NCT06305247

Brief Summary

The purpose of this study is to determine the appropriate dosage, safety and effectiveness of the study drug, IPN01194 in adults with advanced solid tumours. The participants in this study will have advanced solid tumours. 'Advanced solid tumours' refers to cancers that can occur in several places, including cancers in organs or tissues that have spread from their original site to nearby tissues or other parts of the body. In this study, all participants will receive the study drug, which will be taken by mouth (orally).

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
220

participants targeted

Target at P75+ for phase_1

Timeline
23mo left

Started Apr 2024

Longer than P75 for phase_1

Geographic Reach
3 countries

12 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress53%
Apr 2024Mar 2028

First Submitted

Initial submission to the registry

February 27, 2024

Completed
14 days until next milestone

First Posted

Study publicly available on registry

March 12, 2024

Completed
22 days until next milestone

Study Start

First participant enrolled

April 3, 2024

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 20, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 20, 2028

Last Updated

April 30, 2026

Status Verified

April 1, 2026

Enrollment Period

4 years

First QC Date

February 27, 2024

Last Update Submit

April 29, 2026

Conditions

Outcome Measures

Primary Outcomes (4)

  • Phase 1: Percentage of participants with dose limiting toxicity (DLT)

    Within 28 days of first dose

  • Phase 1: Percentage of participants experiencing Treatment-Emergent Adverse Events (TEAEs) and Treatment-Emergent Serious Adverse Events (TE SAEs)

    An Adverse event (AE) is any untoward medical occurrence in a clinical study participant, temporally associated with the use of study intervention, whether or not considered related to the study intervention.

    At 30 days following the last administration of study intervention

  • Phase 1: Percentage of participants with dose interruptions and permanent treatment discontinuations

    At 30 days following the last administration of study intervention

  • Phase 2a: Objective response rate (ORR)

    Defined as the percentage of participants with best overall response (BOR) of complete response (CR) or partial response (PR) as determined by investigator.

    At end of treatment (up to approximately 32 months)

Secondary Outcomes (14)

  • Phase 1: Time to maximum observed drug concentration (Tmax) after single and multiple doses of IPN01194

    At Day 1 and Day 15.

  • Phase 1: Maximum observed drug concentration (Cmax) after single and multiple doses of IPN01194

    At Day 1 and Day 15.

  • Phase 1: Area under the plasma concentration time curve (AUCtau) after single and multiple doses of IPN01194

    At Day 1 and Day 15.

  • Phase 1: Geometric mean ratio of Cmax of IPN01194 administered in fed state relative to fasted state

    Between Day -8 and Day -3 (fasted period) and between Day -10 and Day -7 (fed state period)

  • Phase 1: Geometric mean ratio of AUClast of IPN01194 administered in fed state relative to fasted state

    Between Day -8 and Day -3 (fasted period) and between Day -10 and Day -7 (fed state period)

  • +9 more secondary outcomes

Study Arms (2)

Phase I (Dose Escalation with Backfilling)

EXPERIMENTAL

Nine dose levels are planned to be tested.

Drug: IPN01194

Phase IIa (Cohort Expansion)

EXPERIMENTAL

Study intervention will be administered at one of two doses of interest determined at the end of Phase I.

Drug: IPN01194

Interventions

IPN01194 will be taken orally over a period of 28 days (a "Cycle") at the assigned dose level. The dose limiting toxicity (DLT) observation period consists of the first 28 days of treatment with IPN01194 (Cycle 1). Participants will receive IPN01194 treatment beyond Cycle 1 until treatment is precluded by toxicity, disease progression, or upon participant's request or investigator decision.

Phase I (Dose Escalation with Backfilling)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants must be ≥18 years of age
  • Participants with histologically confirmed metastatic solid tumour (melanoma, metastatic colorectal cancer (CRC), pancreatic ductal adenocarcinoma (PDAC) or head and neck squamous cell carcinoma (HNSCC)) for whom no suitable alternative standard therapy exists.
  • Participants must bear tumours harbouring selected classes of genetic mutations, (MAPKm).
  • Participants must have measurable disease per Response Evaluation Criteria in Solid Tumours (RECIST) version 1.1
  • Eastern Cooperative Oncology Group (ECOG)/performance status (PS) of 0 or 1.
  • Participants must consent to the use of archival tumour tissue or, if not available, collection of fresh tumour biopsy at screening
  • Male and female participants Contraceptive use by men or women should be consistent with local regulations regarding the methods of contraception for those participating in clinical trials.

You may not qualify if:

  • Gastrointestinal conditions that could impair absorption of IPN01194 or inability to swallow oral medications.
  • Any evidence of severe active infection or inflammatory condition.
  • Non-adequate cardiac function
  • Have one or more of study defined ophthalmological findings/conditions
  • Known psychiatric or substance abuse disorder, or any other cognitive disorder per the opinion of the investigator that would interfere with the participant's ability to cooperate with the requirements of the study.
  • Underlying medical conditions that, in the investigator's or sponsor's opinion, will obscure the interpretation of toxicity determination or AEs.
  • Known second malignancy within the last 2 years prior to first dose of study intervention..
  • Major surgery within 28 days prior to first dose of study intervention.
  • Ongoing AEs caused by any prior anti-cancer therapy ≥Grade 2 (National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE) version 5.0).
  • Active brain metastases or leptomeningeal metastases
  • Current enrolment or past participation in any other clinical trial involving an investigational study treatment within the last 28 days.
  • Live vaccine(s) within 28 days prior to first dose of study intervention
  • Concurrent treatment with any other anti-cancer therapy (including radiotherapy or investigational agents).
  • Treatment with medications that prolong the QT/QTc interval.
  • Treatment with strong and moderate CYP3A4 inducers
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

The Angeles Clinic and Research Institute - California

Los Angeles, California, 90025, United States

RECRUITING

UC San Diego Health System - La Jolla

San Diego, California, 92037, United States

WITHDRAWN

Yale Cancer Center - New Heaven

New Haven, Connecticut, 06510, United States

RECRUITING

Sarah Cannon Research Institute (SCRI) - Nashville

Nashville, Tennessee, 37203, United States

RECRUITING

Virginia Cancer Specialist

Fairfax, Virginia, 22031, United States

RECRUITING

Centre Léon Bérard - Lyon

Lyon, France

RECRUITING

Paris Saint-Louis

Paris, France

RECRUITING

Institut de Cancerologie de l'Ouest (St-Herblain)

Saint-Herblain, France

RECRUITING

IGR-Villejuif

Villejuif, France

RECRUITING

Barcelona - Val D'Hebron

Barcelona, Spain

RECRUITING

Fundacion Jimenez Diaz - Madrid

Madrid, Spain

RECRUITING

M.D. Anderson Cancer Center Madrid

Madrid, Spain

RECRUITING

MeSH Terms

Conditions

MelanomaSquamous Cell Carcinoma of Head and NeckColorectal Neoplasms

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue DiseasesCarcinoma, Squamous CellCarcinomaNeoplasms, Glandular and EpithelialHead and Neck NeoplasmsIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Study Officials

  • Ipsen Medical Director

    Ipsen

    STUDY DIRECTOR

Central Study Contacts

Ipsen Clinical Study Enquiries

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Model Details: Phase I is a dose escalation with backfill in participants with selected MAPKm advanced solid tumours. Phase IIa (cohort expansion) is an open label randomised study.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 27, 2024

First Posted

March 12, 2024

Study Start

April 3, 2024

Primary Completion (Estimated)

March 20, 2028

Study Completion (Estimated)

March 20, 2028

Last Updated

April 30, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Qualified researchers may request access to patient level data and related study documents including the clinical study report, study protocol with any amendments, annotated case report form, statistical analysis plan, and dataset specifications. Patient level data will be anonymized and study documents will be redacted to protect the privacy of study participants.

Time Frame
Where applicable, data from eligible studies are available 6 months after the studied medicine and indication have been approved in the US and/or EU.
Access Criteria
Further details on Ipsen's sharing criteria and process for sharing are available here (https://www.ipsen.com/science/clinical-trials/clinical-data-transparency/).
More information

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