NCT05849480

Brief Summary

Background: Biliary tract carcinoma (BTC) is cancer of the slender tubes that carry fluids in the liver. People with advanced BTC have few treatment options, and their survival rates are very low. Objective: To test a study drug (CDX-1140) combined 3 other drugs (capecitabine, oxaliplatin, Keytruda) in people with BTC. Eligibility: Adults aged 18 years or older with BTC that progressed after treatment and is not eligible for surgery or liver transplant. Design: Participants will be screened. They will have a physical exam. They will have blood tests and tests of their heart function. They will have imaging scans. They may need to have a biopsy: A small sample of tissue will be taken from their tumor using a small needle. Three of the drugs are given through a tube attached to a needle inserted into a vein in the arm (intravenous). The fourth drug is a pill taken by mouth with water. Participants will be treated in 21-day cycles. They will receive intravenous treatments on day 1 and day 8 of the first 6 cycles. After that, they will receive intravenous treatments only on day 1 of each cycle. Participants will take the pill twice a day only for the first 2 weeks of each cycle. They will stop taking this drug after 6 cycles. Imaging scans will be repeated every 9 weeks. Participants may continue receiving the study treatment for up to 2 years. Follow-up visits, including imaging scans, will continue for 3 more years. These images may be taken at other locations and sent to the researchers.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
60

participants targeted

Target at P75+ for phase_1

Timeline
194mo left

Started May 2024

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress12%
May 2024Jun 2042

First Submitted

Initial submission to the registry

May 8, 2023

Completed
1 day until next milestone

First Posted

Study publicly available on registry

May 9, 2023

Completed
1 year until next milestone

Study Start

First participant enrolled

May 8, 2024

Completed
16.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2040

Expected
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2042

Last Updated

March 24, 2026

Status Verified

January 22, 2026

Enrollment Period

16.1 years

First QC Date

May 8, 2023

Last Update Submit

March 21, 2026

Conditions

Keywords

ImmunotherapyPembrolizumabCAPOXCDX-1140CD40 agonist

Outcome Measures

Primary Outcomes (3)

  • Phase I: Safe dose of CDX-1140 in combination with CAPOX and Keytruda(R)

    Estimation of safe dose will be determined based on number of dose limiting toxicities (DLTs) experienced.

    35 days

  • Phase II: 6-month progression free survival (PFS) probability

    6-month PFS probability will be calculated using the Kaplan-Meier method.

    Study start - 6 months after start of study drug

  • Phase II: Overall response rate (ORR)

    The fraction of participants who experience a response (PR + CR) evaluated every 9 (+/- 4) weeks. Results will be reported along with 80% and 95% two-sided confidence intervals.

    Study start until disease progression or 5 years after initiation of study therapy, whichever occurs first.

Secondary Outcomes (2)

  • Safety of CDX-1140, CAPOX and Keytruda(R) in participants with advanced BTC as determined by toxicities experienced

    Day 1 of Cycle 1 through 90 days after the study agents were last administered

  • 5-year overall survival

    Study start - 5 years

Study Arms (2)

Phase I

EXPERIMENTAL

Keytruda, oxaliplatin, capecitabine and escalating doses of CDX-1140

Drug: oxaliplatinDrug: capecitabineBiological: KeytrudaBiological: CDX-1140

Phase II

EXPERIMENTAL

Keytruda, oxaliplatin, capecitabine and estimated safe dose of CDX-1140

Drug: oxaliplatinDrug: capecitabineBiological: KeytrudaBiological: CDX-1140

Interventions

Oxaliplatin (130 mg/m2) will be administered IV on Day 1 of each cycle, every 21 days (up to 6 cycles).

Phase IPhase II

Capecitabine (750 mg/m2 every 12 hours) will be administered orally with an intermittent schedule: 2 weeks on, 1 week off, of each cycle, every 21 days (up to 6 cycles).

Phase IPhase II
KeytrudaBIOLOGICAL

Pembrolizumab (200 mg) will be given IV on Day 8 of each cycle every 21 days (up to 6 cycles).

Phase IPhase II
CDX-1140BIOLOGICAL

CDX-1140 (0.36-1.5 mg/kg; per assigned dose level) will be given IV on Day 8 of each cycle every 21 days (up to 6 cycles).

Phase IPhase II

Eligibility Criteria

Age18 Years - 120 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants must have histopathological confirmation of BTC or histopathological confirmation of carcinoma in the setting of clinical and radiological characteristics which, together with the pathology, are highly suggestive of a diagnosis of BTC.
  • The maximum tumor size of any individual tumor or metastasis must be \<= 8 cm.
  • Participants should have progressed on standard of care first line systemic treatment or refused standard treatment.
  • Participants must have a disease that is not amenable to potentially curative resection or liver transplantation.
  • Participants must have evaluable or measurable disease per RECIST 1.1
  • ECOG performance status of 0 to 1
  • Participants must have adequate organ and marrow function as defined below:
  • Absolute neutrophil count
  • (ANC) \>= 1,000/mcL
  • Platelets \>= 100,000/mcL
  • Total bilirubin \<= 2.5 x ULN
  • ALT and AST \<= 5 x ULN.
  • Creatinine OR Measured or calculated creatinine clearance (CrCl) (estimated glomerular filtration rate (eGFR) may also be used in place of CrCl)
  • \<1.5x institution upper limit of normal OR
  • \>= 45 mL/min/1.73 m2 for participant with creatinine levels
  • +7 more criteria

You may not qualify if:

  • Participants who have had standard-of-care anti-cancer therapy or therapy with investigational agents (e.g., chemotherapy, endocrine therapy, targeted therapy, biologic therapy, tumor embolization, monoclonal antibodies, or other investigation agents) or large field radiotherapy within 4 weeks prior to treatment initiation.
  • Prior therapy with anti- CD40.
  • Receiving of live vaccines within 30 days prior to the treatment initiation. Examples of live vaccines include, but are not limited to, the following: measles, mumps, rubella, varicella/zoster, yellow fever, rabies, Bacillus Calmette-Guerin, and typhoid vaccine. Seasonal influenza vaccines for injection are generally killed virus vaccines and are allowed; however, intranasal influenza vaccines (e.g., FluMist(R)) are live attenuated vaccines and are not allowed.
  • Major surgery within 4 weeks prior to treatment initiation.
  • Active central nervous system metastases and/or carcinomatous meningitis.
  • HIV-infected participants.
  • History of (non-infectious) pneumonitis or current pneumonitis.
  • History of allergic reactions attributed to compounds of similar chemical or biologic composition to study drugs or other agents used in study, such as nivolumab, dacetuzumab, APX005M, ADC-1013.
  • Prior invasive malignancies within the past 3 years prior to treatment initiation (with the exception of non-melanoma skin cancers, non-invasive bladder cancer, or localized prostate cancer for whom systemic therapy is not required).
  • Any medical condition that requires chronic systemic steroid therapy, or any other form of immunosuppressive medication (inhaled and topical steroids are permitted).
  • Fridericia's corrected QT interval (QTcF) \>= 480 msec or other factors that increase the risk of QT prolongation or arrhythmic events (e.g., heart failure, hypokalemia, family history of long QT interval syndrome.
  • Participants who were not able to tolerate prior immune checkpoint inhibitor therapy.
  • Uncontrolled intercurrent illness or psychiatric illness/social situations that would limit compliance with study requirements.
  • Pregnancy.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

National Institutes of Health Clinical Center

Bethesda, Maryland, 20892, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Biliary Tract NeoplasmsBile Duct Neoplasms

Interventions

OxaliplatinCapecitabinepembrolizumab

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsBiliary Tract DiseasesDigestive System DiseasesBile Duct Diseases

Intervention Hierarchy (Ancestors)

Coordination ComplexesOrganic ChemicalsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsFluorouracilUracilPyrimidinonesDeoxyribonucleosidesNucleosidesNucleic Acids, Nucleotides, and Nucleosides

Study Officials

  • Tim F Greten, M.D.

    National Cancer Institute (NCI)

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Donna Hrones, C.R.N.P.

CONTACT

Tim F Greten, M.D.

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 8, 2023

First Posted

May 9, 2023

Study Start

May 8, 2024

Primary Completion (Estimated)

June 1, 2040

Study Completion (Estimated)

June 1, 2042

Last Updated

March 24, 2026

Record last verified: 2026-01-22

Data Sharing

IPD Sharing
Will share

All IPD recorded in the medical record will be shared with intramural investigators upon request. All IPD recorded in the medical record will be shared with intramural investigators upon request. In addition, all large scale genomic sequencing data will be shared with subscribers to dbGaP. All collected IPD will be shared with collaborators under the terms of collaborative agreements.

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Clinical data available during the study and indefinitely. Genomic data are available once genomic data are uploaded per protocol GDS plan for as long as database is active.
Access Criteria
Clinical data will be made available via subscription to BTRIS and with the permission of the study PI. Genomic data are made available via dbGaP through requests to the data custodians.

Locations