NCT06541704

Brief Summary

This study is researching experimental (study) drugs called pozelimab and cemdisiran. The study is focused on participants who have Geographic Atrophy (GA) caused by Age-related Macular Degeneration (AMD). Geographic atrophy is a medical term that refers to later-stage cases of AMD which is an eye condition affecting central vision (what one sees straight ahead). The purpose of this study is to evaluate the progression rate of Geographic Atrophy in eyes of patients treated with cemdisiran alone or in combination with pozelimab compared to those treated with placebo. The study is looking at several other research questions, including:

  • What side effects may happen from taking the study drug(s)
  • How much study drug(s) are in the blood at different times
  • Whether the body makes antibodies against the study drug(s) (which could make the study drug(s) less effective or could lead to side effects)

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
975

participants targeted

Target at P75+ for phase_3

Timeline
73mo left

Started Oct 2024

Longer than P75 for phase_3

Geographic Reach
10 countries

216 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress20%
Oct 2024May 2032

First Submitted

Initial submission to the registry

August 2, 2024

Completed
5 days until next milestone

First Posted

Study publicly available on registry

August 7, 2024

Completed
3 months until next milestone

Study Start

First participant enrolled

October 30, 2024

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 29, 2027

Expected
4.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 21, 2032

Last Updated

May 7, 2026

Status Verified

March 1, 2026

Enrollment Period

3.1 years

First QC Date

August 2, 2024

Last Update Submit

May 6, 2026

Conditions

Keywords

GA secondary to AMD

Outcome Measures

Primary Outcomes (1)

  • Growth rate (slope) of total GA lesion area (mm^2 /year) from baseline, measured by Fundus Autofluorescence (FAF)

    To week 52

Secondary Outcomes (15)

  • Loss of Best Corrected Visual Acuity (BCVA) ≥15 letters [Early Treatment Diabetic Retinopathy Study (ETDRS)] from baseline

    At week 52 and week 104

  • Change from baseline in Low-Contrast quantitative Visual Acuity (LC-qVA)

    At week 52 and week 104

  • Change from baseline in Low-Luminance Low-Contrast quantitative Visual Acuity (LL-LC-qVA)

    At week 52 and week 104

  • Change from baseline in quantitative Contrast Sensitivity Function (qCSF)

    At week 52 and week 104

  • Growth rate (slope) of total GA lesion area (mm^2 /year) from baseline measured by FAF

    To week 104

  • +10 more secondary outcomes

Study Arms (3)

Pozelimab + Cemdisiran treatment group

EXPERIMENTAL

Randomized 1:1:1

Drug: PozelimabDrug: Cemdisiran

Cemdisiran monotherapy treatment group

EXPERIMENTAL

Randomized 1:1:1

Drug: Cemdisiran

Placebo treatment group

PLACEBO COMPARATOR

Randomized 1:1:1

Drug: Placebo

Interventions

Subcutaneous (SC) injection

Also known as: REGN3918
Pozelimab + Cemdisiran treatment group

SC injection

Also known as: ALN-CC5
Cemdisiran monotherapy treatment groupPozelimab + Cemdisiran treatment group

SC injection

Placebo treatment group

Eligibility Criteria

Age50 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Study eye with diagnosis of GA of the macula secondary to AMD as described in the protocol
  • Total GA area in the study eye measuring between ≥2.5 mm\^2 and ≤17.5 mm\^2 as described in the protocol
  • BCVA of 55 letters or better using ETDRS charts (20/80 Snellen equivalent) in the study eye as described in the protocol
  • Sufficiently clear ocular media, adequate pupillary dilation and fixation to permit quality fundus imaging in the study eye as described in the protocol
  • Willing and able to comply with clinic visits and study-related procedures, including completion of the full series of meningococcal vaccinations and pneumococcal vaccination required per protocol

You may not qualify if:

  • GA in either eye due to causes other than AMD, such as Stargardt disease, cone rod dystrophy or toxic maculopathies like hydroxychloroquine maculopathy
  • History or current evidence of Macular Neovascularization (MNV) and/or exudation or Peripapillary Choroidal Neovascularization (PPCNV) in either eye as described in the protocol
  • Prior or current Intravitreal (IVT) treatment of any kind for any indication in study eye or fellow eye, except approved or investigational IVT complement inhibitor therapy or anti-VEGF therapy, as long as last dose was ≥6 months prior to randomization
  • Prior intraocular surgery except cataract extraction or minimally invasive glaucoma surgery in study eye as long as date of these procedures was ≥3 months prior to randomization
  • Comorbid progressive ocular condition (eg, diabetic retinopathy, macular edema, uncontrolled glaucoma, full thickness macular hole) in study eye that could affect central vision and confound study
  • Any ophthalmologic condition that reduces the clarity of the media and that, in the opinion of the investigator interferes with ophthalmologic examination of the study eye (e.g., advanced cataract or corneal abnormalities) as described in the protocol
  • History or current use of systemic complement inhibitor therapy within 6 months prior to randomization as described in the protocol
  • History of solid organ or bone marrow transplantation
  • Use of chronic (\>14 days) systemic corticosteroids (oral or parenteral, ≥20 mg oral prednisone or equivalent) within the previous 30 days prior to the first screening visit as described in the protocol
  • Current or prior use of systemic immunosuppressive therapy other than corticosteroids within 12 months prior to randomization or the likelihood of treatment with any such agent during the study inclusive of the screening period as described in the protocol
  • Not meeting meningococcal or pneumococcal vaccination requirements as described in the protocol
  • Carrier of Neisseria meningitidis based on culture collected during screening
  • Has a hemoglobin A1C ≥ 8.0% during screening as described in the protocol

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (216)

Barnet Dulaney Perkins Eye Center-Ophthamalogy

Chandler, Arizona, 85224, United States

RECRUITING

Barnet Dulaney Perkins Eye Center

Phoenix, Arizona, 85016, United States

RECRUITING

Associated Retina Consultants

Phoenix, Arizona, 85020, United States

RECRUITING

Retinal Research Institute

Phoenix, Arizona, 85053, United States

RECRUITING

Retina Macula Institute of Arizona

Scottsdale, Arizona, 85255, United States

RECRUITING

Retina Associates of Tuscan

Tucson, Arizona, 85712, United States

RECRUITING

Retina Partners of Northwest Arkansas, PLLC

Springdale, Arkansas, 72764, United States

RECRUITING

Retina Vitreous Associates Medical Group

Beverly Hills, California, 90211, United States

RECRUITING

Retina Specialists of Beverly Hills- Department of Ophthalmology

Beverly Hills, California, 90212, United States

RECRUITING

The Retina Partners

Encino, California, 91436, United States

RECRUITING

Eye Medical Center of Fresno

Fresno, California, 93720, United States

RECRUITING

Retina Consultants of Orange County

Fullerton, California, 92835, United States

RECRUITING

Salehi Retina Institute dba Retina Associates of Southern California

Huntington Beach, California, 92647, United States

RECRUITING

University of California Irvine

Irvine, California, 92617, United States

RECRUITING

University of California San Diego, Jacobs Retina Center

La Jolla, California, 92093, United States

RECRUITING

South Coast Retina Center

Long Beach, California, 90807, United States

RECRUITING

American Institute of Research

Los Angeles, California, 90017, United States

RECRUITING

Kaiser Permanente Los Angeles Medical Center

Los Angeles, California, 90027, United States

RECRUITING

Jules Stein Eye Institute in David Geffen School of Medicine at Ucla

Los Angeles, California, 90095, United States

RECRUITING

Retinal Consultants Medical Group Inc Modesto

Modesto, California, 95356, United States

RECRUITING

Northern California Retina Vitreous Associates Medical Group, Inc.

Mountain View, California, 94040, United States

RECRUITING

California Retina Consultants

Oxnard, California, 93036, United States

RECRUITING

Desert Retina Consultants

Palm Desert, California, 92211, United States

WITHDRAWN

California Eye Specialists Medical Group Inc.

Pasadena, California, 91107, United States

RECRUITING

Retina Consultants San Diego

Poway, California, 92064, United States

RECRUITING

California Eye Specialists Medical Group, Inc.

Redlands, California, 92373, United States

RECRUITING

Optic Eye Care

Rowland Heights, California, 91748, United States

RECRUITING

UC Davis Health Eye Center

Sacramento, California, 95817, United States

RECRUITING

Vrmg Inc

Sacramento, California, 95825, United States

RECRUITING

Retinal Consultants Medical Group (RCMG) - Greenback Lane Retina Center

Sacramento, California, 95841, United States

RECRUITING

West Coast Retina Medical Group, Inc.

San Francisco, California, 94109, United States

RECRUITING

Orange County Retina Medical Group

Santa Ana, California, 92705, United States

RECRUITING

Macula Retina Vitreous Research Institute

Torrance, California, 90503, United States

RECRUITING

University of Colorado

Aurora, Colorado, 80045, United States

RECRUITING

Retina Consultants of Southern Colorado

Colorado Springs, Colorado, 80909, United States

RECRUITING

Retina Specialists of Colorado - Denver

Denver, Colorado, 80222, United States

RECRUITING

Southwest Retina Research Center

Durango, Colorado, 81303, United States

RECRUITING

Colorado Retina - Lakewood

Lakewood, Colorado, 80228, United States

RECRUITING

Eye care Center of Northern Colorado doing business as Advanced Vision Research Institute

Longmont, Colorado, 80503, United States

RECRUITING

Retina Group of New England

Waterford, Connecticut, 06385, United States

TERMINATED

Advanced Retina Institute-Ophthalmology

Bonita Springs, Florida, 34134, United States

RECRUITING

Advanced Research

Coral Springs, Florida, 33067, United States

RECRUITING

Retina Group of Florida

Fort Lauderdale, Florida, 33308, United States

RECRUITING

National Ophthalmic Research Institute

Fort Myers, Florida, 33912, United States

WITHDRAWN

ClearVista Clinical Research, Retina Center Tampa Bay

Hudson, Florida, 34667, United States

RECRUITING

Florida Retina Institute, Jacksonville Perimeter Park- Ophthalmology

Jacksonville, Florida, 32216, United States

RECRUITING

Florida Retina Consultants

Lakeland, Florida, 33805, United States

RECRUITING

Bascom Palmer Eye Institute

Naples, Florida, 34103, United States

RECRUITING

Florida Retina Institute - Orlando

Orlando, Florida, 32806, United States

RECRUITING

Retina Care Specialists

Palm Beach Gardens, Florida, 33410, United States

RECRUITING

Eye Associates of Pinellas

Pinellas Park, Florida, 33782, United States

RECRUITING

Retina Group of Florida, RAS-Sarasota Retina Center-Ophthalmology

Sarasota, Florida, 34232, United States

RECRUITING

Retina Vitreous Associates of Florida Saint Petersburg

St. Petersburg, Florida, 33711, United States

RECRUITING

University of South Florida Ophthalmology

Tampa, Florida, 33612, United States

RECRUITING

Center for Retina and Macular Disease

Winter Haven, Florida, 33880, United States

RECRUITING

Southeast Retina Center

Augusta, Georgia, 30909, United States

RECRUITING

Georgia Retina - Marietta

Marietta, Georgia, 30060, United States

RECRUITING

University of Illinois at Chicago

Chicago, Illinois, 60612, United States

RECRUITING

Retinal Vitreal Consultants

Chicago, Illinois, 60616, United States

RECRUITING

The University of Chicago

Chicago, Illinois, 60637, United States

RECRUITING

University Retina and Macula Associates PC - Lemont

Lemont, Illinois, 60439, United States

RECRUITING

Illinois Retina Associates

Oak Park, Illinois, 60304, United States

RECRUITING

Springfield Clinic Main Campus East

Springfield, Illinois, 62703, United States

RECRUITING

Retina Associates, LLC

Lenexa, Kansas, 66215, United States

RECRUITING

University of Louisville

Louisville, Kentucky, 40202, United States

RECRUITING

Retina Associates New Orleans

Metairie, Louisiana, 70006, United States

RECRUITING

Ross Davis Retina

Metairie, Louisiana, 70006, United States

RECRUITING

Ochsner Health

New Orleans, Louisiana, 70121, United States

RECRUITING

Eye Assoc. of NE LA dba Haik Humble Eye Ctr

West Monroe, Louisiana, 71291, United States

RECRUITING

Eye Associates of Northeast Louisiana dba Haik Humble Eye Center

West Monroe, Louisiana, 71291, United States

RECRUITING

The Retina Care Center

Baltimore, Maryland, 21209, United States

RECRUITING

The Retina Group of Washington

Chevy Chase, Maryland, 20815, United States

RECRUITING

Cumberland Valley Retina Consultants-Ophthalmology

Hagerstown, Maryland, 21740, United States

RECRUITING

Mid Atlantic Retina Specialist

Hagerstown, Maryland, 21740, United States

RECRUITING

Massachusetts Eye And Ear Infirmary

Boston, Massachusetts, 02114, United States

RECRUITING

Opthalmic Consultants of Boston

Boston, Massachusetts, 02114, United States

RECRUITING

New England Retina Consultants, PC

Springfield, Massachusetts, 01107, United States

RECRUITING

Retina Associates of Michigan

Grand Blanc, Michigan, 48439, United States

RECRUITING

Mississippi Retina Associates

Madison, Mississippi, 39110, United States

RECRUITING

Deep Blue Retina Clinical Research PLLC

Southaven, Mississippi, 38671, United States

RECRUITING

Retina Research Institute, LLC

St Louis, Missouri, 63144, United States

RECRUITING

Mid Atlantic Retina - Cherry Hill

Cherry Hill, New Jersey, 08034, United States

RECRUITING

New Jersey Retina

Teaneck, New Jersey, 07666, United States

RECRUITING

New Jersey Retina

Toms River, New Jersey, 08755, United States

RECRUITING

Vision Research Center at Eye Associates of New Mexico

Albuquerque, New Mexico, 87109, United States

RECRUITING

University of New Mexico, HSC

Albuquerque, New Mexico, 87131, United States

RECRUITING

Sight MD

Brentwood, New York, 11717, United States

RECRUITING

Retina Vitreous Surgeons of Central New York, PC

Liverpool, New York, 13088, United States

RECRUITING

MaculaCare, PLLC

New York, New York, 10021, United States

RECRUITING

New York Ear & Eye- East 85th

New York, New York, 10028, United States

RECRUITING

Northwell Health- Manhattan, Ear, Eye and Throat Hospital- Ophthalmology

New York, New York, 10065, United States

RECRUITING

Retina Associates of New York, Upper East Side

New York, New York, 10075, United States

RECRUITING

Seeta Eye center

Poughkeepsie, New York, 12603, United States

RECRUITING

Western Carolina Retinal Associates

Asheville, North Carolina, 28803, United States

RECRUITING

NC Retina Associates

Cary, North Carolina, 27511, United States

RECRUITING

Graystone Eye

Hickory, North Carolina, 28602, United States

RECRUITING

North Carolina Retina Associates

Wake Forest, North Carolina, 27587, United States

RECRUITING

Piedmont Retina Specialist

Winston-Salem, North Carolina, 27103, United States

RECRUITING

Cincinnati Eye Institute

Cincinnati, Ohio, 45242, United States

RECRUITING

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

RECRUITING

The Ohio State University

Columbus, Ohio, 43212, United States

RECRUITING

Midwest Retina, Inc

Dublin, Ohio, 43016, United States

RECRUITING

Retina Vitreous Center - Edmond

Edmond, Oklahoma, 73013, United States

RECRUITING

Tulsa Retina Consultants

Tulsa, Oklahoma, 74114, United States

RECRUITING

Verum Research LLC

Eugene, Oregon, 97401, United States

RECRUITING

Retina Northwest, The Highlands Building

Portland, Oregon, 97221, United States

RECRUITING

EyeHealth Northwest

Portland, Oregon, 97225, United States

RECRUITING

OHSU-Casey Eye Institute, Marquam Hill-Ophthalmology

Portland, Oregon, 97239, United States

RECRUITING

Cascade Medical Research Institute LLC

Springfield, Oregon, 97477, United States

RECRUITING

Mid Atlantic Retina

Bethlehem, Pennsylvania, 18017, United States

RECRUITING

Erie Retinal Surgery & Erie Retina Research

Erie, Pennsylvania, 16507, United States

RECRUITING

Mid Atlantic Retina, Wills Eye Hospital

Philadelphia, Pennsylvania, 19107, United States

RECRUITING

Vision Research Solutions - the Eye Institute

Philadelphia, Pennsylvania, 19141, United States

RECRUITING

Sewickley Eye Group

Sewickley, Pennsylvania, 15143, United States

RECRUITING

Retina Consultants of Carolina

Greenville, South Carolina, 29605, United States

RECRUITING

Charleston Neuroscience Institute LLC

Ladson, South Carolina, 29456, United States

RECRUITING

Charleston Neuroscience Institute, LLC

Mt. Pleasant, South Carolina, 29464, United States

RECRUITING

Palmetto Retina Center

West Columbia, South Carolina, 29169, United States

RECRUITING

Black Hills Regional Eye Institute

Rapid City, South Dakota, 57701, United States

RECRUITING

Tennessee Retina, PC

Nashville, Tennessee, 37203, United States

RECRUITING

Vanderbilt Eye Institute

Nashville, Tennessee, 37232, United States

RECRUITING

Retina Research Institute of Texas

Abilene, Texas, 79606, United States

RECRUITING

Austin Research Center for Retina

Austin, Texas, 78705, United States

RECRUITING

Austin Retina Associates

Austin, Texas, 78705, United States

RECRUITING

Austin Clinical Research LLC

Austin, Texas, 78750, United States

WITHDRAWN

Retina Consultants Texas

Bellaire, Texas, 77401, United States

RECRUITING

Star Retina PLLC

Burleson, Texas, 76028, United States

RECRUITING

Retina Foundation of the Southwest

Dallas, Texas, 75231, United States

RECRUITING

Texas Retina Associates

Dallas, Texas, 75231, United States

RECRUITING

University of Texas Southwestern Medical Center

Dallas, Texas, 75390, United States

RECRUITING

Retina Consultants of Texas

Katy, Texas, 77494, United States

RECRUITING

Valley Retina Institute, P.A.

McAllen, Texas, 78503, United States

RECRUITING

Red River Research Partners (Formerly AXIS Clinical)

Plano, Texas, 75024, United States

RECRUITING

Austin Retina Associates

Round Rock, Texas, 78681, United States

RECRUITING

Medical Center Ophthalmology Associates

San Antonio, Texas, 78240, United States

RECRUITING

Retina Associates of South Texas

San Antonio, Texas, 78240, United States

RECRUITING

Retina Consultants of Texas

San Antonio, Texas, 78240, United States

RECRUITING

Retina Consultants of Texas Brown Retina Institute

San Antonio, Texas, 78251, United States

RECRUITING

Retina Center of Texas

Southlake, Texas, 76092, United States

RECRUITING

Retina Consultants Texas

The Woodlands, Texas, 77384, United States

RECRUITING

Tyler Retina Research Institute- Ophthalmology

Tyler, Texas, 75703, United States

RECRUITING

Retina Associates Of Utah Retina Specialist

Salt Lake City, Utah, 84107, United States

RECRUITING

Rocky Mountain Retina Consultants

Salt Lake City, Utah, 84107, United States

RECRUITING

Salt Lake Retina- Ophthalmology

West Jordan, Utah, 84088, United States

RECRUITING

University of Vermont

Burlington, Vermont, 05401, United States

RECRUITING

Southeastern Retina Associates

Bristol, Virginia, 24201, United States

RECRUITING

Retina Group of Washington

Fairfax, Virginia, 22031, United States

RECRUITING

Piedmont Eye Center

Lynchburg, Virginia, 24502, United States

RECRUITING

Virginia Eye Institute

Richmond, Virginia, 23226, United States

RECRUITING

Retina Institute of Virginia

Richmond, Virginia, 23235, United States

COMPLETED

Spokane Eye Clinical Research

Spokane, Washington, 99204, United States

RECRUITING

West Virginia University Eye Institute

Morgantown, West Virginia, 26506, United States

RECRUITING

Medical University Graz

Graz, Styria, 8036, Austria

RECRUITING

Medical University of Vienna

Vienna, 1090, Austria

RECRUITING

VIROS - Vienna Institute for Research in Ocular Surgery

Vienna, 1140, Austria

RECRUITING

Retina Centre of Ottawa - Department of Ophthalmology

Ottawa, Ontario, K2B 7E9, Canada

RECRUITING

Centre Hospitalier Universitaire de Quebec Universite Laval

Québec, G1S 4L8, Canada

RECRUITING

Centre Hospitalier Universitaire de Nice

Nice, Alpes Maritimes, 6002, France

RECRUITING

Hopital Saint Joseph

Marseille, Bouches Du Rhone, 13008, France

RECRUITING

Centre Hospitalier Universitaire De Poitiers

Poitiers, New Aquitaine, 86000, France

RECRUITING

Toulouse University Hospital

Toulouse, Occitanie, 31059, France

RECRUITING

Centre Hospitalier Intercommunal de Creteil

Créteil, 94010, France

RECRUITING

Centre Hospitalier Universitaire Francois Mitterrand

Dijon, 21000, France

RECRUITING

Hopital De La Croix-Rousse

Lyon, 69317, France

RECRUITING

Pole Vision Val d'Ouest

Lyon, 69317, France

RECRUITING

Centre Monticelli Paradis

Marseille, 13008, France

RECRUITING

Centre Hospitalier Universitaire de Nantes

Nantes, 44000, France

RECRUITING

Hopital Lariboisiere

Paris, 75010, France

RECRUITING

University of Ulm

Ulm, Baden-Wurttemberg, 89081, Germany

RECRUITING

Charite - Universitaetsmedizin Berlin

Berlin, Brandenburg, 12203, Germany

RECRUITING

Augenzentrum Frankfurt

Frankfurt am Main, Hesse, 60549, Germany

RECRUITING

Universitaetsklinikum Marburg, Klinik fuer Augenheilkunde

Marburg, Hesse, 35043, Germany

RECRUITING

Dietrich Bonhoeffer Klinikum

Neubrandenburg, Mecklenburg-Vorpommern, 17036, Germany

RECRUITING

Universitatsklinikum Bonn

Bonn, North Rhine-Westphalia, 53127, Germany

RECRUITING

Klinik fur Augenheilkunde Universitatsklinikum Dusseldorf

Düsseldorf, North Rhine-Westphalia, 40225, Germany

RECRUITING

Universitaetsklinikum Muenster

Münster, North Rhine-Westphalia, 48149, Germany

RECRUITING

Klinikum Ludwigshafen Augenklinik

Ludwigshafen am Rhein, Rhineland-Palatinate, 67063, Germany

RECRUITING

Saarland University Medical Center

Homburg, Saarland, 66421, Germany

RECRUITING

Knappschaftsklinikum Saar GmbH- Eye Clnic Sulzbach

Sulzbach, Saarland, 66280, Germany

RECRUITING

University Hospital Hamburg Eppendorf

Hamburg, 20246, Germany

RECRUITING

University Medical Center of the Johannes Gutenberg-University Mainz

Mainz, 55131, Germany

RECRUITING

St. Franziskus-Hospital

Münster, 48145, Germany

RECRUITING

Ganglion Medical Center

Pécs, Baranya, 7621, Hungary

RECRUITING

University Of Szeged

Szeged, Csongrad-Csanad, 6720, Hungary

RECRUITING

University Of Debrecen, Hungary

Debrecen, Hajdú-Bihar, 4032, Hungary

RECRUITING

Semmelweis University

Budapest, 1085, Hungary

RECRUITING

Budapest Retina Associates

Budapest, 1133, Hungary

RECRUITING

University Hospital PTV

Rome, Lazio, 00133, Italy

RECRUITING

Fondazione Policlinico Gemelli

Rome, Lazio, 00168, Italy

RECRUITING

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, Lombardy, 20122, Italy

RECRUITING

IRCCS MultiMedica

Milan, Lombardy, 20123, Italy

RECRUITING

Ospedale San Raffaele (HSR) - Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS)

Milan, Milano, 20132, Italy

RECRUITING

Azienda Ospedaliero Universitaria Careggi

Florence, Tuscany, 50134, Italy

RECRUITING

Azienda Ospedaliero Universitaria delle Marche

Ancona, 60126, Italy

RECRUITING

Universita degli Studi di Milano

Milan, 20157, Italy

RECRUITING

Fondazione G.B.Bietti Per Lo Studio E La Ricerca In Oftalmologia

Rome, 00184, Italy

RECRUITING

Oftalmika Sp. z o.o.

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, 85-631, Poland

RECRUITING

Caminomed

Tarnowskie Góry, Silesian Voivodeship, 42-600, Poland

RECRUITING

Centrum Diagnostyki I Mikrochirurgii Oka Lens Sp zoo

Olsztyn, Warmian-Masurian Voivodeship, 10-424, Poland

RECRUITING

Hospital Arruzafa

Córdoba, Andalusia, 14012, Spain

RECRUITING

Bellvitge University Hospital

L'Hospitalet de Llobregat, Barcelona, 8907, Spain

RECRUITING

Hospital de Terrassa (Consorci Sanitari de Terrassa)

Terrassa, Barcelona, 08227, Spain

RECRUITING

Oftalvist Clinic. IMED Hospital

Burjassot, Valencia, 46100, Spain

RECRUITING

Centro de Oftalmologia Barraquer

Barcelona, 08021, Spain

RECRUITING

Instituto de Microcirugia Ocular

Barcelona, 08035, Spain

RECRUITING

Institut Catala De Retina S.L.

Barcelona, 8022, Spain

RECRUITING

Hospital Universitario Virgen Macarena

Seville, 41009, Spain

RECRUITING

Fundacion Aiken De La Comunitat Valenciana

Valencia, 46004, Spain

RECRUITING

Hospital Clinico Universitario Lozano Blesa. IIS Aragon

Zaragoza, 50009, Spain

RECRUITING

Miguel Servet University Hospital

Zaragoza, 50009, Spain

RECRUITING

Liverpool University Hospitals NHS Foundation Trust-Royal Liverpool University Hospital, St Paul's Eye Unit-Ophthalmology

Liverpool, Merseyside, L7 8XP, United Kingdom

RECRUITING

York and Scarborough Teaching Hospitals NHS Foundation Trust

York, North Yorkshire, YP31 8HE, United Kingdom

RECRUITING

University Hospitals Bristol NHS Foundation Trust

Bristol, BS1 2LX, United Kingdom

RECRUITING

Moorfields Eye Hospital NHS Foundation Trust, Moorfields Eye Hospital

London, EC1V 2PD, United Kingdom

RECRUITING

Imperial College Healthcare NHS Trust

London, NW1 5QH, United Kingdom

RECRUITING

The Newcastle Upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, NE1 4LP, United Kingdom

RECRUITING

MeSH Terms

Conditions

Macular DegenerationGeographic Atrophy

Condition Hierarchy (Ancestors)

Retinal DegenerationRetinal DiseasesEye Diseases

Study Officials

  • Clinical Trial Management

    Regeneron Pharmaceuticals

    STUDY DIRECTOR

Central Study Contacts

Clinical Trials Administrator

CONTACT

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 2, 2024

First Posted

August 7, 2024

Study Start

October 30, 2024

Primary Completion (Estimated)

November 29, 2027

Study Completion (Estimated)

May 21, 2032

Last Updated

May 7, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

All Individual Patient Data (IPD) that underlie publicly available results will be considered for sharing.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR, ANALYTIC CODE
Time Frame
When Regeneron has: * received marketing authorization from major health authorities (e.g., FDA, European Medicines Agency (EMA), Pharmaceuticals and Medical Devices Agency (PMDA), etc.) for the product and indication or has globally discontinued development of the product for all indications on or after April 2020 and has no plans for future development * made the study results publicly available (e.g., scientific publication, scientific conference, clinical trial registry) * the legal authority to share the data, and * ensured the ability to protect participant privacy.
Access Criteria
Qualified researchers can submit a proposal for access to individual patient or aggregate level data from a Regeneron-sponsored clinical trial through Vivli. Regeneron's Independent Research Request Evaluation Criteria can be found at: https://www.regeneron.com/sites/default/files/Regeneron-External-Data-Sharing-Policy-and-Independent-Research-Request-Evaluation-Criteria.pdf
More information

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