NCT06007690

Brief Summary

The primary objective is to determine the safety and efficacy of belzupacap sarotalocan (bel-sar) compared to sham control in patients with primary indeterminate lesions (IL) or small choroidal melanoma (CM).

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
100

participants targeted

Target at P25-P50 for phase_3

Timeline
28mo left

Started Dec 2023

Longer than P75 for phase_3

Geographic Reach
13 countries

69 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress52%
Dec 2023Aug 2028

First Submitted

Initial submission to the registry

August 17, 2023

Completed
6 days until next milestone

First Posted

Study publicly available on registry

August 23, 2023

Completed
4 months until next milestone

Study Start

First participant enrolled

December 6, 2023

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 15, 2027

Expected
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 15, 2028

Last Updated

March 2, 2026

Status Verified

February 1, 2026

Enrollment Period

3.9 years

First QC Date

August 17, 2023

Last Update Submit

February 26, 2026

Conditions

Keywords

Uveal MelanomaEye CancerOcular MelanomaChoroidal Melanoma

Outcome Measures

Primary Outcomes (1)

  • Time to reach tumor progression

    Tumor Progression

    65 weeks

Secondary Outcomes (1)

  • Time to composite endpoint

    65 weeks

Study Arms (3)

High dose bel-sar treatment arm & laser application

EXPERIMENTAL

High dose of bel-sar + laser application

Drug: Bel-sarDevice: Suprachoroidal MicroinjectorDevice: Infrared Laser

Low dose bel-sar treatment arm & laser application

EXPERIMENTAL

Low dose of bel-sar + laser application

Drug: Bel-sarDevice: Suprachoroidal MicroinjectorDevice: Infrared Laser

Sham control arm & sham laser

SHAM COMPARATOR

Sham injection + sham laser

Device: Sham Infrared LaserDevice: Sham Microinjector

Interventions

Bel-sar via suprachoroidal administration followed by laser application.

Also known as: AU-011
High dose bel-sar treatment arm & laser applicationLow dose bel-sar treatment arm & laser application

Suprachoroidal injection device

Also known as: SCS Microinjector
High dose bel-sar treatment arm & laser applicationLow dose bel-sar treatment arm & laser application

Laser application

High dose bel-sar treatment arm & laser applicationLow dose bel-sar treatment arm & laser application

Sham laser application

Sham control arm & sham laser

Sham injection device

Sham control arm & sham laser

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Clinical diagnosis of primary indeterminate lesion or small choroidal melanoma (IL/CM)
  • Have no evidence of metastatic disease confirmed by imaging
  • Be treatment naive for IL/CM (subjects who received PDT may be eligible)

You may not qualify if:

  • Have known contraindications or sensitivities to the study drug or laser
  • Active ocular infection or disease

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (71)

Retina Consultants of Alabama

Birmingham, Alabama, 35233, United States

WITHDRAWN

UCSD Shiley Eye Institute, Jacobs Retina Center

La Jolla, California, 92093, United States

RECRUITING

Doris Stein Eye Research Center

Los Angeles, California, 90095, United States

RECRUITING

Stanford University School of Medicine

Palo Alto, California, 94303, United States

RECRUITING

Retinal Consultants Medical Group, Inc.

Sacramento, California, 95825, United States

RECRUITING

Bascom Palmer Eye Institute

Miami, Florida, 33136, United States

WITHDRAWN

Retina Associates of Florida, PA

Tampa, Florida, 33609, United States

RECRUITING

Emory Eye Center

Atlanta, Georgia, 30322, United States

RECRUITING

University of Illinois at Chicago

Chicago, Illinois, 60612, United States

RECRUITING

Tufts Medical Center New England Eye Center

Boston, Massachusetts, 02111, United States

RECRUITING

Massachusetts Eye and Ear

Boston, Massachusetts, 02114, United States

RECRUITING

W.K. Kellogg Eye Center - University of Michigan

Ann Arbor, Michigan, 48105, United States

RECRUITING

Associated Retinal Consultants (ARC) P.C.

Royal Oak, Michigan, 48073, United States

RECRUITING

Mayo Clinic

Rochester, Minnesota, 55905, United States

RECRUITING

Washington University

St Louis, Missouri, 63110, United States

RECRUITING

Nebraska Medicine's Truhlsen Eye Institute

Omaha, Nebraska, 68105, United States

RECRUITING

Columbia University Irving Medical Center

New York, New York, 10032, United States

RECRUITING

Duke Eye Center

Durham, North Carolina, 27705, United States

RECRUITING

Cole Eye Institute

Cleveland, Ohio, 44195, United States

RECRUITING

Dean McGee Eye Institute

Oklahoma City, Oklahoma, 73104, United States

RECRUITING

Retina Consultants of Oklahoma

Oklahoma City, Oklahoma, 73112, United States

RECRUITING

Shields & Shields PC-Wills Eye Institute

Philadelphia, Pennsylvania, 19107, United States

RECRUITING

Retina Consultants of Carolina

Greenville, South Carolina, 29605, United States

RECRUITING

Southeastern Retina Associates

Chattanooga, Tennessee, 37421, United States

RECRUITING

Tennessee Retina, PC

Nashville, Tennessee, 37203, United States

RECRUITING

Austin Retina Associates

Austin, Texas, 78705, United States

RECRUITING

Texas Retina Associates

Dallas, Texas, 75231, United States

RECRUITING

UT, Southwestern Medical Center

Dallas, Texas, 75390, United States

RECRUITING

Retina Associates of South Texas, P.A.

San Antonio, Texas, 78240, United States

RECRUITING

Retina Center of Texas

Southlake, Texas, 76092, United States

RECRUITING

Retina Consultants of Texas

The Woodlands, Texas, 77401, United States

RECRUITING

Retina Associates of Utah

Salt Lake City, Utah, 84107, United States

RECRUITING

Vitreoretinal Associates of Washington

Bellevue, Washington, 98004, United States

RECRUITING

Pacific NW Retina

Burlington, Washington, 98233, United States

RECRUITING

University of Washington Medical Center

Seattle, Washington, 98104, United States

RECRUITING

University of Wisconsin Madison

Madison, Wisconsin, 53705, United States

RECRUITING

Terrace Eye Centre

Brisbane, Queensland, 4000, Australia

RECRUITING

Eye Research Australia

East Melbourne, Victoria, 3002, Australia

RECRUITING

Medical University Graz

Graz, 8036, Austria

RECRUITING

Medizinische Universität Wien, Department of Ophthalmology and Optometry

Vienna, 1090, Austria

RECRUITING

Cliniques universitaires Saint-Luc

Brussels, Belgium

RECRUITING

UZ Leuven

Leuven, 3000, Belgium

RECRUITING

Serac Eye and Skin Care Centre

Calgary, Alberta, T2V 4Y8, Canada

RECRUITING

Centre Hospitalier de l'Universite Laval

Québec, Quebec, G1S 4L8, Canada

RECRUITING

Fakultni Thomayerova nemocnice

Prague, Krč, 14059, Czechia

RECRUITING

Fakultni nemocnice Plzen

Pilsen, Plzenský Kraj, 32300, Czechia

RECRUITING

Ustredni vojenska nemocnice Vojenska fakultni nemocnice Praha

Prague, 16902, Czechia

RECRUITING

Centre Hospitalier Universitaire de Nice

Nice, Cedex 1, 06001, France

RECRUITING

Hospices Civils de Lyon - Hôpital de La Croix Rousse - Hospital

Lyon, Rhone, 69004, France

RECRUITING

Charité - Universitätsmedizin Berlin KöR

Berlin, 12203, Germany

RECRUITING

University Hospital Cologne (AöR)

Cologne, 50937, Germany

NOT YET RECRUITING

Universitätsmedizin Essen

Essen, 45147, Germany

RECRUITING

Uniklinikum Hamburg Eppendorf

Hamburg, 20246, Germany

RECRUITING

Universitätsklinikum Schleswig-Holstein Klinik für Augenheilkunde

Lübeck, 23538, Germany

RECRUITING

Klinikum der LMU Muenchen

München, 80336, Germany

RECRUITING

Universitätsklinikum Tübingen

Tübingen, 72076, Germany

RECRUITING

The Chaim Sheba Medical Center

Tel-Hashomer, Central District, 5262100, Israel

RECRUITING

Hadassah Medical Center, Ein-Karem

Jerusalem, Jerusalem, 9112001, Israel

RECRUITING

AOUC Azienda Ospedaliero-Universitaria Careggi

Florence, 50134, Italy

RECRUITING

Istituto Nazionale dei Tumori, Fondazione IRCCS

Milan, 20133, Italy

RECRUITING

Ospedale Fatebenefratelli e Oftalmico, ASST Fatebenefratelli Sacco

Milan, 20157, Italy

RECRUITING

Universita'Cattolica Del Sacro Cuore - UNICATT

Roma, 00168, Italy

RECRUITING

Leids Universitair Medisch Centrum (LUMC)

Leiden, 2333 ZE, Netherlands

RECRUITING

Erasmus MC

Rotterdam, 3015AA, Netherlands

RECRUITING

Auckland Eye Ltd

Auckland, 1050, New Zealand

RECRUITING

Hospital Universitario de Bellvitge

Barcelona, 08907, Spain

RECRUITING

Hospital Provincial de Conxo

Santiago de Compostela, 15706, Spain

RECRUITING

Hospital Virgen Macarena

Seville, 41009, Spain

RECRUITING

Hospital Universitario Y Politécnico La Fe

Valencia, 46026, Spain

RECRUITING

Moorfields Eye Hospital NHS Foundation Trust

London, EC1V 2PD, United Kingdom

RECRUITING

Nhs Foundation Trust - Royal Hallamshire Hospital

Sheffield, S10 2JF, United Kingdom

RECRUITING

Related Links

MeSH Terms

Conditions

Uveal MelanomaEye Neoplasms

Condition Hierarchy (Ancestors)

MelanomaNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasUveal NeoplasmsNeoplasms by SiteEye DiseasesUveal Diseases

Study Officials

  • Medical Monitor

    Aura Biosciences

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, OUTCOMES ASSESSOR
Masking Details
Subject, Assessor, and Sponsor masked trial.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 17, 2023

First Posted

August 23, 2023

Study Start

December 6, 2023

Primary Completion (Estimated)

November 15, 2027

Study Completion (Estimated)

August 15, 2028

Last Updated

March 2, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will not share

Locations