NCT02813694

Brief Summary

This study evaluates the safety and efficacy of lefamulin, a pleuromutilin, for the treatment of adults with moderate community-acquired bacterial pneumonia

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
738

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Aug 2016

Geographic Reach
20 countries

155 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 20, 2016

Completed
7 days until next milestone

First Posted

Study publicly available on registry

June 27, 2016

Completed
1 month until next milestone

Study Start

First participant enrolled

August 1, 2016

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2018

Completed
1.8 years until next milestone

Results Posted

Study results publicly available

October 23, 2019

Completed
Last Updated

October 23, 2019

Status Verified

September 1, 2019

Enrollment Period

1.4 years

First QC Date

June 20, 2016

Results QC Date

August 28, 2019

Last Update Submit

October 22, 2019

Conditions

Keywords

PneumoniaCABPCAPCommunity acquired bacterial pneumonia

Outcome Measures

Primary Outcomes (1)

  • Early Clinical Response (ECR)

    ECR was defined as survival with improvement in at least 2 signs and symptoms of CABP (relative to baseline), no worsening of any CABP sign or symptom, and no use of concomitant antibiotics for the treatment of CABP through the ECR assessment

    96 hours +/- 24 hours after first dose of study drug

Secondary Outcomes (1)

  • Investigator's Assessment of Clinical Response (IACR)

    IACR was assessed at the Test-of-Cure Visit; 5 to 10 days after last dose of study drug

Study Arms (2)

lefamulin

EXPERIMENTAL

oral lefamulin, 600mg

Drug: lefamulin

Moxifloxacin

ACTIVE COMPARATOR

oral moxifloxacin, 400mg

Drug: Moxifloxacin

Interventions

antibacterial agent

Also known as: BC-3781
lefamulin

antibacterial agent

Also known as: Avelox
Moxifloxacin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Each subject must:
  • Be male or female at least 18 years of age.
  • Provide written informed consent and be willing and able to adhere to the study-specified procedures and restrictions.
  • Have an acute illness (less than or equal to 7 days duration) with at least 3 of the following symptoms consistent with a lower respiratory tract infection (new or worsening):
  • Dyspnea.
  • New or increased cough.
  • Purulent sputum production.
  • Chest pain due to pneumonia.
  • Have at least 2 of the following vital sign abnormalities:
  • Fever (body temperature \> 38.0 °C (100.4 °F) measured orally or equivalent temperature from an alternate body site) or hypothermia (body temperature \< 35.0 °C (95.0 °F) measured orally or equivalent temperature from an alternate body site).
  • Hypotension (systolic blood pressure \< 90 mmHg).
  • Tachycardia (heart rate \> 100 beats/min).
  • Tachypnea (respiratory rate \> 20 breaths/min).
  • Have at least 1 other clinical sign or laboratory finding of CABP:
  • Hypoxemia (i.e., O2 saturation \< 90 % on room air or while receiving supplemental oxygen at subject's baseline requirement or PaO2 \< 60 mmHg).
  • +4 more criteria

You may not qualify if:

  • Each subject must NOT:
  • Have received more than a single dose of a short-acting oral or IV antibacterial for CABP within 72 hours before randomization.
  • Require concomitant systemic antibacterial therapy potentially effective against CABP pathogens.
  • Have been hospitalized for 2 or more days within 90 days prior to the onset of symptoms or have resided in a nursing home or long-term healthcare facility within 30 days prior to the onset of symptoms. NOTE: Residence in an independent living facility is permitted.
  • Have confirmed or suspected CABP caused by a pathogen known to be resistant to any of the study drugs (e.g., MRSA, Pseudomonas aeruginosa, any pathogen of the Enterobacteriaceae Family) or attributable to etiologies other than community acquired bacterial pathogens (e.g., ventilator associated pneumonia, hospital acquired bacterial pneumonia, bacterial aspiration pneumonia, Pneumocystis jiroveci pneumonia or other fungal pneumonia, viral or mycobacterial infection of the lung).
  • Have a noninfectious cause of pulmonary infiltrates (e.g., pulmonary embolism, chemical pneumonitis from aspiration, hypersensitivity pneumonia, congestive heart failure, bronchial obstruction, lung cancer, cystic fibrosis).
  • Have confirmed or suspected pleural empyema (does not include sterile parapneumonic effusions).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (155)

1080

Beverly Hills, California, United States

Location

Site 1065

Fresno, California, 93701, United States

Location

1078

Northridge, California, United States

Location

Site 1072

Oxnard, California, 93030, United States

Location

Site 1070

Sacramento, California, 95817, United States

Location

1079

Sherman Oaks, California, United States

Location

Site 1053

Sylmar, California, 91342, United States

Location

Site 1064

DeBary, Florida, 32713, United States

Location

Site 1052

DeLand, Florida, 32720, United States

Location

1076

Miami, Florida, United States

Location

Site 1051

Michigan City, Indiana, 46360, United States

Location

Site 1057

Natchitoches, Louisiana, 71457, United States

Location

Site 1073

New Bedford, Massachusetts, 02740, United States

Location

Site 1055

Detroit, Michigan, 48201, United States

Location

Site 1062

Detroit, Michigan, 48235, United States

Location

Site 1068

Royal Oak, Michigan, 48073, United States

Location

Site 1058

St Louis, Missouri, 63110, United States

Location

Site 1054

Butte, Montana, 59701, United States

Location

Site 1067

Lima, Ohio, 45801, United States

Location

Site 1056

Rapid City, South Dakota, 57702, United States

Location

1077

Hendersonville, Tennessee, United States

Location

Site 1060

Houston, Texas, 77070, United States

Location

Site 1069

Houston, Texas, 77093, United States

Location

Site 1066

Splendora, Texas, 77372, United States

Location

Site 1059

Charlottesville, Virginia, 22908, United States

Location

Site 3056

Buenos Aires, Argentina

Location

Site 3059

Buenos Aires AV, Argentina

Location

Site 3054

Córdoba, X5000EPU, Argentina

Location

Site 3052

Córdoba, Argentina

Location

Site 3057

Córdoba, Argentina

Location

Site 3058

General Pacheco, Argentina

Location

Site 3051

La Plata, Argentina

Location

Site 3053

La Plata, Argentina

Location

Site 3154

Belo Horizonte, 30150-221, Brazil

Location

Site 3153

Passo Fundo, 99010-080, Brazil

Location

Site 3152

São José do Rio Preto, 15090-000, Brazil

Location

4162

Rousse, 7002, Bulgaria

Location

Site 4154

Sliven, 8800, Bulgaria

Location

Site 4160

Sofia, 1233, Bulgaria

Location

Site 4157

Sofia, 1336, Bulgaria

Location

Site 4153

Sofia, 1606, Bulgaria

Location

Site 4156

Sofia, 1606, Bulgaria

Location

Site 4161

Sofia, 1680, Bulgaria

Location

4163

Sofia, Bulgaria

Location

4164

Sofia, Bulgaria

Location

4165

Sofia, Bulgaria

Location

Site 4158

Stara Zagora, 6000, Bulgaria

Location

Site 4159

Vidin, 3700, Bulgaria

Location

Site 4152

Vratsa, 3000, Bulgaria

Location

Site 3353

Santiago, Chile

Location

Site 3356

Santiago, Chile

Location

Site 3357

Santiago, Chile

Location

Site 3354

Talca, Chile

Location

Site 3352

Temuco, Chile

Location

Site 3355

Valdivia, Chile

Location

Site 4256

Batumi, Georgia

Location

Site 4253

Tbilisi, 101, Georgia

Location

Site 4255

Tbilisi, 159, Georgia

Location

Site 4252

Tbilisi, 179, Georgia

Location

Site 4254

Tbilisi, 186, Georgia

Location

Site 4354

Budapest, 1122, Hungary

Location

Site 4353

Budapest, 1134, Hungary

Location

Site 4352

Mátraháza, 3233, Hungary

Location

Site 4351

Törökbálint, 2045, Hungary

Location

Site 4451

Liepāja, LV3414, Latvia

Location

Site 4453

Riga, LV-1002, Latvia

Location

Site 4452

Valmiera, LV 4201, Latvia

Location

Site 1153

Aguascalientes, 20230, Mexico

Location

Site 1154

Guadalajara, 44280, Mexico

Location

Site 1151

Monterrey, 64460, Mexico

Location

Site 1152

Toluca, 52140, Mexico

Location

Site 3264

Grau, Lima region, Peru

Location

Site 3262

Arequipa, Peru

Location

Site 3263

Cusco, Peru

Location

Site 3261

Cuzco, Peru

Location

Site 3254

Ica, Peru

Location

Site 3259

Iquitos, Peru

Location

Site 3251

La Libertad, Peru

Location

Site 3252

Lima, Peru

Location

Site 3253

Lima, Peru

Location

Site 3255

Lima, Peru

Location

Site 3257

Lima, Peru

Location

Site 3260

Lima, Peru

Location

Site 3265

Lima, Peru

Location

Site 3258

Lima Lima, Peru

Location

Site 3256

Piura, Peru

Location

Site 2053

Caloocan, 1400, Philippines

Location

Site 2055

Cebu, 6000, Philippines

Location

Site 2052

Iloilo City, 5000, Philippines

Location

Site 2054

Quezon, 1109, Philippines

Location

Site 2056

Quezon City, 1100, Philippines

Location

Site 2051

Quezon City, Philippines

Location

Site 4755

Bochnia, 32-700, Poland

Location

Site 4754

Chodzież, 64-800, Poland

Location

Site 4753

Krakow, 31-011, Poland

Location

Site 4756

Krakow, 31-202, Poland

Location

Site 4757

Siedlce, 08-110, Poland

Location

Site 4855

Bucharest, 21105, Romania

Location

Site 4858

Bucharest, 21659, Romania

Location

Site 4854

Bucharest, 30303, Romania

Location

Site 4853

Cluj-Napoca, 400371, Romania

Location

Site 4851

Codlea, 505100, Romania

Location

Site 4857

Craiova, 200515, Romania

Location

Site 4856

Timișoara, 300310, Romania

Location

Site 4953

Barnaul, 656045, Russia

Location

Site 4957

Moscow, 117913, Russia

Location

Site 4952

Moscow, 119192, Russia

Location

Site 4954

Novosibirsk, 6300, Russia

Location

Site 4955

Saint Petersburg, 1962, Russia

Location

Site 4951

Saint Petersburg, 198205, Russia

Location

Site 4959

Saratov, 410053, Russia

Location

Site 4958

Smolensk, 214019, Russia

Location

Site 5052

Belgrade, 11000, Serbia

Location

Site 5056

Belgrade, 11000, Serbia

Location

Site 5051

Belgrade, 11080, Serbia

Location

5057

Belgrade, Serbia

Location

Site 5053

Kamenitz, 21204, Serbia

Location

Site 5055

Knez-Selo, 1820, Serbia

Location

Site 5054

Kragujevac, 34000, Serbia

Location

Site 5151

Bloemfontein, 9301, South Africa

Location

Site 5154

Krugersdorp, 1739, South Africa

Location

Site 5155

Middelburg, 1050, South Africa

Location

Site 5156

Pretoria, South Africa

Location

Site 5152

Queenswood, 186, South Africa

Location

Site 5153

Witbank, 1035, South Africa

Location

Site 2254

Uijeongbu-si, Gyeonggi-do, 11765, South Korea

Location

Site 2257

Bucheon-si, 14647, South Korea

Location

Site 2253

Daegu, 42415, South Korea

Location

Site 2255

Seoul, 143-914, South Korea

Location

Site 2256

Seoul, 152-703, South Korea

Location

Site 2251

Seoul, 2259, South Korea

Location

Site 2252

Seoul, 7985, South Korea

Location

Site 4554

Alicante, 3203, Spain

Location

Site 4556

Badalona, 8916, Spain

Location

Site 4552

Barcelona, 8003, Spain

Location

Site 4555

Barcelona, 8035, Spain

Location

Site 4553

Madrid, 28040, Spain

Location

Site 4551

Madrid, 28046, Spain

Location

Site 2352

Kaohsiung City, 82445, Taiwan

Location

Site 2351

Kaohsiung City, Taiwan

Location

Site 2354

Taipei, Taiwan

Location

Site 5264

Chernivtsi, 58001, Ukraine

Location

Site 5261

Ivano-Frankivsk, 76018, Ukraine

Location

Site 5258

Ivano-Frankivsk, 7601, Ukraine

Location

Site 5256

Kharkiv, 61124, Ukraine

Location

Site 5254

Kharkiv, 61157, Ukraine

Location

Site 5255

Kherson, 73000, Ukraine

Location

Site 5263

Kyiv, 1133, Ukraine

Location

SIte 5252

Kyiv, 2091, Ukraine

Location

Site 5251

Kyiv, 3680, Ukraine

Location

Site 5265

Kyiv, 3680, Ukraine

Location

Site 5259

Poltava, 3603, Ukraine

Location

Site 5260

Vinnytsia, 21029, Ukraine

Location

Site 5253

Zaporizhzhya, 69035, Ukraine

Location

Site 5257

Zaporizhzhya, 69065, Ukraine

Location

Related Publications (2)

  • File TM Jr, Alexander E, Goldberg L, Das AF, Sandrock C, Paukner S, Moran GJ. Lefamulin efficacy and safety in a pooled phase 3 clinical trial population with community-acquired bacterial pneumonia and common clinical comorbidities. BMC Pulm Med. 2021 May 8;21(1):154. doi: 10.1186/s12890-021-01472-z.

  • Alexander E, Goldberg L, Das AF, Moran GJ, Sandrock C, Gasink LB, Spera P, Sweeney C, Paukner S, Wicha WW, Gelone SP, Schranz J. Oral Lefamulin vs Moxifloxacin for Early Clinical Response Among Adults With Community-Acquired Bacterial Pneumonia: The LEAP 2 Randomized Clinical Trial. JAMA. 2019 Nov 5;322(17):1661-1671. doi: 10.1001/jama.2019.15468.

MeSH Terms

Conditions

Community-Acquired PneumoniaPneumonia

Interventions

lefamulinMoxifloxacin

Condition Hierarchy (Ancestors)

Community-Acquired InfectionsInfectionsRespiratory Tract InfectionsRespiratory Tract DiseasesLung Diseases

Intervention Hierarchy (Ancestors)

Fluoroquinolones4-QuinolonesQuinolonesQuinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Results Point of Contact

Title
Jennifer Schranz, M.D., Chief Medical Officer
Organization
Nabriva Therapeutics US, Inc

Study Officials

  • Leanne Gasink, MD

    Nabriva Therapeutics AG

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 20, 2016

First Posted

June 27, 2016

Study Start

August 1, 2016

Primary Completion

January 1, 2018

Study Completion

January 1, 2018

Last Updated

October 23, 2019

Results First Posted

October 23, 2019

Record last verified: 2019-09

Locations