NCT05513612

Brief Summary

The primary purpose of this study is to determine the safety and efficacy of novel autologous CAR-T cells in patients with hematopoietic and lymphoid malignancies.

Trial Health

50
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Timeline
8mo left

Started Aug 2020

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress90%
Aug 2020Dec 2026

Study Start

First participant enrolled

August 1, 2020

Completed
2.1 years until next milestone

First Submitted

Initial submission to the registry

August 22, 2022

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 24, 2022

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2025

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2026

Expected
Last Updated

March 1, 2023

Status Verified

February 1, 2023

Enrollment Period

5.4 years

First QC Date

August 22, 2022

Last Update Submit

February 27, 2023

Conditions

Keywords

CD123 CAR-TCD19 CAR-TBCMA CAR-TCD7 CAR-THematopoietic and Lymphoid Malignancies

Outcome Measures

Primary Outcomes (3)

  • TEAEs

    Incidence and severity of Treatment Emergent Adverse Event.

    4 weeks

  • TRAEs

    Incidence and severity of Treatment Related Adverse Events.

    4 weeks

  • AESIs

    Incidence and severity of AEs of Special Interest.

    4 weeks

Secondary Outcomes (3)

  • Duration of Overall Response (DOR)

    12 months

  • Progression-Free Survival (PFS)

    12 months

  • Overall survival (OS)

    12 months

Study Arms (1)

Autologous CAR-T cells

EXPERIMENTAL

A conditioning chemotherapy regimen of fludarabine and cyclophosphamide will be administered followed by investigational treatment, CAR-T cells. CAR-T cells targeted CD19/BCMA/CD123/CD7 are autologous genetically modified T cells.

Biological: Autologous CAR-T cellsDrug: FludarabineDrug: Cyclophosphamide

Interventions

CAR-T cells will be infused intravenously.

Autologous CAR-T cells

Administered according to package insert

Also known as: Fludara
Autologous CAR-T cells

Administered according to package insert

Also known as: Cytoxan
Autologous CAR-T cells

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Ability to understand and the willingness to sign informed consent.
  • Patients with relapsed or refractory Acute Myeloid Leukemia (AML), B-cell Non-Hodgkin's Lymphoma (B-NHL), Multiple Myeloma (MM), Adult T-cell Leukemia/Lymphoma (ATL), B-cell Acute Lymphoblastic Leukemia (B-ALL) after at least two cycles of first-line therapy or autologous hematopoietic stem cell transplantation (auto-HSCT).
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0\~2.
  • Adequate organ functions:
  • Sufficient bone marrow function evaluated by investigator to receive lymphodepleting preparative regimen;
  • Serum creatinine (Cr) ≤ 1.5 × upper limit of normal (ULN), or creatinine clearance rate (as estimated by Cockcroft Gault) \> 30 mL/min/1.73 m\^2;
  • Alanine aminotransferase (ALT) ≤ 5×ULN; and total bilirubin (TBIL) \<2.0mg/dL; TBIL of patients with Gilbert's Syndrome or liver involvement must less than 3.0 mg/dL;
  • Left ventricular ejection fraction (LVEF) \> 40%.
  • Subjects who have previously received CD19 targeted therapy must have biopsy-proven lymphoma lesions still express CD19 antigen.

You may not qualify if:

  • Lymphomas involving only the central nervous system (CNS) (subjects with secondary CNS lymphomas are admitted).
  • History of another malignancy that has not been in remission for at least 2 year (the following conditions may be excluded from the 2-year restriction: non-melanoma skin cancer, completely resected stage I tumor with low probability of recurrence, limited-stage prostate cancer after treatment, biopsy-proven cervical carcinoma in situ, or PAP smear showing squamous epithelium internal lesions).
  • History of treatment with Alemtuzumab within 6 months prior to leukapheresis, or Fludarabine or Cladribine within 3 months prior to leukapheresis.
  • Active hepatitis C (HCV), hepatitis B (HBV), human immunodeficiency virus (HIV), or syphilis infection.
  • Uncontrolled fungal, bacterial, viral, or other infection.
  • Acute or chronic graft-versus-host disease (GVHD).
  • History of any of the following cardiovascular diseases within the past 6 months: Class III or IV heart failure as defined by the New York Heart Association (NYHA), cardiac angioplasty or stent, myocardial infarction, unstable angina, or other clinically significant heart disease.
  • History or clinical evidence of CNS disease.
  • Female subjects who are pregnant or lactating.
  • Prior CAR-T therapy or other genetically modified T cell therapy.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Shanghai Pudong Hospital, Fudan University Affiliated Pudong Medical Center

Shanghai, Shanghai Municipality, 201399, China

Location

MeSH Terms

Conditions

Leukemia, Myeloid, AcuteLymphoma, B-CellMultiple MyelomaPrecursor T-Cell Lymphoblastic Leukemia-LymphomaBurkitt Lymphoma

Interventions

fludarabinefludarabine phosphateCyclophosphamide

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoma, Non-HodgkinLymphomaLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesNeoplasms, Plasma CellHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHemorrhagic DisordersPrecursor Cell Lymphoblastic Leukemia-LymphomaLeukemia, LymphoidEpstein-Barr Virus InfectionsHerpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus Infections

Intervention Hierarchy (Ancestors)

Phosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus Compounds

Study Officials

  • Zhiguo Long

    Shanghai Pudong Hospital

    PRINCIPAL INVESTIGATOR
0

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 22, 2022

First Posted

August 24, 2022

Study Start

August 1, 2020

Primary Completion

December 31, 2025

Study Completion (Estimated)

December 31, 2026

Last Updated

March 1, 2023

Record last verified: 2023-02

Data Sharing

IPD Sharing
Will not share

Locations