NCT03412890

Brief Summary

The purpose of this study was to determine the long-term efficacy and safety of relugolix 40 milligrams (mg) once daily co-administered with estradiol (E2) and norethindrone acetate (NETA) for 28 weeks on heavy menstrual bleeding associated with uterine fibroids in participants who previously completed a 24-week treatment period in one of the pivotal studies (MVT-601-3001 or MVT-601-3002).

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
477

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Oct 2017

Typical duration for phase_3

Geographic Reach
9 countries

150 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 19, 2017

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

January 19, 2018

Completed
10 days until next milestone

First Posted

Study publicly available on registry

January 29, 2018

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 21, 2020

Completed
12 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 13, 2021

Completed
3.3 years until next milestone

Results Posted

Study results publicly available

May 9, 2024

Completed
Last Updated

May 9, 2024

Status Verified

April 1, 2024

Enrollment Period

2.3 years

First QC Date

January 19, 2018

Results QC Date

November 13, 2023

Last Update Submit

April 15, 2024

Conditions

Keywords

Uterine FibroidHeavy Menstrual BleedingMenstrual Blood Volume

Outcome Measures

Primary Outcomes (1)

  • Percentage Of Participants Who Achieved Or Maintained An MBL Volume Of <80 Milliliters (mL) And At Least A 50% Reduction From Baseline MBL Volume At Week 52/End Of Treatment

    A responder was a participant who had MBL volume of \< 80 mL and at least a 50% reduction from baseline MBL volume over the last 35 days of treatment (up to Week 52). All returned feminine products collected at each clinical visit were analyzed by the alkaline hematin method to obtain the MBL volume. MBL volume was measured over the Week 52/early termination feminine product collection interval (up to 35 days prior to the last dose of treatment). The percentage of participants who were responders are presented.

    Week 52/End of Treatment

Secondary Outcomes (13)

  • Change From Pivotal Study Baseline In MBL Volume At Week 52

    Week 52

  • Percentage Of Participants Who Achieved Or Maintained Amenorrhea Over The Last 35 Days Of Treatment

    Week 24 up to last 35 days of treatment (up to Week 52)

  • Percentage Of Participants With A Hemoglobin Level ≤10.5 Gram/Deciliter (g/dL) At Pivotal Study Baseline Who Achieved An Increase Of >2 g/dL From Pivotal Study Baseline At Week 52

    Week 52

  • Number Of Participants With Hemoglobin Increase Of ≥1 g/dL From Pivotal Study Baseline At Week 52 Among Those With A Hemoglobin Concentration Below Lower Limit Of Normal At Pivotal Baseline

    Week 52

  • Change From Pivotal Study Baseline In Hemoglobin Concentration At Week 52

    Week 52

  • +8 more secondary outcomes

Other Outcomes (1)

  • Change From Pivotal Study Baseline In European Quality Of Life Five Dimension Five Level (EQ-5D-5L) Scale At Week 52

    Week 52

Study Arms (1)

Relugolix plus E2/NETA

EXPERIMENTAL

Relugolix co-administered with E2/NETA for 28 weeks.

Drug: RelugolixDrug: Estradiol/norethindrone acetate

Interventions

Relugolix 40-mg tablet administered orally once daily

Also known as: MVT-601, TAK-385
Relugolix plus E2/NETA

Capsule containing co-formulated tablet of E2 (1 mg) and NETA (0.5 mg) administered orally once daily

Also known as: E2/NETA
Relugolix plus E2/NETA

Eligibility Criteria

Age18 Years - 50 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • \. Completed 24 weeks of study drug treatment and study participation in either pivotal study, MVT-601-3001 or MVT-601-3002

You may not qualify if:

  • Has undergone myomectomy, ultrasound-guided laparoscopic radiofrequency ablation, or any other surgical procedure for fibroids, uterine artery embolization, magnetic resonance-guided focused ultrasound for fibroids, or endometrial ablation for abnormal uterine bleeding at any time during the pivotal study (MVT-601-3001 or MVT-601-3002)
  • Met a withdrawal criterion in the pivotal study (MVT-601-3001 or MVT-601-3002).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (150)

Andalusia

Andalusia, Alabama, 36420, United States

Location

Birmingham

Birmingham, Alabama, 35205, United States

Location

Mobile

Mobile, Alabama, 36608, United States

Location

Mesa

Mesa, Arizona, 85209, United States

Location

Tucson

Tucson, Arizona, 85712, United States

Location

Little Rock

Little Rock, Arkansas, 72204, United States

Location

Canoga Park

Canoga Park, California, 91303, United States

Location

Huntington Beach

Huntington Beach, California, 92647, United States

Location

La Mesa

La Mesa, California, 91942, United States

Location

Long Beach

Long Beach, California, 90806, United States

Location

Los Angeles

Los Angeles, California, 90036, United States

Location

Los Angeles

Los Angeles, California, 90057, United States

Location

Norwalk

Norwalk, California, 90650, United States

Location

Panorama

Panorama City, California, 91402, United States

Location

San Diego

San Diego, California, 92108, United States

Location

San Diego

San Diego, California, 92111, United States

Location

Denver

Denver, Colorado, 80209, United States

Location

Lakewood

Lakewood, Colorado, 80228, United States

Location

Washington

Washington D.C., District of Columbia, 20036, United States

Location

Aventura

Aventura, Florida, 33180, United States

Location

Clearwater

Clearwater, Florida, 33759, United States

Location

DeLand

DeLand, Florida, 32720, United States

Location

Ft. Lauderdale

Fort Lauderdale, Florida, 33316, United States

Location

Fort Myers

Fort Myers, Florida, 33912, United States

Location

Hialeah

Hialeah, Florida, 33016, United States

Location

Jacksonville

Jacksonville, Florida, 32207, United States

Location

Jupiter

Jupiter, Florida, 33458, United States

Location

Loxahatchee

Loxahatchee Groves, Florida, 33470, United States

Location

Margate

Margate, Florida, 33063, United States

Location

Miami

Miami, Florida, 33126, United States

Location

Miami

Miami, Florida, 33155, United States

Location

Miami

Miami, Florida, 33165, United States

Location

New Port Richey

New Port Richey, Florida, 34652, United States

Location

Orlando

Orlando, Florida, 32808, United States

Location

Oviedo

Oviedo, Florida, 32765, United States

Location

Palm Harbor

Palm Harbor, Florida, 34684, United States

Location

Saint Cloud

Saint Cloud, Florida, 34769, United States

Location

Sarasota

Sarasota, Florida, 34239, United States

Location

Tampa

Tampa, Florida, 33606, United States

Location

Tampa

Tampa, Florida, 33613, United States

Location

West Palm Beach

West Palm Beach, Florida, 33409, United States

Location

Weston

Weston, Florida, 33327, United States

Location

Atlanta

Atlanta, Georgia, 30342, United States

Location

Atlanta

Atlanta, Georgia, 30363, United States

Location

Augusta

Augusta, Georgia, 30904, United States

Location

College Park

College Park, Georgia, 30349, United States

Location

Decatur

Decatur, Georgia, 30034, United States

Location

Duluth

Duluth, Georgia, 30097, United States

Location

Norcross

Norcross, Georgia, 30093, United States

Location

Savannah

Savannah, Georgia, 31406, United States

Location

Chicago

Chicago, Illinois, 60611, United States

Location

Naperville

Naperville, Illinois, 60540, United States

Location

Oakbrook

Oakbrook Terrace, Illinois, 60523, United States

Location

Shawnee

Shawnee Mission, Kansas, 66218, United States

Location

Covington

Covington, Louisiana, 70433, United States

Location

Marrero

Marrero, Louisiana, 70072, United States

Location

Metairie

Metairie, Louisiana, 70001, United States

Location

Metairie

Metairie, Louisiana, 70006, United States

Location

Baltimore

Baltimore, Maryland, 21208, United States

Location

Towson

Towson, Maryland, 21204, United States

Location

Canton

Canton, Michigan, 48187, United States

Location

Detroit

Detroit, Michigan, 48201, United States

Location

Saginaw

Saginaw, Michigan, 48604, United States

Location

Lincoln

Lincoln, Nebraska, 68510, United States

Location

Las Vegas

Las Vegas, Nevada, 89109, United States

Location

Las Vegas

Las Vegas, Nevada, 89113, United States

Location

Las Vegas

Las Vegas, Nevada, 89128, United States

Location

Lawrenceville

Lawrenceville, New Jersey, 08648, United States

Location

Albuquerque

Albuquerque, New Mexico, 87102, United States

Location

Brooklyn

Brooklyn, New York, 11201, United States

Location

New York

New York, New York, 10022, United States

Location

Williamsville

Williamsville, New York, 14221, United States

Location

Durham

Durham, North Carolina, 27713, United States

Location

Raleigh

Raleigh, North Carolina, 27607, United States

Location

Raleigh

Raleigh, North Carolina, 27612, United States

Location

Winston-Salem

Winston-Salem, North Carolina, 27103, United States

Location

Cincinnati

Cincinnati, Ohio, 45212, United States

Location

Cincinnati

Cincinnati, Ohio, 45219, United States

Location

Columbus

Columbus, Ohio, 43231, United States

Location

Englewood

Englewood, Ohio, 45322, United States

Location

Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

Bluffton

Bluffton, South Carolina, 29910, United States

Location

Charleston

Charleston, South Carolina, 29406, United States

Location

Columbia

Columbia, South Carolina, 29201, United States

Location

Chattanooga

Chattanooga, Tennessee, 37404, United States

Location

Memphis

Memphis, Tennessee, 38119, United States

Location

Memphis

Memphis, Tennessee, 38120, United States

Location

Beaumont

Beaumont, Texas, 77702, United States

Location

Dallas

Dallas, Texas, 75231, United States

Location

Fort Worth

Fort Worth, Texas, 76104, United States

Location

Houston

Houston, Texas, 77030, United States

Location

Houston

Houston, Texas, 77054, United States

Location

Houston

Houston, Texas, 77074, United States

Location

Longview

Longview, Texas, 75605, United States

Location

San Antonio

San Antonio, Texas, 78229, United States

Location

San Antonio

San Antonio, Texas, 78258, United States

Location

Sugar Land

Sugar Land, Texas, 77479, United States

Location

Webster

Webster, Texas, 77598, United States

Location

Salt Lake City

Salt Lake City, Utah, 84107, United States

Location

Salt Lake City

Salt Lake City, Utah, 84124, United States

Location

Norfolk

Norfolk, Virginia, 23502, United States

Location

Norfolk

Norfolk, Virginia, 23507, United States

Location

Richmond

Richmond, Virginia, 23225, United States

Location

Spokane

Spokane, Washington, 99207, United States

Location

La Louvière

La Louvière, Hainaut, 7100, Belgium

Location

Gent

Ghent, Oost-vlaanderen, 9000, Belgium

Location

Brussels

Brussels, 1200, Belgium

Location

Jette

Jette, 1090, Belgium

Location

Santo Andre

Santo André, Santo Andre, 09190-510, Brazil

Location

Santo André

Santo André, São Paulo, 09190-510, Brazil

Location

São Bernardo Do Campo

São Bernardo do Campo, São Paulo, 09715-090, Brazil

Location

Sao Paulo

São Paulo, São Paulo, 01317-000, Brazil

Location

Sao Paulo

São Paulo, São Paulo, 04266-010, Brazil

Location

Botucatu

Botucatu, 18618-686, Brazil

Location

Porto Alegre

Porto Alegre, 90035-903, Brazil

Location

Porto Alegre

Porto Alegre, 90510-040, Brazil

Location

Providencia

Providencia, 7510186, Chile

Location

San Ramon

San Ramón, 8880465, Chile

Location

Region Metropolitana

Santiago, 8320165, Chile

Location

Santiago

Santiago, 8360160, Chile

Location

Ceské Budejovice

České Budějovice, 370 01, Czechia

Location

Jihlava

Jihlava, 586 33, Czechia

Location

Olomouc

Olomouc, 772 00, Czechia

Location

Pisek

Písek, 39701, Czechia

Location

Gyula

Gyula, Bekes County, 5700, Hungary

Location

Kecskemét

Kecskemét, Bács-Kiskun county, 6000, Hungary

Location

Debrecen

Debrecen, Hajdú-Bihar, 4024, Hungary

Location

Nyíregyháza

Nyíregyháza, Szabolcs-Szatmár-Bereg, 4400, Hungary

Location

Debrecen

Debrecen, 4025, Hungary

Location

Szentes

Szentes, 6600, Hungary

Location

Catanzaro

Catanzaro, 88100, Italy

Location

Firenze

Florence, 50134, Italy

Location

Roma

Roma, 00168, Italy

Location

Siena

Siena, 53100, Italy

Location

Torino

Torino, 10126, Italy

Location

Poznan

Poznan, Greater Poland Voivodeship, 60-192, Poland

Location

Skórzewo

Skórzewo, Greater Poland Voivodeship, 60-185, Poland

Location

Lublin

Lublin, Lublin Voivodeship, 20-632, Poland

Location

Warszawa

Warsaw, Masovian Voivodeship, 02-201, Poland

Location

Katowice

Katowice, Silesian Voivodeship, 40-123, Poland

Location

Szczecin

Szczecin, West Pomeranian Voivodeship, 71-270, Poland

Location

Bialystok

Bialystok, 15-464, Poland

Location

Lódz

Lódz, Łódź Voivodeship, 90-602, Poland

Location

Centurion

Centurion, Gauteng, 0157, South Africa

Location

Roodepoort

Roodepoort, Gauteng, 1724, South Africa

Location

Durban

Durban, KwaZulu-Natal, 4001, South Africa

Location

Bloemfontein

Bloemfontein, 9301, South Africa

Location

Cape Town

Cape Town, 7405, South Africa

Location

Cape Town

Cape Town, 7500, South Africa

Location

Port Elizabeth

Port Elizabeth, 6001, South Africa

Location

Related Publications (3)

  • Stewart EA, Al-Hendy A, Lukes AS, Madueke-Laveaux OS, Zhu E, Proehl S, Schulmann T, Marsh EE. Relugolix combination therapy in Black/African American women with symptomatic uterine fibroids: LIBERTY Long-Term Extension study. Am J Obstet Gynecol. 2024 Feb;230(2):237.e1-237.e11. doi: 10.1016/j.ajog.2023.10.030. Epub 2023 Oct 18.

  • Al-Hendy A, Lukes AS, Venturella R, Villarroel C, McKain L, Li Y, Wagman RB, Stewart EA. A plain language summary of the long-term relugolix combination therapy study for uterine fibroids. J Comp Eff Res. 2023 Aug;12(8):e230069. doi: 10.57264/cer-2023-0069. Epub 2023 Jul 21.

  • Al-Hendy A, Lukes AS, Poindexter AN 3rd, Venturella R, Villarroel C, McKain L, Li Y, Wagman RB, Stewart EA. Long-term Relugolix Combination Therapy for Symptomatic Uterine Leiomyomas. Obstet Gynecol. 2022 Dec 1;140(6):920-930. doi: 10.1097/AOG.0000000000004988. Epub 2022 Nov 2.

MeSH Terms

Conditions

MenorrhagiaLeiomyoma

Interventions

relugolixestradiol, norethindrone drug combination

Condition Hierarchy (Ancestors)

Uterine HemorrhageUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesHemorrhagePathologic ProcessesPathological Conditions, Signs and SymptomsMenstruation DisturbancesNeoplasms, Muscle TissueNeoplasms, Connective and Soft TissueNeoplasms by Histologic TypeNeoplasms

Results Point of Contact

Title
Clinical Trials at Myovant
Organization
Myovant Sciences GmbH

Study Officials

  • Myovant Medical Monitor

    Myovant Sciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Model Details: Open-Label Extension
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 19, 2018

First Posted

January 29, 2018

Study Start

October 19, 2017

Primary Completion

January 21, 2020

Study Completion

January 13, 2021

Last Updated

May 9, 2024

Results First Posted

May 9, 2024

Record last verified: 2024-04

Data Sharing

IPD Sharing
Will not share

Locations