NCT03056989

Brief Summary

Ascending dose, 7-day, open label safety trial of SPX-101 Inhalation Solution in adult subjects with cystic fibrosis.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
5

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started May 2017

Shorter than P25 for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 15, 2017

Completed
2 days until next milestone

First Posted

Study publicly available on registry

February 17, 2017

Completed
3 months until next milestone

Study Start

First participant enrolled

May 31, 2017

Completed
2 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 2, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 2, 2017

Completed
Last Updated

September 5, 2017

Status Verified

September 1, 2017

Enrollment Period

2 months

First QC Date

February 15, 2017

Last Update Submit

September 1, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Number of participants with adverse events

    Day 1 through Day 15

Secondary Outcomes (2)

  • Relative change from baseline through Day 8 in percent predicted FEV1

    Screening and Day 1 through Day 8

  • Change from baseline through Day 8 in clinical laboratory tests

    Screening and Day 1 through Day 8

Study Arms (3)

SPX-101 Low Dose

EXPERIMENTAL

Inhalation Solution twice daily for 7 days.

Drug: SPX-101

SPX-101 Mid Dose

EXPERIMENTAL

Inhalation Solution twice daily for 7 days.

Drug: SPX-101

SPX-101 High Dose

EXPERIMENTAL

Inhalation Solution twice daily for 7 days.

Drug: SPX-101

Interventions

Inhalation solution twice daily for 7 days.

SPX-101 High DoseSPX-101 Low DoseSPX-101 Mid Dose

Eligibility Criteria

Age18 Years - 50 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Confirmed diagnosis of CF
  • FEV1 ≥ 40% predicted normal
  • Stable CF lung disease
  • Non-pregnant, non-lactating females

You may not qualify if:

  • Significant unstable co-morbidities within 28 days of screening as judged by the Investigator.
  • Has received an investigational drug within the past 30 days

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Saint Michael's Hospital

Toronto, Ontario, M5B1W8, Canada

Location

Related Publications (1)

  • Couroux P, Farias P, Rizvi L, Griffin K, Hudson C, Crowder T, Tarran R, Tullis E. First clinical trials of novel ENaC targeting therapy, SPX-101, in healthy volunteers and adults with cystic fibrosis. Pulm Pharmacol Ther. 2019 Oct;58:101819. doi: 10.1016/j.pupt.2019.101819. Epub 2019 Jul 11.

MeSH Terms

Conditions

Cystic Fibrosis

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, Diseases

Study Officials

  • Elizabeth Tullis, MD

    Unity Health Toronto

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 15, 2017

First Posted

February 17, 2017

Study Start

May 31, 2017

Primary Completion

August 2, 2017

Study Completion

August 2, 2017

Last Updated

September 5, 2017

Record last verified: 2017-09

Locations