NCT02559310

Brief Summary

This study evaluates the safety and efficacy of lefamulin, a pleuromutilin, for the treatment of adults with moderate to severe community-acquired bacterial pneumonia.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
551

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Sep 2015

Geographic Reach
18 countries

99 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2015

Completed
21 days until next milestone

First Submitted

Initial submission to the registry

September 22, 2015

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 24, 2015

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2017

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2017

Completed
2.5 years until next milestone

Results Posted

Study results publicly available

October 23, 2019

Completed
Last Updated

October 23, 2019

Status Verified

October 1, 2019

Enrollment Period

1.6 years

First QC Date

September 22, 2015

Results QC Date

August 28, 2019

Last Update Submit

October 22, 2019

Conditions

Keywords

PneumoniaCABPCAPCommunity acquired bacterial pneumonia

Outcome Measures

Primary Outcomes (1)

  • Early Clinical Response (ECR)

    ECR was defined as survival with improvement in at least 2 signs and symptoms of CABP (relative to baseline), no worsening of any CABP sign or symptom, and no use of concomitant antibiotics (other than adjunctive linezolid, as allowed by the study protocol) for the treatment of CABP through the ECR assessment.

    ECR was assessed 96 +/- 24 hours after the first dose of study drug.

Secondary Outcomes (2)

  • Investigator's Assessment of Clinical Response (IACR)

    IACR was assessed at the Test-of-Cure visit; 5-10 days after the last dose of study drug.

  • Investigator's Assessment of Clinical Response (IACR)

    IACR was assessed at the Test of Cure visit, 5 - 10 days after the last dose of study drug.

Study Arms (2)

Lefamulin

EXPERIMENTAL

Intravenous lefamulin with potential step-down to oral lefamulin

Drug: lefamulin

Moxifloxacin +/- Linezolid

ACTIVE COMPARATOR

Intravenous moxifloxacin with potential step-down to oral moxifloxacin +/- linezolid

Drug: MoxifloxacinDrug: Linezolid

Interventions

antibacterial agent

Also known as: BC-3781
Lefamulin

antibacterial agent

Also known as: Avelox
Moxifloxacin +/- Linezolid

antibacterial agent

Also known as: Zyvox
Moxifloxacin +/- Linezolid

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Be male or female at least 18 years of age.
  • Provide written informed consent and be willing and able to adhere to the study-specified procedures and restrictions.
  • Have an acute illness (7 days duration) with at least 3 of the following symptoms consistent with a lower respiratory tract infection (new or worsening):
  • Dyspnea
  • New or increased cough
  • Purulent sputum production
  • Chest pain due to pneumonia
  • Have at least 2 of the following vital sign abnormalities:
  • Fever (body temperature \>38.0°C (100.4°F) measured orally or equivalent temperature from an alternate body site) or hypothermia (body temperature \<35.0°C (95.0°F) measured orally or equivalent temperature from an alternate body site)
  • Hypotension (systolic blood pressure \<90 mmHg)
  • Tachycardia (heart rate \>100 beats/min)
  • Tachypnea (respiratory rate \>20 breaths/min)
  • Have at least 1 other clinical sign or laboratory finding of CABP:
  • Hypoxemia (i.e., O2 saturation \<90% on room air or while receiving supplemental oxygen at subject's baseline requirement or PaO2 \<60 mmHg)
  • Auscultatory and/or percussion findings consistent with pneumonia (e.g., crackles, egophony, dullness)
  • +3 more criteria

You may not qualify if:

  • Have received more than a single dose of a short-acting oral or IV antibacterial for CABP within 72 hours before randomization
  • Require concomitant systemic antibacterial therapy potentially effective against CABP pathogens
  • Have been hospitalized for 2 or more days within 90 days prior to the onset of symptoms or have resided in a nursing home or long-term healthcare facility within 30 days prior to the onset of symptoms. NOTE: Residence in an independent living facility is permitted.
  • Have confirmed or suspected CABP caused by a pathogen known to be resistant to any of the study drugs (e.g., Pseudomonas aeruginosa, any pathogen of the Enterobacteriaceae Family) or attributable to etiologies other than community acquired bacterial pathogens (e.g., ventilator associated pneumonia, hospital acquired bacterial pneumonia, bacterial aspiration pneumonia, Pneumocystis jiroveci pneumonia or other fungal pneumonia, viral or mycobacterial infection of the lung).
  • Have a noninfectious cause of pulmonary infiltrates (e.g., pulmonary embolism, chemical pneumonitis from aspiration, hypersensitivity pneumonia, congestive heart failure, bronchial obstruction, lung cancer, cystic fibrosis).
  • Have confirmed or suspected pleural empyema (does not include sterile parapneumonic effusions).
  • Require mechanical ventilation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (99)

Site 1006

Hazard, Kentucky, 41701, United States

Location

Site 1008

Shreveport, Louisiana, 71103, United States

Location

Site 1005

Minneapolis, Minnesota, 55415, United States

Location

Site 1001

Butte, Montana, 59701, United States

Location

Site 1009

Akron, Ohio, 44309, United States

Location

Site 1002

Dayton, Ohio, 45402, United States

Location

Site 1004

Splendora, Texas, 77372, United States

Location

Site 3005

La Plata, Buenos Aires, 1900, Argentina

Location

Site 3006

Rosario, Santa Fe Province, S2000CVB, Argentina

Location

Site 3003

Córdoba, X5000EPU, Argentina

Location

Site 3007

Córdoba, X5000JRD, Argentina

Location

Site 3001

Córdoba, X5004CDT, Argentina

Location

Site 3004

Córdoba, X5016KEH, Argentina

Location

Site 4003

Mostar, 88000, Bosnia and Herzegovina

Location

Site 4001

Tuzla, 75000, Bosnia and Herzegovina

Location

Site 4004

Zenica, 72000, Bosnia and Herzegovina

Location

Site 3104

Belo Horizonte, Minas Gerais, 30150-221, Brazil

Location

Site 3102

Passo Fundo, Rio Grande Do Sol, 99010-080, Brazil

Location

Site 3103

Campinas, São Paulo, 13059-900, Brazil

Location

Site 3101

Sao Paulo Do Rio Preto, São Paulo, 15090-000, Brazil

Location

Site 4105

Gabrovo, 5300, Bulgaria

Location

Site 4107

Lovech, 5500, Bulgaria

Location

Site 4112

Pernik, 2300, Bulgaria

Location

Site 4103

Rousse, 7002, Bulgaria

Location

Site 4108

Smolyan, 4700, Bulgaria

Location

Site 4102

Sofia, 1202, Bulgaria

Location

Site 4101

Sofia, 1233, Bulgaria

Location

Site 4106

Sofia, 1233, Bulgaria

Location

Site 4110

Sofia, 1606, Bulgaria

Location

Site 4111

Sofia, 1606, Bulgaria

Location

Site 4104

Veliko Tarnovo, 5000, Bulgaria

Location

Site 4109

Vidin, 3700, Bulgaria

Location

Site 4206

Tbilisi, 0101, Georgia

Location

Site 4204

Tbilisi, 0144, Georgia

Location

Site 4205

Tbilisi, 0144, Georgia

Location

Site 4201

Tbilisi, 0159, Georgia

Location

Site 4202

Tbilisi, 0186, Georgia

Location

Site 4305

Budapest, 1121, Hungary

Location

Site 4306

Csorna, 9300, Hungary

Location

Site 4304

Debrecen, 4043, Hungary

Location

Site 4302

Farkasgyepű, 8582, Hungary

Location

Site 4307

Miskolc, 3529, Hungary

Location

Site 4308

Miskolc, 3529, Hungary

Location

Site 4303

Törökbálint, 2045, Hungary

Location

Site 4403

Daugavpils, LV-5417, Latvia

Location

Site 4401

Liepāja, LV-3414, Latvia

Location

Site 4402

Riga, LV-1038, Latvia

Location

Site 4603

Almelo, Overijssel, 7609 PP, Netherlands

Location

Site 4602

Helmond, 5707 HA, Netherlands

Location

Site 3205

Trujillo, La Libertad, Peru

Location

Site 3202

Lima, Lima 18, Peru

Location

Site 3204

Lima, Lima 1, Peru

Location

Site 3201

Lima, Lima 29, Peru

Location

Site 2005

Iloilo City, 5000, Philippines

Location

Site 2003

Manila, 1000, Philippines

Location

Site 2004

Manila, 1012, Philippines

Location

Site 2002

Quezon City, 1100, Philippines

Location

Site 2001

Quezon City, 1114, Philippines

Location

Site 4703

Skierniewice, Lódzkie, 96-100, Poland

Location

Site 4704

Warsaw, Masovian Voivodeship, 02-097, Poland

Location

Site 4701

Lódz, 90-153, Poland

Location

Site 4702

Wilkowice, 43-365, Poland

Location

Site 4802

Palazu Mare, Constanța County, 900002, Romania

Location

Site 4810

Bucharest, 030303, Romania

Location

Site 4801

Bucharest, 21105, Romania

Location

Site 4806

Bucharest, 21105, Romania

Location

Site 4811

Cluj-Napoca, 040000, Romania

Location

Site 4803

Craiova, 200515, Romania

Location

Site 4808

Craiova, 200515, Romania

Location

Site 4807

Timișoara, 300310, Romania

Location

Site 4809

Timișoara, 300310, Romania

Location

Site 4904

Chelyabinsk, 454021, Russia

Location

Site 4902

Novosibirsk, 630102, Russia

Location

Site 4903

Saint Petersburg, 191163, Russia

Location

Site 4901

Saint Petersburg, 197706, Russia

Location

Site 4906

Smolensk, 214019, Russia

Location

Site 4905

Yaroslavl, 150062, Russia

Location

Site 5003

Niš, Nišavski Okrug, 18204, Serbia

Location

Site 5002

Belgrade, 11000, Serbia

Location

Site 5004

Kamenitz, 11080, Serbia

Location

Site 5001

Kragujevac, Šumadijski Okrug, 34000, Serbia

Location

Site 5103

Benoni, Gauteng, 1500, South Africa

Location

Site 5104

Pretoria, Gauteng, 181, South Africa

Location

Site 5105

Thabazimbi, Limpopo, 380, South Africa

Location

Site 5101

Middelburg, Mpumalanga, 1050, South Africa

Location

Site 5102

Krugersdorp, 1724, South Africa

Location

Site 2103

Nonthaburi, 10110, Thailand

Location

Site 5203

Chernivtsi, Chernivtsi Oblast, 58005, Ukraine

Location

Site 5204

Ivano-Frankivsk, Ivano-Frankivsk Oblast, 76018, Ukraine

Location

Site 5201

Kharkiv, Kharkivs’ka Oblast’, 61124, Ukraine

Location

Site 5209

Kherson, Kherson Oblast, 73000, Ukraine

Location

Site 5211

Odesa, Odesa Oblast, 65025, Ukraine

Location

Site 5210

Zaporizhzhia, Zaporizhzhia Oblast, 69118, Ukraine

Location

Site 5207

Kiyiv, 03680, Ukraine

Location

Site 5202

Kyiv, 01133, Ukraine

Location

Site 5205

Kyiv, 03680, Ukraine

Location

Site 5208

Sumy, 40022, Ukraine

Location

Site 5212

Zaporizhzhia, 69035, Ukraine

Location

Site 5206

Zhytomyr, 10002, Ukraine

Location

Related Publications (2)

  • File TM Jr, Alexander E, Goldberg L, Das AF, Sandrock C, Paukner S, Moran GJ. Lefamulin efficacy and safety in a pooled phase 3 clinical trial population with community-acquired bacterial pneumonia and common clinical comorbidities. BMC Pulm Med. 2021 May 8;21(1):154. doi: 10.1186/s12890-021-01472-z.

  • File TM, Goldberg L, Das A, Sweeney C, Saviski J, Gelone SP, Seltzer E, Paukner S, Wicha WW, Talbot GH, Gasink LB. Efficacy and Safety of Intravenous-to-oral Lefamulin, a Pleuromutilin Antibiotic, for the Treatment of Community-acquired Bacterial Pneumonia: The Phase III Lefamulin Evaluation Against Pneumonia (LEAP 1) Trial. Clin Infect Dis. 2019 Nov 13;69(11):1856-1867. doi: 10.1093/cid/ciz090.

MeSH Terms

Conditions

Community-Acquired PneumoniaPneumonia

Interventions

lefamulinMoxifloxacinLinezolid

Condition Hierarchy (Ancestors)

Community-Acquired InfectionsInfectionsRespiratory Tract InfectionsRespiratory Tract DiseasesLung Diseases

Intervention Hierarchy (Ancestors)

Fluoroquinolones4-QuinolonesQuinolonesQuinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsAcetamidesAmidesOrganic ChemicalsAcetatesAcids, AcyclicCarboxylic AcidsOxazolidinonesOxazolesAzolesHeterocyclic Compounds, 1-Ring

Results Point of Contact

Title
Jennifer Schranz, MD, Chief Medical Officer
Organization
Nabriva Therapeutics US, Inc.

Study Officials

  • Jennifer Schranz, MD

    Nabriva Therapeutics

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 22, 2015

First Posted

September 24, 2015

Study Start

September 1, 2015

Primary Completion

April 1, 2017

Study Completion

May 1, 2017

Last Updated

October 23, 2019

Results First Posted

October 23, 2019

Record last verified: 2019-10

Locations