NCT04279769

Brief Summary

This is a phase 1b multiple ascending dose escalation study to evaluate the safety and tolerability of arginase inhibitor CB-280 in subjects with cystic fibrosis.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
32

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Jul 2020

Geographic Reach
2 countries

20 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 10, 2020

Completed
11 days until next milestone

First Posted

Study publicly available on registry

February 21, 2020

Completed
4 months until next milestone

Study Start

First participant enrolled

July 3, 2020

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 23, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 23, 2021

Completed
Last Updated

April 13, 2022

Status Verified

April 1, 2022

Enrollment Period

1.4 years

First QC Date

February 10, 2020

Last Update Submit

April 11, 2022

Conditions

Keywords

Arginase inhibitorCB-280

Outcome Measures

Primary Outcomes (1)

  • Determine the safety and tolerability of CB-280 in adult cystic fibrosis patients: incidence and severity of adverse event (AEs) assessed by Common Terminology Criteria for Adverse Events, version 5 (CTCAE v5.0)

    Start of treatment to Day 28

Secondary Outcomes (2)

  • Pharmacokinetics of plasma CB-280 measured by Peak Plasma Concentration (Cmax)

    Day 14

  • Pharmacokinetics of plasma CB-280 measured by area under the plasma concentration versus time curve, from time 0 to the last observed non-zero concentration (AUC 0-t)

    Day 14

Study Arms (5)

Cohort 1

EXPERIMENTAL

CB-280 twice daily at 50 mg for 14 days

Drug: CB-280

Cohort 2

EXPERIMENTAL

CB-280 twice daily at 100 mg for 14 days

Drug: CB-280

Cohort 3

EXPERIMENTAL

CB-280 twice daily at 200 mg for 14 days

Drug: CB-280

Cohort 4

EXPERIMENTAL

CB-280 twice daily at 400 mg for 14 days

Drug: CB-280

Placebo

PLACEBO COMPARATOR

Placebo twice daily for 14 days

Drug: Placebos

Interventions

CB-280DRUG

CB-280, oral capsule administered twice daily at the assigned dose level for 14 days

Cohort 1Cohort 2Cohort 3Cohort 4

Placebo oral capsule administrated twice daily at the assigned dose level for 14 days

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Written Informed Consent in accordance with federal, local, and institutional guidelines
  • Confirmed diagnosis of cystic fibrosis
  • Male or female subjects ≥ 18 years on the date of informed consent
  • Percent predicted FEV1 of 40-90% at screening per Global Lung Function Initiative (GLI) equation
  • Clinically stable with no significant changes in health status within 28 days prior to Day 1
  • Chronic lung infection with P. aeruginosa defined as at least one positive culture in the last two years and more than 50% of cultures positive since then
  • Stable cystic fibrosis medication regimen for at least 28 days inclusive of CFTR modulators prior to Day 1
  • Hemoglobin \> 10 g/dL at screening
  • Glomerular filtration rate \> 50 mL/min/1.73 m2 at screening
  • Normal liver function at screening

You may not qualify if:

  • History of any comorbidity that, in the opinion of the Investigator, might pose an additional risk in administering study drug to the subject or confound the results of the study
  • Lung infection with organisms associated with a more rapid decline in pulmonary status (including, but not limited to, Burkholderia cenocepacia, Burkholderia dolosa, and Mycobacterium abscessus)
  • Unable to receive study medication per os (PO)
  • Females who are pregnant, have a positive pregnancy test at screening, or are nursing (lactating)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

University of Arkansas for Medical Sciences

Little Rock, Arkansas, 72205, United States

Location

Long Beach Memorial Medical Center

Long Beach, California, 90806, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

The Cystic Fibrosis Institute

Glenview, Illinois, 60025, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Johns Hopkins University

Baltimore, Maryland, 21287, United States

Location

Boston Children's Hospital, Brigham & Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Billings Clinic

Billings, Montana, 59101, United States

Location

New York Medical College at Westchester Medical Center

Hawthorne, New York, 10532, United States

Location

UNC Marsico Clinical Research Center

Chapel Hill, North Carolina, 27514, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

Hershey Medical Center Pennsylvania State University

Hershey, Pennsylvania, 17033, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

University of Utah

Salt Lake City, Utah, 84132, United States

Location

Vermont Lung Center at the University of Vermont Medical Center

Colchester, Vermont, 05446, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23219, United States

Location

University of Calgary

Calgary, Alberta, T2N 4N1, Canada

Location

St. Pauls' Hospital

Vancouver, British Columbia, V6Z1Y6, Canada

Location

McGill University Health Center

Montreal, Quebec, H4A 3J1, Canada

Location

MeSH Terms

Conditions

Cystic Fibrosis

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, Diseases

Study Officials

  • Emil T Kuriakose, MD

    Calithera Bioscience

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 10, 2020

First Posted

February 21, 2020

Study Start

July 3, 2020

Primary Completion

November 23, 2021

Study Completion

November 23, 2021

Last Updated

April 13, 2022

Record last verified: 2022-04

Data Sharing

IPD Sharing
Will not share

Locations