NCT04451772

Brief Summary

Systemic Lupus Erythematosus (SLE) is an immune-mediated disease associated with inflammation of multiple organ systems. This study will evaluate how well elsubrutinib and upadacitinib given alone or as the ABBV-599 combination (elsubrutinib/upadacitinib) works within the body, in participants who completed study M19-130. This study will assess the change in disease symptoms. ABBV-599 is an investigational drug being developed for the treatment of Systemic Lupus Erythematosus (SLE). This study is "double-blinded", which means that neither the trial participants nor the study doctors will know who will be given which study drug. Study doctors put the participants into 1 of 4 groups called treatment arms. Each group receives a different treatment. Adult participants with a diagnosis of SLE will be enrolled. Around 260 participants will be enrolled in the study in approximately 100 sites worldwide. Participants will receive the following for up to 56 weeks: Participants will receive oral elsubrutinib capsules and/or oral upadacitinib tablets once daily for up to 56 weeks. Participants who were receiving elsubrutinib and/or upadacitnib in M19-130 will continue to receive the same treatment in this study. Participants who were receiving placebo in M19-130 will be re-randomized to one of the 2 combination treatment arms in this study. Arm 1: Elsubrutinib Dose A and Upadacitinib Dose A Arm 2: Elsubrutinib Dose A and Upadacitinib Dose B There may be higher burden for participants in this trial compared to their standard of care. Participants will attend monthly visits during the course of the study at a hospital or clinic. The effect of the treatment will be checked by medical assessments, blood tests, checking for side effects and completing questionnaires.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
185

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jul 2020

Typical duration for phase_2

Geographic Reach
18 countries

87 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 29, 2020

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 30, 2020

Completed
27 days until next milestone

Study Start

First participant enrolled

July 27, 2020

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 3, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 3, 2024

Completed
1 year until next milestone

Results Posted

Study results publicly available

January 14, 2025

Completed
Last Updated

January 14, 2025

Status Verified

December 1, 2024

Enrollment Period

3.4 years

First QC Date

June 29, 2020

Results QC Date

December 19, 2024

Last Update Submit

December 19, 2024

Conditions

Keywords

Systemic Lupus ErythematosusABBV-599ABBV-105ABT-494ElsubrutinibUpadacitinib

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Treatment-Emergent Adverse Events

    An adverse event (AE) is defined as any untoward medical occurrence in a patient or clinical investigation participant administered a pharmaceutical product and which does not necessarily have a causal relationship with this treatment. A serious adverse event (SAE) is an event that results in death, is life-threatening, requires or prolongs hospitalization, results in a congenital anomaly, persistent or significant disability/incapacity or is an important medical event that, based on medical judgment, may jeopardize the participant and may require medical or surgical intervention to prevent any of the outcomes listed above. Treatment-emergent events (TEAEs) are defined as an adverse event with an onset date that is on or after the first dose of study drug from Study M20-186, and no more than 30 days after the last dose of study drug from Study M20-186. For more details on adverse events please see the Adverse Event section.

    From the first dose of study drug in Study M20-186 up to 30 days after the last dose of study drug, up to 442 days

Secondary Outcomes (4)

  • Percentage of Participants Achieving Systemic Lupus Erythematosus (SLE) Responder Index (SRI)-4

    Baseline of Study M19-130 (Week 0), Weeks 56, 64, 72, 80, 88, 96, 104

  • Percentage of Participants Achieving British Isles Lupus Assessment Group (BILAG)-Based Combined Lupus Assessment (BICLA) Response

    Baseline of Study M19-130 (Week 0), Weeks 56, 64, 72, 80, 88, 96, 104

  • Change From Baseline in Daily Prednisone Dose Over Time

    Baseline of M19-130 (Week 0), Weeks 56, 64, 72, 80, 88, 96, 104

  • Number of Flares Per Patient-year by Safety of Estrogens in Lupus Erythematosus National Assessment (SELENA) SLE Disease Activity Index (SLEDAI) Flare Index Through Week 104

    From Week 56 through Week 104

Study Arms (6)

ABBV-599 High Dose (Elsubrutinib 60 mg/upadacitinib 30 mg) -> ABBV-599 High Dose

EXPERIMENTAL

Participants received elsubrutinib 60 mg capsules once a day by mouth and upadacitinib 30 mg film-coated tablets once a day by mouth for 48 weeks in Study M19-130. Participants continued on this regimen in the current study (M20-186) for up to 56 weeks.

Drug: ElsubrutinibDrug: Upadacitinib

Elsubrutinib placebo/upadacitinib 30 mg -> Elsubrutinib placebo/upadacitinib 30 mg

EXPERIMENTAL

Participants received placebo capsules for elsubrutinib once a day by mouth and upadacitinib 30 mg film-coated tablets once a day by mouth for 48 weeks in Study M19-130. Participants continued on this regimen in the current study (M20-186) for up to 56 weeks.

Drug: Placebo for ElsubrutinibDrug: Upadacitinib

Elsubrutinib placebo/upadacitinib placebo -> ABBV-599 High Dose

EXPERIMENTAL

Participants received placebo capsules for elsubrutinib once a day by mouth and placebo film-coated tablets for upadacitinib once a day by mouth for 48 weeks in Study M19-130. Participants received elsubrutinib 60 mg capsules once a day by mouth and upadacitinib 30 mg film-coated tablets once a day in the current study (M20-186) for up to 56 weeks.

Drug: ElsubrutinibDrug: Upadacitinib

ABBV-599 Low Dose (Elsubrutinib 60 mg/upadacitinib 15 mg) -> ABBV-599 Low Dose

EXPERIMENTAL

Participants received elsubrutinib 60 mg capsules once a day by mouth and upadacitinib 15 mg film-coated tablets once a day by mouth for 48 weeks in Study M19-130. Participants continued on this regimen in the current study (M20-186) for up to 56 weeks.

Drug: ElsubrutinibDrug: Upadacitinib

Elsubrutinib 60 mg/upadacitinib placebo -> Elsubrutinib 60 mg/upadacitinib placebo

EXPERIMENTAL

Participants received elsubrutinib 60 mg capsules once a day by mouth and placebo film-coated tablets for upadacitinib once a day by mouth for 48 weeks in Study M19-130. Participants continued on this regimen in the current study (M20-186) for up to 56 weeks.

Drug: ElsubrutinibDrug: Placebo for Upadacitinib

Elsubrutinib placebo/upadacitinib placebo -> ABBV-599 Low Dose

EXPERIMENTAL

Participants received placebo capsules for elsubrutinib once a day by mouth and placebo film-coated tablets for upadacitinib once a day by mouth for 48 weeks in Study M19-130. Participants received elsubrutinib 60 mg capsules once a day by mouth and upadacitinib 15 mg film-coated tablets once a day by mouth for 48 weeks in the current study (M20-186) for up to 56 weeks.

Drug: ElsubrutinibDrug: Upadacitinib

Interventions

Capsule; Oral

Also known as: ABBV-105
ABBV-599 High Dose (Elsubrutinib 60 mg/upadacitinib 30 mg) -> ABBV-599 High DoseABBV-599 Low Dose (Elsubrutinib 60 mg/upadacitinib 15 mg) -> ABBV-599 Low DoseElsubrutinib 60 mg/upadacitinib placebo -> Elsubrutinib 60 mg/upadacitinib placeboElsubrutinib placebo/upadacitinib placebo -> ABBV-599 High DoseElsubrutinib placebo/upadacitinib placebo -> ABBV-599 Low Dose

Capsule; Oral

Elsubrutinib placebo/upadacitinib 30 mg -> Elsubrutinib placebo/upadacitinib 30 mg

Film-coated tablet; Oral

Also known as: ABT-494, RINVOQ
ABBV-599 High Dose (Elsubrutinib 60 mg/upadacitinib 30 mg) -> ABBV-599 High DoseABBV-599 Low Dose (Elsubrutinib 60 mg/upadacitinib 15 mg) -> ABBV-599 Low DoseElsubrutinib placebo/upadacitinib 30 mg -> Elsubrutinib placebo/upadacitinib 30 mgElsubrutinib placebo/upadacitinib placebo -> ABBV-599 High DoseElsubrutinib placebo/upadacitinib placebo -> ABBV-599 Low Dose

Film-coated tablet; Oral

Elsubrutinib 60 mg/upadacitinib placebo -> Elsubrutinib 60 mg/upadacitinib placebo

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Completed Study M19-130 (i.e., the randomized controlled trial of elsubrutinib, upadacitinib, and ABBV-599 \[elsubrutinib/upadacitinib\] combination or matching placebo) and will not have developed any laboratory or clinical discontinuation criteria as defined in that study.
  • On stable background treatment for SLE throughout the study.

You may not qualify if:

  • Active, chronic, or recurrent viral, or bacterial infection.
  • Active tuberculosis (TB)
  • History of gastrointestinal (GI) perforation, diverticulitis, or a significantly increased risk for GI perforation per investigator assessment.
  • Participant require vaccination with live vaccine during study participation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (87)

Duplicate_AZ Arthritis and Rheumotology Research, PLLC /ID# 227833

Phoenix, Arizona, 85032-9306, United States

Location

Wallace Rheumatic Studies Center, LLC /ID# 224374

Beverly Hills, California, 90211, United States

Location

Valerius Medical Group & Research Center /ID# 223922

Los Alamitos, California, 90720-5402, United States

Location

East Bay Rheumatology Medical /ID# 225493

San Leandro, California, 94578, United States

Location

University of Colorado Hospital /ID# 245087

Aurora, Colorado, 80045, United States

Location

Duplicate_Arthritis & Rheumatic Disease Specialties /ID# 227828

Aventura, Florida, 33180, United States

Location

Millennium Research /ID# 233192

Ormond Beach, Florida, 32174, United States

Location

IRIS Research and Development, LLC /ID# 227814

Plantation, Florida, 33324, United States

Location

Deerbrook Medical Associates /ID# 227330

Libertyville, Illinois, 60048, United States

Location

Qualmedica Research, LLC /ID# 227817

Evansville, Indiana, 47714-0805, United States

Location

The Center for Rheumatology and Bone Research /ID# 225479

Wheaton, Maryland, 20902, United States

Location

Beth Israel Deaconess Medical Center /ID# 222505

Boston, Massachusetts, 02215-5400, United States

Location

June DO, PC /ID# 221841

Lansing, Michigan, 48911, United States

Location

Duplicate_NYU Langone Health/NYU School of Medicine /ID# 245088

New York, New York, 10016-2772, United States

Location

STAT Research, Inc. /ID# 221840

Vandalia, Ohio, 45377-9464, United States

Location

Allegheny Health Network Research Institute /ID# 245086

Pittsburgh, Pennsylvania, 15224, United States

Location

Dr. Ramesh Gupta /ID# 225524

Memphis, Tennessee, 38119, United States

Location

Tekton Research, Inc. /ID# 224411

Austin, Texas, 78745, United States

Location

Accurate Clinical Management /ID# 225509

Houston, Texas, 77084, United States

Location

SW Rheumatology Res. LLC /ID# 225485

Mesquite, Texas, 75150, United States

Location

Carilion Clinic /ID# 227832

Roanoke, Virginia, 24016, United States

Location

Hospital Militar Central Cirujano Mayor Dr. Cosme Argerich /ID# 222569

Ciudad Autonoma Buenos Aires, Buenos Aires, 1426, Argentina

Location

Hospital Interzonal General de Agudos General Jose de San Martin /ID# 221893

La Plata, Buenos Aires, 1900, Argentina

Location

CER Instituto Medico /ID# 223175

Quilmes, Buenos Aires, 1878, Argentina

Location

Aprillus Asistencia e Investigacion /ID# 221890

Ciudad Autonoma de Buenos Aire, Buenos Aires F.D., 1958, Argentina

Location

Instituto CAICI S.R.L /ID# 221892

Rosario, Santa Fe Province, 2000, Argentina

Location

Centro de Investigaciones Medicas Tucuman /ID# 221888

San Miguel de Tucumán, Tucumán Province, 4000, Argentina

Location

Investigaciones Clinicas Tucuman /ID# 221889

San Miguel de Tucumán, Tucumán Province, 4000, Argentina

Location

Rheumatology Research Unit Sunshine Coast /ID# 221816

Maroochydore, Queensland, 4558, Australia

Location

Emeritus Research /ID# 223027

Camberwell, Victoria, 3124, Australia

Location

Monash Medical Centre /ID# 221814

Clayton, Victoria, 3168, Australia

Location

UMHAT Sveti Ivan Rilski /ID# 223358

Sofia, 1431, Bulgaria

Location

UMHAT Sveti Ivan Rilski /ID# 223359

Sofia, 1431, Bulgaria

Location

Duplicate_Peking Union Medical College Hospital /ID# 222950

Beijing, Beijing Municipality, 100730, China

Location

Guangdong Provincial People's Hospital /ID# 222851

Guangzhou, Guangdong, 510080, China

Location

People's Hospital of Xinjiang /ID# 222928

Urumqi, Guizhou, 830001, China

Location

Huashan Hospital, Fudan University /ID# 222929

Shanghai, Shanghai Municipality, 200040, China

Location

Duplicate_Centro Integral de Reumatologia del Caribe Circaribe SAS /ID# 221879

Barranquilla, Atlántico, 80002, Colombia

Location

Duplicate_Centro de Investigacion en Reumatologia y Especialidades Medicas- CIRE /ID# 221884

Bogota, Cundinamarca, 110221, Colombia

Location

Preventive Care Sas /Id# 221881

Chía, Cundinamarca, 250001, Colombia

Location

Healthy Medical Center S.A.S /ID# 221882

Zipaquirá, Cundinamarca, 250252, Colombia

Location

Clinica Universitaria Bolivari /ID# 221880

Medellin, Valle del Cauca Department, 050034, Colombia

Location

Duplicate_Charite Universitaetsmedizin Berlin - Campus Mitte /ID# 222963

Berlin, 10117, Germany

Location

Universitaetsklinikum Carl Gustav Carus an der TU Dresden /ID# 222964

Dresden, 01307, Germany

Location

Duplicate_Debreceni Egyetem Klinikai Kozpont /ID# 222480

Debrecen, Hajdú-Bihar, 4032, Hungary

Location

Vital Medicina Kft /ID# 222479

Veszprém, Veszprém megye, 8200, Hungary

Location

Duplicate_Azienda Ospedaliero-Universitaria di Ferrara-Arcispedale Sant Anna /ID# 221919

Cona, Ferrara, 44124, Italy

Location

Chukyo Hospital /ID# 223398

Nagoya, Aichi-ken, 457-8510, Japan

Location

NHO Nagoya Medical Center /ID# 222397

Nagoya, Aichi-ken, 460-0001, Japan

Location

Hospital of the University of Occupational and Environmental Health, Japan /ID# 222499

Kitakyushu-shi, Fukuoka, 807-8556, Japan

Location

Hiroshima Red Cross Hospital & Atomic-bomb Survivors Hospital /ID# 222393

Hiroshima, Hiroshima, 730-8619, Japan

Location

National Hospital Organization Asahikawa Medical Center /ID# 222394

Asahikawa-shi, Hokkaido, 070-8644, Japan

Location

EIRAKU Internal Medicine Clinic /ID# 222385

Kagoshima, Kagoshima-ken, 890-0063, Japan

Location

Tohoku University Hospital /ID# 222392

Sendai, Miyagi, 9808574, Japan

Location

Shinshu University Hospital /ID# 222395

Matsumoto-shi, Nagano, 390-8621, Japan

Location

Saitama Medical Center /ID# 222389

Kawagoe-shi, Saitama, 350-8550, Japan

Location

Keio University Hospital /ID# 222498

Shinjuku-ku, Tokyo, 160-8582, Japan

Location

Morales Vargas Centro de Investigacion S.C. /ID# 221912

León, Guanajuato, 37000, Mexico

Location

Centro Integral en Reumatologia S.A de C.V /ID# 221914

Guadalajara, Jalisco, 44160, Mexico

Location

Centro de Estudios de Investigación Básica y Clínica, S.C. /ID# 221910

Guadalajara, Jalisco, 44690, Mexico

Location

RM Pharma Specialists S.A de C.V. /ID# 221915

Mexico City, Mexico City, 03100, Mexico

Location

CINTRE, Centro de Investigación y Tratamiento Reumatológico SC /ID# 221913

Mexico City, Mexico City, 11850, Mexico

Location

Medical Care & Research SA de CV /ID# 221911

Mérida, Yucatán, 97070, Mexico

Location

North Shore Hospital /ID# 221850

Takapuna, Auckland, 0622, New Zealand

Location

Ortopedyczno-Rehabilitacyjny Szpital Kliniczny im. Wiktora Degi /ID# 221859

Poznan, Greater Poland Voivodeship, 61-545, Poland

Location

Centrum Nowoczesnych Terapii Dobry Lekarz Sp. z o.o. /ID# 224430

Krakow, Lesser Poland Voivodeship, 31-011, Poland

Location

WroMedica I. Bielicka, A. Strzalkowska s.c. /ID# 221860

Wroclaw, Lower Silesian Voivodeship, 51-685, Poland

Location

MTZ Clinical Research Powered by Pratia /ID# 224431

Warsaw, Masovian Voivodeship, 02-172, Poland

Location

GCM Medical Group PSC /ID# 224394

San Juan, 00917-3104, Puerto Rico

Location

Mindful Medical Research /ID# 222513

San Juan, 00918-3756, Puerto Rico

Location

Seoul National University Hospital /ID# 221897

Seoul, Seoul Teugbyeolsi, 03080, South Korea

Location

HUA - Txagorritxu /ID# 221992

Vitoria-Gasteiz, Alava, 01009, Spain

Location

Consorci Corporacio Sanitaria Parc Tauli Sabadell /ID# 221995

Sabadell, Barcelona, 08208, Spain

Location

Hospital Universitario Basurto /ID# 221999

Bilbao, Vizcaya, 48013, Spain

Location

Hospital Universitario de Galdakao /ID# 221996

Galdakao, Vizcaya, 48960, Spain

Location

Duplicate_Hospital Universitario A Coruna - CHUAC /ID# 221993

A Coruña, 15006, Spain

Location

Hospital Universitario 12 de Octubre /ID# 221994

Madrid, 28041, Spain

Location

Hospital Universitario Virgen de Valme /ID# 221997

Seville, 41014, Spain

Location

Hospital Universitario y Politecnico La Fe /ID# 221998

Valencia, 46026, Spain

Location

Taichung Veterans General Hospital /ID# 221748

Taichung, Keelung, 40705, Taiwan

Location

Taipei Veterans General Hosp /ID# 221746

Taipei, Keelung, 11217, Taiwan

Location

National Taiwan University Hospital /ID# 221745

Taipei City, Taipei, 100, Taiwan

Location

China Medical University Hospital /ID# 221747

Taichung, 40447, Taiwan

Location

Taipei Medical University Hospital /ID# 227653

Taipei, 11031, Taiwan

Location

Linkou Chang Gung Memorial Hospital /ID# 222469

Taoyuan, 333, Taiwan

Location

Guys and St Thomas NHS Foundation Trust /ID# 221863

London, London, City of, SE1 9RT, United Kingdom

Location

Duplicate_Manchester University NHS Foundation Trust /ID# 221861

Manchester, M13 9WL, United Kingdom

Location

MeSH Terms

Conditions

Lupus Erythematosus, Systemic

Interventions

upadacitinib

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Global Medical Services
Organization
AbbVie

Study Officials

  • ABBVIE INC.

    AbbVie

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 29, 2020

First Posted

June 30, 2020

Study Start

July 27, 2020

Primary Completion

January 3, 2024

Study Completion

January 3, 2024

Last Updated

January 14, 2025

Results First Posted

January 14, 2025

Record last verified: 2024-12

Data Sharing

IPD Sharing
Will share

AbbVie is committed to responsible data sharing regarding the clinical trials we sponsor. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information (e.g., protocols, analyses plans, clinical study reports), as long as the trials are not part of an ongoing or planned regulatory submission. This includes requests for clinical trial data for unlicensed products and indications.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
For details on when studies are available for sharing visit https://vivli.org/ourmember/abbvie/
Access Criteria
Access to this clinical trial data can be requested by any qualified researchers who engage in rigorous independent scientific research, and will be provided following review and approval of a research proposal and statistical analysis plan and execution of a data sharing statement. Data requests can be submitted at any time after approval in the US and/or EU and a primary manuscript is accepted for publication. For more information on the process, or to submit a request, visit the following link https://www.abbvieclinicaltrials.com/hcp/data-sharing/
More information

Locations