NCT01738035

Brief Summary

The objective of the study is to evaluate efficacy and safety of two different doses of NEFECON in the treatment of patients with primary IgA nephropathy (IgAN) at risk of developing end-stage renal disease, under rigorous blood pressure control with an angiotensin-converting enzyme inhibitor (ACEI) and/or angiotensin II receptor I blocker (ARB).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
150

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Dec 2012

Geographic Reach
10 countries

58 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 25, 2012

Completed
4 months until next milestone

First Posted

Study publicly available on registry

November 30, 2012

Completed
1 day until next milestone

Study Start

First participant enrolled

December 1, 2012

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2015

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2015

Completed
Last Updated

September 24, 2015

Status Verified

September 1, 2015

Enrollment Period

2.5 years

First QC Date

July 25, 2012

Last Update Submit

September 23, 2015

Conditions

Keywords

IgA nephropathy

Outcome Measures

Primary Outcomes (1)

  • Change from baseline in urine protein creatinine ratio

    9 months

Secondary Outcomes (3)

  • Change from baseline in urine albumin creatinine ratio

    9 months

  • Change from baseline in 24 hour albuminuria

    9 months

  • Change from baseline in estimated GFR

    9 months

Other Outcomes (4)

  • Change from baseline in urine protein creatinine ratio

    3-12 months

  • Change in urine albumin creatinine ratio

    3-12 months

  • Change from baseline in 24 hour albuminuria

    3-12 months

  • +1 more other outcomes

Study Arms (3)

NEFECON 8 mg/day

EXPERIMENTAL

NEFECON 8 mg/day (2 active + 2 placebo capsules daily) for 9 months

Drug: NEFECON

NEFECON 16 mg/day

EXPERIMENTAL

NEFECON 16 mg/day (4 active capsules daily) for 9 months

Drug: NEFECON

Placebo

PLACEBO COMPARATOR

Placebo (4 placebo capsules daily) for 9 months

Other: Placebo

Interventions

All patients will receive a maximum recommended daily dose of an ACEI and/or ARB (or maximum tolerated dose not exceeding the maximum recommended daily dose) for the duration of the treatment and follow-up phases.

Also known as: Budesonide modified-released capsules (4 mg/capsule)
NEFECON 16 mg/dayNEFECON 8 mg/day
PlaceboOTHER

All patients will receive a maximum recommended daily dose of an ACEI and/or ARB (or maximum tolerated dose not exceeding the maximum recommended daily dose) for the duration of the treatment and follow-up phases.

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Female or male patients ≥18 years
  • Biopsy-verified IgA nephropathy
  • Urine protein creatinine ratio ≥0.5 g/g OR urine protein ≥0.75 g/24hr
  • Estimated GFR (using the CKD-EPI formula) OR measured GFR ≥50 mL/min per 1.73 m2 OR ≥45 mL/min per 1.73m2 for patients on a maximum recommended or maximum tolerated dose of an ACEI and/or ARB
  • Willing to change antihypertensive medication regimen if applicable
  • Willing and able to give informed consent

You may not qualify if:

  • Secondary forms of IgA nephropathy as defined by the treating physician (for example, Henoch-Schönlein purpura patients and those with associated alcoholic cirrhosis)
  • Presence of crescent formation in ≥50% of glomeruli assessed on renal biopsy
  • Kidney transplanted patients 4. Severe gastrointestinal disorders (including peptic ulcer disease and inflammatory bowel disease) which may impair drug effect, or other conditions which could modify the effect of the trial drug as judged by the Investigator
  • Patients currently treated with systemic immunosuppressive or systemic corticosteroid drugs (excluding topical or nasal steroids) or have been previously treated for more than one week within the last 24 months.
  • Patients currently treated chronically (daily dosing) with inhaled corticosteroid drugs or have previously been treated chronically for more than one month within the last 12 months
  • Patients previously treated with immunosuppressive or systemic corticosteroids for the treatment of IgA nephropathy
  • Patients unable to take oral medication or intolerant to budesonide or other corticosteroid preparations
  • Patients with known allergy or intolerance to ACEI, ARB or to any component of the trial drug formulation
  • Patients with acute or chronic infectious disease incl. hepatitis, HIV positive patients and patients with chronic urinary tract infections
  • Severe liver disease according to the discretion of the Investigator
  • Patients with Type 1 or 2 diabetes
  • Patients with uncontrolled cardiovascular disease as judged by the Investigator
  • Patients with current malignancy or history of malignancy during the last three years
  • For women only; pregnant or breast feeding or unwilling to use adequate contraception during the trial (only women of child bearing potential)
  • Completion of the Run-in Phase
  • +5 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (58)

University Hospital of Antwerp

Antwerp, Belgium

Location

Imelda Hospital

Bonheiden, Belgium

Location

Ghent University Hospital

Ghent, Belgium

Location

University Hospitals Leuven

Leuven, Belgium

Location

Heilig Hartziekenhuis Roeselare-Menen

Roeselare, Belgium

Location

University Hospital

Olomouc, Czechia

Location

Charles University & General University Hospital

Prague, Czechia

Location

Institut klinické a experimentální medicíny

Prague, Czechia

Location

Rigshospitalet

Copenhagen, Denmark

Location

Herlev Hospital

Herlev, Denmark

Location

Odense University Hospital

Odense, Denmark

Location

Helsinki University Central Hospital

Helsinki, Finland

Location

Tampere University Hospital

Tampere, Finland

Location

Turku University Central Hospital

Turku, Finland

Location

RWTH Aachen

Aachen, Germany

Location

Klinikum Augsburg

Augsburg, Germany

Location

Charité Hospital

Berlin, Germany

Location

Charité-Virchow Clinic

Berlin, Germany

Location

Vivantes Klinikum im Friedrichshain

Berlin, Germany

Location

Klinikum-Bremen-Mitte

Bremen, Germany

Location

University Hospital Carl Gustav Carus

Dresden, Germany

Location

Studienzentrum Karlstrasse

Düsseldorf, Germany

Location

Universitätsklinikum Erlangen

Erlangen, Germany

Location

Universitätsmedizin Göttingen

Göttingen, Germany

Location

University Hospital

Heidelberg, Germany

Location

University of Jena

Jena, Germany

Location

Universitätsklinikum Magdeburg

Magdeburg, Germany

Location

Universität München

Munich, Germany

Location

Universitätsklinikum Münster

Münster, Germany

Location

Universitätsklinikum Regensburg

Regensburg, Germany

Location

Deutsche Klinik für Diagnostik

Wiesbaden, Germany

Location

Würzburg University Hospital

Würzburg, Germany

Location

Policlinico di Bari

Bari, Italy

Location

Azienda Ospedaliera G. Brotzu

Cagliari, Italy

Location

Ospedale A Manzoni

Lecco, Italy

Location

Bassini Hospital

Milan, Italy

Location

Ospedale S. G. Bosco

Torino, Italy

Location

Belcolle Hospital

Viterbo, Italy

Location

University Medical Center

Leiden, Netherlands

Location

Fundación Puigver

Barcelona, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, Spain

Location

12 de Octubre Hospital

Madrid, Spain

Location

Fundación Jimenez Diaz Hospital

Madrid, Spain

Location

Hospital Universitario Gregorio Marañon

Madrid, Spain

Location

Central sjukhuset

Karlstad, Sweden

Location

Karlstad Central Hospital

Karlstad, Sweden

Location

University Hospital

Linköping, Sweden

Location

Danderyds Hospital

Stockholm, Sweden

Location

Karolinska University Hospital

Stockholm, Sweden

Location

Uppsala University Hospital

Uppsala, Sweden

Location

Belfast City Hospital

Belfast, United Kingdom

Location

Ulster Hospital

Belfast, United Kingdom

Location

Royal Derby Hospital

Derby, United Kingdom

Location

Edinburgh Royal Infirmary

Edinburgh, United Kingdom

Location

Western Infirmary

Glasgow, United Kingdom

Location

The Leeds Teaching Hospitals NHS Trust

Leeds, United Kingdom

Location

Leicester General Hospital

Leicester, United Kingdom

Location

James Cook University Hospital

Middlesbrough, United Kingdom

Location

Related Publications (2)

  • Fellstrom BC, Barratt J, Cook H, Coppo R, Feehally J, de Fijter JW, Floege J, Hetzel G, Jardine AG, Locatelli F, Maes BD, Mercer A, Ortiz F, Praga M, Sorensen SS, Tesar V, Del Vecchio L; NEFIGAN Trial Investigators. Targeted-release budesonide versus placebo in patients with IgA nephropathy (NEFIGAN): a double-blind, randomised, placebo-controlled phase 2b trial. Lancet. 2017 May 27;389(10084):2117-2127. doi: 10.1016/S0140-6736(17)30550-0. Epub 2017 Mar 28.

  • Yeo SC, Liew A, Barratt J. Emerging therapies in immunoglobulin A nephropathy. Nephrology (Carlton). 2015 Nov;20(11):788-800. doi: 10.1111/nep.12527.

MeSH Terms

Conditions

Glomerulonephritis, IGA

Condition Hierarchy (Ancestors)

GlomerulonephritisNephritisKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Bengt Fellström, MD, PhD

    Professor of Medicine Department of Medical Sciences, Renal Medicine Uppsala University Hospital, Sweden

    PRINCIPAL INVESTIGATOR
  • Alex Mercer, PhD

    Pharmalink AB, Stockholm, Sweden

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 25, 2012

First Posted

November 30, 2012

Study Start

December 1, 2012

Primary Completion

June 1, 2015

Study Completion

September 1, 2015

Last Updated

September 24, 2015

Record last verified: 2015-09

Locations