NCT03298451

Brief Summary

This is a randomized, open-label, multi-center, global, Phase III study to assess the efficacy and safety of durvalumab plus tremelimumab combination therapy and durvalumab monotherapy versus sorafenib in the treatment of patients with no prior systemic therapy for unresectable HCC. The patients cannot be eligible for locoregional therapy

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,324

participants targeted

Target at P75+ for phase_3 hepatocellular-carcinoma

Timeline
4mo left

Started Oct 2017

Longer than P75 for phase_3 hepatocellular-carcinoma

Geographic Reach
17 countries

160 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress97%
Oct 2017Aug 2026

First Submitted

Initial submission to the registry

September 19, 2017

Completed
13 days until next milestone

First Posted

Study publicly available on registry

October 2, 2017

Completed
9 days until next milestone

Study Start

First participant enrolled

October 11, 2017

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 27, 2021

Completed
1.8 years until next milestone

Results Posted

Study results publicly available

June 18, 2023

Completed
3.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 27, 2026

Expected
Last Updated

March 20, 2026

Status Verified

March 1, 2026

Enrollment Period

3.9 years

First QC Date

September 19, 2017

Results QC Date

August 26, 2022

Last Update Submit

March 19, 2026

Conditions

Keywords

Hepatocellular Carcinoma Non-Resectable

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS) - Treme 300 mg x1 Dose + Durva 1500 mg vs Sora 400 mg

    OS was defined as the time from the date of randomization until death due to any cause, regardless of whether the participant withdrew from randomized therapy or received another anticancer therapy. Any participant not known to have died at the DCO date was censored based on the last recorded date on which the participant was known to be alive. If the last known date alive or if the date of death was after the DCO date, participants were censored at the DCO date. This primary outcome measure presents OS analysis of Treme 300mg x1 dose + Durva 1500 mg vs Sora 400 mg at the time of the final analysis DCO (27Aug2021).

    From the date of randomization until death due to any cause, assessed up to the data cut-off date (27Aug2021, to a maximum of approximately 46 months).

Secondary Outcomes (16)

  • Overall Survival (OS) - Durva 1500 mg vs Sora 400 mg

    From the date of randomization until death due to any cause, assessed up to the data cut-off date (27Aug2021, to a maximum of approximately 46 months).

  • Overall Survival (OS) at 18, 24, and 36 Months After Randomization

    At 18, 24, and 36 months post-randomization. Assessed at the final analysis DCO (27Aug2021).

  • Progression Free Survival (PFS)

    Tumor scans performed at baseline, every 8 weeks for the first 48 weeks following randomization, and every 12 weeks thereafter until RECIST 1.1-defined progression. Assessed up to DCO (27Aug2021, to a maximum of approximately 46 months)

  • Time To Progression (TTP)

    From the date of randomization until objective tumor progression, assessed until the final analysis DCO (27Aug2021, to a maximum of approximately 46 months).

  • Objective Response Rate (ORR)

    From the date of randomization until objective tumor progression, assessed until the final analysis DCO (27Aug2021, to a maximum of approximately 46 months).

  • +11 more secondary outcomes

Study Arms (4)

Arm 1

EXPERIMENTAL

Durvalumab

Drug: Durvalumab

Arm 2

EXPERIMENTAL

Durvalumab in combination with tremelimumab (Regimen 1)

Drug: Tremelimumab (Regimen 1)Drug: Durvalumab (Regimen 1)

Arm 3

EXPERIMENTAL

Durvalumab in combination with tremelimumab (Regimen 2)

Drug: Tremelimumab (Regimen 2)Drug: Durvalumab (Regimen 2)

Arm 4

ACTIVE COMPARATOR

Sorafenib

Drug: Sorafenib

Interventions

Durvalumab IV (intravenous infusion).

Also known as: MEDI4736
Arm 1

Tremelimumab IV (intravenous infusion).

Arm 2

Tremelimumab IV (intravenous infusion).

Arm 3

Sorafenib, as per standard of care

Arm 4

Durvalumab IV (intravenous infusion).

Arm 2

Durvalumab IV (intravenous infusion).

Arm 3

Eligibility Criteria

Age18 Years - 100 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • HCC based on histopathological confirmation
  • No prior systemic therapy for HCC
  • Barcelona Clinic Liver Cancer (BCLC) stage B (that is not eligible for locoregional therapy) or stage C
  • Child-Pugh Score class A
  • ECOG performance status of 0 or 1 at enrollment

You may not qualify if:

  • Hepatic encephalopathy within past 12 months or requirement for medication to prevent or control encephalopathy
  • Clinically meaningful ascites
  • Main portal vein tumor thrombosis
  • Active or prior documented GI bleeding (eg, esophageal varices or ulcer bleeding) within 12 months
  • HBV and HVC co-infection, or HBV and Hep D co-infection

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (160)

Research Site

Los Angeles, California, 90048, United States

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Orange, California, 92868, United States

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San Francisco, California, 94158, United States

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Washington D.C., District of Columbia, 20007, United States

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Fort Myers, Florida, 33916, United States

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Jacksonville, Florida, 32224, United States

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Westwood, Kansas, 66205, United States

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Baltimore, Maryland, 21231, United States

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Ann Arbor, Michigan, 48109, United States

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Rochester, Minnesota, 55905, United States

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New York, New York, 10065, United States

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Charlotte, North Carolina, 28262, United States

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Portland, Oregon, 97213, United States

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Pittsburgh, Pennsylvania, 15237, United States

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Dallas, Texas, 74235, United States

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Dallas, Texas, 75216, United States

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Dallas, Texas, 75235, United States

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Houston, Texas, 77030, United States

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Houston, Texas, 77090, United States

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Murray, Utah, 84107, United States

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Barretos, Brazil

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Curitiba, Brazil

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Florianópolis, Brazil

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Porto Alegre, Brazil

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Rio de Janeiro, Brazil

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São Paulo, Brazil

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Calgary, Alberta, T2N 4N2, Canada

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Edmonton, Alberta, T6G 1Z2, Canada

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Hamilton, Ontario, L8V 5C2, Canada

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Kingston, Ontario, K7L 2V7, Canada

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London, Ontario, N6A 4L6, Canada

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Toronto, Ontario, M4N 3M5, Canada

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Montreal, Quebec, H2X 0A9, Canada

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Québec, Quebec, G1R 2J6, Canada

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Sherbrooke, Quebec, J1H 5N4, Canada

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Beijing, China

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Changchun, China

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Changsha, China

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Chengdu, China

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Dalian, China

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Fuzhou, China

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Guangzhou, China

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Hangzhou, China

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Harbin, China

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Hefei, China

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Nanchang, China

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Nanjing, China

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Nanning, China

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Shanghai, China

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Suzhou, China

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Wuhan, China

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Xi'an, China

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Zhengzhou, China

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Clichy, France

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Lille, France

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Marseille, France

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Montpellier, France

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Nancy, France

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Nantes, France

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Nice, France

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Pessac, France

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Poitiers, France

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Reims, France

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Rouen, France

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Saint-Etienne, France

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Toulouse, France

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Villejuif, France

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Aachen, Germany

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Cologne, Germany

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Essen, Germany

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Hanover, Germany

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Heidelberg, Germany

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Leipzig, Germany

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Mainz, Germany

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München, Germany

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Tübingen, Germany

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Ulm, Germany

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Hong Kong, Hong Kong

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Bangalore, India

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Bhubneshwar, India

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Chennai, India

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Hubli, India

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Hyderabad, India

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Karmsad, India

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Mumbai, India

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Nashik, India

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New Delhi, India

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Benevento, Italy

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Meldola, Italy

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Milan, Italy

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Naples, Italy

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Perugia, Italy

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Pisa, Italy

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Roma, Italy

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Rozzano, Italy

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Bunkyoku, Japan

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Chiba, Japan

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Fukuoka, Japan

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Hiroshima, Japan

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Iizuka, Japan

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Kanazawa, Japan

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Kōtoku, Japan

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Kumamoto, Japan

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Kurume, Japan

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Matsuyama, Japan

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Mitakashi, Japan

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Musashino, Japan

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Nagoya, Japan

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Okayama, Japan

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Osaka, Japan

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Ōgaki, Japan

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Ōsaka-sayama, Japan

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Saga, Japan

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Sapporo, Japan

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Shiwa, Japan

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Suntogun, Japan

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Tsu, Japan

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Yokohama, Japan

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Moscow, Russia

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Murmansk, Russia

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Nizhny Novgorod, Russia

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Novosibirsk, Russia

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Obninsk, Russia

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Omsk, Russia

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Saint Petersburg, Russia

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Ufa, Russia

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Ilsan, Gyeonggi-do, 10408, South Korea

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Seongnam-si, Gyeonggi-do, 13620, South Korea

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Busan, 49241, South Korea

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Daegu, 41944, South Korea

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Seoul, 3080, South Korea

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Seoul, 3722, South Korea

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Seoul, 5505, South Korea

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Seoul, 6351, South Korea

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Barcelona, Spain

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Madrid, Spain

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Oviedo, Spain

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Pamplona Madrid, Spain

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Santander, Spain

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Chiayi City, Taiwan

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Kaohsiung City, Taiwan

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Taichung, Taiwan

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Tainan, Taiwan

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Taipei, Taiwan

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Taoyuan District, Taiwan

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Bangkok, Thailand

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Chang Mai, Thailand

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Khon Kaen, Thailand

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Phitsanulok, Thailand

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Songkhla, Thailand

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Dnipro, Ukraine

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IvanoFrankivsk, Ukraine

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Kharkiv, Ukraine

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Kropyvnitskyi, Ukraine

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Kyiv, Ukraine

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Lviv, Ukraine

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Odesa, Ukraine

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Uzhhorod, Ukraine

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Hanoi, Vietnam

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Hochiminh, Vietnam

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Related Publications (7)

  • Chan SL, Kudo M, Sangro B, Kelley RK, Kim JH, Pham B, Hong JY, Waldschmidt DT, Marino D, Joycelyn Lee JX, Gerolami R, Burgoyne AM, Li Q, Nakamura H, Sun P, Baur B, Rimassa L. Early Safety Results from the Phase 3b SIERRA Study of Durvalumab and Tremelimumab as First-Line Treatment for Participants with Unresectable Hepatocellular Carcinoma and a Poor Prognosis. Liver Cancer. 2025 Dec 18. doi: 10.1159/000549955. Online ahead of print.

  • Rimassa L, Chan SL, Sangro B, Lau G, Kudo M, Reig M, Breder V, Ryu MH, Ostapenko Y, Sukeepaisarnjaroen W, Varela M, Tougeron D, Crysler OV, Bouattour M, Van Dao T, Tam VC, Faccio A, Furuse J, Jeng LB, Kang YK, Kelley RK, Paskow MJ, Ran D, Xynos I, Kurland JF, Negro A, Abou-Alfa GK. Five-year overall survival update from the HIMALAYA study of tremelimumab plus durvalumab in unresectable HCC. J Hepatol. 2025 Oct;83(4):899-908. doi: 10.1016/j.jhep.2025.03.033. Epub 2025 Apr 11.

  • Lau G, Abou-Alfa GK, Cheng AL, Sukeepaisarnjaroen W, Van Dao T, Kang YK, Thungappa SC, Kudo M, Sangro B, Kelley RK, Furuse J, Park JW, Sunpaweravong P, Fasolo A, Yau T, Kawaoka T, Azevedo S, Reig M, Assenat E, Yarchoan M, He AR, Makowsky M, Gupta C, Negro A, Chan SL. Outcomes in the Asian subgroup of the phase III randomised HIMALAYA study of tremelimumab plus durvalumab in unresectable hepatocellular carcinoma. J Hepatol. 2025 Feb;82(2):258-267. doi: 10.1016/j.jhep.2024.07.017. Epub 2024 Jul 31.

  • Sangro B, Galle PR, Kelley RK, Charoentum C, De Toni EN, Ostapenko Y, Heo J, Cheng AL, Wilson Woods A, Gupta C, Abraham J, McCoy CL, Patel N, Negro A, Vogel A, Abou-Alfa GK. Patient-Reported Outcomes From the Phase III HIMALAYA Study of Tremelimumab Plus Durvalumab in Unresectable Hepatocellular Carcinoma. J Clin Oncol. 2024 Aug 10;42(23):2790-2799. doi: 10.1200/JCO.23.01462. Epub 2024 May 28.

  • Abou-Alfa GK, Lau G, Kudo M, Chan SL, Kelley RK, Furuse J, Sukeepaisarnjaroen W, Kang YK, Van Dao T, De Toni EN, Rimassa L, Breder V, Vasilyev A, Heurgue A, Tam VC, Mody K, Thungappa SC, Ostapenko Y, Yau T, Azevedo S, Varela M, Cheng AL, Qin S, Galle PR, Ali S, Marcovitz M, Makowsky M, He P, Kurland JF, Negro A, Sangro B. Tremelimumab plus Durvalumab in Unresectable Hepatocellular Carcinoma. NEJM Evid. 2022 Aug;1(8):EVIDoa2100070. doi: 10.1056/EVIDoa2100070. Epub 2022 Jun 6.

  • Addendum 1: Society for Immunotherapy of Cancer (SITC) clinical practice guideline on immunotherapy for the treatment of hepatocellular carcinoma. J Immunother Cancer. 2023 Sep;11(9):e002794add1. doi: 10.1136/jitc-2021-002794add1. No abstract available.

  • Patel TH, Brewer JR, Fan J, Cheng J, Shen YL, Xiang Y, Zhao H, Lemery SJ, Pazdur R, Kluetz PG, Fashoyin-Aje LA. FDA Approval Summary: Tremelimumab in Combination with Durvalumab for the Treatment of Patients with Unresectable Hepatocellular Carcinoma. Clin Cancer Res. 2024 Jan 17;30(2):269-273. doi: 10.1158/1078-0432.CCR-23-2124.

Related Links

MeSH Terms

Conditions

Carcinoma, Hepatocellular

Interventions

durvalumabtremelimumabSorafenib

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsLiver NeoplasmsDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Intervention Hierarchy (Ancestors)

Phenylurea CompoundsUreaAmidesOrganic ChemicalsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsNiacinamideNicotinic AcidsAcids, HeterocyclicHeterocyclic CompoundsPyridinesHeterocyclic Compounds, 1-Ring

Results Point of Contact

Title
Global Clinical Lead
Organization
AstraZeneca Clinical Study Information Center

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 19, 2017

First Posted

October 2, 2017

Study Start

October 11, 2017

Primary Completion

August 27, 2021

Study Completion (Estimated)

August 27, 2026

Last Updated

March 20, 2026

Results First Posted

June 18, 2023

Record last verified: 2026-03

Locations