NCT04849351

Brief Summary

A Multi-center, Single-arm, Open-label Clinical Study to Evaluate the Efficacy and Safety of HMPL-689 in Patients with Relapsed/Refractory Marginal Zone Lymphoma (MZL) and Follicular Lymphoma (FL)

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
178

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Apr 2021

Typical duration for phase_2

Geographic Reach
1 country

58 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 13, 2021

Completed
2 days until next milestone

Study Start

First participant enrolled

April 15, 2021

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 19, 2021

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 29, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 29, 2024

Completed
Last Updated

April 6, 2025

Status Verified

April 1, 2025

Enrollment Period

2.9 years

First QC Date

April 13, 2021

Last Update Submit

April 3, 2025

Conditions

Keywords

Marginal Zone LymphomaFollicular LymphomaPhosphatidylinositol 3-kinase inhibitor

Outcome Measures

Primary Outcomes (1)

  • Overall response rate (ORR)

    Defined as the proportion of patients with CR or PR

    Baseline up to the last patient has completed 12 months after treatment.

Secondary Outcomes (5)

  • Complete response (CR) rate

    Baseline up to the last patient has completed 12 months after treatment.

  • Progression-free survival (PFS)

    Baseline up to the last patient has completed 12 months after treatment.

  • Time to response (TTR)

    Baseline up to the last patient has completed 12 months after treatment.

  • Duration of response (DoR)

    Baseline up to the last patient has completed 12 months after treatment.

  • Overall survival (OS)

    Baseline up to the last patient has completed 12 months after treatment.

Study Arms (1)

Relapsed/Refractory MZL and FL

EXPERIMENTAL

Relapsed/Refractory Marginal Zone Lymphoma and Follicular Lymphoma

Drug: HMPL-689

Interventions

All patients are to receive monotherapy of HMPL-689 30 mg QD continuously in 28-day treatment cycles.

Also known as: Phosphatidylinositol 3-kinase-δ inhibitor
Relapsed/Refractory MZL and FL

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥18 years;
  • Patients with relapsed/refractory marginal zone lymphoma or follicular lymphoma
  • Eastern Cooperative Oncology Group (ECOG) Performance Status score 0-2;
  • At least one measurable lesion by computerised tomography (CT) / magnetic resonance imaging (MRI) (the longest diameter of nodal lesion \> 1.5 cm or extranodal lesion \> 1 cm);
  • Expected survival of more than 12 weeks;

You may not qualify if:

  • Having lymphoma with central nervous system (CNS) or cerebral pia mater invasion;
  • Known histologic transformation to aggressive lymphomas such as diffuse large B-cell lymphoma (DLBCL);
  • Prior use of any phosphatidylinositol 3-kinase (PI3K) inhibitor;
  • Inadequate organ function of liver and kidney;
  • Currently known active infection with human immunodeficiency virus (HIV), hepatitis B virus (HBV) or hepatitis C virus (HCV);
  • Having received systemic antitumor therapy or radiotherapy within 4 weeks prior to the first dose of the investigational product;
  • Toxicity of previous antitumor therapy not recovered to CTCAE grade ≤ 1, except alopecia, prior to the first dose of the investigational product;
  • Complicated with uncontrolled systemic infection requiring intravenous antibiotic treatment;
  • Pregnant (positive serum pregnancy test) or lactating women;
  • Any other disease, metabolic abnormality, physical examination abnormality or clinically significant laboratory test abnormality, one disease or state providing a reason to suspect that the subject is not suitable for HMPL-689 at the investigator's discretion, or one condition that will affect interpretation of the study results or bring the subject at high risk.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (58)

The Second Hospital of Anhui Medical University

Hefei, Anhui, 230601, China

Location

Beijing Chao-yang Hospital, Capital Medical University

Beijing, Beijing Municipality, 100020, China

Location

Beijing Friendship Hospital, Capital Medical University

Beijing, Beijing Municipality, 100050, China

Location

Peking University Third Hospital

Beijing, Beijing Municipality, 100191, China

Location

Beijing GoBroad Boren Hospital

Beijing, Beijing Municipality, China

Location

Beijing Tongren Hospital, Capital Medical University

Beijing, Beijing Municipality, China

Location

Chongqing University Cancer Hospital

Chongqing, Chongqing Municipality, 400030, China

Location

Fujian Cancer Hospital

Fuzhou, Fujian, 350014, China

Location

The First Affiliated Hospital of Xiamen University

Xiamen, Fujian, 361001, China

Location

Sun Yat-sen University Cancer Center

Guangzhou, Guangdong, 510060, China

Location

Nanfang Hospital, Southern Medical University

Guangzhou, Guangdong, 510515, China

Location

Cancer Hospital of Shantou University Medical College

Shantou, Guangdong, 515031, China

Location

The Fifth Affiliated Hospital of Sun Yat-sen University

Zhuhai, Guangdong, China

Location

Guangxi Medical University Affiliated Tumor Hospital

Nanning, Guangxi, 530021, China

Location

Hainan General Hospital

Haikou, Hainan, 570311, China

Location

Affiliated Hospital of Chengde Medical University

Chengde, Hebei, China

Location

The Fourth Hospital of Hebei Medical University

Shijiazhuang, Hebei, China

Location

Xingtai People's Hospital

Xingtai, Hebei, China

Location

The First Affiliated Hospital of Harbin Medical University

Harbin, Heilongjiang, China

Location

The First Hospital of Harbin

Harbin, Heilongjiang, China

Location

The First Affiliated Hospital of Henan University of Science and Technology

Luoyang, Henan, China

Location

Puyang Oilfield General Hospital

Puyang, Henan, 410900, China

Location

Henan Cancer Hospital

Zhengzhou, Henan, 450003, China

Location

Henan Provincial People's Hospital

Zhengzhou, Henan, 450003, China

Location

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, 450052, China

Location

Union Hospital affiliated to Tongji Medical College of Huazhong University of Science and Technology

Wuhan, Hubei, 430000, China

Location

People's Hospital of Wuhan University

Wuhan, Hubei, 430061, China

Location

Hunan Cancer Hospital

Changsha, Hunan, 410013, China

Location

The Second Xiangya Hospital of Central South University

Changsha, Hunan, China

Location

The Second People's Hospital of Huaihua

Huaihua, Hunan, China

Location

The Central Hospital of YongZhou

Yongzhou, Hunan, 425006, China

Location

The First People's Hospital of Nantong

Nantong, Jiangsu, 226001, China

Location

The Second Affiliated Hospital of Suzhou University

Suzhou, Jiangsu, China

Location

The First Affiliated Hospital of Gannan Medical University

Gannan, Jiangxi, China

Location

Ganzhou People's Hospital

Ganzhou, Jiangxi, China

Location

The First Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, 330006, China

Location

Jiangxi Provincial Cancer Hospital

Nanchang, Jiangxi, China

Location

The First Hospital of Jilin University

Changchun, Jilin, 130000, China

Location

The First Affiliated Hospital of Jinzhou Medical University

Jinzhou, Liaoning, China

Location

Shengjing Hospital of China Medical University

Shengyang, Liaoning, China

Location

Affiliated Hospital of Binzhou Medical University

Binzhou, Shandong, China

Location

Jinan Central Hospital

Jinan, Shandong, China

Location

Qilu Hospital of Shandong University

Jinan, Shandong, China

Location

The affiliated hospital of Qingdao University

Qingdao, Shandong, 266000, China

Location

Xinhua Hospital affiliated to Shanghai Jiaotong University School of Medicine

Shanghai, Shanghai Municipality, 200092, China

Location

Fudan University Shanghai Cancer Center

Shanghai, Shanghai Municipality, 200433, China

Location

Shanghai East Hospital, Tongji University School of Medicine

Shanghai, Shanghai Municipality, China

Location

Shanxi Bethune Hospital

Taiyuan, Shanxi, 30002, China

Location

The First Hospital of Shanxi Medical University

Taiyuan, Shanxi, China

Location

West China Hospital Sichuan University

Chengdu, Sichuan, 610041, China

Location

Affiliated Hospital of North Sichuan Medical College

Nanchong, Sichuan, 637000, China

Location

Tianjin Medical University Cancer Institute and Hospital

Tianjin, Tianjin Municipality, 300060, China

Location

Cancer Hospital Affiliated to Xinjiang Medical University

Ürümqi, Xinjiang, 830000, China

Location

First Affiliated Hospital of Kunming Medical University

Kunming, Yunnan, China

Location

Yunnan Cancer Hospital

Kunming, Yunnan, China

Location

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310003, China

Location

Zhejiang Cancer Hospital

Hangzhou, Zhejiang, 310022, China

Location

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, Zhejiang, 325000, China

Location

MeSH Terms

Conditions

Lymphoma, B-Cell, Marginal ZoneLymphoma, Follicular

Condition Hierarchy (Ancestors)

Lymphoma, B-CellLymphoma, Non-HodgkinLymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Study Officials

  • junning Cao, Ph.D

    Fudan University

    PRINCIPAL INVESTIGATOR
  • Zhiming Li, post-doc

    Sun Yat-sen University

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 13, 2021

First Posted

April 19, 2021

Study Start

April 15, 2021

Primary Completion

February 29, 2024

Study Completion

February 29, 2024

Last Updated

April 6, 2025

Record last verified: 2025-04

Locations