NCT00660179

Brief Summary

The AC-055-302/SERAPHIN study will be an event-driven Phase III study, comparing two different doses of macitentan (ACT-064992) (3 and 10 mg) vs placebo in patients with symptomatic PAH. The main study objective is to demonstrate that macitentan (ACT-064992) prolongs time to the first morbidity or mortality event, and to evaluate the benefit/risk profile of macitentan (ACT-064992) in the treatment of patients with symptomatic PAH.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
742

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started May 2008

Typical duration for phase_3

Geographic Reach
35 countries

147 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 14, 2008

Completed
3 days until next milestone

First Posted

Study publicly available on registry

April 17, 2008

Completed
14 days until next milestone

Study Start

First participant enrolled

May 1, 2008

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2012

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2012

Completed
2.1 years until next milestone

Results Posted

Study results publicly available

May 5, 2014

Completed
Last Updated

September 28, 2015

Status Verified

August 1, 2015

Enrollment Period

3.8 years

First QC Date

April 14, 2008

Results QC Date

November 5, 2013

Last Update Submit

September 10, 2015

Conditions

Keywords

pulmonary arterial hypertension SERAPHIN

Outcome Measures

Primary Outcomes (1)

  • Time to First Confirmed Morbidity or Mortality Event up to the End of Treatment (Kaplan-Meier Estimate of Patients Without a Morbidity or Mortality Event)

    Morbidity or mortality events were defined as: a) Death; b) Atrial septostomy; c) Lung transplantation; d) Initiation of intravenous (i.v.) or subcutaneous prostanoids, or; e) Other worsening of pulmonary arterial hypertension (PAH). Other worsening of PAH was defined by the combined occurrence of all the following 3 events: At least 15% decrease in the 6 minute walk distance from baseline, confirmed by 2 tests performed on separate days, within 2 weeks. AND worsening of PAH symptoms including at least one of the following: a) Increase in WHO Functional Class (WHO FC), or no change in patients in WHO FC IV at baseline; b) Appearance or worsening of signs of right heart failure that did not respond to optimized oral diuretic therapy AND need for new treatment(s) for PAH that included the following: a) Oral or inhaled prostanoids; b) Oral phosphodiesterase inhibitors; c) Endothelin receptor antagonists (only after discontinuation of study treatment; d) i.v. diuretics

    Up to end of treatment (data presented up to month 36)

Secondary Outcomes (7)

  • Time to Death Due to PAH or Hospitalisation for PAH up to the End of Treatment (Kaplan-Meier Estimate of Patients Without an Event)

    Up to end of treatment (data presented up to month 36)

  • Time to Death Due to Any Cause up to the End of Treatment (Kaplan-Meier Estimate of Patients Without an Event)

    Up to end of treatment (data presented up to month 36)

  • Time to Death Due to Any Cause up to the End of Study (Kaplan-Meier Estimate of Patients Without an Event)

    Up to end of study (data presented up to month 36)

  • Change From Baseline to Month 6 in 6-minute Walk Distance

    Baseline to month 6

  • Number of Patients With Improvements in World Health Organization Functional Class From Baseline to Month 6

    Baseline to month 6

  • +2 more secondary outcomes

Other Outcomes (1)

  • Summary of the First Causes of Morbidity or Mortality

    Up to end of treatment (Up to 36 months)

Study Arms (3)

1

EXPERIMENTAL

Macitentan (ACT-064992) tablet, 3 mg, once daily

Drug: macitentan (ACT-064992)

2

EXPERIMENTAL

Macitentan (ACT-064992) tablet, 10 mg, once daily

Drug: macitentan (ACT-064992)

3

PLACEBO COMPARATOR

Matching placebo, once daily

Drug: placebo

Interventions

Tablet, 3 mg dosage, once daily

1

Matching placebo, once daily

3

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Signed informed consent prior to initiation of any study mandated procedure.
  • Patients with symptomatic pulmonary arterial hypertension (PAH) in modified World Health Organization (WHO) functional class II to IV.
  • Patients with the following types of pulmonary arterial hypertension (PAH) belonging to groups 1.1 to 1.3 of the Venice classification:
  • Idiopathic (IPAH);
  • Familial (FPAH); or
  • Related to:
  • Collagen vascular disease;
  • Simple, congenital systemic-to-pulmonary shunts at least 1 year post surgical repair;
  • Human immunodeficiency virus (HIV) infection; or
  • Drugs and toxins.
  • PAH diagnosis confirmed by hemodynamic evaluation performed prior to randomization and showing all of the following:
  • Mean pulmonary artery pressure (mPAP) \> 25 mmHg at rest;
  • Pulmonary capillary wedge pressure (PCWP) or left ventricular end diastolic pressure (LVEDP) \< 15 mmHg; and
  • Pulmonary vascular resistance (PVR) at rest \>= 320 dyn×sec/cm\^5.
  • minute walk distance (6MWD) \>= 50 m.
  • +1 more criteria

You may not qualify if:

  • PAH associated with portal hypertension, thyroid disorders, glycogen storage disease, Gaucher''s disease, hereditary hemorrhagic telangiectasia, hemoglobinopathies, myeloproliferative disorders or splenectomy.
  • PAH associated with non corrected simple congenital systemic-to-pulmonary shunts, and combined and complex systemic-to-pulmonary shunts, corrected or non corrected.
  • PAH associated with significant venous or capillary involvement (PCWP \> 15 mmHg), known pulmonary veno-occlusive disease, and pulmonary capillary hemangiomatosis.
  • Persistent pulmonary hypertension of the newborn.
  • Pulmonary Hypertension belonging to groups 2 to 5 of the Venice classification.
  • Moderate to severe obstructive lung disease: forced expiratory volume in 1 second/forced vital capacity (FEV1/FVC) \< 70% and FEV1 \< 65% of predicted value after bronchodilator administration.
  • Moderate to severe restrictive lung disease: total lung capacity (TLC) \< 60% of predicted value.
  • Moderate to severe hepatic impairment, i.e., Child-Pugh Class B or C.
  • Estimated creatinine clearance \< 30 mL/min
  • Serum aspartate aminotransferase (AST) and/or alanine aminotransferase (ALT) \> 1.5 times the upper limit of normal.
  • Hemoglobin \< 75% of the lower limit of the normal range.
  • Systolic blood pressure \< 100 mmHg.
  • Acute or chronic physical impairment (other than dyspnea), limiting the ability to comply with study requirements.
  • Pregnant or breast-feeding.
  • Known concomitant life-threatening disease with a life expectancy \< 12 months.
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (153)

University of Alabama at Birmingham

Birmingham, Alabama, 35249-0001, United States

Location

Arizona Pulmonary Specialists

Pheonix, Arizona, 85013, United States

Location

GLVA Healthcare Center

Los Angeles, California, United States

Location

University of California, San Diego

San Diego, California, United States

Location

Santa Barbara Cottage Hospital

Santa Barbara, California, United States

Location

Liu Center for Pulmonary Hypertension

Torrance, California, United States

Location

University of Colorado Health Sciences Center

Denver, Colorado, United States

Location

Mayo Clinic, Jacksonville

Jacksonville, Florida, United States

Location

Emory University Hospital - McKelvey Center for Lung Transplantation & Pulmonary Vascular Disease

Atlanta, Georgia, 30322, United States

Location

Pulmonary & Critical Care of Atlanta

Atlanta, Georgia, 30342, United States

Location

Southeastern Lung Care

Decatur, Georgia, United States

Location

University of Chicago Hospitals

Chicago, Illinois, United States

Location

University of Iowa

Iowa City, Iowa, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Kentuckiana Pulmonary Associate, PLLC

Louisville, Kentucky, United States

Location

Medical Center of Louisiana at New Orleans

New Orleans, Louisiana, United States

Location

Maine Medical Center

Portland, Maine, 04102, United States

Location

University of Maryland School of Medicine

Baltimore, Maryland, 21201, United States

Location

Boston University School of Medicine

Boston, Massachusetts, United States

Location

Pulmonary/Critical Care Division/Tufts New England Medical Center

Boston, Massachusetts, United States

Location

University of Michigan

Ann Arbor, Michigan, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

University of NJ - Robert Wood Johnson Medical School

New Brunswick, New Jersey, United States

Location

Columbia University Medical Center - Pediatric Cardiology

New York, New York, United States

Location

Duke University Medical Center

Durham, North Carolina, United States

Location

University of Cincinnati Ohio Heart Health Center

Cincinnati, Ohio, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Location

University of Texas Medical Center - St. Paul University

Dallas, Texas, 75235, United States

Location

Baylor College of Medicine and the Methodist Hospital

Houston, Texas, 77030, United States

Location

Dept. of Pulmonary Medicine - Latter Day Saints Hospital

Salt Lake City, Utah, United States

Location

Sentara Hospital T/A Sentara Cardiovascular Research Institute

Norfolk, Virginia, 23507, United States

Location

Comprehensive Cardiovascular Care Group

Milwaukee, Wisconsin, United States

Location

Fundacion Favaloro

Buenos Aires, C1093AAS, Argentina

Location

Hospital Britanico

Buenos Aires, Argentina

Location

Sanatorio MITRE

Buenos Aires, Argentina

Location

SANATORIO OTAMENDI y MIROLI

Buenos Aires, Argentina

Location

Instituto Cardiologia Corrientes

Corrientes, Argentina

Location

Htal Italiano Cordoba

Córdoba, Argentina

Location

Htla privado de Cordoba

Córdoba, Argentina

Location

'Hospital Italiano - Garibaldi de Rosario

Santa Fe, Argentina

Location

St. Vincent's Hospital

Darlinghurst, NSW, 2010, Australia

Location

The Alfred Hospital

Melbourne, VIC, 3181, Australia

Location

Royal Brisbane Hospital

Sunshine Coast, 4558, Australia

Location

Medical University of Vienna/ Department of Internal Medicine II, Division of Cardiology

Vienna, Austria

Location

Republican reserach - Pratical Centre of Cardilogy

Minsk, 220036, Belarus

Location

Minsk Regional Clinical Hospital

Minsk, 223040, Belarus

Location

Vitebsk Regional Clinical Hospital

Vitebsk, 210037, Belarus

Location

University Hospital Gasthuisberg / Kliniekhoofd, Interne Geneeskunde - I.G. Pneumologie

Leuven, Belgium

Location

Specialized Hospital for Active Treatment of Cardio-Vascular Diseases / Department of Pediatric Cardiology

Sofia, 1309, Bulgaria

Location

London Health Sciences Centre / Victoria Hospital

London, Ontario, Canada

Location

L'Hopital Laval

Saint-Foy, Quebec, Canada

Location

Peter Lougheed Centre

Calgary, Canada

Location

Toronto General Hospital

Toronto, Canada

Location

Vancouver General Hospital

Vancouver, V6Z 1Y6, Canada

Location

'Pontificia Universidad Catolica de Chile

Santiago, Chile, Chile

Location

Hospital del Torax

Santiago, Chile, Chile

Location

Hospital San Juan de Dios

Santiago, Chile, Chile

Location

Guangdong General Hospital, Cardiology Department

Guangzhou, Guangdong, 510080, China

Location

Jiangsu Province Hospital - Pneumology Department

Nanjing, Jiangsu, 210029, China

Location

Beijing Anzhen Hospital of the Capital University of Medical Sciences, Cardiology Department

Beijing, 100029, China

Location

Peking Union Medcical College Hospital, Rheumatology Department

Beijing, 100032, China

Location

Chinese PLA General Hospital (301 Hospital), Cardiology Department

Beijing, 100853, China

Location

Renji Hospital, Rheumatology Dept

Shanghai, 200001, China

Location

Zhongshan Hospital Fudan University, Cardiology Dept

Shanghai, 200032, China

Location

Renji Hospital, Cardiology Dept

Shanghai, 200127, China

Location

Shanghai Pulmonary Hospital, Dept of Pulmonary Circulation

Shanghai, 200433, China

Location

Fundación Clínica Shaio

Bogotá, Colombia

Location

'Fundacion Cardiovascular de Colombia

Floridablanca, Santander, Colombia

Location

Clinical Hospital Center

Rijeka, 51 000, Croatia

Location

Hôpital Antoine Béclère / Service de Pneumologie

Clamart, 92140, France

Location

Hôpital Arnaud de Villeneuve Service des Maladies Respiratoires

Montpellier, 34295, France

Location

Hopital Haut-Leveque - Maison du Haut-Leveque

Pessac, 33604, France

Location

Unfallkrankenhaus Berlin, Klinik für Innere Medizin

Berlin, Germany

Location

Universität zu Köln, Medizinische Klinik III, Abteilung Kardiologie

Cologne, D-50924, Germany

Location

Medizinische Klinik und Poliklinik I Universitätsklinikum Carl Gustav Carus

Dresden, D-01307, Germany

Location

Universitätsklinikums Gießen und Marburg GmbH / Medizinische Klinik und Poliklinik II, Innere Med.

Giessen, D-35392, Germany

Location

Universität Greifswald / Klinik für Innere Medizin B,

Greifswald, D-17487, Germany

Location

Universitätsklinikum Hamburg-Eppendorf / Onkologie, Hämatologie und Knochenmarktransplantation mit Sektion Pneumologie

Hamburg, D-20246, Germany

Location

Thoraxklinik am Universitätsklinikum Heidelberg

Heidelberg, D-69126, Germany

Location

Universitätskliniken des Saarlandes / Medizinische Klinik und Poliklinik, Innere Medizin V

Homburg/Saar, D-66421, Germany

Location

Universtätsklinik Leipzig

Leipzig, 04103, Germany

Location

Klinikum der Johannes Gutenberg-Universität / II. Medizinische Klinik und Poliklinik

Mainz, D-55131, Germany

Location

Medizinische Klinik und Poliklinik I der Ludwig-Maximilians-Universität München / Klinikum Großhadern, Schwerpunkt Pneumologie

Munich, D-81377, Germany

Location

Universitätsklinikum Regensburg / Innere Medizin II

Regensburg, 93053, Germany

Location

Prince of Wales Hospital/ Division of Rheumatology, Department of Medicine & Therapeutics

Hong Kong, Hong Kong

Location

Queen Mary Hospital / Division of Cardiology, Department of Medicine

Hong Kong, Hong Kong

Location

Gottsegen György Országos Kardiológiai Intézet (Hungarian Institute of Cardiology)

Budapest, H-1096, Hungary

Location

Semmelweis University, Pulmonolgy Clinic

Budapest, H-1125, Hungary

Location

University of Szeged Albert Szent-Györgyi Medical and Pharmaceutical Center, Faculty of General Medicine, II. Internal Medicine Clinic, Cardiology Center

Szeged, Hungary

Location

Life Care Institute of Medical Science & Research, Ahmedabad

Ahmedabad, 382428, India

Location

G B Pant Hospital & Maulana Azad Medical College

Delhi, 110049, India

Location

Care Hospital

Hyderabad, 500001, India

Location

King Edward VII Memorial Hospital (KEM) Hospital

Mumbai, 400 012, India

Location

P D Hinduja National Hospital and Medical Research Centre/ Pulmunory Medicine

Mumbai, 400016, India

Location

Deenanath Mangeshkar Hospital and Research Centre

Pune, 411 004, India

Location

Lady Davis Carmel Medical Center / Department of Cardiovascular Medicine, Pulmonary Division

Haifa, 34362, Israel

Location

Rabin Medical Center - Belinson campus - Pulmonary Institute

Petach - Tikvah, 49100, Israel

Location

Pulmonary Institute, Kaplan Medical Center

Rehovot, 76100, Israel

Location

Sourasky Medical Center - Division of Pulmonary Medicine and Allergy

Tel Aviv, 64239, Israel

Location

The pulmonary institute Sheba Medical centre

Tel Litwinsky, 52621, Israel

Location

Policlinico Umberto I, Cardiologia

Roma, 00161, Italy

Location

Institut Jantung Negara (National Heart Institute)

Kuala Lumpur, 50400, Malaysia

Location

'Instituto Nacional de Cardiología (INC) Ignacio Chávez

Mexico City, 14080, Mexico

Location

Unidad de Investigación Clinica en Medicina, SC

Monterrey Nuevo León, 64020, Mexico

Location

St. Antonius ziekenhuis

Nieuwegein, 3435 CM, Netherlands

Location

Aker University Dept of Cardilogy

Oslo, N0514, Norway

Location

Hospital Alberto Sabogal Sologuren - EsSALUD

Lima, Peru

Location

IInstituto de Enfermedades Respiratorias, Clinica San Gabriel

Lima, Peru

Location

Klinika Chorob Serca i Naczyn Instytut Kardiologii Collegium Medicum UJ

Krakow, 31-202, Poland

Location

Klinika Chorób Wewnętrznych Klatki Piersiowej

Warsaw, 01-138, Poland

Location

III Katedra i Oddział Kliniczny Kardiologii Slaskiego Uniwersytetu Medycznego

Zabrze, 41-800, Poland

Location

Institutul de boli cardiovasculare / Clinica de Cardiologie

Bucharest, 022328, Romania

Location

Institutul de Pneumologie "Marius Nasta" / I. Clinica de Pneumoftiziologie

Bucharest, 50159, Romania

Location

Municipal Health Care Institution "Kemerovo Cardiology Dispensary"

Kemerovo, 650002, Russia

Location

Federal State Institution "Scientific Research Institute of Pulmonology of Roszdrav"

Moscow, 105077, Russia

Location

State Health Care Institution of Moscow "City Clinical Hospital #1 named after N. I. Pirogov"

Moscow, 117049, Russia

Location

Federal State Institution "Russian Cardiology Scientific and Production Complex of Rosmedtechnology"

Moscow, 121552, Russia

Location

Federal State Institution "Federal Center of Heart, Blood and Endocrinology named after V.A. Almazov" of Rosmedtechnology

Saint Petersburg, 194156, Russia

Location

State Educational Institution of High Professional Education

Saint Petersburg, 197 022, Russia

Location

State Institution "Scientific Research Institute of Cardiology" of Tomsk Scientific Center of RAMS, Siberian branch

Tomsk, 634063, Russia

Location

Tomsk Regional Clinical Hospital / Pulmonology Unit

Tomsk, 634063, Russia

Location

Municipal Health Care Institution "Clinical Hospital of Emergency Care named after N.V. Soloviov"

Yaroslavl, 150 003, Russia

Location

Sverdlovsk Regional Clinical Hospital # 1/ Cardiology Department (2nd Therapy Department)

Yekaterinburg, 620102, Russia

Location

University Children's Hospital (UNIVERZITETSKA DEČJA KLINIKA)

Belgrade, 11000, Serbia

Location

University Clinical Center of Serbia / Institute for Lung Diseases and Tuberculosis

Belgrade, 11000, Serbia

Location

Zemun Clinical Hospital (Kliničko-bolnički centar "Zemun" ) / Department of Cardiology

Belgrade, 11080, Serbia

Location

National University Hospital/ The Heart Institute

Singapore, 168752, Singapore

Location

Singapore General Hospital

Singapore, 168752, Singapore

Location

National Institute of Cardiovascular Diseases (Národný ústav srdcových a cievnych chorôb, a.s. - NÚSCH) / Department of Heart Transplantation

Bratislava, 833 48, Slovakia

Location

Slovak Medical University (Slovenská zdravotnícka univerzita) / Faculty of Medical Speciality Studies (Fakulta zdravotníckych špecializačných štúdií), Department of Cardiology and Angiology

Bratislava, 833 48, Slovakia

Location

Netcare Milpark Hospital,Center for Chest Disease

Johannesburg, 2000, South Africa

Location

Chris Hani Baragwanath Hospital, Department of Cardiology

Johannesburg, 27-11-033 8197, South Africa

Location

Tread Research

Parow, 7505, South Africa

Location

Block 4, Vergelegen Medi-Clinic

Somerset West, 7130, South Africa

Location

Hospital Juan Canalejo Servicio de Neumología

A Coruña, 15006, Spain

Location

Hospital Universitario Vall d'Hebron, Pneumology Unit, Planta Baja Hospital General

Barcelona, 08035, Spain

Location

Hospital Clínico I Provincial, Servicio de Neumología.

Barcelona, 08036, Spain

Location

Hospital 12 Octubre/ Cardiology department Planta 5a.

Madrid, 20841, Spain

Location

Hospital Clínico Virgen de la Victoria / Pneumology Unit,

Málaga, 29010, Spain

Location

Hospital Montecelo, Servicio de Neumología

Pontevedra, 36771, Spain

Location

University Hospital in Lund, Heart and Lung Division

Lund, SE-221 85, Sweden

Location

Servicio de Medicina Interna, Unidad de Hipertensión Pulmonar

Uppsala, 751 85, Sweden

Location

Taichung Veterans General Hospital / Division of Allergy, Immunology and Rheumatology

Taichung, 40705, Taiwan

Location

National Taiwan University Hospital/ Thoracic Surgical Division, Surgical Department

Taipei, Taiwan

Location

Ramathibodi Hospital, Mahidol University, Cardiology Unit, Department of Medicine,

Bangkok, 10400, Thailand

Location

Siriraj Hospital/ Department of Pediatrics, Faculty of Medicine, Siriraj Hospital, Mahidol University

Bangkok, 10700, Thailand

Location

Chiang Mai Hospital / Division of Rheumatology, Department of Medicine, Faculty of Medicine, Chiang Mai University

Chiang Mai, Thailand

Location

Srinagarind Hospital/Division of Rheumatology, Department of Medicine, Faculty of Medicine, Khon Kaen University

Khon Kaen, 40002, Thailand

Location

Istanbul University Cardiology Institure

Istanbul, Turkey (Türkiye)

Location

Dnipropetrovsk State Medical Academy / Regional Diagnostic Center, Department of electrophysiologic researches and anaesthesiologic aid

Dnipro, 49060, Ukraine

Location

Danylo Halytskyi Lviv State Medical University

Lviv, 79010, Ukraine

Location

Royal Free Hospital

London, NW3 2QG, United Kingdom

Location

Related Publications (10)

  • Pulido T, Adzerikho I, Channick RN, Delcroix M, Galie N, Ghofrani HA, Jansa P, Jing ZC, Le Brun FO, Mehta S, Mittelholzer CM, Perchenet L, Sastry BK, Sitbon O, Souza R, Torbicki A, Zeng X, Rubin LJ, Simonneau G; SERAPHIN Investigators. Macitentan and morbidity and mortality in pulmonary arterial hypertension. N Engl J Med. 2013 Aug 29;369(9):809-18. doi: 10.1056/NEJMoa1213917.

  • Di Scala L, Bacchi M, Bayer B, Turricchia S. Adjusting Overall Survival Estimates of Macitentan in Pulmonary Arterial Hypertension After Treatment Switching: Results from the SERAPHIN Study. Adv Ther. 2022 Sep;39(9):4346-4358. doi: 10.1007/s12325-022-02253-8. Epub 2022 Aug 1.

  • Souza R, Delcroix M, Galie N, Jansa P, Mehta S, Pulido T, Rubin L, Sastry BKS, Simonneau G, Sitbon O, Torbicki A, Boyanova N, Chamitava L, Stein C, Channick RN. Long-Term Safety, Tolerability and Survival in Patients with Pulmonary Arterial Hypertension Treated with Macitentan: Results from the SERAPHIN Open-Label Extension. Adv Ther. 2022 Sep;39(9):4374-4390. doi: 10.1007/s12325-022-02199-x. Epub 2022 Jul 12.

  • Torbicki A, Bacchi M, Delcroix M, Farber HW, Ghofrani HA, Hennessy B, Jansa P, Mehta S, Perchenet L, Pulido T, Rosenberg D, Rubin LJ, Sastry BKS, Simonneau G, Sitbon O, Souza R, Wei LJ, Channick R, Benza R. Integrating Data From Randomized Controlled Trials and Observational Studies to Assess Survival in Rare Diseases. Circ Cardiovasc Qual Outcomes. 2019 May;12(5):e005095. doi: 10.1161/CIRCOUTCOMES.118.005095.

  • Krause A, Zisowsky J, Dingemanse J. Modeling of pharmacokinetics, efficacy, and hemodynamic effects of macitentan in patients with pulmonary arterial hypertension. Pulm Pharmacol Ther. 2018 Apr;49:140-146. doi: 10.1016/j.pupt.2018.02.005. Epub 2018 Feb 28.

  • McLaughlin VV, Hoeper MM, Channick RN, Chin KM, Delcroix M, Gaine S, Ghofrani HA, Jansa P, Lang IM, Mehta S, Pulido T, Sastry BKS, Simonneau G, Sitbon O, Souza R, Torbicki A, Tapson VF, Perchenet L, Preiss R, Verweij P, Rubin LJ, Galie N. Pulmonary Arterial Hypertension-Related Morbidity Is Prognostic for Mortality. J Am Coll Cardiol. 2018 Feb 20;71(7):752-763. doi: 10.1016/j.jacc.2017.12.010.

  • Jansa P, Pulido T. Macitentan in Pulmonary Arterial Hypertension: A Focus on Combination Therapy in the SERAPHIN Trial. Am J Cardiovasc Drugs. 2018 Feb;18(1):1-11. doi: 10.1007/s40256-017-0260-1.

  • Mehta S, Sastry BKS, Souza R, Torbicki A, Ghofrani HA, Channick RN, Delcroix M, Pulido T, Simonneau G, Wlodarczyk J, Rubin LJ, Jansa P, Hunsche E, Galie N, Perchenet L, Sitbon O. Macitentan Improves Health-Related Quality of Life for Patients With Pulmonary Arterial Hypertension: Results From the Randomized Controlled SERAPHIN Trial. Chest. 2017 Jan;151(1):106-118. doi: 10.1016/j.chest.2016.08.1473. Epub 2016 Sep 23.

  • Simonneau G, Channick RN, Delcroix M, Galie N, Ghofrani HA, Jansa P, Le Brun FO, Mehta S, Perchenet L, Pulido T, Sastry BK, Sitbon O, Souza R, Torbicki A, Rubin LJ. Incident and prevalent cohorts with pulmonary arterial hypertension: insight from SERAPHIN. Eur Respir J. 2015 Dec;46(6):1711-20. doi: 10.1183/13993003.00364-2015. Epub 2015 Oct 22.

  • Channick RN, Delcroix M, Ghofrani HA, Hunsche E, Jansa P, Le Brun FO, Mehta S, Pulido T, Rubin LJ, Sastry BKS, Simonneau G, Sitbon O, Souza R, Torbicki A, Galie N. Effect of macitentan on hospitalizations: results from the SERAPHIN trial. JACC Heart Fail. 2015 Jan;3(1):1-8. doi: 10.1016/j.jchf.2014.07.013. Epub 2014 Nov 11.

MeSH Terms

Conditions

Pulmonary Arterial Hypertension

Interventions

macitentan

Condition Hierarchy (Ancestors)

Hypertension, PulmonaryLung DiseasesRespiratory Tract Diseases

Results Point of Contact

Title
Parisa Danaietash
Organization
Actelion Pharmaceuticals Ltd

Study Officials

  • Loic Perchenet, PhD

    Actelion

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 14, 2008

First Posted

April 17, 2008

Study Start

May 1, 2008

Primary Completion

March 1, 2012

Study Completion

April 1, 2012

Last Updated

September 28, 2015

Results First Posted

May 5, 2014

Record last verified: 2015-08

Locations