NCT06211764

Brief Summary

The purpose of this study is to compare disease free survival (DFS) in participants with recurrence of papillary-only high-risk non-muscle-invasive bladder cancer (HR-NMIBC) within 1 year of last dose of Bacillus Calmette-Guérin (BCG) therapy and who refused or are unfit for Radical Cystectomy (RC), receiving TAR-200 versus investigator's choice of single agent intravesical chemotherapy.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
272

participants targeted

Target at P50-P75 for phase_3

Timeline
60mo left

Started Apr 2024

Longer than P75 for phase_3

Geographic Reach
14 countries

123 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress30%
Apr 2024Apr 2031

First Submitted

Initial submission to the registry

January 9, 2024

Completed
9 days until next milestone

First Posted

Study publicly available on registry

January 18, 2024

Completed
3 months until next milestone

Study Start

First participant enrolled

April 9, 2024

Completed
6.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 27, 2030

Expected
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 14, 2031

Last Updated

April 13, 2026

Status Verified

April 1, 2026

Enrollment Period

6.6 years

First QC Date

January 9, 2024

Last Update Submit

April 9, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Disease-free Survival (DFS)

    DFS will be measured as the time from randomization to the time of the first recurrence of high-risk non-muscle-invasive bladder cancer (HR-NMIBC) \[high grade (HG) Ta, any T1 or carcinoma in situ (CIS)\], progression, or death due to any cause, whichever occurs first.

    Up to 6 years 7 months

Secondary Outcomes (12)

  • Recurrence-Free Survival (RFS)

    Up to 6 years 7 months

  • Time to Next Intervention (TTNI)

    Up to 6 years 7 months

  • Time to Disease Worsening (TTDW)

    Up to 6 years 7 months

  • Time to Progression (TTP)

    Up to 6 years 7 months

  • Overall Survival (OS)

    Up to 6 years 7 months

  • +7 more secondary outcomes

Study Arms (2)

Group A: TAR-200

EXPERIMENTAL

Participants will receive intravesical TAR-200 every 3 weeks during an induction phase and every 12 weeks during a maintenance phase.

Drug: TAR-200

Group B: Mitomycin C (MMC) or Gemcitabine

ACTIVE COMPARATOR

Participants will receive either single agent intravesical MMC or gemcitabine every week during an induction phase and every 4 weeks during a maintenance phase.

Drug: Mitomycin CDrug: Gemcitabine

Interventions

Participants will receive TAR-200 intravesically.

Also known as: JNJ-17000139
Group A: TAR-200

Participants will receive MMC intravesically.

Group B: Mitomycin C (MMC) or Gemcitabine

Participants will receive gemcitabine intravesically.

Group B: Mitomycin C (MMC) or Gemcitabine

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed diagnosis by local pathology (within 90 days of documented informed consent) of recurrent, papillary-only high-risk non-muscle-invasive bladder cancer (HR-NMIBC) \[defined as high-grade Ta or any T1, no carcinoma in situ (CIS)\]
  • Participants with variant histologic subtypes are allowed if tumor(s) demonstrate urothelial (transitional cell histology) predominance. However, neuroendocrine, and small cell variants will be excluded
  • Participants must be ineligible for or have elected not to undergo Radical Cystectomy (RC)
  • Have an Eastern Cooperative Oncology Group (ECOG) performance status Grade of 0, 1, or 2

You may not qualify if:

  • Presence of CIS at any point from time of diagnosis of papillary-only HR-NMIBC recurrence to randomization. Additionally, presence or history of histologically confirmed, muscle-invasive, locally advanced, nonresectable, or metastatic urothelial carcinoma (that is, T2, T3, T4, N+, and/or M+)
  • Presence of any bladder or urethral anatomic feature that, in the opinion of the Investigator, may prevent the safe placement, indwelling use, or removal of TAR-200. Participants with tumors involving the prostatic urethra in men will be excluded
  • A history of clinically significant polyuria with recorded 24-hour urine volumes greater than 4000 milliliters (\>4000 mL)
  • Indwelling catheters are not permitted; however, intermittent catheterization is acceptable
  • Previous treatment with TAR-200

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (123)

Arkansas Urology

Little Rock, Arkansas, 72211, United States

Location

Genesis Research LLC 1

Los Alamitos, California, 90720, United States

Location

USC Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

University of California Irvine Medical Center

Orange, California, 92868, United States

Location

University of California San Francisco

San Francisco, California, 94158 2549, United States

Location

Genesis Research LLC

Torrance, California, 90503, United States

Location

Colorado Clinical Research

Lakewood, Colorado, 80228, United States

Location

Florida Urology Partners

Riverview, Florida, 33578, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

UroPartners

Chicago Ridge, Illinois, 60415, United States

Location

Urology of Indiana

Carmel, Indiana, 46032, United States

Location

First Urology, PSC

Jeffersonville, Indiana, 47130, United States

Location

Wichita Urology Group

Wichita, Kansas, 67226, United States

Location

Comprehensive Urology

Royal Oak, Michigan, 48073, United States

Location

Specialty Clinical Research of St Louis

St Louis, Missouri, 63141, United States

Location

Associated Medical Professionals

Syracuse, New York, 13210, United States

Location

The Urology Group

Cincinnati, Ohio, 45212, United States

Location

Central Ohio Urology Group

Gahanna, Ohio, 43230, United States

Location

Centers for Advanced Urology LLC d b a MidLantic Urology

Bala-Cynwyd, Pennsylvania, 19004, United States

Location

Ralph H. Johnson Veterans Affairs Medical Center

Charleston, South Carolina, 29401, United States

Location

Carolina Urologic Research Center

Myrtle Beach, South Carolina, 29572, United States

Location

Low Country Urology Clinics

North Charleston, South Carolina, 29406, United States

Location

Urology Associates

Nashville, Tennessee, 37209, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Urology Austin

Austin, Texas, 78759, United States

Location

Urology Clinics of North Texas

Dallas, Texas, 75231, United States

Location

University of Texas Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Houston Metro Urology

Houston, Texas, 77027, United States

Location

Spokane Urology

Spokane, Washington, 99202, United States

Location

Clinica Santa Isabel

Buenos Aires, C1406, Argentina

Location

Investigaciones Clinico Moleculares (ICM)

CABA, C1425, Argentina

Location

Cemaic Centro Privado de Especialidades Medicas Ambulatorias e Investigacion Clinica

Córdoba, 5000, Argentina

Location

Centro Urologico Profesor Bengio

Córdoba, X5000KPH, Argentina

Location

Hospital Privado de la Comunidad

Mar del Plata, B7602, Argentina

Location

AZ Sint-Jan

Bruges, 8000, Belgium

Location

Cliniques Universitaires Saint Luc

Brussels, 1200, Belgium

Location

Ziekenhuis Oost-Limburg

Genk, 3600, Belgium

Location

Algemeen ziekenhuis Maria Middelares

Ghent, 9000, Belgium

Location

Algemeen Ziekenhuis Delta

Roeselare, 8800, Belgium

Location

Fundacao Pio XII

Barretos, 14784-400, Brazil

Location

NAIC Nair Antunes Instituto do Cancer

Bauru, 17030-495, Brazil

Location

Hospital das Clinicas da Universidade Estadual de Campinas UNICAMP

Campinas, 13083-872, Brazil

Location

Liga Paranaense de Combate ao Cancer

Curitiba, 81520 060, Brazil

Location

Irmandade Santa Casa de Misericordia de Porto Alegre

Porto Alegre, 90020-090, Brazil

Location

Hospital da Bahia

Salvador, 41810-011, Brazil

Location

Sociedade Beneficente de Senhoras Hospital Sirio Libanes

São Paulo, 01308 901, Brazil

Location

Real e Benemérita Associação Portuguesa de Beneficência

São Paulo, 01323 900, Brazil

Location

Fundacao Antonio Prudente A C Camargo Cancer Center

São Paulo, 01509 900, Brazil

Location

Peking University First Hospital

Beijing, 100034, China

Location

West China School of Medicine/West China Hospital, Sichuan University

Cheng Du Shi, 610041, China

Location

Chongqing Cancer Hospital

Chongqing, 400033, China

Location

Sun Yat Sen University Cancer Center

Guangzhou, 510060, China

Location

Shengjing Hospital Of China Medical University

Shenyang, 110055, China

Location

Tianjin Medical University Cancer Institute and Hospital

Tianjin, 300060, China

Location

The Second Hospital Of Tianjin Medical University

Tianjin, 300211, China

Location

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, 325015, China

Location

Tongji Medical College of Huazhong University Science Technology of Medicine Health Management

Wuhan, 430032, China

Location

Xi an Jiaotong University Hospital

Xi'an, 710063, China

Location

Hopital Claude Huriez

Lille, 59000, France

Location

Polyclinique de Limoges - Francois Chenieux

Limoges, 87000, France

Location

Institut Paoli Calmettes

Marseille, 13009, France

Location

APHP - Hopital Bichat - Claude Bernard

Paris, 75018, France

Location

Clinique de la Croix du Sud

Quint-Fonsegrives, 31130, France

Location

Chu Rennes Hopital Pontchaillou

Rennes, 35000, France

Location

Hopital Foch

Suresnes, 92150, France

Location

Universitaetsklinikum Koeln

Cologne, 50937, Germany

Location

Universitaetsklinikum Halle Saale

Halle, 06120, Germany

Location

Klinikum Leverkusen gGmbH

Leverkusen, 51375, Germany

Location

Universitatsklinikum Schleswig Holstein Campus Lubeck

Lübeck, 23538, Germany

Location

Urologie Neandertal Praxis Mettmann

Mettmann, 40822, Germany

Location

Klinikum der Universitaet Muenchen

München, 81377, Germany

Location

Ospedale San Donato

Arezzo, 52100, Italy

Location

Ospedale Provinciale di Macerata

Macerata, 62100, Italy

Location

San Raffaele Hospital

Milan, 20132, Italy

Location

Istituto Dei Tumori Di Milano

Milan, 20133, Italy

Location

Ospedale S. Maria Delle Croci

Ravenna, 48121, Italy

Location

Universita Campus Bio-Medico di Roma

Roma, 00128, Italy

Location

Istituto Nazionale Tumori Regina Elena

Roma, 00144, Italy

Location

Istituto Clinico Humanitas

Rozzano, 20089, Italy

Location

PO Molinette Azienda Ospedaliero Universitaria Citta della Salute e della Scienza di Torino

Torino, 10126, Italy

Location

Funabashi Municipal Medical Center

Funabashi Shi, 273 8588, Japan

Location

Hakodate Goryoukaku Hospital

Hakodate, 040 8611, Japan

Location

Hyogo Prefectural Amagasaki General Medical Center

Hyōgo, 660-8550, Japan

Location

Niigata Cancer Center Hospital

Niigata, 951-8566, Japan

Location

National Hospital Organization Okayama Medical Center

Okayama, 701-1192, Japan

Location

Toho University Sakura Medical Center

Sakura, 285-8741, Japan

Location

Toranomon Hospital

Tokyo, 105-8470, Japan

Location

Yokohama City University Medical Center

Yokohama, 232 0024, Japan

Location

Uniwersytecki Szpital Kliniczny w Bialymstoku

Bialystok, 15 276, Poland

Location

IN VIVO Sp. z o.o

Bydgoszcz, 85 048, Poland

Location

Szpital Uniwersytecki w Krakowie

Krakow, 30 688, Poland

Location

Uniwersytecki Szpital Kliniczny nr 4

Lublin, 20 090, Poland

Location

Wojewodzki Szpital im Sw Ojca Pio w Przemyslu

Przemyśl, 37 700, Poland

Location

Szpital Wojewodzki im Sw Lukasza SP ZOZ

Tarnów, 33 100, Poland

Location

MICS Centrum Medyczne Torun

Torun, 87-100, Poland

Location

Mazowiecki Szpital Onkologiczny

Wieliszew, 05-135, Poland

Location

Dolnoslaskie Centrum Onkologii

Wroclaw, 53 413, Poland

Location

Centrul Medical Unirea SRL

Brasov, 500091, Romania

Location

Ponderas Academic Hospital

Bucharest, 014142, Romania

Location

Institutul Oncologic Ion Chiricuta

Cluj-Napoca, 400015, Romania

Location

Regina Maria

Cluj-Napoca, 400117, Romania

Location

Spitalul Clinic Judetean de Urgenta Pius Brinzeu

Timișoara, 300723, Romania

Location

Chungbuk National University Hospital

Chungcheongbuk Do, 28644, South Korea

Location

Keimyung University Dongsan Hospital

Daegu, 42601, South Korea

Location

National Cancer Center

Gyeonggi-do, 10408, South Korea

Location

Chonnam National University Hwasun Hospital

Jeollanam-do, 58128, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

The Catholic University of Korea Seoul St Mary s Hospital

Seoul, 06591, South Korea

Location

Pusan National University Yangsan Hospital

Yangsan, 50612, South Korea

Location

Hosp. Univ. Germans Trias I Pujol

Badalona, 08916, Spain

Location

Fund. Puigvert

Barcelona, 08025, Spain

Location

Hosp. Gral. Univ. Gregorio Maranon

Madrid, 28007, Spain

Location

Hosp. Univ. 12 de Octubre

Madrid, 28041, Spain

Location

Hosp Virgen de La Victoria

Málaga, 29010, Spain

Location

Hosp.Univ.Parc Tauli

Sabadell, 08208, Spain

Location

Hosp. Univ. Marques de Valdecilla

Santander, 39008, Spain

Location

Hosp. Virgen Del Rocio

Seville, 41013, Spain

Location

Hosp. Clinico Univ. de Valencia

Valencia, 46010, Spain

Location

St Bartholomews Hospital

London, EC1A 7BE, United Kingdom

Location

Salford Royal Hospital

Salford, M6 8HD, United Kingdom

Location

Southampton University Hospital

Southampton, SO16 6YD, United Kingdom

Location

Lister Hospital

Stevenage, SG1 4AB, United Kingdom

Location

MeSH Terms

Conditions

Non-Muscle Invasive Bladder Neoplasms

Interventions

MitomycinGemcitabine

Condition Hierarchy (Ancestors)

CarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsUrinary Bladder NeoplasmsUrologic NeoplasmsUrogenital NeoplasmsNeoplasms by SiteFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesUrinary Bladder DiseasesUrologic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

MitomycinsIndolequinonesQuinonesOrganic ChemicalsAzirinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingDeoxycytidineCytidinePyrimidine NucleosidesPyrimidines

Study Officials

  • Janssen Research & Development, LLC Clinical trial

    Janssen Research & Development, LLC

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 9, 2024

First Posted

January 18, 2024

Study Start

April 9, 2024

Primary Completion (Estimated)

November 27, 2030

Study Completion (Estimated)

April 14, 2031

Last Updated

April 13, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

The data sharing policy of Johnson \& Johnson Innovative Medicine is available at www.innovativemedicine.jnj.com/our-innovation/clinical-trials/transparency. As noted on this site, requests for access to the study data can be submitted through Yale Open Data Access (YODA) Project site at yoda.yale.edu.

More information

Locations