NCT06347003

Brief Summary

This Phase 3 study will evaluate the safety and efficacy of plozasiran injection (ARO-APOC3) in adult participants with severe hypertriglyceridemia (SHTG). After providing informed consent eligible participants will be randomized to receive 4 doses (once every 3 months) of plozasiran or placebo, and be evaluated for efficacy and safety. After month 12, eligible participants will be offered an opportunity to continue in an optional open-label extension under a separate protocol.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
446

participants targeted

Target at P50-P75 for phase_3

Timeline
4mo left

Started Jul 2024

Geographic Reach
17 countries

196 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress85%
Jul 2024Sep 2026

First Submitted

Initial submission to the registry

March 29, 2024

Completed
6 days until next milestone

First Posted

Study publicly available on registry

April 4, 2024

Completed
4 months until next milestone

Study Start

First participant enrolled

July 22, 2024

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2026

Expected
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2026

Last Updated

October 27, 2025

Status Verified

October 1, 2025

Enrollment Period

1.9 years

First QC Date

March 29, 2024

Last Update Submit

October 24, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percent Change in Fasting Serum Triglyceride (TG) Levels from Baseline to Month 12 Compared to Placebo

    Baseline, Month 12

Secondary Outcomes (20)

  • Percent Change in Fasting Serum TG Levels from Baseline to Month 10 Compared to Placebo

    Baseline, Month 10

  • Proportion of Participants Who Achieve Fasting TG Levels of <500 mg/dL (<5.65 mmol/L) at Month 12 Compared to Placebo

    Baseline, Month 12

  • Proportion of Participants Who Achieve Fasting TG Levels of <150 mg/dL (<1.69 mmol/L) at Month 12 Compared to Placebo

    Baseline, Month 12

  • Percent change in remnant cholesterol (VLDL-C) from baseline to Month 12 compared to placebo

    Baseline, Month 12

  • Percent change in non-HDL-C from baseline to Month 12 compared to placebo

    Baseline, Month 12

  • +15 more secondary outcomes

Study Arms (2)

Plozasiran Injection

EXPERIMENTAL

4 doses of plozasiran (ARO-APOC3) by subcutaneous (sc) injection

Drug: Plozasiran Injection

Placebo

PLACEBO COMPARATOR

calculated volume to match active treatment by sc injection

Drug: Placebo

Interventions

ARO-APOC3 Injection

Also known as: ARO-APOC3
Plozasiran Injection

sterile normal saline (0.9% NaCl)

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males, or nonpregnant (who do not plan to become pregnant) nonlactating females, who are ≥18 years of age at screening
  • Established diagnosis of severe hypertriglyceridemia (SHTG) and prior documented evidence (medical history) of fasting TG levels of ≥ 500 mg/dL (≥5.65mmol/L)
  • Mean fasting TG level ≥500 mg/dL (≥5.65 mmol/L) collected at 2 separate and consecutive visits at least 7 days apart and no more than 17 days apart during the screening period
  • Fasting low density lipoprotein-cholesterol (LDL-C) ≤130 mg/dL (≤3.37 mmol/L) at screening
  • Screening HbA1C ≤9.0%
  • Willing to follow diet counseling and maintain a stable low-fat diet
  • Must be on standard of care lipid and TG lowering medications per local guidelines (unless documented as intolerant as determined by the Investigator, including an inability to safely administer or re-administer a specific drug because of fear, preference, genetic, clinical, or metabolic considerations, or due to a previous adverse reaction associated with, attributed to, or caused by specific drug)

You may not qualify if:

  • Use of any hepatocyte-targeted small interfering ribonucleic acid (siRNA) that targets lipids and/or triglycerides within 365 days before Day 1 (except inclisiran, which is permitted). Administration of investigational drug and inclisiran must be separated by at least 4 weeks
  • Use of any other hepatocyte-targeted siRNA or antisense oligonucleotide molecule within 60 days or within 5-half-lives before Day 1 based on plasma pharmacokinetics (PK), whichever is longer
  • Known diagnosis of familial chylomicronemia syndrome (FCS) (type 1 Hyperlipoproteinemia) by documentation of confirmed homozygote or double heterozygote for loss-of-function mutations in type 1-causing genes
  • Acute pancreatitis within 4 weeks prior to screening
  • Body mass index \>45kg/m\^2

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (196)

Research Center 1

Garden Grove, California, 92844, United States

Location

Research Center 2

Lake Forest, California, 92630, United States

Location

Research Center 3

Montclair, California, 91763, United States

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Research Center 4

Panorama City, California, 91402, United States

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Research Center 5

Redding, California, 96001, United States

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Research Center 6

Colorado Springs, Colorado, 80909, United States

Location

Research Center 7

Hialeah, Florida, 33016, United States

Location

Research Center 8

Lake City, Florida, 32055, United States

Location

Research Center 9

Miami Lakes, Florida, 33014, United States

Location

Research Center 10

Mt. Dora, Florida, 32757, United States

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Research Center 11

Orlando, Florida, 32825, United States

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Research Center 12

Pensacola, Florida, 32503, United States

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Research Center 13

Tamarac, Florida, 33321, United States

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Research Center 14

Tampa, Florida, 33614, United States

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Research Center 15

Macon, Georgia, 31210, United States

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Research Center 16

Savannah, Georgia, 31401, United States

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Research Center 17

Park Ridge, Illinois, 60068, United States

Location

Research Center 18

Eunice, Louisiana, 70535, United States

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Research Center 19

Baltimore, Maryland, 21229, United States

Location

Research Center 20

Flint, Michigan, 48532, United States

Location

Research Center 21

Minneapolis, Minnesota, 55455, United States

Location

Research Center 22

Olive Branch, Mississippi, 38654, United States

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Research Center 23

Jefferson City, Missouri, 65109, United States

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Research Center 24

St Louis, Missouri, 63136, United States

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Research Center 26

Omaha, Nebraska, 68114, United States

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Research Center 25

Omaha, Nebraska, 68144, United States

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Research Center 27

Las Vegas, Nevada, 89119, United States

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Research Center 29

Long Island City, New York, 11106, United States

Location

Research Center 30

New York, New York, 10016, United States

Location

Research Center 31

Rochester, New York, 14642, United States

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Research Center 28

The Bronx, New York, 10455, United States

Location

Research Center 32

Vestal, New York, 13850, United States

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Research Center 33

Morehead City, North Carolina, 28557, United States

Location

Research Center 34

Winston-Salem, North Carolina, 27157, United States

Location

Research Center 35

Cincinnati, Ohio, 45219, United States

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Research Center 36

Columbus, Ohio, 43210, United States

Location

Research Center 37

Norman, Oklahoma, 73072, United States

Location

Research Center 38

Oklahoma City, Oklahoma, 73111, United States

Location

Research Center 39

Powell, Tennessee, 37849, United States

Location

Research Center 40

El Paso, Texas, 79905, United States

Location

Research Center 47

Houston, Texas, 77029, United States

Location

Research Center 45

Houston, Texas, 77030, United States

Location

Research Center 46

Houston, Texas, 77030, United States

Location

Research Center 42

Houston, Texas, 77061, United States

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Research Center 44

Houston, Texas, 77074, United States

Location

Research Center 43

Houston, Texas, 77079, United States

Location

Research Center 41

Houston, Texas, 77095, United States

Location

Research Center 48

Laredo, Texas, 78041, United States

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Research Center 49

Missouri City, Texas, 77459, United States

Location

Research Center 50

Plano, Texas, 75093, United States

Location

Research Center 51

San Antonio, Texas, 78230, United States

Location

Research Center 52

Seattle, Washington, 98109, United States

Location

Research Center 8

Ramos Mejía, Buenos Aires, B1704ETD, Argentina

Location

Research Center 10

San Isidro, Buenos Aires, 1642, Argentina

Location

Research Center 7

Temperley, Buenos Aires, B1834GUK, Argentina

Location

Research Center 4

Córdoba, Córdoba Province, 5000, Argentina

Location

Research Center 9

Córdoba, Córdoba Province, 5008, Argentina

Location

Research Center 5

Córdoba, Córdoba Province, X5000AAW, Argentina

Location

Research Center 3

Córdoba, Córdoba Province, X5006CBI, Argentina

Location

Research Center 6

Buenos Aires, C1417, Argentina

Location

Research Center 2

Buenos Aires, C1425AGC, Argentina

Location

Research Center 1

Buenos Aires, C1430, Argentina

Location

Research Center 1

Blacktown, New South Wales, 2148, Australia

Location

Research Center 4

Concord, New South Wales, 2139, Australia

Location

Research Center 5

Merewether, New South Wales, 2291, Australia

Location

Research Center 2

Box Hill, Victoria, 3138, Australia

Location

Research Center 7

Clayton, Victoria, 3168, Australia

Location

Research Center 3

Heidelberg, Victoria, 3084, Australia

Location

Research Center 6

Crawley, Western Australia, 6009, Australia

Location

Research Center 4

Gozée, 6534, Belgium

Location

Research Center 6

Hasselt, 3500, Belgium

Location

Research Center 3

Mechelen, 2800, Belgium

Location

Research Center 2

Namur, 5101, Belgium

Location

Research Center 5

Roeselare, 8800, Belgium

Location

Research Center 1

Wetteren, 9230, Belgium

Location

Research Center 10

Vitória, Espírito Santo, 29055-450, Brazil

Location

Research Center 12

Salvador, Estado de Bahia, 40050-410, Brazil

Location

Research Center 13

Salvador, Estado de Bahia, 40323-010, Brazil

Location

Research Center 14

Salvador, Estado de Bahia, 41810-010, Brazil

Location

Research Center 5

Belo Horizonte, Minas Gerais, 30220-140, Brazil

Location

Research Center 8

Campina Grande do Sul, Paraná, 83430-000, Brazil

Location

Research Center 2

Curitiba, Paraná, 80730-150, Brazil

Location

Research Center 4

Belém, Pará, 66073-000, Brazil

Location

Research Center 6

Porto Alegre, Rio Grande do Sul, 90035-903, Brazil

Location

Research Center 9

Porto Alegre, Rio Grande do Sul, 90430-001, Brazil

Location

Research Center 1

Campinas, São Paulo, 13083-190, Brazil

Location

Research Center 7

São Paulo, São Paulo, 04266-010, Brazil

Location

Research Center 11

São Paulo, São Paulo, 05403-000, Brazil

Location

Research Center 3

Votuporanga, São Paulo, 15501-405, Brazil

Location

Research Center 8

Burgas, Burgas, 8000, Bulgaria

Location

Research Center 11

Rousse, Ruse, 7000, Bulgaria

Location

Research Center 15

Sofia, Sofia, 1527, Bulgaria

Location

Research Center 7

Sofia, Sofia, 1527, Bulgaria

Location

Research Center 12

Blagoevgrad, 2700, Bulgaria

Location

Research Center 10

Kardzhali, 6600, Bulgaria

Location

Research Center 1

Pleven, 5800, Bulgaria

Location

Research Center 3

Pleven, 5800, Bulgaria

Location

Research Center 4

Plovdiv, 4001, Bulgaria

Location

Research Center 2

Plovdiv, 4002, Bulgaria

Location

Research Center 9

Plovdiv, 4004, Bulgaria

Location

Research Center 13

Sofia, 1336, Bulgaria

Location

Research Center 6

Sofia, 1404, Bulgaria

Location

Research Center 5

Sofia, 1431, Bulgaria

Location

Research Center 14

Sofia, 1680, Bulgaria

Location

Research Center 3

Victoria, British Columbia, V8T 5G4, Canada

Location

Research Center 1

Brampton, Ontario, L6S 0C6, Canada

Location

Research Center 8

London, Ontario, N6A 5A5, Canada

Location

Research Center 2

Sarnia, Ontario, N7T 4X3, Canada

Location

Research Center 5

Waterloo, Ontario, N2TOC1, Canada

Location

Research Center 6

Montreal, Quebec, H2W 1R7, Canada

Location

Research Center 4

Québec, Quebec, G1V 4W2, Canada

Location

Research Center 7

Halifax, B3H 1V7, Canada

Location

Research Center 11

Bengbu, Anhui, 233004, China

Location

Research Center 23

Beijing, Beijing Municipality, 100191, China

Location

Research Center 22

Beijing, Beijing Municipality, 100730, China

Location

Research Center 7

Guangzhou, Guangdong, 510180, China

Location

Research Center 19

Guanzhou, Guangdong, 510080, China

Location

Research Center 8

Liuchow, Guangxi Zhuang, 545006, China

Location

Research Center 13

Xingtai, Hebei, 054099, China

Location

Research Center 6

Luoyang, Henan, 471003, China

Location

Research Center 21

Wuhan, Hubei, 430060, China

Location

Research Center 4

Changsha, Hunan, 410011, China

Location

Research Center 18

Changsha, Hunan, 410015, China

Location

Research Center 16

Baotou, Inner Mongolia, 14010, China

Location

Research Center 10

Suzhou, Jiangsu, 215002, China

Location

Research Center 9

Shanghai, Shanghai Municipality, 2000040, China

Location

Research Center 12

Shanghai, Shanghai Municipality, 200050, China

Location

Research Center 2

Yuncheng, Shanxi, 44000, China

Location

Research Center 17

Chengdu, Sichuan, 610072, China

Location

Research Center 20

Tianjin, Tianjin Municipality, 300121, China

Location

Research Center 1

Beijing, Xicheng, 10034, China

Location

Research Center 15

Wenzhou, Zhejiang, 325000, China

Location

Research Center 5

Hangzhou, 311100, China

Location

Research Center 3

Liaocheng, 252000, China

Location

Research Center 14

Nanchang, 330006, China

Location

Research Center 1

Zagreb, City of Zagreb, 10000, Croatia

Location

Research Center 2

Krapinske Toplice, 49217, Croatia

Location

Research Center 3

Zagreb, 10000, Croatia

Location

Research Center 4

Zagreb, 10000, Croatia

Location

Research Center 8

Prague, Prague, 140 21, Czechia

Location

Research Center 4

Prague, Prague, 140 59, Czechia

Location

Research Center 3

Hodonín, 69501, Czechia

Location

Research Center 6

Hradec Králové, 50005, Czechia

Location

Research Center 1

Ostrava, 70200, Czechia

Location

Research Center 7

Praha 1-Nove Mesto, 11000, Czechia

Location

Research Center 5

Praha 4-Krc, 140 59, Czechia

Location

Research Center 2

Uherské Hradiště, 68601, Czechia

Location

Research Center 9

Ústí nad Labem, 40113, Czechia

Location

Research Center 1

Budapest, 1033, Hungary

Location

Research Center 4

Budapest, 1051, Hungary

Location

Research Center 2

Budapest, 1132, Hungary

Location

Research Center 6

Budapest, 1152, Hungary

Location

Research Center 3

Szeged, 6725, Hungary

Location

Research Center 5

Veszprém, 8200, Hungary

Location

Research Center 3

Rozzano, Milano, 20089, Italy

Location

Research Center 2

Palermo, Sicily, 90127, Italy

Location

Research Center 6

Bologna, 40138, Italy

Location

Research Center 5

Brescia, 25123, Italy

Location

Research Center 4

Milan, 20162, Italy

Location

Research Center 1

Roma, 00168, Italy

Location

Research Center 15

Żarów, Swidnica, 58-130, Poland

Location

Research Center 7

Bydgoszcz, 85-231, Poland

Location

Research Center 11

Elblag, 82-300, Poland

Location

Research Center 10

Katowice, 40-752, Poland

Location

Research Center 13

Krakow, 30-727, Poland

Location

Research Center 17

Krakow, 31-202, Poland

Location

Research Center 8

Krakow, 31-501, Poland

Location

Research Center 12

Lodz, 91-363, Poland

Location

Research Center 18

Warsaw, 00-215, Poland

Location

Research Center 9

Warsaw, 03-291, Poland

Location

Research Center 16

Wroclaw, 53-030, Poland

Location

Research Center 14

Wroclaw, 53-673, Poland

Location

Research Center 3

Brasov, Brașov County, 500091, Romania

Location

Research Center 1

Bucharest, București, 010192, Romania

Location

Research Center 2

Cluj-Napoca, Cluj, 400000, Romania

Location

Research Center 6

Alba Iulia, Jud. Alba, 510053, Romania

Location

Research Center 4

Ploieşti, Jud. Prahova, 100342, Romania

Location

Research Center 5

Timișoara, Timiș County, 300362, Romania

Location

Research Center 8

Deva, 330084, Romania

Location

Research Center 7

Galati, 800291, Romania

Location

Research Center 9

Târgu Mureş, 540136, Romania

Location

Research Center 4

Banská Bystrica, Banská Bystrica Region, 97401, Slovakia

Location

Research Center 1

Košice, Košice Region, 040 01, Slovakia

Location

Research Center 3

Moldava nad Bodvou, Košice Region, 045 01, Slovakia

Location

Research Center 6

Bardejov, 08501, Slovakia

Location

Research Center 5

Bratislava, 81109, Slovakia

Location

Research Center 2

Žilina, Žilina Region, 10010, Slovakia

Location

Research Center 2

Barcelona, 08023, Spain

Location

Research Center 3

Barcelona, 08035, Spain

Location

Research Center 1

Valencia, 46010, Spain

Location

Research Center 4

Zaragoza, 50009, Spain

Location

Research Center 3

Torpoint, Cornwall, PL11 2TB, United Kingdom

Location

Research Center 5

Torquay, Devon, TQ2 7AA, United Kingdom

Location

Research Center 2

Plymouth, Devpn, PL5 3JB, United Kingdom

Location

Research Center 1

London, EC1M 6BQ, United Kingdom

Location

Research Center 4

London, N12 8BU, United Kingdom

Location

MeSH Terms

Conditions

Hypertriglyceridemia

Interventions

plozasiran

Condition Hierarchy (Ancestors)

HyperlipidemiasDyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 29, 2024

First Posted

April 4, 2024

Study Start

July 22, 2024

Primary Completion (Estimated)

June 1, 2026

Study Completion (Estimated)

September 1, 2026

Last Updated

October 27, 2025

Record last verified: 2025-10

Data Sharing

IPD Sharing
Will not share

Locations