NCT05443087

Brief Summary

Targeted therapy drug monitoring in digestive oncology: Dosage of plasma levels of various multikinase inhibitors (MKI) in patients treated for advanced digestive cancer (gastrointestinal stromal tumor (GIST), metastatic colorectal cancer (mCRC), hepatocellular carcinoma (HCC), gastroenteropancreatic neuroendocrine tumor (gepNET), or pancreatic neuroendocrine tumor (pNET)), with the aim of determine the optimal dose adapted for each patient, in the future.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
330

participants targeted

Target at P75+ for not_applicable

Timeline
13mo left

Started Aug 2022

Longer than P75 for not_applicable

Geographic Reach
1 country

29 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress78%
Aug 2022Jun 2027

First Submitted

Initial submission to the registry

June 23, 2022

Completed
12 days until next milestone

First Posted

Study publicly available on registry

July 5, 2022

Completed
2 months until next milestone

Study Start

First participant enrolled

August 29, 2022

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2026

Expected
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2027

Last Updated

March 30, 2025

Status Verified

March 1, 2025

Enrollment Period

3.9 years

First QC Date

June 23, 2022

Last Update Submit

March 25, 2025

Conditions

Keywords

multi kinases inhibitorstherapeutic drug monitoringpharmacokineticspharmacodynamicsadvanced digestive cancers

Outcome Measures

Primary Outcomes (1)

  • Trough concentration (Ctrough)

    Trough concentration (Ctrough) shows the blood concentration reached by a drug immediately before the next dose is administered, once steady state has been attained. It can also be defined as the minimal drug concentration in the patient's body. Plasmatic measures will be performed by liquid chromatography with tandem mass spectrometry after protein precipitation by acetonitrile.

    From inclusion untill the end of treatment up to 4 years

Secondary Outcomes (5)

  • Progression-free survival

    4 years

  • Overall survival

    4 years

  • Objective response rate

    4 years

  • Disease control rate

    4 years

  • Safety: drug toxicity

    Throughout study completion, up to 4 years

Study Arms (5)

Regorafenib - mCRC, GIST, HCC

EXPERIMENTAL

3 x 30 = 90 patients Patients with mCRC, GIST or HCC treated with Regorafenib

Other: Blood sampling to build population pharmacokinetics model

Everolimus - gepNET

EXPERIMENTAL

60 patients Patients with gepNET treated with Everolimus

Other: Blood sampling to build population pharmacokinetics model

Sunitinib - pNET, GIST

EXPERIMENTAL

2 x 30 = 60 patients Patients with pNET and GIST, treated with Sunitinib

Other: Blood sampling to build population pharmacokinetics model

Cabozantinib - HCC

EXPERIMENTAL

60 patients Patients with HCC treated with Cabozantinib

Other: Blood sampling to build population pharmacokinetics model

Encorafenib - Cetuximab - mCRC

EXPERIMENTAL

60 patients Patients with mCRC treated with the association Encorafenib - Cetuximab

Other: Blood sampling to build population pharmacokinetics model

Interventions

Determine for each drug plasmatic exposure (Css, trough) through the PopPK model. Concentrations measured at the following time points: * 1 month after the first treatment administration * 2 months after the first treatment administration * In case of progression * In case of severe toxicities (AESI) related to the drug received

Cabozantinib - HCCEncorafenib - Cetuximab - mCRCEverolimus - gepNETRegorafenib - mCRC, GIST, HCCSunitinib - pNET, GIST

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patient aged 18 years or over
  • Advanced digestive cancer (histologically confirmed or confirmed by imaging for HCC) for which a standard treatment (according to each drug SmPC and as per standard of care) planned with:
  • Regorafenib for GIST, mCRC, and HCC,
  • Everolimus for gepNET,
  • Sunitinib for pNET or GIST,
  • Cabozantinib for HCC,
  • Encorafenib - cetuximab for mCRC
  • Life expectancy of greater than 3 months - at the discretion of the investigator
  • Measurable disease according to tumor evaluation criteria as per local practice (Response Evaluation Criteria in Solid Tumors (RECIST) Version 1.1, etc.)
  • Patients must be affiliated to a Social Security System (or equivalent)
  • Patient must have signed a written informed consent form prior to any trial specific procedures. When the patient is physically unable to give their written consent, a trusted person of their choice, independent from the investigator or the sponsor, can confirm in writing the patient's consent.

You may not qualify if:

  • Other concomitant anticancer systemic treatment (chronic chemotherapy, antitumor hormone therapy or immunotherapy) than the one studied
  • Unresolved toxicity higher than NCI-CTCAE v5.0 Grade 1 attributed to any prior therapy/procedure excluding alopecia and peripheral neuropathy
  • Prior treatment with the same MKI molecule(s) planned to be given in the cohort. If different MKI molecules (from the one(s) planned in the study) have been previously taken, a wash out period of 2 weeks before treatment should be observed.
  • Other invasive malignancies either currently active or active in the last 3 years, except adequately treated in situ carcinoma of the cervix and basal or squamous cell carcinoma of the skin
  • Any condition that may jeopardize patient participation in the study as well as non contraception for male and female with child-bearing potential, pregnancy or breast feeding.
  • Patient unwilling or unable to comply with the medical follow-up required by the standard treatment taken (including PK sampling during treatment phase and vital status collection during follow-up phase) because of psychosocial, familial, social or geographical reasons
  • Patient deprived of their liberty or under protective custody or guardianship

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (29)

CHU d'Amiens Pcardie - Hopital Sud

Amiens, France

RECRUITING

CH d'Auxerre

Auxerre, France

RECRUITING

Institut du Cancer Avignon - Institut Sainte Catherine

Avignon, France

WITHDRAWN

CH de Bayeux - Onconormandie

Bayeux, France

WITHDRAWN

Centre Jean Perrin

Clermont-Ferrand, France

RECRUITING

Hôpital Beaujon APHP

Clichy, France

RECRUITING

Centre Georges Francois Leclerc

Dijon, France

WITHDRAWN

Institut de Cancérologie de Bourgogne

Dijon, France

RECRUITING

CH Eure Seine - Hopital d'Evreux Vernon

Évreux, France

NOT YET RECRUITING

Centre Oscar Lambret

Lille, France

RECRUITING

Groupement des hôpitaux de l'Institut Catholique de Lille - Hôpital Saint Vincent de Paul

Lille, France

NOT YET RECRUITING

Centre Léon Bérard

Lyon, France

WITHDRAWN

Hôpital Européen Marseille

Marseille, France

NOT YET RECRUITING

CHRU de Nancy - Hôpital de Brabois Adulte

Nancy, France

RECRUITING

CHU de Nantes - Hôtel Dieu

Nantes, France

RECRUITING

Centre Antoine Lacassagne

Nice, France

WITHDRAWN

APHP Pitié Salpétrière

Paris, France

RECRUITING

Hôpital Saint Joseph

Paris, France

RECRUITING

Institut Mutualiste de Montsouris

Paris, France

RECRUITING

Hôpital Privé des Côtes d'Armor - SAS

Plérin, France

RECRUITING

CHU de Poitiers

Poitiers, France

NOT YET RECRUITING

CHU de Reims - Hôpital Robert Debré

Reims, France

RECRUITING

Institut Jean Godinot

Reims, France

RECRUITING

Centre Eugène Marquis

Rennes, France

NOT YET RECRUITING

CHU Rouen - Hôpital Charles Nicolle

Rouen, France

RECRUITING

CH Saint Malo - Hôpital Broussais

St-Malo, France

RECRUITING

ICANS

Strasbourg, France

RECRUITING

CHU de Tours

Tours, France

RECRUITING

Gustave Roussy

Villejuif, France

RECRUITING

MeSH Terms

Conditions

Gastrointestinal NeoplasmsColorectal NeoplasmsCarcinoma, HepatocellularNeuroendocrine Tumors

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesIntestinal NeoplasmsColonic DiseasesIntestinal DiseasesRectal DiseasesAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeLiver NeoplasmsLiver DiseasesNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms, Nerve Tissue

Study Officials

  • David MALKA, Dr

    Gustave ROUSSY - VILLEJUIF

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Michaël CHEVROT, Ph.D

CONTACT

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 23, 2022

First Posted

July 5, 2022

Study Start

August 29, 2022

Primary Completion (Estimated)

August 1, 2026

Study Completion (Estimated)

June 1, 2027

Last Updated

March 30, 2025

Record last verified: 2025-03

Locations