NCT06002659

Brief Summary

The purpose is to study the safety, tolerability, pharmacokinetics, pharmacodynamics and efficacy of CAR20(NAP)-T for patients with B-cell malignancies.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
18

participants targeted

Target at P25-P50 for phase_1

Timeline
18mo left

Started May 2024

Typical duration for phase_1

Geographic Reach
1 country

2 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress62%
May 2024Dec 2027

First Submitted

Initial submission to the registry

January 6, 2023

Completed
8 months until next milestone

First Posted

Study publicly available on registry

August 21, 2023

Completed
8 months until next milestone

Study Start

First participant enrolled

May 1, 2024

Completed
3.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 30, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 30, 2027

Last Updated

May 9, 2024

Status Verified

May 1, 2024

Enrollment Period

3.7 years

First QC Date

January 6, 2023

Last Update Submit

May 7, 2024

Conditions

Keywords

CAR T cellB cell lymphomaCD20HP-NAP

Outcome Measures

Primary Outcomes (3)

  • Incidence of dose limiting toxicity

    The incidence of dose limiting toxicity (DLT). Number of Participants Experiencing Adverse Events (AEs) Defined as Dose Limiting Toxicities (DLTs)

    First infusion up to 30 days

  • Adverse events

    The nature, frequency, severity, and tolerability of adverse events (AEs) including clinically significant laboratory data, and their relation to dosage.

    24 months

  • Pharmacodynamic (PD) and pharmacokinetic (PK)

    PD is assessed by determine circulating B cell level; PK is assessed by determine circulating CAR20(NAP)-T cells.

    Either 24 month or 15 years during long-term follow up if clinically indicated

Secondary Outcomes (5)

  • Objective response rate [ORR]

    24 months

  • Progression free survival [PFS]

    24 months

  • Best Objective Response

    24 months

  • Duration of Response (DOR)

    24 months

  • Overall Survival (OS)

    either 24 months or 15 years during long-term follow up if clinically indicated

Other Outcomes (2)

  • Anti-NAP response

    either 24 months or 15 years during long-term follow up if clinically indicated

  • Bystander immunity activation

    either 24 months or 15 years during long-term follow up if clinically indicated

Study Arms (1)

Treatment

EXPERIMENTAL

CAR20(NAP)-T treatment

Biological: CAR20(NAP)-TDrug: CyclophosphamideDrug: Fludarabine

Interventions

CAR20(NAP)-TBIOLOGICAL

Autologous CAR-T cells targeting CD20 and upon target recognition express and secrete NAP

Also known as: ELC-301
Treatment

pre-conditioning chemotherapy

Treatment

pre-conditioning chemotherapy

Treatment

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Signed informed consent.
  • Relapsed or refractory CD20+ diffuse large B-cell lymphoma, mantle cell lymphoma or indolent lymphoma.
  • The patient should have been treated with at least two lines of therapy and have no curative treatment option, specifically
  • Relapsed or refractory CD20+ B-cell lymphoma that are not eligible to receive clinically approved CD19-directed CAR T cell treatment.
  • Relapsed or refractory CD20+ B-cell lymphoma who are CD19 negative.
  • Relapsed or refractory B-cell lymphoma who relapse after CD19 CAR T cell treatment.
  • In phase I age \>18 years, in phase II all ages
  • Measurable disease per Lugano classification.
  • Performance status ECOG 0-2.
  • Adequate bone marrow function as evidenced by:
  • Absolute neutrophil count (ANC) ≥ 1x10\^9/l/L
  • Platelet ≥ 50x 10\^9/l
  • Absolute lymphocyte count ≥ 0,1x10\^9/L
  • Adequate renal, hepatic, cardiac, and pulmonary function as evidenced by:
  • Creatinine clearance (Cockcroft Gault) ≥ 30 mL/min
  • +4 more criteria

You may not qualify if:

  • Other CD20-positive lymphomas i.e Burkitt lymphoma, primary CNS lymphoma, plasmablastic lymphoma or CLL transformed to DLBCL/HGBL (Richter transformation)
  • Any significant medical or psychiatric illness that would prevent the subject from giving informed consent or from following the study procedures.
  • Known human immunodeficiency virus (HIV) infection.
  • Impending organ-compromising disease.
  • Rapidly progressing disease
  • Active and/or severe infection (e.g., tuberculosis, sepsis and opportunistic infections, active hepatitis B virus (HBV) or active hepatitis C virus (HCV) infection.
  • Other serious underlying medical conditions, which, in the Investigator's judgment, could impair the ability of the subject to perform the treatment.
  • Treatment with an investigational product within 30 days prior to enrolment
  • Potential sign of hypersensitivity reaction to tocilizumab or any of the agents used in this study
  • Systemic corticosteroid treatment (\>10mg/day) \<5 days prior to IMP treatment or \<7 days prior leukapheresis.
  • Pregnancy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Karolinska University Hospital

Stockholm, Sweden

ACTIVE NOT RECRUITING

Uppsala University Hospital

Uppsala, Sweden

RECRUITING

Related Publications (1)

  • Jin C, Ma J, Ramachandran M, Yu D, Essand M. CAR T cells expressing a bacterial virulence factor trigger potent bystander antitumour responses in solid cancers. Nat Biomed Eng. 2022 Jul;6(7):830-841. doi: 10.1038/s41551-022-00875-5. Epub 2022 Apr 4.

    PMID: 35379957BACKGROUND

MeSH Terms

Conditions

Lymphoma, B-Cell

Interventions

Cyclophosphamidefludarabine

Condition Hierarchy (Ancestors)

Lymphoma, Non-HodgkinLymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Phosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus Compounds

Study Officials

  • Di Yu, PhD

    Uppsala University

    STUDY DIRECTOR

Central Study Contacts

Gunilla Enblad, MD/PhD

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 6, 2023

First Posted

August 21, 2023

Study Start

May 1, 2024

Primary Completion (Estimated)

December 30, 2027

Study Completion (Estimated)

December 30, 2027

Last Updated

May 9, 2024

Record last verified: 2024-05

Data Sharing

IPD Sharing
Will not share

Locations