NCT04519476

Brief Summary

This is a pilot study evaluating the safety and efficacy of selinexor among multiple myeloma (MM) patients that are refractory to lenalidomide-containing regimens with or without steroids.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
22

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Nov 2020

Typical duration for phase_1

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 12, 2020

Completed
7 days until next milestone

First Posted

Study publicly available on registry

August 19, 2020

Completed
2 months until next milestone

Study Start

First participant enrolled

November 1, 2020

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 29, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 29, 2023

Completed
Last Updated

October 31, 2023

Status Verified

October 1, 2023

Enrollment Period

3.2 years

First QC Date

August 12, 2020

Last Update Submit

October 30, 2023

Conditions

Keywords

SelinexorLenalidomide-RefractoryMultiple Myeloma

Outcome Measures

Primary Outcomes (2)

  • Overall Response

    Overall Response Rate (\[ORR\]=CR +VGPR+ PR)

    30 months

  • Clinical Benefit Rate

    Clinical Benefit Rate (\[CBR\]= CR+VGPR+PR+MR)

    30 months

Secondary Outcomes (6)

  • Adverse Events Occurrences

    30 months

  • Time to progression (TTP)

    30 months

  • Progression-free survival (PFS)

    30 months

  • Time to first response

    30 months

  • Duration of Response (DOR)

    30 months

  • +1 more secondary outcomes

Other Outcomes (1)

  • Measuring levels of multiple myeloma specific biomarkers such as M-Protein and BCMA

    30 months; duration of each cycle in this study is 28 days

Study Arms (1)

Selinexor/Lenalidomide/Steroids

EXPERIMENTAL

All subjects enrolled will receive: 1) selinexor, PO, at 60 mg once weekly on days 1-28 of a 28-day cycle, 2) lenalidomide, PO, 10 mg daily on days 1-21 of 28-days cycle and 3) methylprednisolone at the same dose and schedule as the last lenalidomide-containing regimen if it contained steroids. If patient's qualifying lenalidomide-containing regimen contained different type of steroid (e.g. prednisone, dexamethasone, etc.) then patient on this study will receive methylprednisolone at the equivalent dose and schedule.

Drug: SelinexorDrug: LenalidomideDrug: Methylprednisolone

Interventions

Selinexor (KPT-330) is a first-in-class, oral selective exportin 1 (XPO1) inhibitor (1,2). Selinexor functions by binding with and inhibiting the nuclear export protein XPO1 (also called CRM1), leading to the accumulation of tumor suppressor proteins in the cell nucleus along with inhibition of translation of oncoprotein mRNAs.

Also known as: KPT-330
Selinexor/Lenalidomide/Steroids

Immunomodulatory drug

Also known as: Revlimid
Selinexor/Lenalidomide/Steroids

Glucocorticoid, steroid

Also known as: Medrol
Selinexor/Lenalidomide/Steroids

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥ 18 year of age.
  • Willing and able to provide written informed consent in accordance with federal, local, and institutional guidelines. The patient must provide informed consent prior to the first screening procedure.
  • Able to adhere to the study visit schedule and other protocol requirements.
  • ECOG Performance Status (PS) of ≤ 2.
  • Has a diagnosis of MM based on standard criteria (9) as follows:
  • Major criteria:
  • Plasmacytomas on tissue biopsy.
  • Bone marrow plasmacytosis (greater than 30% plasma cells).
  • Monoclonal immunoglobulin spike on serum electrophoresis IgG greater than 3.5 g/dL or IgA greater than 2.0 g/dL or kappa or lambda light chain excretion greater than 1 g/day on 24-hour urine protein electrophoresis.
  • Minor criteria:
  • Bone marrow plasmacytosis (10% to 30% plasma cells).
  • Monoclonal immunoglobulin present but of lesser magnitude than given under major criteria.
  • Lytic bone lesions.
  • Normal IgM less than 50 mg/dL, IgA less than 100 mg/dL, or IgG less than 600 mg/dL.
  • Any of the following sets of criteria will confirm the diagnosis of multiple myeloma:
  • +21 more criteria

You may not qualify if:

  • Has received selinexor or another XPO1 inhibitor previously.
  • Prior malignancy that required treatment or has shown evidence of recurrence (except for non-melanoma skin cancer or adequately treated cervical carcinoma in situ) during the 5 years prior to randomization. Cancer treated with curative intent for \>5 years previously and without evidence of recurrence will be allowed.
  • Has any concurrent medical condition or disease (e.g., uncontrolled active hypertension, uncontrolled active diabetes, active systemic infection, POEMS syndrome \[polyneuropathy, organomegaly, endocrinopathy, monoclonal protein, and skin changes\], primary amyloidosis, etc.) that is likely to interfere with study procedures.
  • Uncontrolled active infection requiring parenteral antibiotics, antivirals, or antifungals within 1 week prior to Cycle 1 Day 1 (C1D1). Patients on prophylactic antibiotics or with a controlled infection within 1 week prior to C1D1 are acceptable.
  • Known intolerance, hypersensitivity, or contraindication to glucocorticoids.
  • Known hypersensitivity to compounds of similar chemical or biological composition to thalidomide and lenalidomide or steroids.
  • Concurrent use of other anti-cancer agents or treatments.
  • The development of erythema nodosum if characterized by a desquamating rash while taking thalidomide or similar drugs.
  • Severe hypercalcemia, i.e., serum calcium ≥ 12 mg/dL (3.0 mmol/L) corrected for albumin
  • Any condition, including the presence of laboratory abnormalities, which places the subject at unacceptable risk if he/she were to participate in the study or confounds the ability to interpret data from the study.
  • Pregnant or breastfeeding females.
  • BSA \<1.4 m2 at baseline, calculated by the Dubois (58) or Mosteller (59) method.
  • Life expectancy of less than 3 months.
  • Major surgery within 4 weeks prior to C1D1.
  • Active, unstable cardiovascular function, as indicated by the presence of:
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

James R Berenson, MD, Inc.

West Hollywood, California, 90069, United States

RECRUITING

Related Publications (2)

  • Abdul Razak AR, Mau-Soerensen M, Gabrail NY, Gerecitano JF, Shields AF, Unger TJ, Saint-Martin JR, Carlson R, Landesman Y, McCauley D, Rashal T, Lassen U, Kim R, Stayner LA, Mirza MR, Kauffman M, Shacham S, Mahipal A. First-in-Class, First-in-Human Phase I Study of Selinexor, a Selective Inhibitor of Nuclear Export, in Patients With Advanced Solid Tumors. J Clin Oncol. 2016 Dec;34(34):4142-4150. doi: 10.1200/JCO.2015.65.3949. Epub 2016 Oct 31.

    PMID: 26926685BACKGROUND
  • Gounder MM, Zer A, Tap WD, Salah S, Dickson MA, Gupta AA, Keohan ML, Loong HH, D'Angelo SP, Baker S, Condy M, Nyquist-Schultz K, Tanner L, Erinjeri JP, Jasmine FH, Friedlander S, Carlson R, Unger TJ, Saint-Martin JR, Rashal T, Ellis J, Kauffman M, Shacham S, Schwartz GK, Abdul Razak AR. Phase IB Study of Selinexor, a First-in-Class Inhibitor of Nuclear Export, in Patients With Advanced Refractory Bone or Soft Tissue Sarcoma. J Clin Oncol. 2016 Sep 10;34(26):3166-74. doi: 10.1200/JCO.2016.67.6346. Epub 2016 Jul 25.

    PMID: 27458288BACKGROUND

MeSH Terms

Conditions

Multiple Myeloma

Interventions

selinexorLenalidomideMethylprednisolone

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

PhthalimidesPhthalic AcidsAcids, CarbocyclicCarboxylic AcidsOrganic ChemicalsPiperidonesPiperidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIsoindolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingPrednisolonePregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Study Officials

  • James R Berenson, MD

    Oncotherapeutics

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Model Details: A pilot study examining selinexor's ability to overcome resistance in multiple myeloma patients who are refractory to lenalidomide-containing therapy.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 12, 2020

First Posted

August 19, 2020

Study Start

November 1, 2020

Primary Completion

December 29, 2023

Study Completion

December 29, 2023

Last Updated

October 31, 2023

Record last verified: 2023-10

Data Sharing

IPD Sharing
Will not share

We will share overall demographics of the study population, clinical responses, AEs and SAEs.

Locations