NCT05286814

Brief Summary

Background: One way to treat liver cancer is to deliver chemotherapy drugs only to the liver (and not to the whole body). Researchers want to see if adding the drug PDS01ADC can improve the treatment. The drug triggers the immune system to fight cancer.\<TAB\> Objective: To see if treatment with HAIPs to deliver liver-directed FUDR and Dexamethasone chemotherapy in combination with PDS01ADC is effective for certain cancers. Eligibility: People aged 18 and older who have cancer of the bile ducts that is only in the liver, or colorectal cancer that has spread to the liver, or cancer of the adrenal glands that has spread to the liver, who are also receiving or planning to receive standard systemic chemotherapy for their disease. Design: Participants will be screened with: Medical history Physical exam Blood tests Pregnancy test (if needed) Tumor biopsy (if needed) Electrocardiogram Computed tomography (CT) scans Participants will have an abdominal operation. A catheter will be placed into an artery that feeds blood to the liver. The catheter will then be attached to the HAIP. The HAIP will lay under the skin on the left side of the abdomen. All participants will have liver-directed FUDR and Dexamethasone chemotherapy drugs or heparin with saline infused into the HAIP every 2 weeks. PDS01ADC will be injected under the skin every 4 weeks. They will receive this treatment until their cancer gets worse or they have bad side effects. Participants will also receive standard systemic chemotherapy for their disease, assigned based on diagnosis, through an IV by their medical oncologist (at NIH or by a local provider) every 2 weeks. Participants will have 2 study visits at NIH each month. They will have CT scans every 8 weeks. At visits, they will repeat some screening tests. Participants will have a follow-up visit 1 month after treatment ends. Then they will be contacted every 6 months for 5 years.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P50-P75 for phase_2

Timeline
32mo left

Started Oct 2022

Longer than P75 for phase_2

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress57%
Oct 2022Dec 2028

First Submitted

Initial submission to the registry

March 12, 2022

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 18, 2022

Completed
7 months until next milestone

Study Start

First participant enrolled

October 24, 2022

Completed
5.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2027

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2028

Last Updated

May 4, 2026

Status Verified

April 30, 2026

Enrollment Period

5.2 years

First QC Date

March 12, 2022

Last Update Submit

May 1, 2026

Conditions

Keywords

Unresectable Liver TumorSMART SystemResponse RatesProgression Free Survival (Pfs)Patient SurvivalOverall Survival (Os)NHS-IL12McrcIccACC

Outcome Measures

Primary Outcomes (1)

  • Determine overall response rates

    Simon optimal two-stage Phase II trial design will be used to determine overall response using RECIST criteria. The clinical response rate (CR+PR) will be determined and reported along with a 95% confidence interval, separately by cohort.

    baseline, every 8 weeks while on treatment, and 4-8 weeks following initial documentation of objective response; an additional scan is performed at Week 12.

Secondary Outcomes (4)

  • Determine overall survival (OS)

    date of enrollment until death from any cause, or after 5 years off treatment

  • Determine extra-hepatic progression-free survival (PFS)

    date of operation to date of first observation of progressive disease within the liver or death, or after 5 years off treatment whichever comes first

  • Evaluate safety of PDS01ADC in combination with HAIP therapy

    on-going from treatment start through end of treatment visit

  • Determine hepatic progression-free survival (PFS)

    date of operation to date of first observation of progressive disease within the liver or death, or after 5 years off treatment whichever comes first

Study Arms (3)

1/ HAIP +PDS01ADC+FOLFOX or FOLFORI

EXPERIMENTAL

PDS01ADC+HAIP FUDR and Dexamethasone chemotherapy in combination with FOLFOX or FOLFIRI

Drug: DexamethasoneDrug: PDS01ADCDevice: Intera 3000 Hepatic Artery Infusion Pump (HAIP)Drug: Floxuridine

2/ HAIP +PDS01ADC+GemOx or FOLFOX

EXPERIMENTAL

PDS01ADC+HAIP FUDR and Dexamethasone chemotherapy in combination with GemOx or FOLFOX

Drug: DexamethasoneDrug: PDS01ADCDevice: Intera 3000 Hepatic Artery Infusion Pump (HAIP)Drug: Floxuridine

3/ HAIP +PDS01ADC+GemOx

EXPERIMENTAL

PDS01ADC+HAIP FUDR and Dexamethasone chemotherapy in combination with GemOx

Drug: DexamethasoneDrug: PDS01ADCDevice: Intera 3000 Hepatic Artery Infusion Pump (HAIP)Drug: Floxuridine

Interventions

HAIP FUDR and Dexamethasone treatment on D1 of every cycle. Dexamethasone: (1 mg/day X pump volume / pump flow rate)

1/ HAIP +PDS01ADC+FOLFOX or FOLFORI2/ HAIP +PDS01ADC+GemOx or FOLFOX3/ HAIP +PDS01ADC+GemOx

PDS01ADC will be administered by subcutaneous injection on Day 15 of every cycle. Cycle 1 at 12 mcg/kg; Cycle 2 reduced to 8 mcg/kg with the addition of systemic chemotherapy, to continue for further cycles. Note: any dose reduction in FUDR = 50% due to liver enzyme elevations means that the dose of PDS01ADC will be reduced to 4 mcg/kg.

1/ HAIP +PDS01ADC+FOLFOX or FOLFORI2/ HAIP +PDS01ADC+GemOx or FOLFOX3/ HAIP +PDS01ADC+GemOx

Intera 3000 HAIP will be filled with mixture of Floxuridine and Dexamethasone in 25,000 units heparin/saline (Heparin + 0.9% Sodium Chloride) on Day 1; Days 1-14 of every cycle pump will perfuse drugs to liver. On Day 15 of each cycle, the pump will be emptied and filled with 30,000 units heparin/saline (Heparin + 0.9% Sodium Chloride); Days 15-28 of every cycle will perfuse heparin/saline to liver.

1/ HAIP +PDS01ADC+FOLFOX or FOLFORI2/ HAIP +PDS01ADC+GemOx or FOLFOX3/ HAIP +PDS01ADC+GemOx

HAIP FUDR and Dexamethasone treatment on D1 of every cycle. Floxuridine: (0.12 mg/kg x ideal average body weight in kg X 30 mL \[pump volume\] / Pump Flow Rate)

1/ HAIP +PDS01ADC+FOLFOX or FOLFORI2/ HAIP +PDS01ADC+GemOx or FOLFOX3/ HAIP +PDS01ADC+GemOx

Eligibility Criteria

Age18 Years - 120 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants must have a documented diagnosis of one of the following cancers:
  • Metastatic colorectal cancer (mCRC)
  • Intrahepatic cholangiocarcinoma (ICC)
  • Adrenocortical carcinoma (ACC) with liver dominant disease
  • Participants must have an identified medical oncologist who has recommended and is planning to oversee treatment with one of the following standard chemotherapy regimens (based on disease type) not to begin sooner than 28 days after initiation of study-directed HAIP intervention:
  • mCRC: FOLFOX or FOLFIRI
  • ICC: GemOx or FOLFOX
  • ACC: GemOx
  • Age \>= 18 years.
  • Negative serum or urine pregnancy test at screening for individuals of childbearing potential (IOCBP).
  • NOTE: IOCBP is defined as any individual who has experienced menarche and who has not undergone successful surgical sterilization or who is not postmenopausal. IOCBP must have a negative pregnancy test (HCG blood or urine) during screening.
  • All participants (regardless of childbearing potential) must agree to use highly effective contraception prior to study entry, for the duration of study participation, and for 3 months after completion of study treatment for those able to father a child or 6 months after completion of study treatment for those of child-bearing potential (i.e., IOCBP). Highly effective birth control (failure rate of less than 1%), e.g., intrauterine device (IUD), intrauterine hormone-releasing system (IUS), bilateral tubal occlusion, vasectomized partner and sexual abstinence. Note: The use of condoms by participants who are able to get other individuals pregnant is required unless the partner of childbearing potential is permanently sterile.
  • Nursing (including breastfeeding) participants must agree to discontinue nursing.
  • Arterial anatomy on CT angiogram or CT chest, abdomen and pelvis multiphase (i.e., CT C/A/P multiphase) amenable to placement of the HAIP.
  • Participant must sign the informed consent form to participate in this study.
  • +40 more criteria

You may not qualify if:

  • Participants who are receiving any other investigational agents.
  • Participants who have previously received rIL-12.
  • Participants with active autoimmune diseases, that might deteriorate when receiving an immunostimulatory agent with the exceptions:
  • diabetes type I, vitiligo, alopecia, psoriasis, hypo- or hyperthyroid disease not requiring immunosuppressive treatment are eligible;
  • participants requiring hormone replacement with corticosteroids are eligible if the steroids are administered only for the purpose of hormonal replacement and at doses \<= 10 mg of prednisone or equivalent per day;
  • administration of steroids for other conditions through a route known to result in a minimal systemic exposure (topical, intranasal, intro-ocular, or inhalation) is eligible.
  • History of organ transplant, except for transplants that do not require immunosuppression.
  • History of or active inflammatory bowel disease (e.g., Crohn s disease, ulcerative colitis).
  • Known hypersensitivity or allergic reactions attributed to any compounds of similar chemical or biologic composition to the study medication, such as recombinant IL-12 or other monoclonal antibodies and history of allergic reactions attributed to compounds of similar chemical composition to FUDR or heparin.
  • Clinically significant (i.e., active) cardiovascular disease: cerebral vascular accident/stroke \< 6 months prior to enrollment, myocardial infarction \< 6 months prior to enrollment, unstable angina, congestive heart failure (\>= NYHA III) or serious cardiac arrhythmia requiring medication.
  • All conditions associated with significant necrosis of nontumor-bearing tissues.
  • Esophageal or gastroduodenal ulcers \< 6 months prior to treatment.
  • Active ischemic bowel disease.
  • Psychiatric illness/social situations that would limit compliance with study requirements.
  • Active concurrent malignancies within the last five years other than colorectal primary except basal cell skin carcinoma and thyroid carcinoma.
  • +17 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

National Institutes of Health Clinical Center

Bethesda, Maryland, 20892, United States

RECRUITING

Related Publications (1)

  • Victory JH, Smith EC, Ryan CE, Lambdin J, Sarvestani AL, Friedman LR, Eade AV, Larrain C, Pu T, Luberice K, Ramamoorthy B, Rainey AJ, Hannah CE, Smith KM, Mabry D, Xie C, Davis JL, Blakely AM, Gulley JL, Schlom J, Monge C, Greten TF, Hernandez JM. Hepatic artery infusion pump (HAIP) therapy in combination with targeted delivery of IL-12 for patients with metastatic colorectal cancer or intrahepatic cholangiocarcinoma: a phase II trial protocol. J Gastrointest Oncol. 2024 Jun 30;15(3):1348-1354. doi: 10.21037/jgo-24-71. Epub 2024 Jun 20.

Related Links

MeSH Terms

Conditions

Colorectal NeoplasmsCholangiocarcinomaCirrhosis, Familial, with Pulmonary HypertensionBile Duct NeoplasmsAdrenocortical CarcinomaAdrenal Gland NeoplasmsAdrenal Cortex Neoplasms

Interventions

DexamethasoneFloxuridine

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal DiseasesAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeBiliary Tract NeoplasmsBile Duct DiseasesBiliary Tract DiseasesEndocrine Gland NeoplasmsAdrenal Cortex DiseasesAdrenal Gland DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

PregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, FluorinatedDeoxyuridineUridinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsDeoxyribonucleosidesNucleosidesNucleic Acids, Nucleotides, and Nucleosides

Study Officials

  • Jonathan M Hernandez, M.D.

    National Cancer Institute (NCI)

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Kathleen M Smith, R.N.

CONTACT

Jonathan M Hernandez, M.D.

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 12, 2022

First Posted

March 18, 2022

Study Start

October 24, 2022

Primary Completion (Estimated)

December 31, 2027

Study Completion (Estimated)

December 31, 2028

Last Updated

May 4, 2026

Record last verified: 2026-04-30

Data Sharing

IPD Sharing
Will share

All IPD recorded in the medical record will be shared with intramural investigators upon request.@@@@@@@@@@@@In addition, all large scale genomic sequencing data will be shared with subscribers to dbGaP.

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Clinical data available during the study and indefinitely.@@@@@@@@@@@@Genomic data are available once genomic data are uploaded per protocol GDS plan for as long as database is active.
Access Criteria
Clinical data will be made available via subscription to BTRIS and with the permission of the study PI. @@@@@@@@@@@@Genomic data are made available via dbGaP through requests to the data custodians.

Locations