NCT04735952

Brief Summary

The study is a breath biomarker validation study. It is anticipated that 300 patients with cystic fibrosis (CF) from 5 clinical sites in the USA will be enrolled. The study is funded by the US NIH and the US Cystic Fibrosis Foundation. Enrollment commenced in May 2019. Sputum, induced sputum, and oropharyngeal swabs will be collected and evaluated at each clinic as part of standard clinical practice. Excess sputum will be sent to Children's Colorado Hospital for molecular analysis. No swabs will be sent anywhere (other than the clinic from which they originate). Breath samples will be taken from all study participants.

Trial Health

47
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
300

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started May 2019

Longer than P75 for all trials

Geographic Reach
2 countries

7 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 3, 2019

Completed
1.7 years until next milestone

First Submitted

Initial submission to the registry

January 21, 2021

Completed
13 days until next milestone

First Posted

Study publicly available on registry

February 3, 2021

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 30, 2024

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2024

Completed
Last Updated

December 5, 2023

Status Verified

December 1, 2023

Enrollment Period

5.6 years

First QC Date

January 21, 2021

Last Update Submit

December 2, 2023

Conditions

Keywords

BreathIMPACT

Outcome Measures

Primary Outcomes (1)

  • Differences in concentrations of individual volatile biomarkers and combinations of biomarkers in breath samples obtained from persons with and without P. aeruginosa lung infections

    Measured using comprehensive two-dimensional gas chromatography of exhaled breath compared to sputum culture (gold standard)

    Enrollment thru 2023. Last Longitudinal Study Visit will be 24 months after last AIM 2 enrollment

Secondary Outcomes (1)

  • Intra-subject changes in concentrations of individual volatile biomarkers and combinations of biomarkers in breath samples

    Thru end of 2025

Study Arms (2)

AIM 1

No-Intervention. Participants in this group will have 1 study visit only. During that visit, breath and sputum samples will be collected.

AIM 2

No-Intervention. Participants in this group will have up to 8 study visits over a 2 year period. During the study visits, breath and sputum samples will be collected.

Eligibility Criteria

Age3 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Participants will have a diagnosis of cystic fibrosis with cultures that are either P. aeruginosa (Pa) negative or Pa positive.

You may qualify if:

  • Aim 1, Cross-Sectional
  • Male or female, ages 8 years and older
  • Diagnosis of CF based on sweat chloride ≥ 60 mmol/L and/or 2 known CF mutations
  • @ BC Children's Hospital only- Non-expectorators are eligible if having a clinically indicated OP swab.
  • FEV1 ≥ 30% predicted for spontaneous expectorators or FEV1 ≥ 40% predicted for subjects undergoing sputum induction
  • Either P. aeruginosa (Pa) negative or chronically infected with P. aeruginosa (Pa positive) as defined below:
  • a. P. aeruginosa negative: must meet one of the following criteria: i: No growth of Pa in previous 12 months and ≥ 4 consecutive Pa-negative cultures, OR ii: No history of Pa positive airway cultures (sputum, OP, Bronchoalveolar lavage) b. P. aeruginosa positive i: Over 50% of cultures positive and at least 2 cultures positive for Pa in previous 18 months
  • Willing to participate in and comply with the study procedures and willingness of the subject, parent or legally authorized representative to provide written informed consent.

You may not qualify if:

  • Age \< 8 years
  • Intermittently infected with Pa
  • FEV1 \< 30%
  • History of lung transplant
  • Presence of a condition or abnormality that in the opinion of the Principal Investigator would compromise the safety of the subject or the quality of the data.
  • Aim 2, Longitudinal
  • Male or female, ages 8-16 years
  • Diagnosis of CF based on sweat chloride ≥ 60 mmol/L and/or 2 known CF mutations
  • @ BC Children's Hospital only- Non-expectorators are eligible if having a clinically indicated OP swab.
  • FEV1 ≥ 30% predicted for spontaneous expectorators or FEV1 ≥ 40% predicted for subjects undergoing sputum induction
  • P. aeruginosa negative, based on one of the following criteria:
  • No growth of Pa in previous 12 months and ≥ 4 consecutive Pa-negative cultures
  • No history of Pa positive airway cultures (sputum, OP, bronchoalveolar lavage)
  • Willing to participate in and comply with the study procedures and willingness of the subject, parent or legally authorized representative to provide written informed consent.
  • Age \< 8 years
  • +15 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (7)

Phoenix Children's Hospital

Phoenix, Arizona, 85016, United States

COMPLETED

Children's Hospital Colorado

Aurora, Colorado, 80045, United States

COMPLETED

National Jewish Health

Denver, Colorado, 80206, United States

COMPLETED

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

NOT YET RECRUITING

Cincinnati Children's Hospital

Cincinnati, Ohio, 45229-3039, United States

COMPLETED

BC Children's Hospital

Vancouver, British Columbia, V6H3N1, Canada

RECRUITING

St. Paul's Hospital

Vancouver, British Columbia, V6Z1Y6, Canada

RECRUITING

Related Links

Biospecimen

Retention: SAMPLES WITH DNA

Breath Samples (The act of analyzing the sample will completely deplete the sample.) Sputum Samples (A portion of the sample may be retained)

MeSH Terms

Conditions

Cystic FibrosisTooth, Impacted

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, DiseasesTooth DiseasesStomatognathic Diseases

Study Officials

  • Jane E Hill, PhD

    University of British Columbia

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Jane E Hill, PhD

CONTACT

Nina Nouribakikomarolya, PhD

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Associate Professor

Study Record Dates

First Submitted

January 21, 2021

First Posted

February 3, 2021

Study Start

May 3, 2019

Primary Completion

November 30, 2024

Study Completion

December 31, 2024

Last Updated

December 5, 2023

Record last verified: 2023-12

Data Sharing

IPD Sharing
Will not share

Locations