NCT04002297

Brief Summary

This is a randomized study to compare the efficacy and safety of zanubrutinib plus rituximab versus bendamustine plus rituximab in previously untreated participants with mantle cell lymphoma (MCL) who are not eligible for stem cell transplantation.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
510

participants targeted

Target at P50-P75 for phase_3

Timeline
19mo left

Started Aug 2019

Longer than P75 for phase_3

Geographic Reach
21 countries

173 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress81%
Aug 2019Dec 2027

First Submitted

Initial submission to the registry

June 27, 2019

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 28, 2019

Completed
2 months until next milestone

Study Start

First participant enrolled

August 20, 2019

Completed
7.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2027

Expected
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2027

Last Updated

September 26, 2025

Status Verified

September 1, 2025

Enrollment Period

7.5 years

First QC Date

June 27, 2019

Last Update Submit

September 25, 2025

Conditions

Keywords

MCL, NHL, BTKi

Outcome Measures

Primary Outcomes (1)

  • Progression-free survival (PFS) determined by independent central review

    PFS is defined as the time from randomization to the date of first documentation of disease progression or death, whichever occurs first.

    Up to approximately 7 years

Secondary Outcomes (9)

  • PFS by investigator assessment

    Up to approximately 7 years

  • Overall response rate (ORR)

    Up to approximately 7 years

  • Duration of response (DOR)

    Up to approximately 7 years

  • Overall survival (OS)

    Up to approximately 7 years

  • Time to Response (TTR)

    Up to approximately 7 years

  • +4 more secondary outcomes

Study Arms (2)

Arm A: zanubrutinib plus rituximab

EXPERIMENTAL

Participants will receive zanubrutinib plus rituximab, followed by zanubrutinib monotherapy until Independent Review Committee (IRC)-confirmed disease progression.

Drug: zanubrutinibDrug: rituximab

Arm B: bendamustine plus rituximab

ACTIVE COMPARATOR

Participants will receive bendamustine plus rituximab, followed by observation.

Drug: bendamustineDrug: rituximab

Interventions

Administered as two 80 mg capsules by mouth twice a day

Also known as: BGB-3111, Brukinsa
Arm A: zanubrutinib plus rituximab

Administered intravenously at a dose of 90 mg/m2/day on Days 1 and 2 of Cycles 1 to 6

Arm B: bendamustine plus rituximab

Administered intravenously at a dose of 375 mg/m2 on Day 1 of Cycles 1 to 6

Arm A: zanubrutinib plus rituximabArm B: bendamustine plus rituximab

Eligibility Criteria

Age60 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • ≥70 years of age at the time of informed consent, OR ≥60 and \<70 years of age with comorbidities precluding autologous stem cell transplantation
  • Histologically confirmed diagnosis of MCL
  • No prior systemic treatments for MCL
  • Measurable disease by CT/MRI
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0-2
  • Adequate marrow and organ function

You may not qualify if:

  • Known central nervous system involvement by lymphoma
  • Participants for whom the goal of therapy is tumor debulking prior to stem cell transplant
  • Clinically significant cardiovascular disease
  • History of severe bleeding disorder
  • Unable to swallow capsules or disease significantly affecting gastrointestinal function
  • Active fungal, bacterial and/or viral infection requiring systemic therapy
  • Requires ongoing treatment with a strong CYP3A inhibitor or inducer

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (176)

Chao Family Comprehensive Cancer Center

Orange, California, 92868, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Beth Israel Deaconess Medical Center (Bidmc)

Boston, Massachusetts, 02215-5400, United States

Location

University of Michigan Health System

Ann Arbor, Michigan, 48109, United States

Location

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89169, United States

Location

Icahn School of Medicine At Mount Sinai

New York, New York, 10029, United States

Location

Clinical Research Alliance, Inc

Westbury, New York, 11590, United States

Location

Providence Portland Medical Center

Portland, Oregon, 97213, United States

Location

West Penn Hospital

Pittsburgh, Pennsylvania, 15224, United States

Location

The University of Texas Md Anderson Cancer Center

Houston, Texas, 77030-4009, United States

Location

Joe Arrington Cancer Research and Treatment Center

Lubbock, Texas, 79410, United States

Location

Seattle Cancer Care Alliance

Seattle, Washington, 98109, United States

Location

Canberra Hospital

Garran, Australian Capital Territory, 2605, Australia

Location

Concord Repatriation General Hospital

Concord, New South Wales, 2139, Australia

Location

The Tweed Valley Hospital

Cudgen, New South Wales, 2487, Australia

Location

Saint Vincents Hospital Sydney

Darlinghurst, New South Wales, 2010, Australia

Location

Gosford Hospital

Gosford, New South Wales, 2250, Australia

Location

Calvary Mater Newcastle

Waratah, New South Wales, 2298, Australia

Location

Sunshine Coast Hospital and Health Service

Birtinya, Queensland, 4575, Australia

Location

Icon Cancer Foundation

South Brisbane, Queensland, 4101, Australia

Location

Flinders Medical Centre

Bedford PK, South Australia, 5042, Australia

Location

Royal Hobart Hospital

Hobart, Tasmania, 7000, Australia

Location

Monash Health

Clayton, Victoria, 3168, Australia

Location

St Vincents Hospital Melbourne

Fitzroy, Victoria, 3065, Australia

Location

Peninsula Private Hospital

Frankston, Victoria, 3199, Australia

Location

Barwon Health the Geelong Hospital

Geelong, Victoria, 3220, Australia

Location

Royal Perth Hospital

Perth, Western Australia, 6000, Australia

Location

Ordensklinikum Linz Gmbh Elisabethinen

Linz, 4020, Austria

Location

Universitatsklinik Fur Innere Medizin Iii Universitatsklinikum Der Pmu Landeskrankenhaus Salzburg

Salzburg, 5020, Austria

Location

Medical University Vienna Oncology

Vienna, 1090, Austria

Location

Az Sint Jan Brugge

Bruges, 8000, Belgium

Location

Universitair Ziekenhuis Brussel

Brussels, 1090, Belgium

Location

Uz Antwerpen

Edegem, 2650, Belgium

Location

Az Groeninge Campus Loofstraat

Kortrijk, 8500, Belgium

Location

Centre Hospitalier Universitaire (Chu) de Liege Site Du Sart Tilman

Liège, 4000, Belgium

Location

Centre Hospitalier Universitaire Universite Catholique de Louvain Site Godinne

Yvoir, 5530, Belgium

Location

The Ottawa Hospital

Ottawa, Ontario, K1H 8M2, Canada

Location

Ciusss de Lestrie Chus

Sherbrooke, Quebec, J1H 5N4, Canada

Location

Peking University Peoples Hospital

Beijing, Beijing Municipality, 100044, China

Location

Beijing Friendship Hospital, Capital Medical University

Beijing, Beijing Municipality, 100050, China

Location

Fujian Medical University Union Hospital

Fuzhou, Fujian, 350001, China

Location

Quanzhou First Affliated Hospital of Fujian Medical University

Quanzhou, Fujian, 362000, China

Location

Sun Yat Sen University Cancer Center

Guangzhou, Guangdong, 510060, China

Location

Guangdong Provincial Peoples Hospital

Guangzhou, Guangdong, 510080, China

Location

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong, 510515, China

Location

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, 150000, China

Location

Henan Cancer Hospital

Zhengzhou, Henan, 450000, China

Location

Tongji Hospital of Tongji Medical College Huazhong University of Science and Technology

Wuhan, Hubei, 430030, China

Location

Hunan Cancer Hospital

Changsha, Hunan, 410013, China

Location

Nanjing Drum Tower Hospital,the Affiliated Hospital of Nanjing University Medical School

Nanjing, Jiangsu, 210008, China

Location

Jiangsu Province Hospital

Nanjing, Jiangsu, 210029, China

Location

The Affiliated Hospital of Xuzhou Medical University

Xuzhou, Jiangsu, 221000, China

Location

The First Affiliated Hospital of Nanchang University Branch Donghu

Nanchang, Jiangxi, 330006, China

Location

Jilin Cancer Hospital

Changchun, Jilin, 130021, China

Location

The First Hospital of Jilin University

Changchun, Jilin, 130021, China

Location

Shengjing Hospital of China Medical University

Shenyang, Liaoning, 110004, China

Location

Fudan University Shanghai Cancer Center

Shanghai, Shanghai Municipality, 200000, China

Location

Shanghai East Hospital

Shanghai, Shanghai Municipality, 200120, China

Location

West China Hospital, Sichuan University

Chengdu, Sichuan, 610041, China

Location

Institute of Hematology and Hospital of Blood Disease

Tianjin, Tianjin Municipality, 300020, China

Location

Tianjin Medical University Cancer Institute and Hospital

Tianjin, Tianjin Municipality, 300060, China

Location

Affiliated Cancer Hospital of Xinjiang Medical University

Ürümqi, Xinjiang, 830000, China

Location

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310003, China

Location

Zhejiang Cancer Hospital

Hangzhou, Zhejiang, 310022, China

Location

Hwa Mei Hospital, University of Chinese Academy of Sciences (Ningbo No Hospital)

Ningbo, Zhejiang, 315000, China

Location

Centre de Lutte Contre Le Cancer Institut Bergonie

Bordeaux, 33076, France

Location

Chru de Brest Hospital Morvan

Brest, 29200, France

Location

Chu Dijon

Dijon, J4V 2H1, France

Location

Chu Grenoble Alpes

Grenoble, 38043, France

Location

Centre Hospitalier Le Mans

Le Mans, 72037, France

Location

Hopital Claude Huriez Chu Lille

Lille, 59000, France

Location

Institut Paoli Calmettes

Marseille, 13009, France

Location

Centre Hospitalier Universitaire Nantes Hotel Dieu

Nantes, 44093, France

Location

Institut Curie

Paris, 75005, France

Location

Necker University Hospital

Paris, 75015, France

Location

Chu Hopital Lyon Sud

PierreBenite, 69495, France

Location

Centre Hospitalier Universitaire de Poitier Hopital de La Miletrie Hopital Jean Bernard

Poitiers, 86000, France

Location

Ch Cornouaille

Quimper, 29000, France

Location

Iuc Toulouse Oncopole

Toulouse, 31059, France

Location

Uniklinik Koln (Aor)

Cologne, 50937, Germany

Location

Universitatsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Dept of Medicine Iii, University Hospitallmu

Munich, 81377, Germany

Location

Universitaetsklinikum Ulm, Innere Medizin Iii

Ulm, 89081, Germany

Location

Petrus Krankenhaus Wuppertal

Wuppertal, 42283, Germany

Location

Cork University Hospital

Cork, t12DC4A, Ireland

Location

Mater Misericordiae University Hospital

Dublin, D7, Ireland

Location

St Jamess Hospital

Dublin, D8, Ireland

Location

University Hospital Galway

Galway, H91 YR71, Ireland

Location

University Hospital Limerick

Limerick, V94F858, Ireland

Location

University Hospital Waterford

Waterford, X91 ER8E, Ireland

Location

Azienda Ospedaliera Nazionale Ssantonio E Biagio E Cesare Arrigo

Alessandria, 15121, Italy

Location

Policlinico Sorsola Malpighi, Aou Di Bologna

Bologna, 40138, Italy

Location

Azienda Ospedaliera Universitaria San Martino

Genova, 16132, Italy

Location

Niguarda Cancer Center Division of Hematology

Milan, 20162, Italy

Location

Aou Maggiore Della Carita

Novara, 28100, Italy

Location

Aoor Villa Sofia Cervello

Palermo, 90146, Italy

Location

Aou Pisana, Stabilimento Di Santa Chiara

Pisa, 56126, Italy

Location

Unita Di Ematologia, Dipartimento Di Ematologia Ed Oncologia

Ravenna, 48121, Italy

Location

Azienda Unita Sanitaria Locale Irccs

Reggio Emilia, 42123, Italy

Location

Universita Degli Studi La Sapienza

Roma, 00161, Italy

Location

Aou Senese Policlinico Santa Maria Alle Scotte

Siena, 53100, Italy

Location

Ao Citta Della Salute E Della Scienza Di Torino Presidio O

Torino, 10126, Italy

Location

University of Verona

Verona, 37142, Italy

Location

National Hospital Organization Nagoya Medical Center

Nagoya, Aichi-ken, 460-0001, Japan

Location

Toyohashi Municipal Hospital

Toyohashi, Aichi-ken, 441-8570, Japan

Location

Chiba Cancer Center

Chiba, Chiba, 260-8717, Japan

Location

Kurume University Hospital

Kurume, Fukuoka, 830-0011, Japan

Location

Hiroshima Red Cross Hospital and Atomic Bomb Survivors Hospital

Hiroshima, Hiroshima, 730-8619, Japan

Location

Kanagawa Cancer Center

Yokohama, Kanagawa, 241-8515, Japan

Location

National Hospital Organization Kumamoto Medical Center

Kumamoto, Kumamoto, 860-0008, Japan

Location

Tohoku University Hospital

Sendai, Miyagi, 980-8574, Japan

Location

Kurashiki Central Hospital

Kurashikishi, Okayama-ken, 710-8602, Japan

Location

Osaka Red Cross Hospital

Osakashi, Osaka, 543-8555, Japan

Location

National Cancer Center Hospital

Chuoku, Tokyo, 104-0045, Japan

Location

University Hospital, Kyoto Prefectural Univ of Medicine

Kyoto, 602-8566, Japan

Location

National Hospital Organization Okayama Medical Center

Okayama, 701-1192, Japan

Location

Osaka Metropolitan University Hospital

Osaka, 545-8586, Japan

Location

Tokyo Medical and Dental University Hospital

Tokyo, 113-8519, Japan

Location

Yokohama Municipal Citizens Hospital

Yokohama, 221-0855, Japan

Location

Admiraal de Ruijter Ziekenhuis

Goes, 4462 RA, Netherlands

Location

University of Medical Center Groningen (Umcg)

Groningen, 9713 GZ, Netherlands

Location

St Antonius Ziekenhuis, Randd Interne Geneeskunde (F)

Nieuwegein, 3435 CM, Netherlands

Location

Albert Schweitzer Ziekenhuis

Nijmegen, 6525 GA, Netherlands

Location

Erasmus Mc

Rotterdam, 3015 GD, Netherlands

Location

Hagaziekenhuis

The Hague, 2545 CH, Netherlands

Location

Christchurch Hospital (Canterbury Health Laboratories)

Christchurch, 8011, New Zealand

Location

Tauranga Hospital

Tauranga, 3112, New Zealand

Location

Szpital Uniwersytecki Nr Im Dr Jana Biziela

Bydgoszcz, 85-168, Poland

Location

Silesian Healthy Blood Clinic

Chorzów, 41-503, Poland

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, 80-952, Poland

Location

Copernicus Podmiot Leczniczy Sp Z Oo Wojewodzkie Centrum Onkologii

Gdask, 80-219, Poland

Location

Szpitale Pomorskie Spolka Z Ograniczona Odpowiedzialnoscia

Gdynia, 81-519, Poland

Location

Pratia McM Krakow

Krakow, 30-727, Poland

Location

Wojewodzki Szpital Specjalistyczny W Legnicy

Legnica, 59-220, Poland

Location

Wielospecjalistyczne Centrum Onkologii I Traumatologii Im M Kopernika W Lodzi

Lodz, 93-510, Poland

Location

Centrum Onkologii Ziemi Lubelskiej

Lublin, 20-090, Poland

Location

Instytut Hematologii I Transfuzjologii W Warszawie

Warsaw, 02-776, Poland

Location

Specjalistyczny Szpital Im Dr Alfreda Sokolowskiego

Wałbrzych, 58-309, Poland

Location

Uniwersytecki Szpital Kliniczny Im Jana Mikulicza Radeckiego We Wroclawiu

Wroclaw, 50-556, Poland

Location

Instituto Portugues Oncologia de Lisboa Francisco Gentil, Epe

Lisbon, 1099-023, Portugal

Location

Chuln Hospital de Santa Maria

Lisbon, 1649-035, Portugal

Location

Centro Hospitalar Universitario Porto

Porto, 4099-001, Portugal

Location

Instituto Portugues de Oncologia Do Porto Francisco Gentil, Epe

Porto, 4200-072, Portugal

Location

Institutul Clinic Fundeni

Bucharest, 022328, Romania

Location

Institutul Regional de Oncologie Iasi

Iași, 700483, Romania

Location

Clinical Hospital, Sp Botkin

Moscow, Moscow, 125284, Russia

Location

Fgu Russian Scientific Research Institute of Hematology and Transfusiology

Saint Petersburg, Sankt-Peterburg, 191024, Russia

Location

Leningrad Regional Clinic and Hospital

Saint Petersburg, Sankt-Peterburg, 194291, Russia

Location

Gbuz Mmcc Kommunarka Dzm

Moscow, 142770, Russia

Location

Hospital Universitario Vall Dhebron

Barcelona, 08035, Spain

Location

Institut Catala Doncologia

Barcelona, 08908, Spain

Location

Ico Hug Trias I Pujol

Barcelona, 08916, Spain

Location

Ico Girona

Girona, 17007, Spain

Location

Hospital Universitario Gregorio Maranon

Madrid, 28009, Spain

Location

Md Anderson Cancer Center Madrid Spain

Madrid, 28033, Spain

Location

Start Madrid Fundacion Jimenez Diaz

Madrid, 28040, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Regional Universitario de Malaga

Málaga, 29010, Spain

Location

Hospital Universitario Virgen Del Rocio

Seville, 41013, Spain

Location

National Cheng Kung University Hospital

Tainan, 704, Taiwan

Location

Chi Mei Hospital Liouying

Tainan, 736, Taiwan

Location

Tri Service General Hospital

Taipei, 114, Taiwan

Location

Dr Abdurrahman Yurtaslan Oncology Teaching and Research Hospital

Ankara, 06620, Turkey (Türkiye)

Location

Hematoloji Ve Hematolik Onkoloji Tani Ve Tedavi Merezi

Ankara, 06700, Turkey (Türkiye)

Location

Gazi University

Ankara, 6500, Turkey (Türkiye)

Location

Tr Trakya University Health Research and Application Center (Hospital)

Edirne, 22030, Turkey (Türkiye)

Location

Vkv American Hospital

Istanbul, 34365, Turkey (Türkiye)

Location

Mersin Universitesi Tip Fakultesi Hastanesi

Mersin, 33000, Turkey (Türkiye)

Location

Cherkasy Regional Oncology Dispensary

Cherkasy, 18009, Ukraine

Location

Municipal Non Profit Enterprise City Clinical Hospital

Dnipro, 49102, Ukraine

Location

National Cancer Institute

Kiev, 3022, Ukraine

Location

Si Institute of Blood Pathology and Transfusion Medicine Nams of Ukraine, Hematology Department

Lviv, 79044, Ukraine

Location

Aneurin Bevan University Health Board

Abergavenny, NP7 7EG, United Kingdom

Location

Birmingham Heartlands Hospital

Birmingham, B9 5SS, United Kingdom

Location

Russells Hall Hopsital

Dudley, DY1 2HQ, United Kingdom

Location

Royal Marsden Nhs Foundation Royal Marsden Hospital

Sutton, SM2 5PT, United Kingdom

Location

Related Publications (1)

  • Dreyling M, Tam CS, Wang M, Smith SD, Ladetto M, Huang H, Novotny W, Co M, Romano A, Holmgren E, Huang J, Gouill SL. A Phase III study of zanubrutinib plus rituximab versus bendamustine plus rituximab in transplant-ineligible, untreated mantle cell lymphoma. Future Oncol. 2021 Jan;17(3):255-262. doi: 10.2217/fon-2020-0794. Epub 2020 Sep 28.

MeSH Terms

Conditions

Lymphoma, Mantle-CellLymphoma, Non-Hodgkin

Interventions

zanubrutinibBendamustine HydrochlorideRituximab

Condition Hierarchy (Ancestors)

LymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

ButyratesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsBenzimidazolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Study Director

    BeiGene

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 27, 2019

First Posted

June 28, 2019

Study Start

August 20, 2019

Primary Completion (Estimated)

March 1, 2027

Study Completion (Estimated)

December 1, 2027

Last Updated

September 26, 2025

Record last verified: 2025-09

Data Sharing

IPD Sharing
Will share

BeiGene shares data on completed studies responsibly and provides qualified scientific and medical researchers access to data and supporting documentation for clinical trials in dossiers for medicines and indications after submission and approval in the United States, China, and Europe. Clinical trials supporting subsequent local approvals, new indications, or combination products are eligible for sharing once corresponding regulatory approvals are achieved. BeiGene shares data only when permitted by applicable data privacy and security laws and regulations, when it is feasible to do so without compromising the privacy of study participants, and other considerations. Qualified researchers with appropriate competencies who are engaged in novel scientific research may submit a request for participant-level data with a research proposal for BeiGene review. Research teams must include a biostatistician and sign a Data Sharing Agreement prior to receiving access to clinical trial data.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
See plan description
Access Criteria
See plan description
More information

Locations