NCT03370120

Brief Summary

The purpose of the study is to evaluate the long-term safety and tolerability of Padsevonil administered at individualized doses as adjunctive treatment for subjects with drug-resistant epilepsy.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
406

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Aug 2018

Geographic Reach
26 countries

141 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 7, 2017

Completed
5 days until next milestone

First Posted

Study publicly available on registry

December 12, 2017

Completed
9 months until next milestone

Study Start

First participant enrolled

August 27, 2018

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 11, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 11, 2020

Completed
1 year until next milestone

Results Posted

Study results publicly available

December 29, 2021

Completed
Last Updated

December 29, 2021

Status Verified

November 1, 2021

Enrollment Period

2.3 years

First QC Date

December 7, 2017

Results QC Date

November 30, 2021

Last Update Submit

November 30, 2021

Conditions

Keywords

Drug-Resistant EpilepsyPadsevonil

Outcome Measures

Primary Outcomes (3)

  • Percentage of Participants With Treatment-Emergent Adverse Events (TEAEs) Reported by the Participant and/or Caregiver or Observed by the Investigator During the Entire Study

    An Adverse Event is any untoward medical occurrence in a participant or clinical investigation participant administered a pharmaceutical product that does not necessarily have a causal relationship with this treatment. A TEAE was defined as any event that was not present prior to the initiation of the first dose of study treatment in this study or any unresolved event already present before initiation of the first dose that worsens in intensity following exposure to the treatment.

    From Entry Visit (Week 0) until the Safety Follow-up Visit (up to approximately 2 years)

  • Percentage of Participants With Treatment-Emergent Adverse Events (TEAEs) Leading to Study Withdrawal

    An Adverse Event is any untoward medical occurrence in a participant or clinical investigation participant administered a pharmaceutical product that does not necessarily have a causal relationship with this treatment. A TEAE was defined as any event that was not present prior to the initiation of the first dose of study treatment in this study or any unresolved event already present before initiation of the first dose that worsens in intensity following exposure to the treatment.

    From Entry Visit (Week 0) until the Safety Follow-up Visit (up to approximately 2 years)

  • Change From Baseline (From the Respective Parent Study [EP0091 or EP0092]) in Observable Focal-onset Seizure Frequency Over the Evaluation Period

    Seizure frequency refers to 28-day adjusted frequency. Observable focal-onset seizures refer to Type IAl, IB, and IC (according to the International League Against Epilepsy (ILAE) Classification of Epileptic Seizures, 1981). Focal-onset seizures include all Type I seizures.

    From Baseline in respective parent study over the Evaluation Period (up to approximately 2 years) in this study

Study Arms (1)

Padsevonil

EXPERIMENTAL

Padsevonil will be administered in an open-label manner. The individual starting dose of each subject will be the one at the end of the parent study. Once subjects enter EP0093 further individual dose adjustments are allowed after 1 week to the extent possible with the combination of tablet strengths available.

Drug: Padsevonil

Interventions

* Pharmaceutical Form: film-coated tablet * Route of Administration: Oral use

Padsevonil

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subject is an adult (18 years of age or more )
  • Subject with epilepsy who has completed 1 of the previous Padsevonil (PSL) studies which allow access to the present study
  • Female subjects of child bearing potential must have a serum negative pregnancy test at the Entry Visit, which is confirmed to be negative by urine testing prior to further dispensing at each study visit thereafter. Subjects will be withdrawn from the study as soon as pregnancy is known. Female subjects will use an efficient form of contraception for the duration of the study and for a period of 3 months after their final dose of PSL.

You may not qualify if:

  • Subject has any severe medical, neurological, or psychiatric condition, or laboratory value which may have an impact on the safety of the subject
  • Subject has active suicidal ideation as indicated by a positive response ('Yes') to either Question 4 or Question 5 of the 'Since Last Visit' version of the Columbia-Suicide Severity Rating Scale (C-SSRS)
  • Subject has \>2x upper limit of normal (ULN) of any of the following: alanine aminotransferase (ALT), aspartate aminotransferase (AST), alkaline phosphatase (ALP), or \>ULN total bilirubin (\>= l.5x ULN total bilirubin if known Gilbert's syndrome) at the Entry Visit
  • Subject has a clinically-significant abnormality on electrocardiogram (ECG) that, in the opinion of the investigator, increases the risks associated with participating in the study
  • Subject has an abnormality on echocardiogram at last echocardiogram assessment, or foreseen in parent study as assessed by central reader that is accompanied by clinical symptoms or a Grade 2\* (or higher)/moderate severity abnormality, or a history of rheumatic heart disease, or other known valvular abnormalities (\*according to the ASE Guidelines, 2017; Zoghbi et al 2017)
  • Female subject who plans to be pregnant or is breastfeeding

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (156)

Ep0093 839

Chandler, Arizona, 85226, United States

Location

Ep0093 815

La Jolla, California, 92037, United States

Location

Ep0093 801

San Francisco, California, 94115, United States

Location

Ep0093 803

Honolulu, Hawaii, 96817, United States

Location

Ep0093 638

Fort Wayne, Indiana, 46804, United States

Location

Ep0093 707

Lexington, Kentucky, 40536, United States

Location

Ep0093 822

Baltimore, Maryland, 21287, United States

Location

Ep0093 818

Bethesda, Maryland, 20817, United States

Location

Ep0093 889

Boston, Massachusetts, 02215, United States

Location

Ep0093 645

Golden Valley, Minnesota, 55422, United States

Location

Ep0093 817

Saint Paul, Minnesota, 55102, United States

Location

Ep0093 806

Hackensack, New Jersey, 07601, United States

Location

Ep0093 893

Syracuse, New York, 13210, United States

Location

Ep0093 895

The Bronx, New York, 10467-24 01, United States

Location

Ep0093 890

Chapel Hill, North Carolina, 27514, United States

Location

Ep0093 884

Charlotte, North Carolina, 28204, United States

Location

Ep0093 642

Columbia, Ohio, 43210, United States

Location

Ep0093 802

Philadelphia, Pennsylvania, 19107, United States

Location

Ep0093 838

Cordova, Tennessee, 38018, United States

Location

Ep0093 835

Nashville, Tennessee, 37232, United States

Location

Ep0093 805

Austin, Texas, 78701, United States

Location

Ep0093 844

Austin, Texas, 78758, United States

Location

Ep0093 824

Round Rock, Texas, 78681, United States

Location

Ep0093 870

San Antonio, Texas, 78229, United States

Location

Ep0093 639

Renton, Washington, 98055, United States

Location

Ep0093 855

Box Hill, Australia

Location

Ep0093 857

Clayton, Australia

Location

Ep0093 850

Fitzroy, Australia

Location

Ep0093 853

Heidelberg, Australia

Location

Ep0093 859

Herston, Australia

Location

Ep0093 852

Melbourne, Australia

Location

Ep0093 856

Randwick, Australia

Location

Ep0093 854

Westmead, Australia

Location

Ep0093 102

Bruges, Belgium

Location

Ep0093 101

Brussels, Belgium

Location

Ep0093 105

Ghent, Belgium

Location

Ep0093 100

Leuven, Belgium

Location

Ep0093 107

Ottignies, Belgium

Location

Ep0093 075

Sarajevo, Bosnia and Herzegovina

Location

Ep0093 082

Tuzla, Bosnia and Herzegovina

Location

Ep0093 150

Blagoevgrad, Bulgaria

Location

Ep0093 151

Pleven, Bulgaria

Location

Ep0093 153

Pleven, Bulgaria

Location

Ep0093 156

Pleven, Bulgaria

Location

Ep0093 152

Sofia, Bulgaria

Location

Ep0093 154

Sofia, Bulgaria

Location

Ep0093 155

Sofia, Bulgaria

Location

Ep0093 200

Greenfield Park, Canada

Location

Ep0093 205

London, Canada

Location

Ep0093 201

Montreal, Canada

Location

Ep0093 125

Zagreb, Croatia

Location

Ep0093 254

Brno, Czechia

Location

Ep0093 255

Ostrava, Czechia

Location

Ep0093 250

Prague, Czechia

Location

Ep0093 251

Prague, Czechia

Location

Ep0093 253

Prague, Czechia

Location

Ep0093 016

Aarhus, Denmark

Location

Ep0093 015

Odense, Denmark

Location

Ep0093 276

Tallinn, Estonia

Location

Ep0093 277

Tallinn, Estonia

Location

Ep0093 275

Tartu, Estonia

Location

Ep0093 027

Tampere, Finland

Location

Ep0093 307

Clermont-Ferrand, France

Location

Ep0093 309

Dijon, France

Location

Ep0093 300

Lille, France

Location

Ep0093 302

Montpellier, France

Location

Ep0093 303

Rennes, France

Location

Ep0093 301

Strasbourg, France

Location

Ep0093 365

Berlin, Germany

Location

Ep0093 362

Bernau, Germany

Location

Ep0093 363

Bielefeld, Germany

Location

Ep0093 358

Bonn, Germany

Location

Ep0093 350

Frankfurt, Germany

Location

Ep0093 360

Freiburg im Breisgau, Germany

Location

Ep0093 368

Jena, Germany

Location

Ep0093 366

Kehl, Germany

Location

Ep0093 357

Leipzig, Germany

Location

Ep0093 353

Marburg, Germany

Location

Ep0093 354

München, Germany

Location

Ep0093 351

Münster, Germany

Location

Ep0093 356

Osnabrück, Germany

Location

Ep0093 352

Tübingen, Germany

Location

Ep0093 426

Thessaloniki, Greece

Location

Ep0093 427

Thessaloniki, Greece

Location

Ep0093 400

Budapest, Hungary

Location

Ep0093 403

Budapest, Hungary

Location

Ep0093 402

Debrecen, Hungary

Location

Ep0093 035

Cork, Ireland

Location

Ep0093 462

Bologna, Italy

Location

Ep0093 450

Cagliari, Italy

Location

Ep0093 451

Foggia, Italy

Location

Ep0093 461

Foggia, Italy

Location

Ep0093 452

Milan, Italy

Location

Ep0093 459

Pavia, Italy

Location

Ep0093 458

Pozzilli, Italy

Location

Ep0093 455

Roma, Italy

Location

Ep0093 457

Roma, Italy

Location

Ep0093 460

Roma, Italy

Location

Ep0093 526

Asahikawa, Japan

Location

Ep0093 501

Asaka, Japan

Location

Ep0093 521

Bunkyō City, Japan

Location

Ep0093 511

Fukuoka, Japan

Location

Ep0093 504

Hamamatsu, Japan

Location

Ep0093 505

Hiroshima, Japan

Location

Ep0093 513

Hōfu, Japan

Location

Ep0093 507

Itami, Japan

Location

Ep0093 514

Kyoto, Japan

Location

Ep0093 512

Nagakute, Japan

Location

Ep0093 510

Niigata, Japan

Location

Ep0093 515

Saitama, Japan

Location

Ep0093 509

Shizuoka, Japan

Location

Ep0093 529

Yonago, Japan

Location

Ep0093 703

Kaunas, Lithuania

Location

Ep0093 702

Vilnius, Lithuania

Location

Ep0093 553

Culiacán, Mexico

Location

Ep0093 552

México, Mexico

Location

Ep0093 601

Gdansk, Poland

Location

Ep0093 607

Grodzisk Mazowiecki, Poland

Location

Ep0093 605

Katowice, Poland

Location

Ep0093 616

Katowice, Poland

Location

Ep0093 603

Krakow, Poland

Location

Ep0093 614

Krakow, Poland

Location

Ep0093 604

Lublin, Poland

Location

Ep0093 610

Lublin, Poland

Location

Ep0093 606

Nowa Sól, Poland

Location

Ep0093 600

Poznan, Poland

Location

Ep0093 609

Poznan, Poland

Location

Ep0093 602

Świdnik, Poland

Location

Ep0093 926

Bucharest, Romania

Location

Ep0093 327

Belgrade, Serbia

Location

Ep0093 004

Bardejov, Slovakia

Location

Ep0093 662

Alicante, Spain

Location

Ep0093 668

Barakaldo, Spain

Location

Ep0093 651

Barcelona, Spain

Location

Ep0093 652

Barcelona, Spain

Location

Ep0093 664

Barcelona, Spain

Location

Ep0093 666

Córdoba, Spain

Location

Ep0093 658

L'Hospitalet de Llobregat, Spain

Location

Ep0093 656

Madrid, Spain

Location

Ep0093 660

Madrid, Spain

Location

Ep0093 667

Madrid, Spain

Location

Ep0093 674

Madrid, Spain

Location

Ep0093 659

Málaga, Spain

Location

Ep0093 665

Terrassa, Spain

Location

Ep0093 657

Valencia, Spain

Location

Ep0093 653

Valladolid, Spain

Location

Ep0093 900

Istanbul, Turkey (Türkiye)

Location

Ep0093 901

Istanbul, Turkey (Türkiye)

Location

Ep0093 904

Istanbul, Turkey (Türkiye)

Location

Ep0093 906

Istanbul, Turkey (Türkiye)

Location

Ep0093 909

Istanbul, Turkey (Türkiye)

Location

Ep0093 752

Birmingham, United Kingdom

Location

Ep0093 766

Brighton, United Kingdom

Location

Ep0093 751

Swansea, United Kingdom

Location

Ep0093 753

Swansea, United Kingdom

Location

Ep0093 764

Swansea, United Kingdom

Location

MeSH Terms

Conditions

Drug Resistant EpilepsySeizures

Interventions

padsevonil

Condition Hierarchy (Ancestors)

EpilepsyBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
UCB
Organization
Cares

Study Officials

  • UCB Cares

    001 844 599 2273 (UCB)

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 7, 2017

First Posted

December 12, 2017

Study Start

August 27, 2018

Primary Completion

December 11, 2020

Study Completion

December 11, 2020

Last Updated

December 29, 2021

Results First Posted

December 29, 2021

Record last verified: 2021-11

Data Sharing

IPD Sharing
Will share

Data from this trial may be requested by qualified researchers six months after product approval in the US and/or Europe, or global development is discontinued, and 18 months after trial completion. Investigators may request access to anonymized individual patient-level data and redacted trial documents which may include: analysis-ready datasets, study protocol, annotated case report form, statistical analysis plan, dataset specifications, and clinical study report. Prior to use of the data, proposals need to be approved by an independent review panel at www.Vivli.org and a signed data sharing agreement will need to be executed. All documents are available in English only, for a prespecified time, typically 12 months, on a password protected portal. This plan may change if the risk of re-identifying trial participants is determined to be too high after the trial is completed; in this case and to protect participants, individual patient-level data would not be made available.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data from this trial may be requested by qualified researchers six months after product approval in the US and/or Europe or global development is discontinued, and 18 months after trial completion.
Access Criteria
Qualified researchers may request access to anonymized IPD and redacted study documents which may include: raw datasets, analysis-ready datasets, study protocol, blank case report form, annotated case report form, statistical analysis plan, dataset specifications, and clinical study report. Prior to use of the data, proposals need to be approved by an independent review panel at www.Vivli.org and a signed data sharing agreement will need to be executed. All documents are available in English only, for a pre-specified time, typically 12 months, on a password protected portal.
More information

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