NCT04322539

Brief Summary

This is a global, randomized, double-blind, placebo-controlled, multicenter phase 3 clinical trial to compare the efficacy and safety of fruquintinib plus best supportive care (BSC) versus placebo plus BSC in participants with refractory metastatic colorectal cancer (mCRC). 691 participants were randomized to one of the following treatment arms in a 2:1 ratio, fruquintinib plus BSC or placebo plus BSC.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
691

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Aug 2020

Typical duration for phase_3

Geographic Reach
12 countries

144 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 24, 2020

Completed
2 days until next milestone

First Posted

Study publicly available on registry

March 26, 2020

Completed
5 months until next milestone

Study Start

First participant enrolled

August 12, 2020

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 29, 2022

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

September 14, 2023

Completed
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 24, 2024

Completed
Last Updated

April 4, 2025

Status Verified

March 1, 2025

Enrollment Period

2 years

First QC Date

March 24, 2020

Results QC Date

July 28, 2023

Last Update Submit

March 17, 2025

Conditions

Keywords

coloncolorectalmcrccrcmetastatic colonmetastatic colorectalVEGFVEGFR

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS)

    OS was defined as the time (months) from date of randomization to death from any cause. OS was calculated as (date of death or last known alive - date of randomization + 1)/30.4375. Participants without report of death at the time of analysis will be censored at the date last known alive.

    From date of randomization to death from any cause (up to 22 months)

Secondary Outcomes (15)

  • Progression Free Survival (PFS), as Assessed by the Investigator Using Response Evaluation Criteria In Solid Tumors (RECIST) v1.1

    From randomization until the first documentation of objective progression or death, whichever comes first (up to 22 months)

  • Objective Response Rate (ORR) Per Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1)

    From randomization until the first documentation of best overall response (up to 22 months)

  • Disease Control Rate (DCR) Per Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1)

    From randomization until the first documentation of best overall response (up to 22 months)

  • Duration of Response (DOR) Per Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1)

    From first occurrence of PR or CR until the first documentation progression or death, whichever comes first (up to 22 months

  • Number of Participants With Treatment-emergent Adverse Events (TEAEs) and Serious TEAEs

    From start of study drug administration up to approximately 40 months

  • +10 more secondary outcomes

Study Arms (2)

Fruquintinib Plus Best Supportive Care (BSC) Group

EXPERIMENTAL

Participants will be orally administered Fruquintinib 5 mg in combination with BSC once daily for 3 weeks of continuous dosing followed by a 1-week break (with each cycle length of 28 days).

Drug: Fruquintinib

Placebo Plus BSC Group

PLACEBO COMPARATOR

Participants will be orally administered Placebo 5 mg in combination with BSC once daily for 3 weeks of continuous dosing followed by a 1-week break (with each cycle length of 28 days).

Drug: Placebo

Interventions

Oral VEGFR inhibitor

Also known as: HMPL-013
Fruquintinib Plus Best Supportive Care (BSC) Group

Placebo capsule

Placebo Plus BSC Group

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Provide written informed consent;
  • Age ≥18 years;
  • Histologically and/or cytologically documented metastatic colorectal adenocarcinoma. RAS, BRAF, and microsatellite instability microsatellite instability (MSI)/mismatch repair (MMR) status for each patient must be documented, according to country level guidelines;
  • Participants must have progressed on or been intolerant to treatment with either trifluridine/tipiracil (TAS-102) or regorafenib. Participants are considered intolerant to TAS-102 or regorafenib if they have received at least 1 dose of either agents and were discontinued from therapy for reasons other than disease progression. Participants who have been treated with both TAS-102 and regorafenib are permitted. Participants must also have been previously treated with standard approved therapies: fluoropyrimidine-, oxaliplatin-, and irinotecan-based chemotherapy, an anti-VEGF biological therapy, and, if RAS wild-type, an anti-EGFR therapy;
  • Participants with microsatellite-high (MSI-H) or mismatch repair deficient (dMMR) tumors must have been treated with immune checkpoint inhibitors if approved and available in the participant's country unless the patient is ineligible for treatment with a checkpoint inhibitor;
  • Participants who received oxaliplatin in the adjuvant setting and developed metastatic disease during or within 6 months of completing adjuvant therapy are considered eligible without receiving oxaliplatin in the metastatic setting. Participants who developed metastatic disease more than 6 months after completion of oxaliplatin-containing adjuvant treatment must be treated with oxaliplatin-based therapy in the metastatic setting to be eligible;
  • Body weight ≥40kg;
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0-1;
  • Have measurable disease according to RECIST Version 1.1, assessed locally. Tumors that were treated with radiotherapy are not measurable per RECIST Version 1.1, unless there has been documented progression of those lesions;
  • Expected survival \>12 weeks.
  • For female participants of childbearing potential and male participants with partners of childbearing potential, agreement to use a highly effective form(s) of contraception, that results in a low failure rate (\<1% per year) when used consistently and correctly, starting during the screening period, continuing throughout the entire study period, and for 90 days after taking the last dose of study drug. Such methods include: oral hormonal contraception (combined estrogen/ progestogen, or progestogen-only) associated with inhibition of ovulation, intrauterine device (IUD), intrauterine hormone-releasing system (IUS), bilateral tubal ligation, vasectomized partner, or true sexual abstinence in line with the preferred and usual lifestyle of the participant. Highly effective contraception should always be combined with an additional barrier method (eg, diaphragm, with spermicide). The same criteria are applicable to male participants involved in this clinical trial if they have a partner of childbirth potential, and male participants must always use a condom.
  • Participants with BRAF-mutant tumors must have been treated with a BRAF inhibitor if approved and available in the participant's home country unless the patient is ineligible for treatment with a BRAF inhibitor.

You may not qualify if:

  • Absolute neutrophil count (ANC) \<1.5×109/L, platelet count \<100×109/L, or hemoglobin \<9.0 g/dL. Blood transfusion within 1 week prior to enrollment for the purpose of increasing the likelihood of eligibility is not allowed;
  • Serum total bilirubin \>1.5 × the upper limit of normal (ULN). Participants with Gilbert syndrome, bilirubin \<2 X ULN, and normal AST/ALT are eligible;
  • Alanine aminotransferase (ALT) or aspartate aminotransferase (AST) \>2.5 × ULN in participants without hepatic metastases; ALT or AST \>5 × ULN in participants with hepatic metastases;
  • Serum creatinine \>1.5 × ULN or creatinine clearance \<60 mL/min. Creatinine clearance can either be measured in a 24-hour urine collection or estimated by the Cockroft-Gault equation.
  • Urine dipstick protein ≥2+ or 24-hour urine protein ≥1.0 g/24-h. Participants with greater than 2+ proteinuria by dipstick must undergo a 24-hour urine collection to assess urine protein level;
  • Uncontrolled hypertension, defined as: systolic blood pressure ≥140 mm Hg and/or diastolic blood pressure ≥90 mm Hg despite optimal medical management. Participants were required to have blood pressure values below both limits. Repeated assessments were permitted;
  • International Normalized Ratio (INR) \>1.5 x ULN or activated partial thromboplastin time (aPTT) \>1.5 × ULN, unless the patient is currently receiving or intended to receive anticoagulants for prophylactic purposes;
  • History of, or active gastric/duodenal ulcer or ulcerative colitis, active hemorrhage of an unresected gastrointestinal tumor, history of perforation or fistulas; or any other condition that could, in the investigator's judgment, result in gastrointestinal hemorrhage or perforation; within the 6 months prior to screening;
  • History or presence of hemorrhage from any other site (eg, hemoptysis or hematemesis) within 2 months prior to screening;
  • History of a thromboembolic event, including deep vein thrombosis (DVT), pulmonary embolism (PE), or arterial embolism within 6 months prior to screening.
  • Stroke and/or transient ischemic attack within 12 months prior to screening;
  • Clinically significant cardiovascular disease, including but not limited to acute myocardial infarction or coronary artery bypass surgery within 6 months prior to enrollment, severe or unstable angina pectoris, New York Heart Association Class III/IV congestive heart failure, ventricular arrhythmias requiring treatment, or left ventricular ejection fraction (LVEF) \<50% by echocardiogram;
  • Mean corrected QT interval using the Fridericia method (QTcF) \>480 msec or any factors that increase the risk of QTc prolongation or risk of arrhythmic events such as hypokalemia, congenital long QT syndrome, family history of long QT syndrome, or unexplained sudden death under 40 years of age in a first-degree relative.
  • Concomitant medications with a known risk of causing QT prolongation and/or Torsades de Pointes.
  • Systemic small molecule targeted therapies (eg, tyrosine kinase inhibitors) within 5 half-lives or 4 weeks (whichever is shorter) prior to the first dose of study drug;
  • +17 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (153)

Mayo Clinic Arizona

Phoenix, Arizona, 85054, United States

Location

Arizona Oncology Associates, PC-HOPE

Tucson, Arizona, 85704, United States

Location

California Research Institute (CRI)

Los Angeles, California, 90027, United States

Location

City of Hope Comprehensive Cancer Center

Los Angeles, California, 91010, United States

Location

Rocky Mountain Cancer Center

Aurora, Colorado, 80012, United States

Location

The George Washington University Medical Center

Washington D.C., District of Columbia, 20052, United States

Location

Sarah Cannon Research Institute-S-Ft. Myers (FCS South)

Fort Myers, Florida, 33901, United States

Location

Mayo Clinic Florida

Jacksonville, Florida, 32224, United States

Location

Mount Sinai Medical Center

Miami Beach, Florida, 33140, United States

Location

Cancer Care Centers of Brevard, Inc.

Palm Bay, Florida, 32901, United States

Location

Sarah Cannon Research Institute-N-St Pete (FCS North)

St. Petersburg, Florida, 33705, United States

Location

Sarah Cannon Research Institute-Pan-Tallahassee (FCS Panhandle)

Tallahassee, Florida, 32308, United States

Location

Sarah Cannon Research-E-WPB (Florida Cancer Specialists-FCS East)

West Palm Beach, Florida, 33401, United States

Location

Emory Winship Cancer Institute

Atlanta, Georgia, 30322, United States

Location

Illinois Cancer Specialists

Arlington Heights, Illinois, 60005, United States

Location

University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Affiliated Oncologists

Chicago Ridge, Illinois, 60415, United States

Location

XCancer / Central Care Cancer Center

Garden City, Kansas, 67846, United States

Location

University of Louisville - James Brown Cancer Center

Louisville, Kentucky, 40202, United States

Location

Norton Cancer Institute Audubon

Louisville, Kentucky, 40217, United States

Location

Hematology Oncology Clinic

Baton Rouge, Louisiana, 70809, United States

Location

XCancer / Pontchartrain Cancer Center

Hammond, Louisiana, 70403, United States

Location

Maryland Oncology Hematology, P.A.

Columbia, Maryland, 21044, United States

Location

University of Michigan Health System

Ann Arbor, Michigan, 48109, United States

Location

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Minnesota Oncology

Minneapolis, Minnesota, 55404, United States

Location

Mayo Clinic Rochester

Rochester, Minnesota, 55905, United States

Location

Center for Pharmaceutical Research

Kansas City, Missouri, 64114, United States

Location

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89169, United States

Location

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08901, United States

Location

XCancer / New Mexico Oncology & Hematology Consultants

Albuquerque, New Mexico, 87109, United States

Location

Charleston Oncology

Charleston, South Carolina, 29414, United States

Location

Sarah Cannon Tennessee Oncology

Nashville, Tennessee, 37203, United States

Location

Vanderbilt Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

Texas Oncology - Austin

Austin, Texas, 78705, United States

Location

Texas Oncology Baylor Sammons

Dallas, Texas, 75246, United States

Location

Texas Oncology-El Paso

El Paso, Texas, 79902, United States

Location

MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Texas Oncology-McAllen

McAllen, Texas, 78503, United States

Location

Texas Oncology-San Antonio

San Antonio, Texas, 78217, United States

Location

Texas Oncology-Tyler

Tyler, Texas, 75702, United States

Location

Virginia Oncology Associates

Norfolk, Virginia, 23502, United States

Location

Providence Regional Cancer Partnership

Everett, Washington, 98201, United States

Location

Northwest Cancer Specialists, P.C.

Vancouver, Washington, 98684, United States

Location

Medical College of Wisconsin/ Froedtert Hospital

Milwaukee, Wisconsin, 53226, United States

Location

Integrated Clinical Oncology Network Pty Ltd (Icon)

Brisbane, Queensland, 4001, Australia

Location

The Queen Elizabeth Hospital

Adelaide, South Australia, 5011, Australia

Location

Flinders Medical Centre

Adelaide, South Australia, 5042, Australia

Location

Western Health

Melbourne, Victoria, 3021, Australia

Location

Austin Hopistal Medical Oncology Unit

Melbourne, Victoria, 3084, Australia

Location

Monash Health

Melbourne, Victoria, 3168, Australia

Location

Ordensklinikum Linz Barmherzige Schwestern

Linz, AUT, 4010, Austria

Location

Schwerpunktkrankenhaus Feldkirch

Rankweil, AUT, 6830, Austria

Location

Klinikum Steyr

Steyr, AUT, 4400, Austria

Location

Wiener Gesundheitsverbund - Klinik Ottakring

Vienna, AUT, 1160, Austria

Location

Klinikum Wels-Grieskirchen GmbH

Wels, AUT, 4600, Austria

Location

Landesklinikum Wiener Neustadt

Wiener Neustadt, AUT, 2700, Austria

Location

Onze-Lieve-Vrouwziekenhuis OLV - Campus Aalst

Aalst, BEL, 9300, Belgium

Location

UCL St-Luc

Brussels, BEL, 1200, Belgium

Location

Grand Hopital de Charleroi

Charleroi, BEL, 6000, Belgium

Location

UZ Antwerpen

Edegem, BEL, 2650, Belgium

Location

Centres Hospitaliers Jolimont

Haine-Saint-Paul, BEL, 7100, Belgium

Location

UZ Leuven

Leuven, BEL, 3000, Belgium

Location

AZ Delta Roeselare

Roeselare, BEL, 8800, Belgium

Location

AZ Turnhout

Turnhout, BEL, 2300, Belgium

Location

CHU Mont-Godinne

Yvoir, BEL, 5530, Belgium

Location

Clinique CHC MontLegia

Liège, Wallonia, 4000, Belgium

Location

CHU de Lige - Domaine Universitaire du Sart Tilman

Liège, Wallonia, 4001, Belgium

Location

Masaryk Memorial Cancer Institute, Hematoonkologie

Brno, Moravia, 60200, Czechia

Location

Fakultni nemocnice Olomouc, Onkologicka klinika

Olomouc, Moravia, 77900, Czechia

Location

Vseobecna Fakultni Nemocnice VFN, Onkologicka Klinika

Prague, 12808, Czechia

Location

East Tallinn Central Hospital Centre of Oncology

Tallinn, Harju, 11312, Estonia

Location

Sihtasutus Pohja-Eesti Regionaalhaigla (PERH) (North Estonia Medical Centre)

Tallinn, Harju, 13419, Estonia

Location

Tartu University Hospital Clinic of Haematology and Oncology

Tartu, 50406, Estonia

Location

CHU Besancon

Besançon, Franche-Comte, 25000, France

Location

Institut Bergonie

Bordeaux, FRA, 33000, France

Location

Unicancer

Caen, FRA, 14000, France

Location

Centre Georges-Francois Leclerc

Dijon, FRA, 21000, France

Location

ICM-Val d'Aurelle

Montpellier, FRA, 34298, France

Location

Saint-Louis Hospital

Paris, FRA, 75010, France

Location

Hopital St Antoine

Paris, FRA, 75012, France

Location

Hopital Pitie Salptriere

Paris, FRA, 75013, France

Location

CHU Poitiers

Poitiers, FRA, 86000, France

Location

Centre hospitalier Annecy Genevois

Pringy, FRA, 74370, France

Location

Centre Hospitalier Universitaire CHU de Rennes - Hopital de Pontchaillou

Rennes, FRA, 35033, France

Location

Institut de cancerologie Strasbourg-Europe

Strasbourg, FRA, 67033, France

Location

Institut Gustave Roussy

Villejuif, Paris, 94805, France

Location

Universitaetsklinikum Erlangen

Erlangen, Bavaria, 91054, Germany

Location

HELIOS Klinikum Berlin-Buch Saarow

Berlin, DEU, 13125, Germany

Location

Charite - Universitaetsmedizin Berlin

Berlin, DEU, 13353, Germany

Location

Universitaetsklinik Dresden

Dresden, DEU, 1307, Germany

Location

University Hospital Essen

Essen, DEU, 45147, Germany

Location

Institut fr Klinisch Onkologische ForschungKrankenhaus Nordwest GmbH

Frankfurt am Main, DEU, 60488, Germany

Location

Haematologisch-Onkologische Praxis Hamburg Eppendorf

Hamburg, DEU, 20249, Germany

Location

Asklepios Tumorzentrum Hamburg AK Altona

Hamburg, DEU, 22763, Germany

Location

Universitaeres Krebszentrum Leipzig

Leipzig, DEU, 4103, Germany

Location

RKH Kliniken

Ludwigsburg, DEU, 22763, Germany

Location

Universitaetsmedizin Mannheim- III. Medizinische Klinik

Mannheim, DEU, 68167, Germany

Location

Klinikum Neuperlach

München, DEU, 81737, Germany

Location

Zentrum für Hämatologie und Onkologie MVZ GmbH

Porta Westfalica, DEU, 32457, Germany

Location

Del-Pesti Centrumkorhaz Orszagos Hematologiai es Infektologiai Intezet, Szent Laszlo Korhaz

Budapest, HUN, 1097, Hungary

Location

National Institute of Oncology

Budapest, HUN, 1122, Hungary

Location

Magyar Honvedseg Egeszsegugyi Kozpont

Budapest, HUN, H-1062, Hungary

Location

Debreceni Egyetem Klinikai Kozpont

Debrecen, HUN, 4032, Hungary

Location

Bacs- Kiskun Megyei Korhaz

Kecskemét, HUN, 6000, Hungary

Location

Szabolcs-Szatmar-Bereg megyei Korhazak es Egyetemi Oktatokorhaz

Nyíregyháza, HUN, 4400, Hungary

Location

Hetenyi G Korhaz, Onkologiai Kozpont

Szolnok, HUN, 5004, Hungary

Location

Szent Borbala Korhaz

Tatabánya, HUN, 2800, Hungary

Location

Somogy Megyei Kaposi Mor Oktato Korhaz, Klinikai Onkologiai Osztaly

Kaposvár, Somogy County, 7400, Hungary

Location

Zala Megyei Szent Rafael Korhaz, Onkologiai Osztaly, F epulet 3. em.

Zalaegerszeg, Zala County, 8900, Hungary

Location

Bekes Megyei Kozponti Korhaz, Pandy Kalman Tagkorhaz, Megyei Onkologiai Kozpont

Gyula, 5700, Hungary

Location

Fondazione Poliambulanza Hospital

Brescia, ITA, 25124, Italy

Location

Policlinico San Martino di Genova

Genova, ITA, 16132, Italy

Location

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, ITA, 20133, Italy

Location

ASST Grande Ospedale Metropolitano Niguarda

Milan, ITA, 20162, Italy

Location

Istituto Nazionale Tumori IRCCS Fondazione G. Pascale

Naples, ITA, 80131, Italy

Location

Istituto Oncologico Veneto Irccs

Padua, ITA, 35128, Italy

Location

Azienda Ospedaliero Universitaria Pisana

Pisa, ITA, 56126, Italy

Location

Azienda USL-IRCCS di Reggio Emilia

Reggio Emilia, ITA, 42123, Italy

Location

AO Card G Panico

Tricase, ITA, 73039, Italy

Location

Ospedale San Bortolo Azienda ULSS8 Berica - Distretto Est

Vicenza, ITA, 36100, Italy

Location

Istituto Clinico Humanitas

Rozzano MI, Lombardy, 20089, Italy

Location

Aichi Cancer Center

Nagoya, Aichi-ken, 464-8681, Japan

Location

National Cancer Center Hospital East

Kashiwa-shi, Chiba, 277-8577, Japan

Location

Shikoku Cancer Center

Matsuyama, Ehime, 791-0280, Japan

Location

Kyushu Cancer Center

Fukuoka, Fukuoka, 811-1395, Japan

Location

Hokkaido University Hospital

Sapporo, Hokkaido, 060-8648, Japan

Location

St. Marianna University School of Medicine Hospital

Kawasaki-shi, Kanagawa, 216-8511, Japan

Location

Kindai University Hospital

Osakasayama-shi, Osaka, 589-8511, Japan

Location

Osaka University Hospital

Suita-shi, Osaka, 565-0871, Japan

Location

Shizuoka Cancer Center

Shizuoka, Sunto-gun, 411-8777, Japan

Location

National Cancer Center Hospital

Chuo-ku, Tokyo, 104-0045, Japan

Location

M Sklodowska Curie Memorial Cancer Center, Klinika Gastroenterologii Onkologicznej

Warsaw, Masovia, 02034, Poland

Location

Bialostockie Centrum Onkologii im. Marii Skodowskiej-Curie

Bialystok, Podlaskie Voivodeship, 15-027, Poland

Location

Hospital Universitari Vall dHebron

Barcelona, ESP, 8035, Spain

Location

Hospital Universitario Reina Sofa

Córdoba, ESP, 14004, Spain

Location

Hospital General Universitario de Elche

Elche, ESP, 3203, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, ESP, 28034, Spain

Location

Hospital Clinico San Carlos

Madrid, ESP, 28040, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, ESP, 28041, Spain

Location

Hospital Universitario La Paz

Madrid, ESP, 28046, Spain

Location

Hospital Universitario HM Sanchinarro

Madrid, ESP, 28050, Spain

Location

Hospital Universitario Puerta de Hierro

Majadahonda, ESP, 28222, Spain

Location

Hospital Regional Universitario Carlos Haya

Málaga, ESP, 29010, Spain

Location

Hospital Universitario Central de Asturias

Oviedo, ESP, 33013, Spain

Location

Hospital Universitario Marques de Valdecilla

Santander, ESP, 39008, Spain

Location

Hospital ClÃ-nico Universitario de Santiago-CHUS

Santiago de Compostela, ESP, 15706, Spain

Location

Hospital General Universitario Gregorio Maranon HGUGM

Madrid, 28007, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, 46010, Spain

Location

Aberdeen Royal Infirmary

Aberdeen, GBR, AB25 2ZN, United Kingdom

Location

The Royal Marsden Hospital

London, GBR, SW3 6JJ, United Kingdom

Location

Sarah Cannon Research Institute UK

London, Middlesex, W1G 6AD, United Kingdom

Location

Related Publications (4)

  • Kotani D, Yoshino T, Masuishi T, Sunakawa Y, Takashima A, Yamazaki K, Kawakami H, Nishina T, Komatsu Y, Esaki T, Eng C, Ukrainskyj S, Pallai R, Nanda S, Yang Z, Schelman W, Kania M, Satoh T. Efficacy and safety of fruquintinib in patients with refractory metastatic colorectal cancer: a FRESCO-2 subgroup analysis of patients enrolled in Japan. Int J Clin Oncol. 2025 Oct;30(10):2043-2052. doi: 10.1007/s10147-025-02852-9. Epub 2025 Sep 1.

  • Sobrero A, Dasari A, Aquino J, Lonardi S, Garcia-Carbonero R, Elez E, Yoshino T, Yao J, Garcia-Alfonso P, Kocsis J, Gracian AC, Sartore-Bianchi A, Satoh T, Randrian V, Tomasek J, Chong G, Price T, Yu Z, Geiger A, Chen L, Yang Z, Schelman WR, Kania M, Tabernero J, Eng C. Health-related quality of life associated with fruquintinib in patients with metastatic colorectal cancer: Results from the FRESCO-2 study. Eur J Cancer. 2025 Mar 11;218:115268. doi: 10.1016/j.ejca.2025.115268. Epub 2025 Jan 29.

  • Dasari A, Lonardi S, Garcia-Carbonero R, Elez E, Yoshino T, Sobrero A, Yao J, Garcia-Alfonso P, Kocsis J, Cubillo Gracian A, Sartore-Bianchi A, Satoh T, Randrian V, Tomasek J, Chong G, Paulson AS, Masuishi T, Jones J, Csoszi T, Cremolini C, Ghiringhelli F, Shergill A, Hochster HS, Krauss J, Bassam A, Ducreux M, Elme A, Faugeras L, Kasper S, Van Cutsem E, Arnold D, Nanda S, Yang Z, Schelman WR, Kania M, Tabernero J, Eng C; FRESCO-2 Study Investigators. Fruquintinib versus placebo in patients with refractory metastatic colorectal cancer (FRESCO-2): an international, multicentre, randomised, double-blind, phase 3 study. Lancet. 2023 Jul 1;402(10395):41-53. doi: 10.1016/S0140-6736(23)00772-9. Epub 2023 Jun 15.

  • Dasari A, Sobrero A, Yao J, Yoshino T, Schelman W, Yang Z, Chien C, Kania M, Tabernero J, Eng C. FRESCO-2: a global Phase III study investigating the efficacy and safety of fruquintinib in metastatic colorectal cancer. Future Oncol. 2021 Aug;17(24):3151-3162. doi: 10.2217/fon-2021-0202. Epub 2021 May 17.

MeSH Terms

Conditions

Colorectal NeoplasmsColonic Neoplasms

Interventions

HMPL-013

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Results Point of Contact

Title
William Schelman, MD, PhD
Organization
HUTCHMED International

Study Officials

  • William Schelman, MD, PhD

    HUTCHMED International Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 24, 2020

First Posted

March 26, 2020

Study Start

August 12, 2020

Primary Completion

July 29, 2022

Study Completion

April 24, 2024

Last Updated

April 4, 2025

Results First Posted

September 14, 2023

Record last verified: 2025-03

Data Sharing

IPD Sharing
Will not share

Locations