapolis, Indiana, 46260, United States

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Scarborough, Maine, 04074, United States

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Baltimore, Maryland, 21201, United States

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Baltimore, Maryland, 21231, United States

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Silver Spring, Maryland, 20910, United States

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Ann Arbor, Michigan, 48109, United States

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Ann Arbor, Michigan, 48197, United States

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Detroit, Michigan, 48201, United States

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Minneapolis, Minnesota, 55404, United States

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Camden, New Jersey, 08103, United States

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Paramus, New Jersey, 07652, United States

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Albuquerque, New Mexico, 87109, United States

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Brooklyn, New York, 11220, United States

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Stony Brook, New York, 11794, United States

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The Bronx, New York, 10461, United States

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White Plains, New York, 10601, United States

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Greenville, North Carolina, 27834, United States

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Pinehurst, North Carolina, 28374, United States

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Cincinnati, Ohio, 45220, United States

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Cleveland, Ohio, 44106, United States

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Cleveland, Ohio, 44109, United States

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Columbus, Ohio, 43219, United States

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Dayton, Ohio, 45459, United States

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Hilliard, Ohio, 43026, United States

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Sylvania, Ohio, 43560, United States

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Portland, Oregon, 97239, United States

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Bethlehem, Pennsylvania, 18015, United States

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Hershey, Pennsylvania, 17033, United States

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Pittsburgh, Pennsylvania, 15213, United States

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Pittsburgh, Pennsylvania, 15224, United States

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Willow Grove, Pennsylvania, 19090, United States

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York, Pennsylvania, 17403, United States

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Sioux Falls, South Dakota, 57104, United States

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Sioux Falls, South Dakota, 57105, United States

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Knoxville, Tennessee, 37920, United States

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Nashville, Tennessee, 37232, United States

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Austin, Texas, 78758, United States

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Houston, Texas, 77030, United States

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Tyler, Texas, 75702, United States

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Fairfax, Virginia, 22031, United States

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Falls Church, Virginia, 22042, United States

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Norfolk, Virginia, 23502, United States

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Richmond, Virginia, 23298, United States

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Roanoke, Virginia, 24016, United States

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Kennewick, Washington, 99336, United States

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Seattle, Washington, 98104, United States

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Morgantown, West Virginia, 26505, United States

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Waukesha, Wisconsin, 53188, United States

NOT YET RECRUITING

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Capital Federal, C1417DTB, Argentina

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Ciudad Autonoma Buenos Aires, 1405, Argentina

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Ciudad de Buenos Aires, C1118AAT, Argentina

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Córdoba, 2356, Argentina

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Córdoba, X5004FHP, Argentina

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Cuidad Autónoma de Buenos Aire, C1426ANZ, Argentina

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La Rioja, 5300, Argentina

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Pergamino, B2700CPM, Argentina

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Viedma, R8500ACE, Argentina

NOT YET RECRUITING

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Malvern, 3144, Australia

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Melbourne, 3000, Australia

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Randwick, 2031, Australia

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St Leonards, 2065, Australia

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Subiaco, 6008, Australia

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Westmead, 2145, Australia

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Graz, 8036, Austria

NOT YET RECRUITING

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Innsbruck, 6020, Austria

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Vienna, 1090, Austria

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Brussels, 1070, Belgium

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Brussels, 1200, Belgium

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Charleroi, 6000, Belgium

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Edegem, 2650, Belgium

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Ghent, 9000, Belgium

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Ghent, 9000, Belgium

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Leuven, 3000, Belgium

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Liège, 4000, Belgium

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Namur, 5000, Belgium

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Belém, 66073-005, Brazil

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Belo Horizonte, 30360-680, Brazil

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Bento Gonçalves, 95700-084, Brazil

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Blumenau, 89010-340, Brazil

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Curitiba, 80510-130, Brazil

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Curitiba, 80810-050, Brazil

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Florianópolis, 88020-210, Brazil

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Natal, 59062-000, Brazil

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Porto Alegre, 90020-090, Brazil

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Porto Alegre, 90470-340, Brazil

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Porto Alegre, 90610-001, Brazil

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Recife, 50070-480, Brazil

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Recife, 52010-075, Brazil

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Ribeirão Preto, 14026-040, Brazil

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Rio de Janeiro, 22281-100, Brazil

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Rio de Janeiro, 22775-001, Brazil

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Salvador, 41950-640, Brazil

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São Caetano do Sul, 09541-270, Brazil

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São Paulo, 01317-000, Brazil

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São Paulo, 01323-000, Brazil

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São Paulo, 01323-020, Brazil

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São Paulo, 01509-900, Brazil

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Sorocaba, 18030-005, Brazil

RECRUITING

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Sorocaba, 18052-210, Brazil

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Taubaté, 12030-200, Brazil

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Teresina, 64049-200, Brazil

NOT YET RECRUITING

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Edmonton, Alberta, T6G 1Z2, Canada

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Winnipeg, Manitoba, R3A 1R9, Canada

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Hamilton, Ontario, L8V 5C2, Canada

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Kingston, Ontario, K7L 2V7, Canada

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Montreal, Quebec, H2X 0C1, Canada

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Montreal, Quebec, H3T 1E2, Canada

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Beijing, 100021, China

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Beijing, 100026, China

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Beijing, 100044, China

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Beijing, 100730, China

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Changchun, 130021, China

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Changsha, 410011, China

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Changsha, 410013, China

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Chengdu, 610041, China

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Chongqing, 400030, China

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Dalian, 116023, China

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Fuzhou, 350014, China

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Guangzhou, 510120, China

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Hangzhou, 310006, China

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Hangzhou, 310022, China

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Jinan, 250012, China

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Jinan, 250117, China

NOT YET RECRUITING

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Nanchang, 330006, China

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Nanjing, 210004, China

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Shanghai, 200011, China

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Shanghai, 200025, China

NOT YET RECRUITING

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Shanghai, 200072, China

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Shenyang, 110004, China

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Shenyang, 110042, China

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Shenzhen, 518116, China

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Shijiazhuang, 050011, China

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Tianjin, 300060, China

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Tianjin, 300110, China

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Wenzhou, 325000, China

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Wuhan, 430022, China

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Wuhan, 430030, China

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Xi'an, 710061, China

NOT YET RECRUITING

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Zhanjiang, 524001, China

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Zhengzhou, 450002, China

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Brno, 625 00, Czechia

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Brno, 656 53, Czechia

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Hradec Králové, 500 05, Czechia

NOT YET RECRUITING

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Nový Jičín, 74101, Czechia

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Ostrava, 708 502, Czechia

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Prague, 12808, Czechia

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Prague, 180 81, Czechia

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V Uvalu 84, 150 06, Czechia

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Herlev, 2730, Denmark

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Kuopio, 70210, Finland

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Tampere, 33520, Finland

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Turku, 20520, Finland

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Avignon, 84918, France

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Besançon, 25000, France

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Bordeaux, 33076, France

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Chambray-lès-Tours, 37170, France

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Cholet, 49300, France

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Créteil, 94010, France

NOT YET RECRUITING

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Grenoble, 38000, France

RECRUITING

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Lille, 59000, France

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Limoges, 87042, France

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Lyon, 69008, France

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Nantes, 44000, France

NOT YET RECRUITING

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Nîmes, 30029, France

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Paris, 75014, France

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Paris, 75020, France

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Paris, 75900, France

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Plerin SUR MER, 22190, France

NOT YET RECRUITING

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Rennes, 35000, France

NOT YET RECRUITING

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Toulouse, 31059, France

NOT YET RECRUITING

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Batumi, 6000, Georgia

NOT YET RECRUITING

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Tbilisi, 0159, Georgia

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Tbilisi, 0186, Georgia

NOT YET RECRUITING

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Amberg, 92224, Germany

NOT YET RECRUITING

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Chemnitz, 09116, Germany

NOT YET RECRUITING

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Dresden, 01307, Germany

NOT YET RECRUITING

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Essen, 45130, Germany

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Frankfurt am Main, 60596, Germany

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Freiburg im Breisgau, 79106, Germany

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Hamburg, 20246, Germany

NOT YET RECRUITING

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Heidelberg, 69120, Germany

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Heilbronn, 74078, Germany

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Mainz, 55131, Germany

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Münster, 48149, Germany

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Paderborn, 33161, Germany

NOT YET RECRUITING

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Regensburg, 93053, Germany

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Schwäbisch Hall, 74523, Germany

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Ulm, 89075, Germany

NOT YET RECRUITING

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Witten, 58452, Germany

NOT YET RECRUITING

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Athens, 115 28, Greece

RECRUITING

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Athens, 11528, Greece

NOT YET RECRUITING

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Athens, 14564, Greece

NOT YET RECRUITING

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Thessaloniki, 55236, Greece

RECRUITING

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Budapest, 1082, Hungary

NOT YET RECRUITING

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Budapest, 1122, Hungary

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Debrecen, 4032, Hungary

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Győr, 9024, Hungary

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Ashdod, 7747629, Israel

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Hadera, 38100, Israel

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Haifa, 3109601, Israel

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Holon, 5822012, Israel

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Jerusalem, 9103102, Israel

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Jerusalem, 9112001, Israel

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Nahariya, 2210001, Israel

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Ramat Gan, 5262000, Israel

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Safed, 13100, Israel

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Tel Aviv, 6423906, Israel

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Alessandria, 15121, Italy

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Aviano, 33081, Italy

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Bologna, 40138, Italy

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Catania, 95126, Italy

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Florence, 50134, Italy

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Haifa, 34362, Italy

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Milan, 20132, Italy

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Milan, 20141, Italy

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Milan, 20159, Italy

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Milan, 20162, Italy

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Milan, 35128, Italy

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Monza, 20900, Italy

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Naples, 80131, Italy

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Parma, 43126, Italy

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Pisa, 56100, Italy

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Ponderano, 13875, Italy

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Roma, 00168, Italy

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Torino, 10128, Italy

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Vicenza, 36100, Italy

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Chūōku, 104-0045, Japan

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Hidaka-shi, 350-1298, Japan

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Isehara-shi, 259-1193, Japan

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Kashiwa-shi, 277-8567, Japan

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Kōtoku, 135-8550, Japan

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Kurume-shi, 830-0011, Japan

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Matsuyama, 791-0280, Japan

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Minatoku, 105-8471, Japan

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Nagoya, 464-8681, Japan

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Nakagami-gun, 903-0215, Japan

NOT YET RECRUITING

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Niigata, 951-8510, Japan

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Okayama, 700-8558, Japan

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Osaka, 637086, Japan

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Sapporo, 003-0804, Japan

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Sapporo, 060-8638, Japan

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Sendai, 980-8574, Japan

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Suita, 565-0871, Japan

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Sunto-gun, 411-8777, Japan

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Toon-Shi, 791-0295, Japan

ACTIVE NOT RECRUITING

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Tsu, 514-8507, Japan

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Yokohama, 236-0004, Japan

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Kaunas, LT50009, Lithuania

NOT YET RECRUITING

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Vilnius, 08661, Lithuania

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Vilnius, 8660, Lithuania

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Amsterdam, 1081 HV, Netherlands

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Maastricht, 6202 AZ, Netherlands

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Lodz, 93-338, Poland

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Siedlce, 08-110, Poland

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Singapore, 119082, Singapore

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Singapore, 217562, Singapore

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Ljubljana, 1000, Slovenia

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Maribor, 2000, Slovenia

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Goyang-si, 410-769, South Korea

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Gwangjin-gu, 110-744, South Korea

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Seoul, 03722, South Korea

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Seoul, 06273, South Korea

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Seoul, 135-710, South Korea

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Songpa-gu, 05505, South Korea

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Suwon, 16499, South Korea

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Badalona, 8916, Spain

NOT YET RECRUITING

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Barcelona, 8025, Spain

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Barcelona, 8035, Spain

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Córdoba, 14004, Spain

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El Palmar (Murcia), 30120, Spain

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Hospitalet DEL Llobregat, 8908, Spain

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Madrid, 28033, Spain

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Madrid, 28041, Spain

NOT YET RECRUITING

Research Site

Málaga, 29010, Spain

RECRUITING

Research Site

Oviedo, 33011, Spain

RECRUITING

Research Site

Santiago de Compostela, 15706, Spain

RECRUITING

Research Site

Seville, 41013, Spain

RECRUITING

Research Site

Seville, 41014, Spain

RECRUITING

Research Site

Valencia, 46010, Spain

NOT YET RECRUITING

Research Site

New Taipei City, 220, Taiwan

RECRUITING

Research Site

Taichung, 40705, Taiwan

RECRUITING

Research Site

Tainan, 70403, Taiwan

RECRUITING

Research Site

Taipei, 100, Taiwan

RECRUITING

Research Site

Taipei, 10449, Taiwan

RECRUITING

Research Site

Bebington, CH63 4JY, United Kingdom

RECRUITING

Research Site

Canterbury, CT1 3NG, United Kingdom

RECRUITING

Research Site

Derby, DE22 3NE, United Kingdom

NOT YET RECRUITING

Research Site

London, E1 1BB, United Kingdom

NOT YET RECRUITING

Research Site

London, W2 1NY, United Kingdom

RECRUITING

Research Site

Manchester, M20 4BX, United Kingdom

RECRUITING

Research Site

Northwood, HA6 2RN, United Kingdom

NOT YET RECRUITING

Research Site

Truro, TR1 3LJ, United Kingdom

RECRUITING

MeSH Terms

Conditions

Endometrial NeoplasmsNeoplasm MetastasisUterine Neoplasms

Interventions

DoxorubicinPaclitaxel

Condition Hierarchy (Ancestors)

Genital Neoplasms, FemaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

DaunorubicinAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsAminoglycosidesGlycosidesCarbohydratesTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicDiterpenesTerpenes

Study Officials

  • Brian Slomovitz, MD

    Icahn School of Medicine at Mount Sinai

    PRINCIPAL INVESTIGATOR
  • Stephanie Gaillard, MD, PhD

    Johns Hopkins University - Sidney Kimmel Comprehensive Cancer Center (SKCCC)

    PRINCIPAL INVESTIGATOR
  • Nicole Concin, Prof.

    Head of the Division of General Gynecology and Gynecologic Oncology at the Department of Obstetrics and Gynecology of MedUni Vienna and University

    PRINCIPAL INVESTIGATOR

Central Study Contacts

AstraZeneca Clinical Study Information Center

CONTACT

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Masking Details
Open label
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Single Open-Label
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 23, 2025

First Posted

June 30, 2025

Study Start

August 1, 2025

Primary Completion (Estimated)

January 20, 2028

Study Completion (Estimated)

July 17, 2029

Last Updated

April 13, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal Vivli.org. All requests will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA PhRMA Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the anonymized individual patient-level data via secure research environment Vivli.org. Signed Data Usage Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information.
More information

Locations