NCT06360354

Brief Summary

The study aims to determine maximum tolerated dose (MTD) or recommended combination dose of the MTA-cooperative PRMT5 inhibitor Anvumetostat administered in combination with other therapies in adult participants with metastatic or locally advanced methylthioadenosine phosphorylase (MTAP)-deleted gastrointestinal, biliary tract, or pancreatic cancers. The study also aims to determine the safety profile of Anvumetostat administered in combination with other therapies in adult participants with metastatic or locally advanced MTAP-deleted gastrointestinal, biliary tract, or pancreatic cancers.

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
350

participants targeted

Target at P75+ for phase_1

Timeline
34mo left

Started May 2024

Longer than P75 for phase_1

Geographic Reach
16 countries

77 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress41%
May 2024Feb 2029

First Submitted

Initial submission to the registry

April 8, 2024

Completed
3 days until next milestone

First Posted

Study publicly available on registry

April 11, 2024

Completed
2 months until next milestone

Study Start

First participant enrolled

May 29, 2024

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 26, 2027

Expected
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

February 25, 2029

Last Updated

March 31, 2026

Status Verified

March 1, 2026

Enrollment Period

2.7 years

First QC Date

April 8, 2024

Last Update Submit

March 26, 2026

Conditions

Keywords

Advanced CancerMethylthioadenosine PhosphorylaseAMG 193Oncology

Outcome Measures

Primary Outcomes (3)

  • Number of Participants Experiencing Dose Limiting Toxicities (DLT)

    Up to 28 days

  • Number of Participants Experiencing Treatment Emergent Adverse Events (TEAE)

    Any clinically significant changes in vital signs, electrocardiogram, or lab parameters will be recorded as TEAEs.

    Up to approximately 2 years

  • Number of Participants Experiencing Serious Adverse Events (SAE)

    Up to approximately 2 years

Secondary Outcomes (12)

  • Objective Response (OR) per Response Evaluation Criteria in Solid Tumors (RECIST v1.1)

    Up to approximately 2 years

  • Disease Control (DC) per RECIST v1.1

    Up to approximately 2 years

  • Duration of Response (DOR) per RECIST v1.1

    Up to approximately 2 years

  • Time to Response (TTR) per RECIST v1.1

    Up to approximately 2 years

  • Overall Survival (OS) per RECIST v1.1

    Up to approximately 2 years

  • +7 more secondary outcomes

Study Arms (4)

Subprotocol B: Pancreatic Ductal Adenocarcinoma (PDAC) Arm A

EXPERIMENTAL

Part 1: Participants with MTAP-deleted PDAC will receive doses of Anvumetostat orally in combination with gemcitabine and nab-paclitaxel IV. Part 2: Participants with MTAP-deleted PDAC will receive the recommended dose of Anvumetostat in combination with gemcitabine and nab-paclitaxel.

Drug: AnvumetostatDrug: GemcitabineDrug: Nab-paclitaxel

Subprotocol B: PDAC Arm B

EXPERIMENTAL

Part 1: Participants with MTAP-deleted PDAC will receive doses of Anvumetostat orally in combination with mFOLFIRINOX (irinotecan, fluorouracil, leucovorin calcium, oxaliplatin) IV. Part 2: Participants with MTAP-deleted PDAC will receive the recommended dose of Anvumetostat in combination with mFOLFIRINOX.

Drug: AnvumetostatDrug: Modified FOLFIRINOX

Subprotocol C: Dose Exploration

EXPERIMENTAL

Part 1: Participants with MTAP-deleted PDAC will receive oral doses of Anvumetostat and RMC-6236.

Drug: AnvumetostatDrug: RMC-6236

Subprotocol C: Dose Expansion

EXPERIMENTAL

Part 2: Participants with MTAP-deleted PDAC will receive oral doses of Anvumetostat andRMC-6236.

Drug: AnvumetostatDrug: RMC-6236

Interventions

Administered IV

Subprotocol B: Pancreatic Ductal Adenocarcinoma (PDAC) Arm A

Administered IV

Subprotocol B: Pancreatic Ductal Adenocarcinoma (PDAC) Arm A

Modified FOLFIRINOX consists of irinotecan, 5-FU, LV, and oxaliplatin administered IV

Subprotocol B: PDAC Arm B

Administered orally

Subprotocol C: Dose ExpansionSubprotocol C: Dose Exploration

Administered Orally

Also known as: AMG 193
Subprotocol B: PDAC Arm BSubprotocol B: Pancreatic Ductal Adenocarcinoma (PDAC) Arm ASubprotocol C: Dose ExpansionSubprotocol C: Dose Exploration

Eligibility Criteria

Age18 Years - 100 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥ 18 years (or ≥ legal age within the country if it is older than 18 years).
  • Histologically or cytologically confirmed diagnosis of metastatic and/or unresectable (locally advanced) adenocarcinoma of the pancreas.
  • Tumor tissue (FFPE sample) or an archival block must be available. Participants without archived tumor tissue available may be allowed to enroll by undergoing tumor biopsy before dosing.
  • Homozygous MTAP-deletion.
  • Disease measurable as defined by RECIST v1.1.
  • Adequate organ function as defined in the protocol.

You may not qualify if:

  • Prior treatment with a MAT2A inhibitor or a PRMT5 inhibitor.
  • Radiation therapy within 28 days of first dose.
  • Major surgery within 28 days of first dose of Anvumetostat.
  • Gastrointestinal tract disease causing the inability to take PO medication, malabsorption syndrome, requirement for IV alimentation, gastric/jejunal tube feeds, uncontrolled inflammatory gastrointestinal disease (eg, Crohn's disease, ulcerative colitis).
  • History of solid organ transplantation.
  • Subprotocol C
  • Age ≥ 18 years (or ≥ legal age within the country if it is older than 18 years).
  • Histologically or cytologically confirmed diagnosis of metastatic and/or unresectable (locally advanced) adenocarcinoma of the pancreas.
  • Homozygous MTAP-deletion.
  • Rat Sarcoma Viral Oncogene Homolog (RAS) mutation
  • Received at least 1 prior systemic therapy for advanced or metastatic PDAC.
  • Disease measurable as defined by RECIST v1.1.
  • Adequate organ function as defined in the protocol.
  • Prior treatment with aMAT2A inhibitor, a PRMT5 inhibitor, or a MAPK pathway inhibitor, including KRAS inhibitors.
  • Gastrointestinal tract disease causing the inability to take PO medication, malabsorption syndrome, requirement for IV alimentation, gastric/jejunal tube feeds, uncontrolled inflammatory gastrointestinal disease (eg, Crohn's disease, ulcerative colitis).
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (77)

Comprehensive Blood and Cancer Center

Bakersfield, California, 93309, United States

RECRUITING

City of Hope National Medical Center

Duarte, California, 91010, United States

RECRUITING

City of Hope Orange County Lennar Foundation Cancer Center

Duarte, California, 91010, United States

RECRUITING

University of California San Diego Moores Cancer Center

La Jolla, California, 92093, United States

RECRUITING

Translational Research in Oncology US Inc, Trio Central Pharmacy

Los Angeles, California, 90095, United States

RECRUITING

University of California Los Angeles

Santa Monica, California, 90404, United States

RECRUITING

Rocky Mountain Cancer Centers

Aurora, Colorado, 80012, United States

RECRUITING

Hartford Hospital

Hartford, Connecticut, 06106, United States

RECRUITING

Yale University

New Haven, Connecticut, 06520, United States

RECRUITING

Norwalk Hospital

Norwalk, Connecticut, 06856, United States

RECRUITING

University of Chicago

Chicago, Illinois, 60637, United States

RECRUITING

Indiana University

Indianapolis, Indiana, 46202, United States

RECRUITING

Norton Cancer Institute

Louisville, Kentucky, 40202, United States

RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

RECRUITING

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

RECRUITING

Washington University

St Louis, Missouri, 63110, United States

RECRUITING

University of Nebraska

Omaha, Nebraska, 68198, United States

RECRUITING

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89169, United States

TERMINATED

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

RECRUITING

Duke University

Durham, North Carolina, 27710, United States

RECRUITING

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

RECRUITING

United States Oncology Regulatory Affairs Corporate Office

Nashville, Tennessee, 37203, United States

RECRUITING

Oncology Consultants Cancer Center

Houston, Texas, 77030, United States

TERMINATED

US Oncology Research Investigational Products Center

Irving, Texas, 75063, United States

RECRUITING

University of Virginia Cancer Center

Charlottesville, Virginia, 22903, United States

RECRUITING

Virginia Cancer Specialists PC

Fairfax, Virginia, 22031, United States

RECRUITING

Fred Hutchinson Cancer Center

Seattle, Washington, 98106, United States

RECRUITING

Northwest Medical Specialties, PLLC

Tacoma, Washington, 98405, United States

RECRUITING

Northwest Cancer Specialists - Vancouver

Vancouver, Washington, 98684, United States

COMPLETED

Chris OBrien Lifehouse

Camperdown, New South Wales, 2050, Australia

RECRUITING

GenesisCare -North Shore Oncology

St Leonards, New South Wales, 2065, Australia

RECRUITING

The Queen Elizabeth Hospital

Woodville South, South Australia, 5011, Australia

RECRUITING

Austin Health, Austin Hospital

Heidelberg, Victoria, 3084, Australia

RECRUITING

Peter MacCallum Cancer Centre

Melbourne, Victoria, 3000, Australia

RECRUITING

Epworth Healthcare

St Albans, Victoria, 3021, Australia

RECRUITING

Universite Catholique de Louvain Cliniques Universitaires Saint Luc

Brussels, 1200, Belgium

RECRUITING

Universitair Ziekenhuis Antwerpen

Edegem, 2650, Belgium

RECRUITING

Universitair Ziekenhuis Leuven - Campus Gasthuisberg

Leuven, 3000, Belgium

RECRUITING

Arthur J E Child Comprehensive Cancer Centre

Calgary, Alberta, T2N 5G2, Canada

RECRUITING

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 1Z5, Canada

RECRUITING

CHU de Quebec Hopital de l Enfant Jesus

Québec, Quebec, G1J 1Z4, Canada

RECRUITING

Mengchao Hepatobiliary Hospital of Fujian Medical University

Fuzhou, Fujian, 350028, China

RECRUITING

Sun Yat-Sen University Cancer Center

Guangzhou, Guangdong, 510030, China

RECRUITING

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, 150000, China

RECRUITING

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, 450052, China

RECRUITING

Union Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, Hubei, 430022, China

RECRUITING

The First Bethune Hospital of Jilin University

Changchun, Jilin, 130021, China

RECRUITING

Herlev og Gentofte Hospital

Herlev, 2730, Denmark

RECRUITING

Institut Bergonie

Bordeaux, 33000, France

RECRUITING

Centre Georges Francois Leclerc

Dijon, 21000, France

RECRUITING

Institut Paoli Calmettes

Marseille, 13009, France

RECRUITING

Gustave Roussy

Villejuif, 94805, France

RECRUITING

Universitaetsklinikum Essen

Essen, 45147, Germany

RECRUITING

Universitaetsklinikum Heidelberg

Heidelberg, 69120, Germany

RECRUITING

Universitaetsklinikum Wuerzburg

Würzburg, 97078, Germany

RECRUITING

Alexandra Hospital

Athens, 11528, Greece

RECRUITING

General Hospital Of Thessaloniki Papageorgiou

Thessaloniki, 56429, Greece

RECRUITING

European Interbalkan Medical Center

Thessaloniki, 57001, Greece

RECRUITING

Queen Mary Hospital, The University of Hong Kong

Hong Kong, Hong Kong

RECRUITING

Prince of Wales Hospital, Chinese University of Hong Kong

Shatin, New Territories, Hong Kong

RECRUITING

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, 20133, Italy

RECRUITING

Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

RECRUITING

IRCCS Istituto Clinico Humanitas

Rozzano MI, 20089, Italy

RECRUITING

Centro Ricerche Cliniche Di Verona Societa responsabilita limitata

Verona, 37134, Italy

RECRUITING

Aichi Cancer Center

Nagoya, Aichi-ken, 464-8681, Japan

RECRUITING

National Cancer Center Hospital East

Kashiwa-shi, Chiba, 277-8577, Japan

RECRUITING

Kanagawa Prefectural Hospital Organization Kanagawa Cancer Center

Yokohama, Kanagawa, 241-8515, Japan

RECRUITING

National Cancer Center Hospital

Chuo-ku, Tokyo, 104-0045, Japan

RECRUITING

Radboud Universitair Medisch Centrum

Nijmegen, 6525 GA, Netherlands

RECRUITING

Hospital Universitario Virgen del Rocio

Seville, Andalusia, 41013, Spain

RECRUITING

Hospital Universitari Vall d Hebron

Barcelona, Catalonia, 08035, Spain

RECRUITING

Hospital General Universitario Gregorio Maranon

Madrid, 28009, Spain

RECRUITING

National Cheng Kung University Hospital

Tainan, 70403, Taiwan

RECRUITING

National Taiwan University Hospital

Taipei, 10002, Taiwan

RECRUITING

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

RECRUITING

Queen Elizabeth Hospital Birmingham

Birmingham, B15 2TH, United Kingdom

RECRUITING

Sarah Cannon Research Institute UK

London, W1G 6AD, United Kingdom

RECRUITING

Related Links

MeSH Terms

Conditions

Pancreatic NeoplasmsNeoplasms

Interventions

Gemcitabine130-nm albumin-bound paclitaxel

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

Heterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-Ring

Study Officials

  • MD

    Amgen

    STUDY DIRECTOR

Central Study Contacts

Amgen Call Center

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 8, 2024

First Posted

April 11, 2024

Study Start

May 29, 2024

Primary Completion (Estimated)

February 26, 2027

Study Completion (Estimated)

February 25, 2029

Last Updated

March 31, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

De-identified individual patient data for variables necessary to address the specific research question in an approved data sharing request.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
Data sharing requests relating to this study will be considered beginning 18 months after the study has ended and either 1) the product and indication have been granted marketing authorization in both the US and Europe or 2) clinical development for the product and/or indication discontinues and the data will not be submitted to regulatory authorities. There is no end date for eligibility to submit a data sharing request for this study.
Access Criteria
Qualified researchers may submit a request containing the research objectives, the Amgen product(s) and Amgen study/studies in scope, endpoints/outcomes of interest, statistical analysis plan, data requirements, publication plan, and qualifications of the researcher(s). In general, Amgen does not grant external requests for individual patient data for the purpose of re-evaluating safety and efficacy issues already addressed in the product labelling. Requests are reviewed by a committee of internal advisors. If not approved, a Data Sharing Independent Review Panel will arbitrate and make the final decision. Upon approval, information necessary to address the research question will be provided under the terms of a data sharing agreement. This may include anonymized individual patient data and/or available supporting documents, containing fragments of analysis code where provided in analysis specifications. Further details are available at the URL below.
More information

Locations