NCT03102320

Brief Summary

The key purpose of the main part of the study is to assess efficacy and safety of anetumab ravtansine as monotherapy or combination therapy for mesothelin expressing advanced solid tumors. The main purpose of the safety lead-in (dose-finding) part of the study is to determine the safety and tolerability of anetumab ravtansine in combination with cisplatin and in combination with gemcitabine, and to determine the MTD of anetumab ravtansine in combination with cisplatin for mesothelin expressing advanced cholangiocarcinoma and in combination with gemcitabine for mesothelin expressing advanced adenocarcinoma of the pancreas. Patients will receive anetumab ravtansine every three weeks in monotherapy for most indications. In cholangiocarinoma and adenocarinoma of the pancreas, 3-weekly anetumab ravtansine is administered in combination with cisplatin or gemcitabine respectively (both administered in a 2 week on / 1 week off schedule). Treatment will continue until disease progression or until another criterion for withdrawal is met. .Efficacy will be measured by evaluating the tumor's objective response rate. Radiological tumor assessments will be performed at defined time points until the patient's disease progresses. Blood samples will be collected for safety, pharmacokinetic and biomarker analysis. Archival or fresh biopsy tissue will also be collected for mesothelin expression testing and biomarker analyses.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
173

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started May 2017

Longer than P75 for phase_1

Geographic Reach
12 countries

72 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 30, 2017

Completed
6 days until next milestone

First Posted

Study publicly available on registry

April 5, 2017

Completed
2 months until next milestone

Study Start

First participant enrolled

May 26, 2017

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 16, 2020

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 26, 2021

Completed
Last Updated

June 30, 2022

Status Verified

June 1, 2022

Enrollment Period

3.3 years

First QC Date

March 30, 2017

Last Update Submit

June 28, 2022

Conditions

Keywords

cholangiocarcinomapancreatic cancertriple-negative breast cancernon-small cell lung cancerthymic carcinomagastric including gastroesophageal junction cancer

Outcome Measures

Primary Outcomes (3)

  • Number of patients in the safety lead-in (SLI) phase who completed Cycle 1 or had a DLT and were not replaced.

    During SLI, patients with cholangiocarcinoma received anetumab ravtansine in combination with cisplatin and patients with pancreatic adenocarcinoma received anetumab ravtansine in combination with gemcitabine. The highest dose of anetumab ravtansine that can be given so that not more than 1 out of 6 patients experiences a dose-limiting toxicity (DLT) during the DLT evaluation period were declared as the MTD for anetumab ravtansine in combination with cisplatin or with gemcitabine.

    At least 3 weeks after the last patient starts treatment

  • Objective response (qualitative improvement from baseline) of anetumab ravtansine for monotherapy and combination therapy in mesothelin expressing advanced solid tumors

    A patient is a responder if the patient has a best response compared to baseline of complete response (CR) or partial response (PR) among all post-baseline tumor assessments, as determined per RECIST 1.1 criteria (ITMIG modified RECIST 1.1 criteria for thymic carcinoma)

    Up to approximately 26 months after patient starts treatment

  • Durable disease control (lack of progression from baseline) of anetumab ravtansine in indications pancreatic and gastric cancer (co-primary endpoint)

    A patient experiences durable disease control if the patient has a tumor response compared to baseline of CR, PR or stable disease (SD) among the post-baseline tumor assessments made at least 180 days from first treatment, without prior disease progression

    Up to approximately 26 months after patient starts treatment

Secondary Outcomes (6)

  • Number of serious and non-serious adverse events (AEs)

    Approximately 26 months (Until 30 days after the last day of study treatment, or until later resolution of adverse events or determination by the investigator that the event will not improve)

  • Disease control rate (DCR)

    Up to approximately 24 months after last patient starts treatment, or until earlier disease progression [assessed every 6 weeks for the first 6 months, every 9 weeks until end of year 1 and every 12 weeks thereafter]

  • Duration of response (DOR)

    Up to approximately 24 months after last patient starts treatment, or until earlier disease progression [assessed every 6 weeks for the first 6 months, every 9 weeks until end of year 1 and every 12 weeks thereafter]

  • Durable response rate (DRR)

    Up to approximately 24 months after last patient starts treatment, or until earlier disease progression [assessed every 6 weeks for the first 6 months, every 9 weeks until end of year 1 and every 12 weeks thereafter]

  • Progression free survival (PFS)

    Up to approximately 24 months after last patient starts treatment, or until earlier disease progression [assessed every 6 weeks for the first 6 months, every 9 weeks until end of year 1 and every 12 weeks thereafter]

  • +1 more secondary outcomes

Study Arms (3)

Cholangiocarcinoma

EXPERIMENTAL

Safety lead-in phase will determine the MTD of anetumab ravtansine administered in combination with cisplatin. Please note the study is no longer recruiting for the cholangiocarcinoma safety lead-in phase. During the main study phase anetumab ravtansine will be administered at the determined MTD in combination with cisplatin. Please note the main study phase for cholangiocarcinoma will no longer be going ahead.

Drug: CisplatinDrug: Anetumab ravtansine (BAY94-9343)

Adenocarcinoma of the pancreas

EXPERIMENTAL

Safety lead-in phase will determine the MTD of anetumab ravtansine administered in combination with gemcitabine During the main study phase, anetumab ravtansine will be administered at the determined MTD in combination with gemcitabine

Drug: GemcitabineDrug: Anetumab ravtansine (BAY94-9343)

Other solid tumors

EXPERIMENTAL

(Non-small cell adenocarcinoma of the lung (NSCLC adenocarcinoma), Adenocarcinoma of the breast - triple negative (TNBC), Gastric adenocarcinoma including gastroesophageal junction (GEJ Cancer, Thymic carcinoma) During the main study phase, anetumab ravtansine will be administered at dose of 6.5 mg/kg in solid tumors

Drug: Anetumab ravtansine (BAY94-9343)

Interventions

Cisplatin 25 mg/m2 IV administered on day 1 and day 8 of 21 day cycle, for up to maximum 6 cycles

Cholangiocarcinoma

Gemcitabine 1000 mg/m2 IV administered on days 1 and 8 of a 21-day cycle

Adenocarcinoma of the pancreas

Anetumab ravtansine 6.5mg/kg IV in monotherapy indications. For combination indications, the MTD determined in safety lead in phase will be administered

Adenocarcinoma of the pancreasCholangiocarcinomaOther solid tumors

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Availability of tumor tissue for mesothelin expression testing and for further biomarker analysis
  • At least one measurable lesion according to Response Evaluation Criteria in Solid Tumors (RECIST 1.1) (or for thymic carcinoma, at least one measurable lesion per International Thymic Malignancy Interest Group (ITMIG) modified RECIST 1.1 criteria
  • Adequate bone marrow, liver, renal and coagulation function
  • Left ventricular ejection fraction (LVEF) ≥ 50% of the lower limit of normal (LLN) according to local institutional ranges
  • Eastern Cooperative Oncology Group (ECOG) 0 or 1

You may not qualify if:

  • Exposure to more than one prior anti-tubulin/microtubule agent
  • Corneal epitheliopathy or any eye disorder that may predispose the patients to this condition
  • Symptomatic Central nervous system (CNS) metastases and/or carcinomatous meningitis
  • Contraindication to both CT and MRI contrast agents
  • Active hepatitis B or C infection
  • Pregnant or breast-feeding patients

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (72)

Mayo Clinic Hospital

Phoenix, Arizona, 85054-4502, United States

Location

University of Southern California

Los Angeles, California, 90033, United States

Location

Stanford Health Care

Stanford, California, 94305, United States

Location

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

Indiana University School of Medicine

Indianapolis, Indiana, 46202, United States

Location

Ochsner Medical Center - New Orleans

New Orleans, Louisiana, 70121, United States

Location

National Cancer Institute - Maryland

Bethesda, Maryland, 20892, United States

Location

Barbara Ann Karmanos Cancer Institute

Farmington Hills, Michigan, 48334, United States

Location

Mayo Clinic - Rochester

Rochester, Minnesota, 55905, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Texas Oncology, PA

Dallas, Texas, 75246, United States

Location

University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Blacktown Cancer & Haematology Centre

Blacktown, New South Wales, 2148, Australia

Location

Mid North Coast Cancer Institute

Coffs Harbour, New South Wales, 2450, Australia

Location

Kinghorn Cancer Centre

Darlinghurst, New South Wales, 2010, Australia

Location

Northern Cancer Institute

St Leonards, New South Wales, 2065, Australia

Location

Flinders Medical Centre

Adelaide, South Australia, 5042, Australia

Location

Epworth HealthCare

Richmond, Victoria, 3122, Australia

Location

Sir Charles Gairdner Hospital

Nedlands, Western Australia, 6009, Australia

Location

St John of God Healthcare

Subiaco, Western Australia, 6008, Australia

Location

Hôpital Erasme/Erasmus Ziekenhuis

Bruxelles - Brussel, 1070, Belgium

Location

UZ Antwerpen

Edegem, 2650, Belgium

Location

UZ Leuven Gasthuisberg

Leuven, 3000, Belgium

Location

CHU de Liège

Liège, 4000, Belgium

Location

Cross Cancer Institute

Edmonton, Alberta, T6G 1Z2, Canada

Location

Princess Margaret Cancer Centre - UHN

Toronto, Ontario, M5G 2M9, Canada

Location

Sir Mortimer B. Davis Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

McGill University Health Center

Montreal, Quebec, H4A 3J1, Canada

Location

Hopital Jean Minjoz

Besançon, 25030, France

Location

Hôpital Henri Mondor

Créteil, 94010, France

Location

Centre Oscar Lambret - Lille

Lille, 59020, France

Location

Centre Léon Bérard

Lyon, 69008, France

Location

C.H.U. Timone

Marseille, 13385, France

Location

Centre René Gauducheau

Nantes, 44805, France

Location

Centre Antoine Lacassagne

Nice, 06102, France

Location

Centre Hospitalier Lyon Sud

Pierre-Bénite, 69495, France

Location

Hôpital de la Milétrie

Poitiers, 86021, France

Location

Hôpital Pontchaillou

Rennes, 35033, France

Location

Centre Eugène Marquis - Rennes Cedex

Rennes, 35062, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

A.O.U. di Bologna Policlinico S.Orsola Malpighi

Bologna, Emilia-Romagna, 40138, Italy

Location

A.O.U. di Modena - Policlinico

Modena, Emilia-Romagna, 41124, Italy

Location

Istituto Clinico Humanitas - Humanitas Mirasole S.p.A.

Milan, Lombardy, 20089, Italy

Location

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, Lombardy, 20133, Italy

Location

ASST Grande Ospedale Metropolitano Niguarda

Milan, Lombardy, 20162, Italy

Location

A.O.U.I. Verona

Verona, Veneto, 37134, Italy

Location

Nederlands Kanker Instituut

Amsterdam, 1066 CX, Netherlands

Location

Maastricht UMC

Maastricht, 6229 HX, Netherlands

Location

National University Hospital

Singapore, 119228, Singapore

Location

National Cancer Center Singapore

Singapore, 169610, Singapore

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Hospital Universitario Quirón de Madrid

Pozuelo de Alarcón, Madrid, 28223, Spain

Location

Hospital del Mar

Barcelona, 08003, Spain

Location

Ciutat Sanitària i Universitaria de la Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Clínic i Provincial de Barcelona

Barcelona, 08036, Spain

Location

Hospital General Universitario Gregorio Marañón | Oncología

Madrid, 28007, Spain

Location

Hospital Ramón y Cajal | Oncología

Madrid, 28034, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Centro Integral Oncológico Clara Campal

Madrid, 28050, Spain

Location

Hospital Virgen de la Victoria

Málaga, 29010, Spain

Location

Ospedale Regionale Bellinzona

Bellinzona, Canton Ticino, 6500, Switzerland

Location

Kantonsspital Graubünden

Chur, Kanton Graubünden, 7000, Switzerland

Location

Leicester Royal Infirmary

Leicester, Leicestershire, LE1 5WW, United Kingdom

Location

Belfast City Hospital

Belfast, North Ireland, BT12 7AB, United Kingdom

Location

Royal Marsden NHS Trust (Surrey)

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Guy's Hospital

London, SE1 9RT, United Kingdom

Location

Royal Marsden Hospital (London)

London, SW3 6JJ, United Kingdom

Location

Christie Hospital

Manchester, M20 4BX, United Kingdom

Location

Related Links

MeSH Terms

Conditions

NeoplasmsCholangiocarcinomaPancreatic NeoplasmsTriple Negative Breast NeoplasmsCarcinoma, Non-Small-Cell LungThymoma

Interventions

CisplatinGemcitabineanetumab ravtansine

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeDigestive System NeoplasmsNeoplasms by SiteEndocrine Gland NeoplasmsDigestive System DiseasesPancreatic DiseasesEndocrine System DiseasesBreast NeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract DiseasesNeoplasms, Complex and MixedThymus NeoplasmsLymphatic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Chlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum CompoundsHeterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-Ring

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 30, 2017

First Posted

April 5, 2017

Study Start

May 26, 2017

Primary Completion

September 16, 2020

Study Completion

July 26, 2021

Last Updated

June 30, 2022

Record last verified: 2022-06

Data Sharing

IPD Sharing
Will not share

Availability of this study's data will later be determined according to Bayer's commitment to the EFPIA/PhRMA "Principles for responsible clinical trial data sharing". This pertains to scope, timepoint and process of data access. As such, Bayer commits to sharing upon request from qualified researchers patient-level clinical trial data, study-level clinical trial data, and protocols from clinical trials in patients for medicines and indications approved in the US and EU as necessary for conducting legitimate research. This applies to data on new medicines and indications that have been approved by the EU and US regulatory agencies on or after January 01, 2014. Interested researchers can use www.clinicalstudydatarequest.com to request access to anonymized patient-level data and supporting documents from clinical studies to conduct research. Information on the Bayer criteria for listing studies and other relevant information is provided in the Study sponsors section of the portal.

Locations