NCT03643965

Brief Summary

The overall aim of the study is to evaluate the efficacy, safety, and tolerability of Nefecon 16 mg per day in the treatment of patients with primary IgAN (Immunoglobulin A nephropathy) at risk of progressing to end-stage renal disease (ESRD), despite maximum tolerated treatment with renin-angiotensin system (RAS) blockade using angiotensin converting enzyme inhibitors (ACEIs) or angiotensin II type I receptor blockers (ARBs).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
365

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Sep 2018

Longer than P75 for phase_3

Geographic Reach
18 countries

137 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 8, 2018

Completed
15 days until next milestone

First Posted

Study publicly available on registry

August 23, 2018

Completed
13 days until next milestone

Study Start

First participant enrolled

September 5, 2018

Completed
4.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 10, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 10, 2023

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

December 3, 2024

Completed
Last Updated

December 3, 2024

Status Verified

November 1, 2024

Enrollment Period

4.8 years

First QC Date

August 8, 2018

Results QC Date

June 17, 2024

Last Update Submit

November 25, 2024

Conditions

Keywords

IgA Nephropathy

Outcome Measures

Primary Outcomes (2)

  • Part A: Ratio of Urine Protein to Creatinine Ratio (UPCR) at 9 Months Compared to Baseline

    Part A primary endpoint: The ratio of Urine Protein to Creatinine Ratio (UPCR) (based on 24-hour urine collections) at 9 months following the first dose of study drug compared to baseline. Ratio being: UPCR at 9 months in g/gram divided with UPCR at Baseline in g/gram

    9 months

  • Part B: Time-weighted Average of Estimated Glomerular Filtration Rate (eGFR)

    Part B Primary endpoint: Time-weighted average of estimated glomerular filtration rate (eGFR) recordings observed at each time point over 2 years. The eGFR (CKD-EPI) at 2 years (which must have been repeated to provide a second value obtained within 14 to 35 days) was the geometric mean of the 2 assessments.

    Up to 2 years and 1 month

Secondary Outcomes (11)

  • Part A: Ratio of eGFR at 9 Months

    9 months

  • Part A: Ratio of eGFR at 12 Months

    12 months

  • Part A: Ratio of Urine Albumin to Creatinine Ratio (UACR) at 9 Months

    9 months

  • Part B: Time to 30% Reduction in eGFR

    Over 2 years

  • Part B: Time to Receiving Rescue Medication.

    Over 2 years

  • +6 more secondary outcomes

Study Arms (2)

Nefecon

EXPERIMENTAL

Nefecon 16 mg once daily by mouth for 9 months.

Drug: Nefecon

Placebo oral capsule

PLACEBO COMPARATOR

Placebo oral capsule once daily by mouth for 9 months.

Drug: Placebo oral capsule

Interventions

Placebo capsules for daily administration by mouth for 9 months.

Also known as: Placebo
Placebo oral capsule

Nefecon 16 mg for daily administration by mouth for 9 months.

Also known as: Budesonide modified released capsule
Nefecon

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Female or male patients ≥18 years
  • Biopsy-verified IgA nephropathy
  • Stable dose of RAS inhibitor therapy (ACEIs and/or ARBs) at the maximum allowed dose or Maximum Tolerated Dose (MTD) according to the 2012 KDIGO (Kidney Disease: Improving Global Outcomes) guidelines
  • Urine protein creatinine ratio ≥1 g/24hr
  • eGFR ≥35 mL/min per 1.73 m2 and ≤90 mL/min per 1.73 m2 using the Chronic Kidney Diseae Epidemiology Collaboration (CKD-EPI) formula
  • Willing and able to give informed consent

You may not qualify if:

  • Systemic diseases that may cause mesangial IgA deposition.
  • Patients who have undergone a kidney transplant.
  • Patients with acute or chronic infectious disease including hepatitis, tuberculosis, human immunodeficiency virus (HIV), and chronic urinary tract infections.
  • Patients with liver cirrhosis, as assessed by the Investigator.
  • Patients with a diagnosis of type 1 or type 2 diabetes mellitus which is poorly controlled.
  • Patients with history of unstable angina, class III or IV congestive heart failure, and/or clinically significant arrhythmia, as judged by the Investigator;
  • Patients with unacceptable blood pressure control defined as a blood pressure consistently above national guidelines for proteinuric renal disease, as assessed by the Investigator
  • Patients with diagnosed malignancy within the past 5 years.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (142)

University of Alabama at Birmingham, 1720 2nd Ave South

Birmingham, Alabama, 35294-3412, United States

Location

Univ of Arizona, 1501 N Campbell Ave

Tucson, Arizona, 85724, United States

Location

Stanford University Medical Center, 777 Welch Rd

Palo Alto, California, 94304, United States

Location

Los Angeles Biomedical Research Institute at HUMC, 1124 W. Carson Street

Torrance, California, 90502, United States

Location

University of Colorado Health Science Center, 1200 East 19th Av.

Aurora, Colorado, 80045, United States

Location

Western Nephrology and Metabolic Bone Disease, PC-Westerminster, 8410 Decatur St.

Westminster, Colorado, 80031, United States

Location

Yale University School of Medicine, 330 Cedar Street

New Haven, Connecticut, 06520, United States

Location

Washington Nephrology Associates-Washington DC, 730 24th Street NW

Washington D.C., District of Columbia, 20037, United States

Location

University of Florida-Gainesville

Gainesville, Florida, 32610, United States

Location

Omega Research Maitland, 7912 Forest City Rd.

Orlando, Florida, 32810, United States

Location

Omega Research Maitland

Orlando, Florida, 32810, United States

Location

Northwestern University the Feinberg School of Medicine, 633 North St. Clair

Chicago, Illinois, 60611, United States

Location

Northshore University Health System, 2650 Ridge Av.

Evanston, Illinois, 60201, United States

Location

University of Kentucky Medical Center, 800 Rose St, Pavillion H 3rd floor

Lexington, Kentucky, 40536, United States

Location

University of Louisville-Nephrology

Louisville, Kentucky, 40202, United States

Location

Kidney Care and Transplant Services of New England, PC, 354 Birnie Av.

Springfield, Massachusetts, 01107, United States

Location

University of Minnesota, 717 Delaware St. SE

Minneapolis, Minnesota, 55414, United States

Location

Clinical Research Consultants, LLC, 3930 Washington St

Kansas City, Missouri, 64111, United States

Location

Queens Hospital Centre

Jamaica, New York, 11432, United States

Location

Icahn School of Medicine at Mount Sinai-James J. Peters VA Medical Center, One Gustave L. Levy Place

New York, New York, 10029, United States

Location

Columbia Univ Medical Center, Div of Nephrology, 51 Audubon Av

New York, New York, 10032, United States

Location

Mountain Kidney & Hypertension Assoc, 10 McDowell St

Asheville, North Carolina, 28801, United States

Location

University of North Carolina at Chapel Hill, Clinical & Translational Research Centre

Chapel Hill, North Carolina, 27599, United States

Location

Southeastern Nephrology-Whiteville, 800 Jefferson St

Whiteville, North Carolina, 28472, United States

Location

Southeastern Nephrology Associates-Wilmington, 1302 Medical Center Drive

Wilmington, North Carolina, 28401, United States

Location

Cleveland Clinic, Glickman Urological & Kidney Institute, 9500 Euclid Av.

Cleveland, Ohio, 44195, United States

Location

The Ohio State University (OSU), Wexner Medical Center, 410 West 10th Av.

Columbus, Ohio, 43210, United States

Location

Oregon Health & Science University, 3181 SW Sam Jackson Park Rd

Portland, Oregon, 97239, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Thomas Jefferson University, 211 S. 9th Street

Philadelphia, Pennsylvania, 19107, United States

Location

Allegheny General Hospital, 4800 Friendship Av.

Pittsburgh, Pennsylvania, 15224, United States

Location

Nephrology Associates, P.C., 28 White Bridge Rd

Nashville, Tennessee, 37205, United States

Location

Renal Disease Research Institute, 1250 Eighth Av. #135

Fort Worth, Texas, 76104, United States

Location

University of Vermont

Burlington, Vermont, 05401, United States

Location

Hospital Britanico de Buenos Aires, Pedriel 74

Capital Federal, C1280AEB, Argentina

Location

Clinica Priv Velez Sarsfield

Córdoba, 5000, Argentina

Location

Hospital Privado-Centro Medico de Cordoba, Naciones Unidas 346, Nefrologia piso 1

Córdoba, 5016, Argentina

Location

Sanatorio Allende, Hipolito Yrigoyen 384, 2 Piso

Córdoba, X5000JHQ, Argentina

Location

Hospital Universitario Austral, Unidad de Investigacion Clinica, Av. J.D. Peron 1500, piso 4

Pilar, B16290DT, Argentina

Location

Clinico de Nefrologia, Urologia Y Enfermedades Cardiovasculares, Av. Gdor Freyre 3074

Santa Fe, 3000, Argentina

Location

Monash Medical Centre

Clayton, Victoria, 3168, Australia

Location

Royal Adelaide Hospital, Port Rd.

Adelaide, 5000, Australia

Location

Box Hill Hospital, Dept of Renal Medicine, Arnold Str 5

Box Hill, 3128, Australia

Location

Austin Health, Dept of Nephrology, 145 Studley Rd.

Heidelberg, 3084, Australia

Location

Melbourne Health, Royal Melbourne Hospital, Dept of Nephrology,Grattan Str.

Parkville, 3052, Australia

Location

Prince of Wales Hospital, Nephrology Dept, Parkes 3 West

Randwick, 2031, Australia

Location

Western Health, Western Hospital-Sunshine Hospital, 176 Furlong Rd, Level 3, WHCRE Building

St Albans, 3021, Australia

Location

Westmead Hospital, Dept of Renal Medicine, Hawkesbury Rd.

Westmead, 2145, Australia

Location

Metro South Hospital and Health Service via Princess Alexandra Hospital, Dept of Nephrology, 199 Ipswich Rd.

Woolloongabba, 4102, Australia

Location

Brest Regional Hospital, 7 Meditsinskaya str.

Brest, 224027, Belarus

Location

Grodno Regional Clinical Hospital, 52 Bulvar Leninskogo Komsomola

Grodno, 230030, Belarus

Location

Gomel Regional Clinical Hospital, 5 Brat'ev Lizukovyh str.

Homyel, 246029, Belarus

Location

4-th N.E. Savchenko City Clinical Hospital, 110, R. Luxemburg str.

Minsk, 220036, Belarus

Location

University Hospital Erasmus (Brussels), Recherche Clinique Nephrologie Transplantation, Route de Lennik 808

Brussels, 1070, Belgium

Location

Cliniques Universitaires Saint-Luc, Nephrology Dept, Av. Hippocrate 10

Brussels, 1200, Belgium

Location

University Hospital Gent, Dept of Medical Nephrology, Corneel Heymanslaan 10

Ghent, 9000, Belgium

Location

Centre Hospitalier Universitaire de Liege, Nephrology Dept. Domaine Universitaire de Sart-Tilman

Liège, 4000, Belgium

Location

AZ Delta, Wilgenstraat 2

Roeselare, 8800, Belgium

Location

Royal Inland Hospital, Kidney Clinic, 7 South, 311 Columbia Street

Kamloops, British Columbia, V2C 2T1, Canada

Location

Interior Health-Kelowna General Hosp (IH KGH), 2268 Pandosy Str.

Kelowna, British Columbia, V1Y 1T2, Canada

Location

Vancouver Coastal Health Authority, Gordon and Leslie Diamond Health Care Centre, 5 th floor, Diamond Building

Vancouver, British Columbia, V5T 3A5, Canada

Location

Queen Elizabeth II Health Sciences Centre, 1276 South Park St

Halifax, Nova Scotia, B3H 2Y9, Canada

Location

Kingston General Hospital

Kingston, Ontario, K7L2V7, Canada

Location

Hospital Maisonneuve-Rosemont, CNIB 3rd Floor, 1929 Bayview Avenue

Toronto, Ontario, M4G 3E8, Canada

Location

Toronto General Hospital, University Health Network, 200 Elizabeth St, 8 N-849

Toronto, Ontario, M5G2C4, Canada

Location

CISSS de la Monteregie-Centre-Hopital Charles LeMoyne, Room E-304, 3120 Taschereau Blvd

Greenfield Park, Quebec, J4V 2H1, Canada

Location

CHUQ-L'Hotel Dieu de Quebec, 11 côte du Palais

Québec, Quebec, G1R 2J6, Canada

Location

Centre Hospiitalier Universitaire de Sherbrooke (CHUS), 3001, 12e Avenue Nord

Sherbrooke, Quebec, J1H 5N4, Canada

Location

Fakultni nemocnice Brno, Interni gastroenterologicka klinika, Jihlavska 20

Brno, 62500, Czechia

Location

Fakultni nemocnice Hradec Kralove, Sokolska 581

Hradec Králové, 50005, Czechia

Location

Fakultni nemocnice Olomouc, I.P. Pavlova 185/6

Olomouc, 77900, Czechia

Location

Fakultni nemocnice Kralovske Vinohrady, Linterni klinika, Srobarova 1150/50

Prague, 10034, Czechia

Location

Vseobecna fakultni nemocnice v Praze, Klinik nefrologie, U Nemocnice 499/2

Prague, 12808, Czechia

Location

Helsinki University Central Hospital (HUCH), Nephrology Clinic, Meilahti Triangle Hospital

Helsinki, 00290, Finland

Location

Study Cor Oy, Hoitajantie 4

Jyväskylä, 40620, Finland

Location

Tampere University Hospital, P O Box 2000, Munuaiskeskus, Erakennus, 1. kerros

Tampere, 33520, Finland

Location

Centre Hospitalier Boulogne sur Mer, 4eme etage Batiment Administratif, Allee Jacques Monod

Boulogne-sur-Mer, 62321, France

Location

CHU Grenoble-Hopital Michallon, Service Nephrologie-Hemodialyse-Aphereses-Transplantation Renale, Boulevard de la Chantourne CS 10217

Grenoble, 30043, France

Location

Lapeyronie Hospital, Univ Hospital Montpellier, 371 Av. du Doyen Gaston Giraud

Montpellier, 34295, France

Location

Hopital Bichat-Claude Bernard, Service de Nephrologie, 46 rue Henri Huchard

Paris, 75877, France

Location

Chu St Etienne-Hopital Nord, Service de Nephrologie Dialyse Transplantation renale, Av. Albert Raimond

Saint-Priest-en-Jarez, 42270, France

Location

Centre Hospitalier de Valenciennes, Service de Nephrologie-Medecine Interne, Av. Desandrouin BP 379

Valenciennes, 59322, France

Location

Uniklinik RWTH Aachen, Medizinische Klinik II, Pauwelsstrasse 30

Aachen, 52074, Germany

Location

Universitaetsklinikum Carl Gustav Carus Dresden, Medizinische Klinik III, Nephrologie, Fetscherstr. 74

Dresden, 01307, Germany

Location

Universitaetsklinikum Erlangen, Medizinisches Klinik 4, Ulmenweg 18

Erlangen, 91054, Germany

Location

Universitaetsklinikum Heidelberg-Nephrologie, Renal Clinic, Im Neuenheimer Feld 162

Heidelberg, 69120, Germany

Location

Universitatsklinik Schleswig-Holstein-Campus Lubek, Medizinische Klinik I, Nephrologie, Ratzeburger Allee 160

Lübeck, 23538, Germany

Location

University Clinic Munich, LMU-Inner City Medical Polyclinic, Nephrologisches Zentrum, Medizinische Klinik und Poliklinik IV

Munich, 80336, Germany

Location

Universitaetsklinikum Regensburg, Abteilung für Nephrologie, Franz-Josef-Strauss Allee 11

Regensburg, 93053, Germany

Location

General Hospital of Athens-Laiko, Nephrology Clinic, 17 Agiou Thoma Street

Athens, 11527, Greece

Location

University Hospital of Heraklion, Nephrology Clinic, Diastaurosi Staurakion-Vouton

Heraklion, 71100, Greece

Location

University General Hospital of Ioannina, Nephrology Clinic, Leof. Stavros Niarchou

Ioannina, 45110, Greece

Location

University Hospital of Larissa Medical School, Nefrology Clinic, Mezourlo

Larissa, 41110, Greece

Location

General Hospital of Nikaia Ag. Panteleimon, Nephrology Clinic, Mantouvalou 3 Str.

Nikaia, 18454, Greece

Location

University General Hospital of Patras, Rio

Pátrai, 26504, Greece

Location

Hippokration General Hosp of Thessaloniki, Nephrology Clinic, 49 Konstantinoupoleos Str

Thessaloniki, 54642, Greece

Location

Azienda Ospedale Policlinico di Bari

Bari, 70124, Italy

Location

ASST di Lecco, Presidio Ospedaliero Alessandro Manzoni, Via dell´Eremo 9/11

Lecco, 23900, Italy

Location

Ospedale San Carlo Borromeo, Via Pio II, 3

Milan, 20153, Italy

Location

Istituti Clinici Scientifici Maugeri Spa-Societa Benefit, Div. di Nephrologia ed Emodialist, Via S. Maugeri 10

Pavia, 27100, Italy

Location

Uniwersyteckie Centrum Kliniczne-Szpital Gdanskiego Uniwersytetu Medycznego

Gdansk, 80-211, Poland

Location

Samodzielny Publiczny Zaklad Opieki Zdrowotnej Centralny Szpital Kliniczny, Uniwersytetu Medycznego w Lodzi, ul Pomorska 251

Lodz, 92-213, Poland

Location

Wojewodzki Szpital Specjalistyczny w Olsztynie, Oddzial Kliniczny Nefrologiczny, Hipertensjologii i Chorob Wewnetrznych, ul. Zolnierska 18

Olsztyn, 10-561, Poland

Location

Sonomed Sp. z.o.o. ul. Bandurskiego 98/U12

Szczecin, 71-685, Poland

Location

Dong-A University Hospital, Won Suk An, 26 Daesingongwon-Ro Seogu

Busan, 49201, South Korea

Location

Kyungpook National University Hospital, 130 Dongdeok-ro Jung-gu

Daegu, 41944, South Korea

Location

Chungnam National University Hospital, 282 Munhwa-ro, Jung-gu

Daejeon, 35015, South Korea

Location

Hallym University Sacred Heart Hospital,22 Gwanpyeong-ro 170 beon-gil, Dongan-gu, Anyang-si

Gyeonggi-do, 14068, South Korea

Location

Seoul National University Hospital, 101 Daehak-Ro, Jongno-Gu

Seoul, 03080, South Korea

Location

Seoul St. Mary´s Hospital, 222 Banpo-Daero, Seocho-gu

Seoul, 06591, South Korea

Location

Chung-Ang University Hospial, 102 Heukseok-ro, Dongiak-gu

Seoul, 06973, South Korea

Location

Hospital Universitario Fundacion Alcorcon, C/Budapest 1

Alcorcón, 28922, Spain

Location

Hospital del Mar, Passeig Maritim 25-29

Barcelona, 08003, Spain

Location

Hospital Universitario Vall d´Hebron, Passeig Vall d´Hebron 119-129

Barcelona, 08035, Spain

Location

Hospital Clinic Barcelona, Escalera 12, Planta 5, Calle Villaroel 170

Barcelona, 08036, Spain

Location

Hospital Universitari Arnau de Vilanova, Avenida Alcalde Rovire Roure 80

Lleida, 25198, Spain

Location

Hospital General Universitario Gregorio Maranon, Servicio de Nefrologica, C/Dr. Esquerdo 46

Madrid, 28007, Spain

Location

Hospital 12 de Octubre, Residencia General (Sotano 1)-Area de Ensayos Clinicos, Avda. Cordoba s/n

Madrid, 28041, Spain

Location

Sahlgrenska University Hospital, Njurmottagningen, Vita Stråket 12

Gothenburg, 41345, Sweden

Location

Universitetssjukhuset Linköping, Njurmedicinska kliniken

Linköping, 58185, Sweden

Location

Karolinska University Hospital-Huddinge, Njur-KBC M87

Stockholm, 14186, Sweden

Location

Danderyds sjukhus, Njurmedicinska kliniken

Stockholm, 18288, Sweden

Location

Uppsala University Hospital, Dept of Nephrology, ing 30, plan 5

Uppsala, 75185, Sweden

Location

Kaohsiung Medical Univ Chung-Ho Memorial Hospital

Kaohsiung City, 80756, Taiwan

Location

China Medical University Hospital, No 2 Yude Rd

Taichung, 40447, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 40705, Taiwan

Location

National Cheng Kung University Hospital, No 138 Sheng Li Rd

Tainan, 704, Taiwan

Location

Cukurova University Medical Faculty, Dept of Internal Disease, Div of Nephrology, Balcali

Adana, 01330, Turkey (Türkiye)

Location

Istanbul University Cerrahpasa, Medical Faculty-Dept of Internal Disease, Fatih-Cerrahpasa, Kocamustafapasa Caddesi No 53

Istanbul, 34098, Turkey (Türkiye)

Location

Ege University Med Faculty Dept of Internal Disease, Div of Nephrology

Izmir, 35100, Turkey (Türkiye)

Location

Erciyes University Faculty of Medicine,Semiha Kibar Organ Nakli ve Dyaliz Hastanesi, Kosk Mah. prof dr Turhan Feyziogly Cad. no 42

Kayseri, 38039, Turkey (Türkiye)

Location

Kocaeli University Medical School-Internal Medicine, Nephrology, Umuttepe Yerleskesi

Kocaeli, 41000, Turkey (Türkiye)

Location

Belfast City Hospital, 51 Lisburn Rd

Belfast, BT9 7AB, United Kingdom

Location

Southmead Hospital, Southmead Rd, Westbury-on-Trym

Bristol, BS10 5NB, United Kingdom

Location

Queen Elizabeth University Hosp-Glasgow, Glasgow Clin Research Facility 5th floor, Institute of Neurosciences

Glasgow, G51 4TF, United Kingdom

Location

Gloucestershire Royal Hospital, Great Western Rd

Gloucester, GL1 3NN, United Kingdom

Location

St James´s University Hospital, Beckett St.

Leeds, LS9 7TF, United Kingdom

Location

Leicester General Hospital, John Walls Renal Unit, Gwendolen Rd

Leicester, LE5 4PW, United Kingdom

Location

The Royal London Hospital, Whitechapel

London, E1 1BB, United Kingdom

Location

University of Manchester, Manchester Royal Infirmary, Oxford Rd

Manchester, M13 9WL, United Kingdom

Location

Nottingham City Hospital, Hucknall Rd

Nottingham, NG5 1PB, United Kingdom

Location

Northern General Hospital, Herries Rd.

Sheffield, S5 7AU, United Kingdom

Location

Related Publications (5)

  • Fellstrom BC, Barratt J, Cook H, Coppo R, Feehally J, de Fijter JW, Floege J, Hetzel G, Jardine AG, Locatelli F, Maes BD, Mercer A, Ortiz F, Praga M, Sorensen SS, Tesar V, Del Vecchio L; NEFIGAN Trial Investigators. Targeted-release budesonide versus placebo in patients with IgA nephropathy (NEFIGAN): a double-blind, randomised, placebo-controlled phase 2b trial. Lancet. 2017 May 27;389(10084):2117-2127. doi: 10.1016/S0140-6736(17)30550-0. Epub 2017 Mar 28.

    PMID: 28363480BACKGROUND
  • Zhang H, Lafayette R, Wang B, Ying L, Zhu Z, Stone A, Kristensen J, Barratt J. Efficacy and Safety of Nefecon in Patients with IgA Nephropathy from Mainland China: 2-Year NefIgArd Trial Results. Kidney360. 2024 Dec 1;5(12):1881-1892. doi: 10.34067/KID.0000000583. Epub 2024 Oct 9.

  • Lafayette R, Kristensen J, Stone A, Floege J, Tesar V, Trimarchi H, Zhang H, Eren N, Paliege A, Reich HN, Rovin BH, Barratt J; NefIgArd trial investigators. Efficacy and safety of a targeted-release formulation of budesonide in patients with primary IgA nephropathy (NefIgArd): 2-year results from a randomised phase 3 trial. Lancet. 2023 Sep 9;402(10405):859-870. doi: 10.1016/S0140-6736(23)01554-4. Epub 2023 Aug 14.

  • Liao J, Zhou Y, Xu X, Huang K, Chen P, Wu Y, Jin B, Hu Q, Chen G, Zhao S. Current knowledge of targeted-release budesonide in immunoglobulin A nephropathy: A comprehensive review. Front Immunol. 2023 Jan 4;13:926517. doi: 10.3389/fimmu.2022.926517. eCollection 2022.

  • Barratt J, Lafayette R, Kristensen J, Stone A, Cattran D, Floege J, Tesar V, Trimarchi H, Zhang H, Eren N, Paliege A, Rovin BH; NefIgArd Trial Investigators. Results from part A of the multi-center, double-blind, randomized, placebo-controlled NefIgArd trial, which evaluated targeted-release formulation of budesonide for the treatment of primary immunoglobulin A nephropathy. Kidney Int. 2023 Feb;103(2):391-402. doi: 10.1016/j.kint.2022.09.017. Epub 2022 Oct 19.

MeSH Terms

Conditions

Glomerulonephritis, IGA

Condition Hierarchy (Ancestors)

GlomerulonephritisNephritisKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Clinical Program Leader
Organization
Calliditas Therapeutics

Study Officials

  • Krassimir Mitchev, MD

    Calliditas AB

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 8, 2018

First Posted

August 23, 2018

Study Start

September 5, 2018

Primary Completion

July 10, 2023

Study Completion

July 10, 2023

Last Updated

December 3, 2024

Results First Posted

December 3, 2024

Record last verified: 2024-11

Data Sharing

IPD Sharing
Will not share

Locations