NCT05059223

Brief Summary

This study is a multi-center, double-blind, placebo-controlled, randomized Phase 3 trial to assess the safety and efficacy of AXS-12 in narcoleptic subjects with cataplexy and excessive daytime sleepiness (EDS).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
90

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Sep 2021

Geographic Reach
2 countries

50 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 9, 2021

Completed
6 days until next milestone

Study Start

First participant enrolled

September 15, 2021

Completed
13 days until next milestone

First Posted

Study publicly available on registry

September 28, 2021

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 15, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 15, 2024

Completed
Last Updated

March 19, 2025

Status Verified

March 1, 2025

Enrollment Period

2.5 years

First QC Date

September 9, 2021

Last Update Submit

March 17, 2025

Conditions

Keywords

AXS-12NarcolepsyCataplexyExcessive daytime sleepinessReboxetineAxsome

Outcome Measures

Primary Outcomes (1)

  • Frequency of cataplexy attacks

    Average number of cataplexy attacks per week

    Change from Baseline to Week 5

Study Arms (2)

AXS-12 (reboxetine)

EXPERIMENTAL

Up to 5 weeks

Drug: AXS-12 (reboxetine)

Placebo

PLACEBO COMPARATOR

Up to 5 weeks

Drug: Placebo

Interventions

AXS-12 tablets, taken twice daily

AXS-12 (reboxetine)

Placebo tablets, taken twice daily

Placebo

Eligibility Criteria

Age15 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female subjects between 15 and 75 years of age, inclusive
  • Primary diagnosis of narcolepsy with cataplexy
  • Willing and able to comply with the study requirements

You may not qualify if:

  • Other clinically significant conditions potentially causing EDS
  • Clinically significant psychiatric disorders

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (50)

Clinical Research Site

Alabaster, Alabama, 35007, United States

Location

Clinical Research Site

Peoria, Arizona, 85381, United States

Location

Clinical Research Site

Phoenix, Arizona, 85054, United States

Location

Clinical Research Site

Redwood City, California, 94063, United States

Location

Clinical Research Site

San Diego, California, 92103, United States

Location

Clinical Research Site

Santa Ana, California, 92705, United States

Location

Clinical Research Site

Santa Monica, California, 90404, United States

Location

Clinical Research Site

Boulder, Colorado, 80301, United States

Location

Clinical Research Site

Colorado Springs, Colorado, 80918, United States

Location

Clinical Research Site

Brandon, Florida, 33511, United States

Location

Clinical Research Site

Clearwater, Florida, 33765, United States

Location

Clinical Research Site

Doral, Florida, 33122, United States

Location

Clinical Research Site

Kissimmee, Florida, 34741, United States

Location

Clinical Research Site

Miami, Florida, 33176, United States

Location

Clinical Research Site

Miami Lakes, Florida, 33016, United States

Location

Clinical Research Site

St. Petersburg, Florida, 33707, United States

Location

Clinical Research Site

Tampa, Florida, 33634, United States

Location

Clinical Research Site

Winter Park, Florida, 32789, United States

Location

Clinical Research Site

Atlanta, Georgia, 30315, United States

Location

Clinical Research Site

Atlanta, Georgia, 30328, United States

Location

Clinical Research Site

Gainesville, Georgia, 30501, United States

Location

Clinical Research Site

Macon, Georgia, 31210, United States

Location

Clinical Research Site

Stockbridge, Georgia, 30281, United States

Location

Clinical Research Site

Honolulu, Hawaii, 96817, United States

Location

Clinical Research Site

Peoria, Illinois, 61637, United States

Location

Clinical Research Site

Fort Wayne, Indiana, 46804, United States

Location

Clinical Research Site

Chevy Chase, Maryland, 20815, United States

Location

Clinical Research Site

Newton, Massachusetts, 02459, United States

Location

Clinical Research Site

North Dartmouth, Massachusetts, 02747, United States

Location

Clinical Research Site

Kalamazoo, Michigan, 49008, United States

Location

Clinical Research Site

Novi, Michigan, 48377, United States

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Clinical Research Site

Maplewood, Missouri, 63143, United States

Location

Clinical Research Site

Las Vegas, Nevada, 89106, United States

Location

Clinical Research Site

West Long Branch, New Jersey, 07764, United States

Location

Clinical Research Site

Brooklyn, New York, 11230, United States

Location

Clinical Research Site

New Hyde Park, New York, 11040, United States

Location

Clinical Research Site

Denver, North Carolina, 28037, United States

Location

Clinical Research Site

Gastonia, North Carolina, 28054, United States

Location

Clinical Research Site

Huntersville, North Carolina, 28078, United States

Location

Clinical Research Site

Cincinnati, Ohio, 45245, United States

Location

Clinical Research Site

Wyomissing, Pennsylvania, 19610, United States

Location

Clinical Research Site

Charleston, South Carolina, 29425, United States

Location

Clinical Research Site

Columbia, South Carolina, 29201, United States

Location

Clinical Research Site

Austin, Texas, 78731, United States

Location

Clinical Research Site

San Antonio, Texas, 78229, United States

Location

Clinical Research Site

Sugar Land, Texas, 77478, United States

Location

Clinical Research Site

Williamsburg, Virginia, 23188, United States

Location

Clinical Research Site

Markham, Ontario, L3R 1A3, Canada

Location

Clinical Research Site

Toronto, Ontario, M4P 1P2, Canada

Location

Clinical Research Site

Toronto, Ontario, M5S 3A3, Canada

Location

Related Links

MeSH Terms

Conditions

NarcolepsyCataplexyDisorders of Excessive Somnolence

Interventions

Reboxetine

Condition Hierarchy (Ancestors)

Sleep Disorders, IntrinsicDyssomniasSleep Wake DisordersNervous System DiseasesMental Disorders

Intervention Hierarchy (Ancestors)

MorpholinesOxazinesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 9, 2021

First Posted

September 28, 2021

Study Start

September 15, 2021

Primary Completion

March 15, 2024

Study Completion

March 15, 2024

Last Updated

March 19, 2025

Record last verified: 2025-03

Data Sharing

IPD Sharing
Will not share

Locations