NCT04273945

Brief Summary

The purpose of this study is to demonstrate superiority of macitentan 75 milligrams (mg) in prolonging the time to the first clinical events committee (CEC)-adjudicated morbidity or mortality (M/M) event in participants with symptomatic pulmonary arterial hypertension (PAH) compared to macitentan 10 mg.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
935

participants targeted

Target at P75+ for phase_3

Timeline
34mo left

Started Jun 2020

Longer than P75 for phase_3

Geographic Reach
39 countries

263 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress68%
Jun 2020Feb 2029

First Submitted

Initial submission to the registry

January 31, 2020

Completed
18 days until next milestone

First Posted

Study publicly available on registry

February 18, 2020

Completed
4 months until next milestone

Study Start

First participant enrolled

June 30, 2020

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 7, 2025

Completed
3.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

February 20, 2029

Expected
Last Updated

April 13, 2026

Status Verified

April 1, 2026

Enrollment Period

5.3 years

First QC Date

January 31, 2020

Last Update Submit

April 9, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Double-blind Treatment Period: Time to First Clinical Events Committee (CEC)-adjudicated Morbidity or Mortality (M/M) Events

    Time to first CEC-adjudicated M/M event on-treatment (ie.,up to 7 days after last dose of DB study intervention) is defined as time from randomization to first of following events: All-cause death, including death caused by on-treatment adverse event that occur within 4 weeks of study DB treatment discontinuation;non-planned Pulmonary Arterial Hypertension(PAH)-related hospitalization(including for worsening of PAH, atrial septostomy, lung transplantation with or without heart transplantation, or initiation of parenteral prostacyclins);PAH-related disease progression, defined as worsening of World Health Organization(WHO) Functional Class(FC) from baseline or deterioration by at least 15% in exercise capacity, as measured by 6-minute walk distance(6MWD), from baseline and confirmed by second 6MWD test performed on different day within 2 week of initial test or appearance or worsening of signs or symptoms of right-sided heart failure that require initiation of intravenous diuretics.

    Up to 4 years

Secondary Outcomes (6)

  • Double-blind Treatment Period: Change From Baseline to Week 24 in 6MWD

    Baseline up to Week 24

  • Double-blind Treatment Period: Number of Participants with CEC-adjudicated Death due to PAH and/or Hospitalizations for PAH (First and Recurrent) Events on-treatment

    Up to 4 years

  • Double-blind Treatment Period: Change From Baseline to Week 24 in PAH Symptoms Based on PAH-SYMPACT Questionnaire- Cardiopulmonary Symptom Domain Score

    Baseline up to Week 24

  • Double-blind Treatment Period: Change From Baseline to Week 24 in PAH Symptoms Based on PAH-SYMPACT Questionnaire- Cardiovascular Symptom Domain Score

    Baseline up to Week 24

  • Double-blind Treatment Period: Time to Death Occurring Between Randomization and End of Double-blind Treatment (EDBT)

    Up to 4 years

  • +1 more secondary outcomes

Study Arms (2)

Macitentan 10 milligrams (mg) + Placebo

ACTIVE COMPARATOR

Run-in period:Participants who are either endothelin receptor antagonist (ERA)-naïve or who are receiving daily dose of macitentan or ambrisentan less (\<) 10 milligrams (mg), or daily dose of bosentan \<250 mg, will enter 4-week open-label run-in period with macitentan 10 mg prior to randomization. ERA-pre-treated participants will bypass run-in period and will be randomized to either macitentan 75 mg or macitentan 10 mg directly.Double-blind Treatment (DBT) Period:Participants will receive macitentan 10 mg orally up to End of DBT.To maintain blind, participants will receive macitentan 37.5 mg-matching placebo for 4 weeks and macitentan 75 mg-matching placebo thereafter up to DBT.Treatment Extension Period:After EDBT, participants will receive macitentan 37.5 mg once a day (qd) orally for 4 weeks, prior to receiving open-label macitentan 75 mg qd orally for 2 years. To maintain blind, participants will receive macitentan 75 mg-matching placebo during 4-week uptitration.

Drug: Macitentan 10 mgDrug: Macitentan 37.5 mgDrug: Macitentan 75 mgDrug: Placebo

Macitentan 75 mg + Placebo

EXPERIMENTAL

Run-in period:Participants who are either ERA-naive or who are receiving a daily dose of macitentan or ambrisentan \<10 mg, or a daily dose of bosentan \<250 mg, will enter 4-week open-label run-in period with macitentan 10 mg prior to randomization. ERA-pre-treated patients will bypass the run-in period and will be randomized to either macitentan 75 mg or macitentan 10 mg directly.DBT Period: participants will receive macitentan 37.5 mg orally for 4 weeks and macitentan 75 mg thereafter up to End of DBT. To maintain the blind, participants will receive macitentan 10 mg-matching placebo up to End of DBT.Treatment Extension Period: After EDBT, participants will continue to receive macitentan 75 mg orally for 2 years. To maintain the blind, participants will receive macitentan 37.5 mg-matching placebo during the 4-week up-titration period.

Drug: Macitentan 10 mgDrug: Macitentan 37.5 mgDrug: Macitentan 75 mgDrug: Placebo

Interventions

Participants will receive macitentan 10 mg film-coated tablets orally.

Also known as: JNJ-67896062
Macitentan 10 milligrams (mg) + PlaceboMacitentan 75 mg + Placebo

Participants will receive macitentan 37.5 mg film-coated tablets orally.

Also known as: JNJ-67896062
Macitentan 10 milligrams (mg) + PlaceboMacitentan 75 mg + Placebo

Participants will receive macitentan 75 mg film-coated tablets orally.

Also known as: JNJ-67896062
Macitentan 10 milligrams (mg) + PlaceboMacitentan 75 mg + Placebo

Participants will receive matching placebo film-coated tablets orally.

Macitentan 10 milligrams (mg) + PlaceboMacitentan 75 mg + Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Target population: greater than or equal to (\>=) 18 (or the legal age of consent in the jurisdiction in which the study is taking place) years of age
  • Target population: Symptomatic Pulmonary Arterial Hypertension (PAH) in World Health Organization Functional Class (WHO FC) II, III, or IV
  • Target population: PAH subtype falling in one of the below classifications: Idiopathic; Heritable; Drug- or toxin-induced; Related to: Connective tissue disease, HIV infection, Portal hypertension, and Congenital heart disease with small/coincidental cardiac defect with systemic-to-pulmonary shunt (for example atrial septal defect, ventricular septal defect, patent ductus arteriosus, atrioventricular septal defect) which does not account for the elevated pulmonary vascular resistance (PVR) or persistent PAH documented by an Right heart catheterization (RHC) \>= 1 year after simple systemic-to pulmonary shunt repair
  • PAH diagnosis confirmed by hemodynamic evaluation at rest at any time prior to screening: Mean pulmonary artery pressure (mPAP) greater than (\>) 20 millimeters of mercury (mm Hg), and; Pulmonary artery wedge pressure (PAWP) or left ventricular end diastolic pressure (LVEDP) less than or equal to (\<=) 15 mm Hg, and PVR \>= 3 Wood Units (that is, \>= 240 dyn\*sec/cm\^5)
  • Able to perform the 6-minute walking test (6MWT) with a minimum distance of 50 meters (m) and maximum distance of 440m at screening. Participants able to walk more than 440m at screening are eligible if they are in WHO FC III or IV and n-terminal prohormone of brain natriuretic peptide or n-terminal pro B-type natriuretic peptide (NT-proBNP) level is \>=300 nanograms per liter (ng/L) at screening, based on central laboratory results

You may not qualify if:

  • Known presence of three or more of the following risk factors for heart failure with preserved ejection fraction at screening, based on records that confirm documented medical history: Body mass index (BMI) \> 30 kilograms per meter square (kg/m\^2), Diabetes mellitus of any type, Essential hypertension (even if well controlled); Coronary artery disease, that is, any of the following: history of stable angina, or known more than 50 percent (%) stenosis in a coronary artery, or history of myocardial infarction, or history of or planned coronary artery bypass grafting and/or coronary artery stenting
  • Presence of moderate or severe obstructive lung disease (forced expiratory volume in 1 second \[FEV1\] / forced vital capacity \[FVC\] \< 70%; and FEV1 \< 60% of predicted after bronchodilator administration) ) in participants with a known or suspected history of significant lung disease as documented by a spirometry test performed within 1 year prior to screening
  • Known moderate to severe hepatic impairment, defined as Child-Pugh Class B or C, based on records that confirm documented medical history
  • Serum aspartate aminotransferase (AST) and/or alanine aminotransferase (ALT) \> 1.5\*upper limit of normal (ULN) at screening
  • Hemoglobin \< 100 gram per liter (g/L) (\< 10 gram per deciliter \[g/dL\]) at screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (274)

Mayo Clinic

Phoenix, Arizona, 85054, United States

Location

Arizona Pulmonary Specialists, Ltd

Scottsdale, Arizona, 85258, United States

Location

Scripps Memorial Hospital

La Jolla, California, 92037, United States

Location

USC Keck

Los Angeles, California, 90033, United States

Location

Jeffrey S. Sager, MD Medical Corporation

Santa Barbara, California, 93105, United States

Location

Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center

Torrance, California, 90502-2006, United States

Location

National Jewish Health

Denver, Colorado, 80206, United States

Location

Cleveland Clinic

Weston, Florida, 33331 3609, United States

Location

Piedmont Healthcare

Atlanta, Georgia, 30309, United States

Location

Northside Hospital

Atlanta, Georgia, 30342, United States

Location

Advocate Christ Medical Center

Oak Lawn, Illinois, 60453, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

St. Vincent Medical Group, Inc.

Indianapolis, Indiana, 46260, United States

Location

University Of Iowa - Hospitals & Clinics

Iowa City, Iowa, 52242, United States

Location

Norton Pulmonary Specialists

Louisville, Kentucky, 40202, United States

Location

Louisiana State University

New Orleans, Louisiana, 70112 7021, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109-5000, United States

Location

Troy Beaumont

Troy, Michigan, 53215, United States

Location

Washington University School Of Medicine

St Louis, Missouri, 63110-1032, United States

Location

Saint Louis University Academic Pavillion

St Louis, Missouri, 63110, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198-2265, United States

Location

Reno Heart Institute

Reno, Nevada, 89511, United States

Location

Winthrop University Hospital

Mineola, New York, 11501, United States

Location

Mount Sinai

New York, New York, 10029, United States

Location

Columbia University

New York, New York, 10032, United States

Location

Stony Brook University Medical Center

Stony Brook, New York, 11794, United States

Location

Duke

Durham, North Carolina, 27710-4000, United States

Location

Lindner Clinical Trial Center/Christ Hospital

Cincinnati, Ohio, 45219, United States

Location

Integris Baptist Office

Oklahoma City, Oklahoma, 73112, United States

Location

The Oregon Clinic

Portland, Oregon, 97220-9442, United States

Location

Oregon Pulmonary Clinic

Portland, Oregon, 97225-6652, United States

Location

Oregon Health And Science University

Portland, Oregon, 97239-3011, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104-5545, United States

Location

Allegheny General Hospital of Research

Pittsburgh, Pennsylvania, 15212, United States

Location

Lankenau Medical Center

Wynnewood, Pennsylvania, 19096, United States

Location

AnMed Health

Anderson, South Carolina, 29621, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Baylor College of Medicine (BCM) - Baylor Heart Clinic

Houston, Texas, 77030, United States

Location

Baylor Scott White - Plano

Plano, Texas, 75093, United States

Location

San Antonio Methodist TX Transplant Physicians Group

San Antonio, Texas, 78229-3771, United States

Location

The Robert Larner, M.D. College of Medicine at The University of Vermont

Burlington, Vermont, 05405, United States

Location

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, 53792, United States

Location

Medical College Of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Sanatorio de la Trinidad Mitre

Buenos Aires, C1039AAO, Argentina

Location

Sanatorio Guemes

C.a.b.a., C1180AAX, Argentina

Location

Hospital Italiano de Buenos Aires

Caba, 1199ABB, Argentina

Location

Sanatorio Ramon Cereijo

Caba, C1048AAN, Argentina

Location

Centro Médico Dra. De Salvo

Caba, C1426ABP, Argentina

Location

Instituto de Cardiologia de Corrientes

Corrientes, W3400AMZ, Argentina

Location

Instituto Medico de La Fundacion Estudios Clinicos

Rosario, 2000, Argentina

Location

Instituto Cardiovascular de Rosario

Rosario, S2000DSR, Argentina

Location

Flinders Medical Centre

Bedford Park, 5042, Australia

Location

Royal Prince Alfred Hospital

Camperdown, 2050, Australia

Location

The Prince Charles Hospital

Chermside, 4032, Australia

Location

St Vincent's hospital

Darlinghurst, 2010, Australia

Location

Royal Hobart Hospital

Hobart, 7000, Australia

Location

Fiona Stanley Hospital

Murdoch, 6150, Australia

Location

Westmead Hospital

Westmead, 2145, Australia

Location

LKH-Univ. Klinikum Graz

Graz, 8036, Austria

Location

Ordensklinikum Linz GmbH Elisabethinen

Linz, 4020, Austria

Location

Medical University Vienna

Vienna, 1090, Austria

Location

The Republican Scientific-Practical Center ''Cardiology''

Minsk, 220036, Belarus

Location

Minsk Regional Clinical Hospital

Minsk, 220143, Belarus

Location

ULB Hôpital Erasme

Brussels, 1070, Belgium

Location

UZ Leuven

Leuven, 3000, Belgium

Location

Universidade Federal De Minas Gerais - Hospital das Clínicas

Belo Horizonte, 30130-100, Brazil

Location

Instituto das Pequenas Missionárias de Maria Imaculada - Hospital Madre Teresa

Belo Horizonte, 30441-070, Brazil

Location

Empresa Brasileira de Servicos Hospitalares-EBSERH-Hospital Universitario de Brasilia

Brasília, 70840-901, Brazil

Location

Sociedade Hospitalar Angelina Caron - Hospital Angelina Caron

Campina Grande do Sul, 83430-000, Brazil

Location

Ceti - Centro de Estudos Em Terapias Inovadoras

Curitiba, 80060-240, Brazil

Location

Ynova Pesquisa Clinica

Florianópolis, 88020-210, Brazil

Location

Universidade Federal de Goias - Hospital das Clinicas da UFG

Goiânia, 74605-020, Brazil

Location

Hospital das Clinicas de Porto Alegre

Porto Alegre, 90035-003, Brazil

Location

Uniao Brasileira de Educacao e Assistencia Hospital Sao Lucas da PUCRS

Porto Alegre, 90610-000, Brazil

Location

Instituto de Medicina Integral Professor Fernando Figueira

Recife, 50070-902, Brazil

Location

Fundacao do ABC Centro Universitario FMABC

Santo André, 09060 870, Brazil

Location

Secretaria de Estado da Saude Instituto Dante Pazzanese de Cardiologia

São Paulo, 04012-909, Brazil

Location

Hospital Das Clinicas Da Faculdade De Medicina Da USP

São Paulo, 05403-000, Brazil

Location

Multiprofile Hospital For Active Treatment National Cardiology Hospital, Ead

Sofia, 1309, Bulgaria

Location

University Multiprofile Hospital for Active Treatment- UMHAT Sveta Anna AD

Sofia, 1750, Bulgaria

Location

St. Joseph's Health Centre

Hamilton, Ontario, L8N 4A6, Canada

Location

University of Ottawa Heart Institute

Ottawa, Ontario, K1Y 4W7, Canada

Location

University Health Network - Toronto General Hospital

Toronto, Ontario, M5G2C4, Canada

Location

Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

Beijing Chaoyang Hospital

Beijing, 100020, China

Location

Beijing Anzhen Hospital

Beijing, 100029, China

Location

Peking Union Medical College Hospital

Beijing, 100730, China

Location

The Second Xiangya Hospital of Central South Hospital

Changsha, 410011, China

Location

West China Hospital Sichuan University

Chengdu, 610041, China

Location

The First Affiliated Hospital of Chongqing Medical University

Chongqing, 400016, China

Location

The First Affiliated Hospital of Guangzhou Medical University

Guangzhou, 510120, China

Location

Shanghai Pulmonary Hospital

Shanghai, 200433, China

Location

Renji Hospital

Shanghai, 201112, China

Location

Zhongshan Hospital Fudan University

Shanghai, China

Location

The General Hospital of Northern Theater Command

Shenyang, 110000, China

Location

Shengjing Hospital Of China Medical University

Shenyang, 110004, China

Location

Tianjin Medical University General Hospital

Tianjin, 300052, China

Location

The First Affiliated Hospital of Xian Jiaotong University

Xi'an, 710061, China

Location

Fundacion Neumologica Colombiana

Bogotá, 1101131, Colombia

Location

Fundacion Cardiovascular de Colombia

Bucaramanga - Piedecuesta - Valle de Menzuli, 6810002, Colombia

Location

Clínica Imbanaco S.A.S.

Cali, 760042, Colombia

Location

Centro Cardiovascular Colombiano Clínica Santa María

Medellín, 681004, Colombia

Location

Hospital Universidad del Norte

Soledad, 0000000, Colombia

Location

General University Hospital II.department of Internal Medicine-cardiology and angiology

Prague, 128 08, Czechia

Location

Århus Universitetshospital, Skejby, Hjertemedicinsk Afdeling B

Aarhus, 8200, Denmark

Location

CHU de Brest - Hopital de la Cavale Blanche

Brest, 29200, France

Location

Hôpital Côte de Nacre

Caen, France

Location

Hopital Bicetre Aphp Hopitaux Universitaires Paris Sud

Le Kremlin-Bicêtre, 94270, France

Location

CHRU de Lille Hopital Claude Huriez

Lille, France

Location

Aphm - Hopital Nord

Marseille, 13915, France

Location

Centre Hospitalier Universitaire - de Nice - Hopital Pasteur

Nice, 06002, France

Location

CHU Saint Etienne Hopital Nord

Saint-Priest-en-Jarez, 42277, France

Location

Hopital Larrey CHU de Toulouse

Toulouse, France

Location

Ruhr Universitat Bochum Diabeteszentrum

Bad Oeynhausen, 32545, Germany

Location

Medizinische Hochschule Hannover

Hanover, 30625, Germany

Location

Medizinische Klinik und Poliklinik V Klinikum Grosshadern der LMU

München, 81377, Germany

Location

Universitaetsklinikum Regensburg

Regensburg, 93053, Germany

Location

University Hospital of Alexandroupolis

Alexandroupoli, 681 00, Greece

Location

Alexandra General Hospital of Athens

Athens, 11528, Greece

Location

University Hospital Of Larissa

Larissa, 41334, Greece

Location

Ahepa University General Hospital of Thessaloniki

Thessaloniki, 54636, Greece

Location

Semmelweis Egyetem,Pulmonológiai Klinika

Budapest, 1083, Hungary

Location

Gottsegen Gyorgy Orszagos Kardiovaszkularis Intezet Felnott kardiologiai osztaly

Budapest, 1096, Hungary

Location

Pecsi Tudomanyegyetem Altalanos Orvostudomanyi Kar

Pécs, 7624, Hungary

Location

Szegedi Tudományegyetem, Általános Orvostudományi Kar, Családorvosi Intézet és rendelő

Szeged, 6720, Hungary

Location

NHL Medical College (SVP Hospital IMSR)

Ahmedabad, 380006, India

Location

Cims Hospital

Ahmedabad, 381060, India

Location

Narayana Hrudayalaya Limited

Bangalore, 560099, India

Location

SRM Medical College Hospital & Research Centre

Chengalpetu, 603203, India

Location

Govindaswamy Kuppuswamy Naidu Memorial Hospital

Coimbatore, 64103, India

Location

HealthWorld Hospitals

Durgapur, 713216, India

Location

Renova Century Hospitals

Hyderabad, 500034, India

Location

Care Hospitals

Hyderbad, 500034, India

Location

Rabindranath Tagore International Institute of Cardiac Sciences

Kolkata, 700099, India

Location

GB Pant Institute of Post Graduate Medical Education & Research

New Delhi, 110002, India

Location

Sir Ganga Ram Hospital

New Delhi, 110060, India

Location

Jawaharlal Institute of Postgraduate Medical Education and Research

Puducherry, 605008, India

Location

B.D. Mehta Mahavir Heart Institute

Surat, 395001, India

Location

Carmel Medical Center

Haifa, 34362, Israel

Location

Shaare Zedek Medical Center

Jerusalem, 91031, Israel

Location

Kaplan Medical Center

Rehovot, 76100, Israel

Location

The Chaim Sheba Medical Center

Tel Litwinsky, 5265601, Israel

Location

Yitzhak Shamir Medical Center

Ẕerifin, 70300, Israel

Location

ASST Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

Location

AOU Di Modena Policlinico Di Modena

Modena, 41125, Italy

Location

Ospedale San Francesco

Nuoro, 08100, Italy

Location

Fondazione IRCCS Policlinico San Matteo

Pavia, 27100, Italy

Location

Fondazione Toscana Gabriele Monasterio CNR

Pisa, 56124, Italy

Location

Policlinico Gemelli Universita Cattolica

Roma, 00168, Italy

Location

The University of Tokyo Hospital

Bunkyō City, 113-8655, Japan

Location

Kyushu University Hospital

Fukuoka, 812 8582, Japan

Location

Kure Kyosai Hospital

Hiroshima, 737-8505, Japan

Location

Kagoshima University Hospital

Kagoshima, 890 8520, Japan

Location

St Marianna University Hospital

Kanagawa, 216 8511, Japan

Location

Kanazawa University Hospital

Kanazawa, 920 8641, Japan

Location

Kobe University Hospital

Kobe, 650 0017, Japan

Location

Kurume University Hospital

Kurume, 830-0011, Japan

Location

University Hospital Kyoto Prefectural University of Medicine

Kyoto, 602-8566, Japan

Location

Kyoto University Hospital

Kyoto, 606 8507, Japan

Location

Shinshu University Hospital

Matsumoto, 390 8621, Japan

Location

Nagasaki University Hospital

Nagasaki, 852-8501, Japan

Location

Nagoya University Hospital

Nagoya, 466 8560, Japan

Location

Nagoya City University Hospital

Nagoya, 467 8602, Japan

Location

Niigata University Medical And Dental Hospital

Niigata, 951 8520, Japan

Location

Okayama University Hospital

Okayama, 700 8558, Japan

Location

National Hospital Organization Okayama Medical Center

Okayama, 701-1192, Japan

Location

Sapporo Medical University Hospital

Sapporo, 060 8543, Japan

Location

Hokkaido University Hospital

Sapporo, 060-8648, Japan

Location

National Cerebral and Cardiovascular Center

Suita-Shi, 564-8565, Japan

Location

Juntendo University Hospital

Tokyo, 113-8431, Japan

Location

Fujita Health University Hospital

Toyoake, 470-1192, Japan

Location

University of Tsukuba Hospital

Tsukuba, 305 8576, Japan

Location

Hospital Pulau Pinang

George Town, 10990, Malaysia

Location

Hospital Serdang

Kajang, 43000, Malaysia

Location

Sarawak Heart Center

Kota Samarahan, 94300, Malaysia

Location

Institut Jantung Negara (National Heart Institute)

Kuala Lumpur, 50400, Malaysia

Location

Consultorio Privado del Dr. Gabriel Arturo Ramos Lopez

Guadalajara, 44657, Mexico

Location

Instituto Nacional de Cardiologia Dr. Ignacio Chavez

Mexico City, 14080, Mexico

Location

Operadora de Hospitales Angeles SA de CV Hospital Angeles Lomas

México, 52787, Mexico

Location

Hospital Universitario Dr Jose Eleuterio Gonzalez

Monterrey, 64460, Mexico

Location

Unidad de Investigacion Clinica en Medicina S.C. (UDICEM)

Monterrey, 64718, Mexico

Location

Centro de Investigacion Clinica Chapultepec

Morelia, 58260, Mexico

Location

VUMC Amsterdam

Amsterdam, 1081 HV, Netherlands

Location

St. Antonius Ziekenhuis Nieuwegein

Nieuwegein, 3435 CM, Netherlands

Location

Radboud Umcn

Nijmegen, 6525 GA, Netherlands

Location

Erasmus MC

Rotterdam, 3015 CN, Netherlands

Location

Akershus Universitetssykehus

Nordbyhagen, 1478, Norway

Location

Oslo University Hospital

Oslo, 372, Norway

Location

Uniwersytecki Szpital Kliniczny w Bialymstoku

Bialystok, 15 276, Poland

Location

Szpital Uniwersytecki nr 2 im dr Jana Biziela w Bydgoszczy, Klinika Kardiologii

Bydgoszcz, 85-168, Poland

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, 80214, Poland

Location

SPSK nr 7 SUM w Katowicach Gornoslaskie Centrum Medyczne im Prof Leszka Gieca

Katowice, 40 635, Poland

Location

Krakowski Szpital Specjalityczny im Jana Pawla II Oddzial Kliniczny Chorob Serca i Naczyn

Krakow, 31 202, Poland

Location

Uniwersytecki Szpital Kliniczny nr 2 PUM w Szczecinie

Szczecin, 70 111, Poland

Location

Panstwowy Instytut Medyczny Ministerstwa Spraw Wewnetrznych i Administracji

Warsaw, 02 507, Poland

Location

Wojewodzki Szpital Specjalistyczny we Wroclawiu Osrodek Badawczo Rozwojowy

Wroclaw, 51 124, Poland

Location

Uls Coimbra - Hosp. Univ. Coimbra

Coimbra, 3004 561, Portugal

Location

Uls Sao Jose - Hosp. Santa Marta

Lisbon, 1169-024, Portugal

Location

Uls Santa Maria - Hosp. Pulido Valente

Lisbon, 1769-001, Portugal

Location

Altay Regional Cardiological Dispensary

Barnaul, 656055, Russia

Location

Chelyabinsk Regional Clinical Hospital

Chelyabinsk, 454076, Russia

Location

State Autonomous HealthCare Institution 'Interregional Clinical Diagnostic Center'

Kazan', 420101, Russia

Location

Scientific and Research Institution of Cardiovascular Diseases Complex Problems

Kemerovo, 650002, Russia

Location

Moscow City Clinical Hospital No.51

Moscow, 121309, Russia

Location

National Medical Research Center of Cardiology of MoH of Russian Federation

Moscow, 121552, Russia

Location

National medical Research Center n.a. V.A.Almazov of MoH of Russian Federation

Saint Petersburg, 197341, Russia

Location

Samara Regional Clinical Cardiological Dispensary

Samara, 443070, Russia

Location

State Autonomous Healthcare Institution of Tyumen Region 'Scientific and Practical Medical Center'

Tyumen, 625032, Russia

Location

Volgograd Regional Clinical Cardiology Center

Volgograd, 400008, Russia

Location

King Faisal Specialist Hospital & Research Center

Riyadh, 11564, Saudi Arabia

Location

King Fahad Medical City

Riyadh, 59046, Saudi Arabia

Location

University Clinical Center of Serbia

Belgrade, 11000, Serbia

Location

Institute for Pulmonary Disease of Vojvodina

Kamenitz, 21204, Serbia

Location

National University Heart Centre, Singapore

Singapore, 119228, Singapore

Location

National Heart Centre (NHC) Singapore

Singapore, 169609, Singapore

Location

Narodny ustav srdcovych a cievnych chorob

Bratislava, 833 48, Slovakia

Location

The Eastern Slovakia Institute of Cardiovascular Diseases

Košice, 040 11, Slovakia

Location

Milpark Hospital

Johannesburg, South Africa

Location

Dr Kalla

Lenasia, 1820, South Africa

Location

Severance Hospital Yonsei University Health System

Seoul, 03722, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Seoul National University Hospital

Seoul, 3080, South Korea

Location

Hosp Univ Vall D Hebron

Barcelona, 08035, Spain

Location

Hosp. Del Mar

Barcelona, 8003, Spain

Location

Hosp. Univ. 12 de Octubre

Madrid, 28041, Spain

Location

Hosp. Univ. La Paz

Madrid, 28046, Spain

Location

Hosp. Univ. Pta. de Hierro Majadahonda

Madrid, 28222, Spain

Location

Hosp. Costa Del Sol

Málaga, 29603, Spain

Location

Hosp Clinico Univ de Salamanca

Salamanca, 37007, Spain

Location

Sahlgrenska Universitetsjukhuset

Gothenburg, 413 45, Sweden

Location

Skanes universitetssjukhus

Lund, 221 85, Sweden

Location

National Cheng Kung University Hospital

Tainan, 704, Taiwan

Location

National Taiwan University Hospital

Taipei, 10002, Taiwan

Location

Mackay Memorial Hospital

Taipei, 10449, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 112, Taiwan

Location

Phramongkutklao Hospital and Medical College

Bangkok, 10400, Thailand

Location

Ramathibodi Hospital Mahidol University

Bangkok, 10400, Thailand

Location

Siriraj Hospital Mahidol University

Bangkok, 10700, Thailand

Location

Maharaj Nakorn Chiang Mai hospital Faculty of Medicine

Chiang Mai, 50020, Thailand

Location

Srinagarind Hospital, Khon Kaen University

Khon Kaen, 40002, Thailand

Location

Songklanagarind hospital

Songkhla, 90110, Thailand

Location

Adana City Hospital

Adana, 01170, Turkey (Türkiye)

Location

Cukurova University Medical Faculty

Adana, 01790, Turkey (Türkiye)

Location

Ankara Etlik Speciality Hospital

Ankara, 06170, Turkey (Türkiye)

Location

Hacettepe University Medical Faculty

Ankara, 06230, Turkey (Türkiye)

Location

Gazi University Medical Faculty

Ankara, 06500, Turkey (Türkiye)

Location

Ankara Bilkent Sehir Hastanesi

Ankara, 06800, Turkey (Türkiye)

Location

Akdeniz University Medical Faculty

Antalya, 07059, Turkey (Türkiye)

Location

Bursa Yuksek Ihtisas Training and Research Hospital

Bursa, 16310, Turkey (Türkiye)

Location

Pamukkale Universitesi Tip Fakultesi Hastanesi

Denizli, 20160, Turkey (Türkiye)

Location

Siyami Ersek Training and Research Hospital

Istanbul, 34668, Turkey (Türkiye)

Location

Marmara University Medical Faculty

Istanbul, 34899, Turkey (Türkiye)

Location

SBU Izmir Tepecik Egitim Ve Arastirma Hastanesi

Izmir, 35020, Turkey (Türkiye)

Location

Ege Universitesi Tip Fakultesi Hastanesi

Izmir, 35100, Turkey (Türkiye)

Location

Dokuz Eylul Universitesi Tip Fakültesi Hastanesi

Izmir, 35330, Turkey (Türkiye)

Location

Kartal Kosuyolu Yuksek Ihtisas Egitim Ve Arastirma Hastanesi

Kartal Istanbul, 34865, Turkey (Türkiye)

Location

Mersin University Medical Faculty

Mersin, 33110, Turkey (Türkiye)

Location

CNE 'Cherkasy Regional Cardiological Center of Cherkasy Regional Council'

Cherkassy, 18000, Ukraine

Location

Communal Noncommercial Enterprise Cherkasy Regional Hospital of Cherkasy Regional Council

Cherkasy, 18009, Ukraine

Location

MI 'Dnipropetrovsk Regional Clinical Center of Cardiology and Cardiac Surgery'

Dnipro, 49070, Ukraine

Location

CNE' City Clinical Hospital #8' of Kharkiv City Council

Kharkiv, 61176, Ukraine

Location

SI National Scientific Center Institute of Cardiology of M.D. Strazhesko of NAMS of Ukraine

Kyiv, 02000, Ukraine

Location

State Institute Of Phthisiology And Pulmonology N.A. F.G. Yanovskiy Of Ams Ukraine

Kyiv, 03680, Ukraine

Location

Communal Noncommercial Enterprise of Lviv Regional Council 'Lviv Regional Clinical Hospital'

Lviv, 79010, Ukraine

Location

Municipal Non-commercial Enterprise Ternopil University Hospital of Ternopil Regional Council

Ternopil, 46002, Ukraine

Location

Royal Free Hospital

London, NW3 2QG, United Kingdom

Location

Freeman Hospital

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Sheffield Teaching Hospitals NHS Foundation Trust Royal Hallamshire Hospital

Sheffield, S10 2RX, United Kingdom

Location

Hanoi Medical University Hospital

Hanoi, Vietnam

Location

Cho Ray Hospital

Ho Chi Minh City, 700000, Vietnam

Location

Tam Anh Hospital

Ho Chi Minh City, 700000, Vietnam

Location

Tam Duc Heart Hospital

Ho Chi Minh City, 700000, Vietnam

Location

University Medical Center Ho Chi Minh city

Ho Chi Minh City, 700000, Vietnam

Location

MeSH Terms

Conditions

Pulmonary Arterial Hypertension

Interventions

macitentan

Condition Hierarchy (Ancestors)

Hypertension, PulmonaryLung DiseasesRespiratory Tract Diseases

Study Officials

  • Actelion Clinical Trials

    Actelion

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 31, 2020

First Posted

February 18, 2020

Study Start

June 30, 2020

Primary Completion

October 7, 2025

Study Completion (Estimated)

February 20, 2029

Last Updated

April 13, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

The data sharing policy of the Janssen Pharmaceutical Companies of Johnson \& Johnson is available at www.janssen.com/clinical-trials/transparency. As noted on this site, requests for access to the study data can be submitted through Yale Open Data Access (YODA) Project site at yoda.yale.edu.

More information

Locations