NCT03229252

Brief Summary

28-Day double-blinded efficacy and safety trial of SPX-101 Inhalation Solution in adult subjects with cystic fibrosis.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
91

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Aug 2017

Geographic Reach
5 countries

25 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 14, 2017

Completed
11 days until next milestone

First Posted

Study publicly available on registry

July 25, 2017

Completed
7 days until next milestone

Study Start

First participant enrolled

August 1, 2017

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 20, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 20, 2019

Completed
6 months until next milestone

Results Posted

Study results publicly available

December 30, 2019

Completed
Last Updated

December 30, 2019

Status Verified

December 1, 2019

Enrollment Period

1.9 years

First QC Date

July 14, 2017

Results QC Date

August 26, 2019

Last Update Submit

December 6, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in Percent Predicted FEV1

    Baseline and Day 28

Secondary Outcomes (2)

  • Number of Participants With Adverse Events

    Day 1 through Day 28

  • Change From Baseline Through Day 28 in Clinical Laboratory Tests

    Day 1 through Day 28

Study Arms (3)

Placebo

PLACEBO COMPARATOR

Placebo Inhalation solution twice daily for 28 days.

Drug: Placebo Inhalation Solution

SPX-101 Low Dose

EXPERIMENTAL

Inhalation solution twice daily for 28 days.

Drug: SPX-101

SPX-101 High Dose

EXPERIMENTAL

Inhalation solution twice daily for 28 days.

Drug: SPX-101

Interventions

Normal Saline Inhalation Solution

Placebo

SPX-101 Inhalation Solution

SPX-101 High DoseSPX-101 Low Dose

Eligibility Criteria

Age18 Years - 50 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Confirmed diagnosis of cystic fibrosis
  • ppFEV1 (percent predicted FEV1) between 50.0% and 80.0%
  • Stable CF Lung Disease
  • Males and non-pregnant, non-lactating females

You may not qualify if:

  • Significant unstable co-morbidities within 28 days of screening
  • Has received an investigational drug within 28 days of screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

University of Calgary Heritage Medical Research Center

Calgary, Alberta, T2N 1N4, Canada

Location

Ottawa Hospital Research Institute/Institut de Recherche de l'Hospital d'Ottawa

Ottawa, Ontario, K1H 8L6, Canada

Location

Saint Michael's Hospital

Toronto, Ontario, M5B1W8, Canada

Location

Hospices Civils de Lyon (HCL)

Pierre-Bénite, Auvergne-Rhône-Alpes, France

Location

Centre Hospitalier Universitaire Brest

Roscoff, Brittany Region, France

Location

CHU de Rouen

Rouen, Haute-Normandie, France

Location

CHU de Montpellier

Montpellier, Languedoc-Roussillon, France

Location

CHU de Angers

Angers, Pays de la Loire Region, France

Location

Hopital Pasteur

Nice, Provence-Alpes-Côte d'Azur Region, France

Location

Assistance Publique-Hôpitaux de Paris Hôpital Cochin

Paris, France

Location

Istituto Giannina Gaslini Ospedale Pediatrico

Genoa, Italy

Location

Hospital de Santa Maria

Lisbon, Portugal

Location

Belfast Health and Social Care Trust

Belfast, United Kingdom

Location

Heart of England NHS Foundation Trust

Birmingham, United Kingdom

Location

University Hospitals Bristol NHS Foundation Trust

Bristol, United Kingdom

Location

Western General Hospital - NHS Lothian

Edinburgh, United Kingdom

Location

Royal Devon and Exeter NHS Foundation Trust

Exeter, United Kingdom

Location

NHS Greater Glasgow and Clyde

Glasgow, United Kingdom

Location

The Leeds Teaching Hospitals NHS Trust

Leeds, United Kingdom

Location

Liverpool Heart and Chest Hospital NHS Foundation Trust

Liverpool, United Kingdom

Location

Barts Health NHS Trust Saint Bartholomews Hospital

London, United Kingdom

Location

Royal Brompton and Harefield NHS Foundation Trust

London, United Kingdom

Location

University Hospital of South Manchester NHS Foundation Trust

Manchester, United Kingdom

Location

Newcastle Upon Tyne Hospitals

Newcastle upon Tyne, United Kingdom

Location

Nottingham University Hospitals NHS Trust

Nottingham, United Kingdom

Location

MeSH Terms

Conditions

Cystic Fibrosis

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, Diseases

Limitations and Caveats

No Limitations or Caveats

Results Point of Contact

Title
Dr. Rob Tarran
Organization
Spyryx Biosciences

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Double-Blind
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 14, 2017

First Posted

July 25, 2017

Study Start

August 1, 2017

Primary Completion

June 20, 2019

Study Completion

June 20, 2019

Last Updated

December 30, 2019

Results First Posted

December 30, 2019

Record last verified: 2019-12

Data Sharing

IPD Sharing
Will not share

Locations