NCT03836040

Brief Summary

This study will evaluate the efficacy and safety of erenumab in migraine prevention in children (6 to \<12 years) and adolescents (12 to \<18 years) with episodic migraine. The study hypothesis is that in pediatric participants with episodic migraine, the combined erenumab dose group has a greater reduction from baseline to week 9 through week 12 (month 3) in monthly migraine days (MMDs) when compared with placebo in the double-blind treatment phase (DBTP).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
457

participants targeted

Target at P50-P75 for phase_3

Timeline
6mo left

Started Jul 2019

Longer than P75 for phase_3

Geographic Reach
16 countries

119 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress93%
Jul 2019Nov 2026

First Submitted

Initial submission to the registry

January 29, 2019

Completed
13 days until next milestone

First Posted

Study publicly available on registry

February 11, 2019

Completed
5 months until next milestone

Study Start

First participant enrolled

July 19, 2019

Completed
6.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 19, 2025

Completed
12 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 15, 2026

Expected
Last Updated

December 23, 2025

Status Verified

December 1, 2025

Enrollment Period

6.3 years

First QC Date

January 29, 2019

Last Update Submit

December 19, 2025

Conditions

Keywords

MigraineHeadachePreventionPediatricEpisodic Migraine

Outcome Measures

Primary Outcomes (1)

  • Change from baseline in MMDs

    To evaluate the effect of erenumab compared with placebo on the change in MMDs from baseline to week 9 through week 12 (month 3) of the double-blind treatment period (DBTP).

    Baseline through week 12 of the double blind treatment phase

Secondary Outcomes (13)

  • Change in monthly headache days from baseline

    Baseline through week 12 of the double blind treatment phase

  • Proportion of participants with at least 50% reduction in MMDs from baseline

    Baseline through week 12 of the double blind treatment phase

  • Change in MMDs from baseline to the average of the first 3 months

    Baseline through week 12 of the double blind treatment phase

  • Change in monthly average severity of migraine attacks from baseline (measured with a visual analogue scale)

    Baseline through week 12 of the double blind treatment phase

  • Change from baseline in migraine-related disability and productivity

    Baseline through week 12 of the double blind treatment phase

  • +8 more secondary outcomes

Study Arms (3)

Dose level 1

EXPERIMENTAL

Participants will be randomized to one of two doses determined by their body weight at Day 1. Participants who enrolled under the original protocol or protocol amendment 1 will be identified as group 1. Those enrolled under protocol amendment 2 will be identified as group 2.

Drug: Erenumab Dose 1Drug: Erenumab Dose 2

Dose level 2

EXPERIMENTAL

Participants will be randomized to one of two doses determined by their body weight at Day 1. Participants who enrolled under the original protocol or protocol amendment 1 will be identified as group 1. Those enrolled under protocol amendment 2 will be identified as group 2.

Drug: Erenumab Dose 2Drug: Erenumab Dose 3

Placebo

PLACEBO COMPARATOR

Participants will be randomized to a placebo comparator.

Other: Placebo

Interventions

Participants in the low body-weight group at day 1 and who are randomized to Dose Level 1 will receive this dose.

Also known as: AMG334, Aimovig®
Dose level 1

Participants in the low body-weight group at day 1 who are randomized to Dose Level 2 and subjects in the high body-weight group at day 1 who are randomized to Dose Level 1 will receive this dose.

Also known as: AMG 334, Aimovig®
Dose level 1Dose level 2

Participants in the high body-weight group at day 1 who are randomized to Dose Level 2 will receive this dose.

Also known as: AMG 334, Aimovig®
Dose level 2
PlaceboOTHER

Placebo matching dose for erenumab dose 1, 2 and 3.

Placebo

Eligibility Criteria

Age6 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Children (6 to less than 12 years of age) or adolescent (12 to less than 18 years of age) at the time of signing, if developmentally appropriate, the formal assent to participate to the study.
  • Participant's parent or legal representative has provided written informed consent before initiation of any study-specific activities/procedures.
  • History of migraine (with or without aura) for greater than or equal to 12 months before screening according to the IHS Classification ICHD-3 (Headache Classification Committee of the International Headache Society, 2013) based on medical records and/or participant self-report or parents' or legal representative's report.
  • The following ICHD-3 specifications for pediatric migraine (participants aged less than 18 years), should be considered for the diagnosis of migraine:
  • Attacks may last 2 to 72 hours.
  • Migraine headache is more often bilateral than in adults; unilateral pain usually emerges in late adolescence or early adult life.
  • Migraine headache is usually frontotemporal. Occipital headache in children is rare and calls for diagnostic caution.
  • A subset of otherwise typical participants have facial location of pain, which is called 'facial migraine' in the literature; there is no evidence that these participants form a separate subgroup of migraine participants.
  • In young children, photophobia and phonophobia may be inferred from their behavior.
  • History of less than 15 headache days per month of which greater than or equal to 4 headache days were assessed by the participant as migraine days in each of the 3 months prior to screening (refer to Section 5.6 for definition of migraine day).
  • Criteria to be assessed prospectively during the 4-week baseline phase and confirmed before randomizing the participant into the DBTP:
  • Migraine frequency: greater than or equal 4 and less than 15 migraine days based on the eDiary data during the last 28 days of the baseline phase if greater than 28 days in duration
  • Headache frequency: less than 15 headache days based on the eDiary data during the last 28 days of the baseline phase if greater than 28 days in duration.
  • Demonstrated at least 80% compliance with the eDiary based on the last 28 days of the baseline period, if greater than 28 days in duration (eg, completing eDiary items for at least 23 out of the last 28 days of the baseline phase).

You may not qualify if:

  • History of cluster headache or hemiplegic migraine headache.
  • No therapeutic response with greater than 2 of the following 10 medication categories for prophylactic treatment of migraine after an adequate therapeutic trial. These medication categories are:
  • Category 1: beta blockers (eg, propranolol, atenolol, bisoprolol, metoprolol, nadolol, nebivolol, pindolol, timolol)
  • Category 2: tricyclic antidepressants (eg, amitriptyline, nortriptyline, protriptyline)
  • Category 3: topiramate
  • Category 4: divalproex sodium, sodium valproate
  • Category 5: serotonin-norepinephrine reuptake inhibitors (eg, venlafaxine, desvenlafaxine, duloxetine, milnacipran)
  • Category 6: cyproheptadine
  • Category 7: flunarizine, cinnarizine
  • Category 8: botulinum toxin
  • Category 9: lisinopril/candesartan
  • Category 10: medications targeting the CGRP pathway.
  • No therapeutic response is defined as no reduction in headache frequency, duration, or severity after administration of the medication for at least 6 weeks at the generally-accepted therapeutic dose(s) based on the investigator's assessment.
  • The following scenarios do not constitute lack of therapeutic response:
  • Lack of sustained response to a medication.
  • +22 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (119)

Paradigm Clinical Research Center Inc

San Diego, California, 92108, United States

Location

Childrens Hospital Colorado

Aurora, Colorado, 80045, United States

Location

Colorado Springs Neurological Associates

Colorado Springs, Colorado, 80907, United States

Location

New England Institute for Clinical Research

Stamford, Connecticut, 06905, United States

Location

Childrens National Health System

Washington D.C., District of Columbia, 20010, United States

Location

Northwest Florida Clinical Research Group Limited Liability Company

Gulf Breeze, Florida, 32561, United States

Location

Nicklaus Childrens Hospital

Miami, Florida, 33155, United States

Location

Pediatric Epilepsy and Neurology Specialists

Tampa, Florida, 33609, United States

Location

TrueBlue Clinical Research

Tampa, Florida, 33612, United States

Location

Premiere Research Institute

West Palm Beach, Florida, 33407, United States

Location

Rare Disease Research Center Pediatrics

Atlanta, Georgia, 30329, United States

Location

CenExel iResearch, LLC

Savannah, Georgia, 31405, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Chicago Headache Center and Research Institute

Chicago, Illinois, 60657, United States

Location

Josephson Wallack Munshower Neurology

Indianapolis, Indiana, 46256, United States

Location

University of Maryland, Baltimore

Baltimore, Maryland, 21201, United States

Location

New England Regional Headache Center Inc

Worcester, Massachusetts, 14226, United States

Location

Michigan Head Pain and Neurological Institute

Ann Arbor, Michigan, 48104, United States

Location

Clinical Research Institute Inc

Minneapolis, Minnesota, 55402, United States

Location

Childrens Mercy Hospital and Clinics

Kansas City, Missouri, 64108, United States

Location

Mercy Research

St Louis, Missouri, 63141, United States

Location

Velocity Clinical Research, Inc

Grand Island, Nebraska, 68803, United States

Location

Dent Neurosciences Research Center

Amherst, New York, 14226, United States

Location

Modern Migraine MD

New York, New York, 10001, United States

Location

Columbia University Irving Medical Center

New York, New York, 10032, United States

Location

Cincinnati Childrens Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Nationwide Childrens Hospital

Columbus, Ohio, 43205, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Childrens Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

Preferred Primary Care Physicians, Inc

Pittsburgh, Pennsylvania, 15236, United States

Location

Palmetto Gastroenterology Clinical Research, LLC

Summerville, South Carolina, 29486, United States

Location

Child Neurology Consultants of Austin

Austin, Texas, 78757, United States

Location

Helios Clinical Research Inc

Burleson, Texas, 76028, United States

Location

Stryde Consulting LLC

Frisco, Texas, 75033, United States

Location

Childrens Specialty Group

Norfolk, Virginia, 23507, United States

Location

Vaught Neurological Services

Crab Orchard, West Virginia, 25827, United States

Location

Marshfield Clinic

Marshfield, Wisconsin, 54449, United States

Location

Universitair Ziekenhuis Brussel

Brussels, 1090, Belgium

Location

Algemeen Ziekenhuis Sint-Maarten

Mechelen, 2800, Belgium

Location

Docteur Simona Sava

Saint-Nicolas, 4420, Belgium

Location

Stollery Childrens Hospital

Edmonton, Alberta, T6G 1C9, Canada

Location

London Health Sciences Centre

London, Ontario, N6A 4G5, Canada

Location

Childrens Hospital of Eastern Ontario

Ottawa, Ontario, K1H 8L1, Canada

Location

The Hospital For Sick Children

Toronto, Ontario, M5G 1X8, Canada

Location

Fundacion Centro de Investigacion Clinica

Medellín, Antioquia, 050021, Colombia

Location

Servicios de Salud Ips Suramericana Sas - Ips Sura Industriales

Medellín, Antioquia, 50021, Colombia

Location

Institucion Prestadora de Servicios de Salud Sociedad Médica Rionegro SA Somer SA

Rionegro, Antioquia, 054040, Colombia

Location

Solano y Terront Servicios Medicos SAS - Unidad Integral de Endocrinologia Uniendo

Bogota, Cundinamarca, 110221, Colombia

Location

Cafam

Bogota, Cundinamarca, 111211, Colombia

Location

Fundacion Hospital Infantil Universitario De San Jose

Bogota, Cundinamarca, 111221, Colombia

Location

Fundacion cardiovascular de Colombia

Bucaramanga, Santander Department, 681017, Colombia

Location

Terveystalo Pulssi

Turku, 20100, Finland

Location

Charite - Universitaetsmedizin Berlin, Campus Virchow

Berlin, 13353, Germany

Location

Universitaetsklinikum Essen

Essen, 45147, Germany

Location

Universitaetsklinikum Greifswald

Greifswald, 17475, Germany

Location

Schmerzklinik Kiel

Kiel, 24149, Germany

Location

Arzneimittelforschung Leipzig GmbH

Leipzig, 04107, Germany

Location

Dr Kenessey Albert Korhaz - Rendelointezet

Balassagyarmat, 2660, Hungary

Location

Dr Altmann Anna egyeni vallalkozo

Budapest, 1026, Hungary

Location

High Tech Medical Kft

Budapest, 1027, Hungary

Location

Semmelweis Egyetem

Budapest, 1094, Hungary

Location

Debreceni Egyetem Klinikai Kozpont

Debrecen, 4032, Hungary

Location

Borsod-Abauj-Zemplen Varmegyei Kozponti Korhaz es Egyetemi Oktatokorhaz

Miskolc, 3526, Hungary

Location

Fondazione IRCCS Istituto Neurologico Carlo Besta

Milan, 20133, Italy

Location

Azienda di Rilievo Nazionale e Alta Specializzazione Civico Di Cristina Benfratelli

Palermo, 90134, Italy

Location

Fondazione Istituto Neurologico Nazionale C Mondino IRCCS

Pavia, 27100, Italy

Location

IRCCS Ospedale Pediatrico Bambino Gesu

Roma, 00165, Italy

Location

Josai Kids Clinic

Nagoya, Aichi-ken, 451-0031, Japan

Location

Medical Corporation Seikokai Takanoko Hospital

Matsuyama, Ehime, 790-0925, Japan

Location

Hiroshima City Hiroshima Citizens Hospital

Hiroshima, Hiroshima, 730-8518, Japan

Location

Kitami Clinic

Sapporo, Hokkaido, 060-0004, Japan

Location

Konan Medical Center

Kobe, Hyōgo, 658-0064, Japan

Location

Umenotsuji Clinic

Kochi, Kochi, 780-8011, Japan

Location

Kumamoto City Hospital

Kumamoto, Kumamoto, 862-8505, Japan

Location

Tatsuoka Neurology Clinic

Kyoto, Kyoto, 600-8811, Japan

Location

Japanese Red Cross Kyoto Daiichi Hospital

Kyoto, Kyoto, 605-0981, Japan

Location

Ishikawa Clinic

Kyoto, Kyoto, 606-0851, Japan

Location

Sendai Headache and Neurology Clinic

Sendai, Miyagi, 982-0014, Japan

Location

Tominaga Hospital

Osaka, Osaka, 556-0017, Japan

Location

Saitama Neuropsychiatric Institute

Saitama-shi, Saitama, 338-8577, Japan

Location

Tokyo Medical University Hospital

Shinjuku-ku, Tokyo, 160-0023, Japan

Location

Keio University Hospital

Shinjuku-ku, Tokyo, 160-8582, Japan

Location

Nagamitsu Clinic

Hofu-shi, Yamaguchi, 747-0802, Japan

Location

Nagaseki Headache Clinic

Kai-shi, Yamanashi, 400-0124, Japan

Location

Uniwersytecki Dzieciecy Szpital Kliniczny im Ludwika Zamenhofa w Bialymstoku

Bialystok, 15-274, Poland

Location

AthleticoMed

Bydgoszcz, 85-752, Poland

Location

Uniwersyteckie Centrum Kliniczne

Gdansk, 80-952, Poland

Location

Instytut Centrum Zdrowia Matki Polki

Lodz, 93-338, Poland

Location

Centrum Medyczne Luxmed Spzoo

Lublin, 20-109, Poland

Location

Centrum Medyczne Hope Clinic Sebastian Szklener

Lublin, 20-701, Poland

Location

Uniwersytecki Szpital Kliniczny w Poznaniu

Poznan, 60-355, Poland

Location

Clinical Research Center Spzoo Medic-R Spolka Komandytowa

Poznan, 61-731, Poland

Location

Dr Sekowska Leczenie Bolu

Warsaw, 01-018, Poland

Location

Next Stage Spzoo

Warsaw, 02-121, Poland

Location

Migre Polskie Centrum Leczenia Migreny Anna Gryglas-Dworak

Wroclaw, 52-210, Poland

Location

Unidade Local de Saude de Coimbra, EPE - Hospital Pediatrico de Coimbra

Coimbra, 3000-602, Portugal

Location

Unidade Local de Saude de Sao Jose, EPE - Hospital Dona Estefania

Lisbon, 1169-045, Portugal

Location

Hospital da Luz, SA

Lisbon, 1500-650, Portugal

Location

Unidade Local de Saude de Santa Maria, EPE - Hospital de Santa Maria

Lisbon, 1649-035, Portugal

Location

Puerto Rico Health and Wellness Institute

Dorado, 00646, Puerto Rico

Location

FSBI Russian Children Clinical Hospital of the MoH RF

Moscow, 119571, Russia

Location

LLC clinic Chaika

Moscow, 125047, Russia

Location

LLC Sibneyromed

Novosibirsk, 630004, Russia

Location

LLC Medical Technologies

Saint Petersburg, 191025, Russia

Location

Hospital Universitario Virgen del Rocio

Seville, Andalusia, 41013, Spain

Location

Hospital Universitari Vall d Hebron

Barcelona, Catalonia, 08035, Spain

Location

Hospital de la Santa Creu i Sant Pau

Barcelona, Catalonia, 08041, Spain

Location

Clinica Universidad de Navarra

Pamplona, Navarre, 31008, Spain

Location

Hospital Universitari i Politecnic La Fe

Valencia, Valencia, 46026, Spain

Location

Universitaets-Kinderspital beider Basel

Basel, 4031, Switzerland

Location

Kopfwehzentrum Hirslanden

Zollikon, 8702, Switzerland

Location

Noahs Ark Childrens Hospital for Wales

Cardiff, CF14 4XW, United Kingdom

Location

Royal Hospital for Children

Glasgow, G51 4TF, United Kingdom

Location

Alder Hey Childrens Hospital

Liverpool, L12 2AP, United Kingdom

Location

Evelina Childrens Hospital

London, SE1 7EU, United Kingdom

Location

Great Ormond Street Hospital for Children

London, WC1N 3JH, United Kingdom

Location

4 Medical Clinical Solutions Manchester

Manchester, M27 8FF, United Kingdom

Location

Oxford Childrens Hospital

Oxford, OX3 9DU, United Kingdom

Location

Related Links

MeSH Terms

Conditions

Migraine DisordersHeadache

Interventions

erenumab

Condition Hierarchy (Ancestors)

Headache Disorders, PrimaryHeadache DisordersBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesPainNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Study Officials

  • MD

    Amgen

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 29, 2019

First Posted

February 11, 2019

Study Start

July 19, 2019

Primary Completion

November 19, 2025

Study Completion (Estimated)

November 15, 2026

Last Updated

December 23, 2025

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will share

De-identified individual patient data for variables necessary to address the specific research question in an approved data sharing request.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
Data sharing requests relating to this study will be considered beginning 18 months after the study has ended and either 1) the product and indication (or other new use) have been granted marketing authorization in both the US and Europe or 2) clinical development for the product and/or indication discontinues and the data will not be submitted to regulatory authorities. There is no end date for eligibility to submit a data sharing request for this study.
Access Criteria
Qualified researchers may submit a request containing the research objectives, the Amgen product(s) and Amgen study/studies in scope, endpoints/outcomes of interest, statistical analysis plan, data requirements, publication plan, and qualifications of the researcher(s). In general, Amgen does not grant external requests for individual patient data for the purpose of re-evaluating safety and efficacy issues already addressed in the product labelling. Requests are reviewed by a committee of internal advisors, and if not approved, may be further arbitrated by a Data Sharing Independent Review Panel. Upon approval, information necessary to address the research question will be provided under the terms of a data sharing agreement. This may include anonymized individual patient data and/or available supporting documents, containing fragments of analysis code where provided in analysis specifications. Further details are available at the URL below.
More information

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