NCT02760433

Brief Summary

The purpose of this study was to determine how effective and safe the study drug Olokizumab was in patients with Rheumatoid Arthritis (RA) who had been already receiving, but not fully responding to treatment with an existing medication called a tumour necrosis factor alpha inhibitor The primary objective of this study was to evaluate the efficacy of olokizumab (OKZ) 64 mg administered subcutaneously (SC) once every 2 weeks (q2w) or once every 4 weeks (q4w) relative to placebo in subjects with moderately to severely active rheumatoid arthritis (RA) inadequately controlled by TNF-α inhibitor (TNFi) therapy.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
368

participants targeted

Target at P50-P75 for phase_3 rheumatoid-arthritis

Timeline
Completed

Started Jan 2017

Typical duration for phase_3 rheumatoid-arthritis

Geographic Reach
11 countries

116 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 29, 2016

Completed
4 days until next milestone

First Posted

Study publicly available on registry

May 3, 2016

Completed
9 months until next milestone

Study Start

First participant enrolled

January 25, 2017

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 12, 2019

Completed
19 days until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2019

Completed
1.8 years until next milestone

Results Posted

Study results publicly available

July 21, 2021

Completed
Last Updated

September 21, 2023

Status Verified

September 1, 2023

Enrollment Period

2.6 years

First QC Date

April 29, 2016

Results QC Date

January 26, 2021

Last Update Submit

September 19, 2023

Conditions

Keywords

moderate Rheumatoid Arthritissevere Rheumatoid ArthritisOlokizumab

Outcome Measures

Primary Outcomes (1)

  • Percentage of Subjects Achieving American College of Rheumatology 20% (ACR20) Response

    The difference between OKZ and placebo in the percentage of subjects achieving an ACR20 response and remaining on randomized treatment and in the study at Week 12. A responder is defined as any subject satisfying ACR20 criteria and remaining on randomized treatment and in the study at Week 12. American College of Rheumatology 20 % response is a composite defined as a ≥ 20% improvement from baseline in the swollen joint counts assessed in 66 joints and in the tender joint count assessed in 68 joints; and a ≥20% improvement from baseline in at least 3 of the 5 remaining core set measures: * Patient Global Assessment of Disease Activity (VAS) * Patient Assessment of Pain (VAS) * HAQ-DI * Physician Global Assessment (VAS) * Level of acute phase reactant (CRP)

    at Week 12

Secondary Outcomes (4)

  • Percentage of Subjects Achieving Low Disease Activity

    at Week 12

  • Improvement of Physical Ability From Baseline to Week 12, as Measured by the Health Assessment Questionnaire Disability Index (HAQ-DI)

    Baseline to Week 12

  • Percentage of Subjects Achieving American College of Rheumatology 50% (ACR50) Response

    at Week 12

  • Percentage of Subjects With Clinical Disease Activity Index (CDAI) ≤ 2.8 (Remission)

    at Week 12

Study Arms (3)

Arm 1: Olokizumab q4w

EXPERIMENTAL

Olokizumab 64mg subcutaneous q4w + placebo + Methotrexate Olokizumab 64 mg subcutaneous q4w + placebo+ concomitant background therapy (Methotrexate) at a stable dose with a stable route of administration (oral, subcutaneous, or intramuscular) in order to maintain the blind, subjects randomized to receive OKZ q4w received placebo injections at the alternate q4w interval (e.g., Week 2, Week 6, etc.)

Drug: OlokizumabDrug: Placebo

Arm 2: Olokizumab q2w

EXPERIMENTAL

Olokizumab 64mg subcutaneous q2w + Methotrexate 64 mg Olokizumab administered subcutaneously once every 2 weeks + concomitant background therapy (Methotrexate) at a stable dose with a stable route of administration (oral, subcutaneous, or intramuscular)

Drug: Olokizumab

Arm 3: Placebo q2w

PLACEBO COMPARATOR

Placebo q2w subcutaneous + Methotrexate Placebo administered subcutaneously once every 2 weeks + concomitant background therapy (Methotrexate) at a stable dose with a stable route of administration (oral, subcutaneous, or intramuscular) Starting at Week 16, all subjects in the placebo group were randomized in a blinded fashion to receive either OKZ 64 mg q2w or OKZ 64 mg q4w; equal numbers of subjects were planned to be assigned to each OKZ treatment group.

Drug: Placebo

Interventions

160 mg/mL sterile solution for SC injection in a 2 mL clear Type I glass vial

Arm 1: Olokizumab q4wArm 2: Olokizumab q2w

sodium chloride 0.9% solution provided as either a 10 mL vial or ampoule, depending on market availability. Each placebo will be packed into a cardboard carton to contain 1 vial or ampoule

Arm 1: Olokizumab q4wArm 3: Placebo q2w

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects may be enrolled in the study only if they meet all of the following criteria.
  • Subjects willing and able to sign informed consent
  • Subjects must have a diagnosis of adult onset RA classified by ACR/EULAR 2010 revised classification criteria for RA for at least 24 weeks prior to Screening.
  • (If the subject was diagnosed according to ACR 1987 criteria previously, the Investigator may classify the subject per ACR 2010 retrospectively, using available source data.)
  • Treatment with oral, SC, or intramuscular (IM) MTX for at least 12 weeks prior to Screening at a dose of 15 to 25 mg/week (or ≥10 mg/week if there is documented intolerance to higher doses)
  • The dose and means of administering MTX must have been stable for at least 6 weeks prior to Screening.
  • Subjects must be willing to take folic acid or equivalent throughout the study.
  • Subjects must have moderately to severely active RA disease as defined by all of the following:
  • ≥6 tender joints (68 joint count) at Screening and baseline; and
  • ≥6 swollen joints (66 joint count) at Screening and baseline; and
  • C-reactive protein (CRP) above Upper limit of normal (ULN) at Screening based on the central laboratory results.
  • Subjects must have a documented inadequate response to treatment (i.e., TNFi failure) with ≥1 licensed TNFi following at least 12 weeks of therapy with that agent. Inadequate response to treatment is classified as either:
  • Primary failure: The absence of any documented clinically significant response; or
  • Secondary failure: Documented initial response with subsequent loss of that response or partial response

You may not qualify if:

  • Diagnosis of any other inflammatory arthritis or systemic rheumatic disease (e.g., gout, psoriatic or reactive arthritis, Crohn's disease, Lyme disease, juvenile idiopathic arthritis, or systemic lupus erythematosus) (However, subjects may have secondary Sjogren's syndrome or hypothyroidism.)
  • Subjects who are Steinbrocker class IV functional capacity (incapacitated, largely or wholly bed-ridden or confined to a wheelchair, with little or no self-care)
  • Prior exposure to any licensed or investigational compound directly or indirectly targeting Interleukin (IL) 6 or IL 6R (including tofacitinib or other Janus kinases and spleen tyrosine kinase \[SYK\] inhibitors)
  • Prior treatment with cell depleting therapies including anti CD20 or investigational agents (e.g., CAMPATH, anti CD4, anti CD5, anti CD3, and anti CD19) with the exception of rituximab, which is allowed if it was discontinued at least 24 weeks prior to baseline (rituximab should not be discontinued to facilitate a subject's participation in the study, but should instead have been previously discontinued as part of a subject's medical management of RA).
  • Prior use of bDMARDs, within the following windows prior to baseline (bDMARDs should not be discontinued to facilitate a subject's participation in the study, but should instead have been previously discontinued as part of a subject's medical management of RA):
  • weeks for etanercept and anakinra
  • weeks for infliximab
  • weeks for adalimumab, certolizumab, and golimumab
  • weeks for abatacept
  • Use of parenteral and/or intra-articular glucocorticoids within 4 weeks prior to baseline
  • Use of oral glucocorticoids greater than 10 mg/day prednisone (or equivalent) or change in dosage within 2 weeks prior to baseline
  • Prior documented history of no response to hydroxychloroquine and sulfasalazine
  • Prior use of cDMARDs (other than MTX) within the following windows prior to baseline (cDMARDs should not be discontinued to facilitate a subject's participation in the study, but should instead have been previously discontinued as part of a subject's medical management of RA):
  • weeks for sulfasalazine, azathioprine, cyclosporine, hydroxychloroquine, chloroquine, gold, penicillamine, minocycline, or doxycycline
  • weeks for leflunomide unless the subject has completed the following elimination procedure at least 4 weeks prior to baseline: Cholestyramine at a dosage of 8 grams 3 times daily for at least 24 hours, or activated charcoal at a dosage of 50 grams 4 times daily for at least 24 hours
  • +27 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (116)

Arizona Arthritis & Rheumatology Associates, P.C.

Phoenix, Arizona, 85032, United States

Location

CHI St. Vincent Hot Springs

Hot Springs, Arkansas, 71913, United States

Location

Medvin Clinical Research

Covina, California, 91722, United States

Location

TriWest Research Associates, LLC

El Cajon, California, 92020-4124, United States

Location

Saint Jude Heritage Medical Grp

Fullerton, California, 92835, United States

Location

С V Mehta MD Med Corp.

Hemet, California, 92543, United States

Location

Advanced Medical Research, LLC

Lakewood, California, 90623, United States

Location

Stanford University School of Medicine

Palo Alto, California, 94304, United States

Location

Riverside Medical Clinic

Riverside, California, 92506, United States

Location

East Bay Rheumatology Medical Group, Inc.

San Leandro, California, 94578, United States

Location

Inland Rheumatology Clinical Trials, Inc.

Upland, California, 91786, United States

Location

Denver Arthritis Clinic

Denver, Colorado, 80230, United States

Location

Javed Rheumatology Associates

Newark, Delaware, 19713, United States

Location

RASF - Clinical Research Center

Boca Raton, Florida, 33486, United States

Location

Suncoast Research Group LLC

Miami, Florida, 33135, United States

Location

Omega Research Consultants

Orlando, Florida, 32810, United States

Location

Family Clinical Trials, LLC.

Pembroke Pines, Florida, 33026, United States

Location

AdventHealth Medical Group, PA

Tampa, Florida, 33614, United States

Location

Institute of Arthritis Research

Idaho Falls, Idaho, 83404, United States

Location

University of Kansas Hospital

Kansas City, Kansas, 66160, United States

Location

Graves Gilbert Clinic

Bowling Green, Kentucky, 42101, United States

Location

The Arthritis & Diabetes Clinic, Inc.

Monroe, Louisiana, 71203, United States

Location

Klein and Associates, M.D., P.A.

Hagerstown, Maryland, 21740, United States

Location

The Center for Rheumatology and Bone Research

Wheaton, Maryland, 20902, United States

Location

Clinical Pharmacology Study Group

Worcester, Massachusetts, 01605, United States

Location

Glacier View Research Instutute-Rheumatology

Kalispell, Montana, 59901, United States

Location

Arthritis & Osteoporosis Associates, PA

Freehold, New Jersey, 07728, United States

Location

Lovelace Scientific Resources, Inc.

Albuquerque, New Mexico, 87114, United States

Location

NYU Langone Ambulatory Care

New York, New York, 11201, United States

Location

Medication Management, LLC

Greensboro, North Carolina, 27408, United States

Location

Cape Fear Arthritis Care

Leland, North Carolina, 28451, United States

Location

Carolina Arthritis Associates

Wilmington, North Carolina, 28401, United States

Location

Trinity Medical Group

Minot, North Dakota, 58701, United States

Location

Cincinnati Rheumatic Disease Study Group

Cincinnati, Ohio, 45242, United States

Location

STAT Research, Inc.

Dayton, Ohio, 45417, United States

Location

Clinical Research Source, Inc.

Perrysburg, Ohio, 43606, United States

Location

Arthritis Group

Philadelphia, Pennsylvania, 19152, United States

Location

Low Country Research Center

Charleston, South Carolina, 29486, United States

Location

Amarillo Center for Clinical Research

Amarillo, Texas, 79124, United States

Location

Austin Regional Clinic, P.A.

Austin, Texas, 78731, United States

Location

Accurate Clinical Research, Inc.

Baytown, Texas, 77521, United States

Location

Precision Comprehensive Clinical Research Solutions

Grapevine, Texas, 76034, United States

Location

Therapeutic Concepts Rheumatology, LLC

Houston, Texas, 77004, United States

Location

Rheumatology Clinic of Houston, P.A.

Houston, Texas, 77065, United States

Location

Accurate Clinical Research, Inc.

Houston, Texas, 77089, United States

Location

Pioneer Research Solutions, Inc.

Houston, Texas, 77429, United States

Location

Accurate Clinical Research, Inc.

League City, Texas, 77573, United States

Location

Endocrinology, Internal Medicine

Lubbock, Texas, 79410, United States

Location

Dr. Alex De Jesus Rheumatology, P.A.

San Antonio, Texas, 78229, United States

Location

Advanced Rheumatology of Houston

Woodville, Texas, 77382, United States

Location

Centro de Investigaciones Medicas Mar del Plata

Mar del Plata, Buenos Aires, B7600FYK, Argentina

Location

Instituto de Investigaciones Clinicas

Mar del Plata, Buenos Aires, B7600FZN, Argentina

Location

Instituto de Investigaciones Clinicas Quilmes

Quilmes, Buenos Aires, B1878GEG, Argentina

Location

Clinica de Higado y Aparato Digestivo

Rosario, Santa Fe Province, S2000CFJ, Argentina

Location

Sanatorio San Martin

Venado Tuerto, Santa Fe Province, S2600KUE, Argentina

Location

Centro Medico Privado de Reumatologia

San Miguel de Tucumán, Tucumán Province, T4000AXL, Argentina

Location

Centro de Investigaciones Reumatológicas

San Miguel de Tucumán, Tucumán Province, T4000BRD, Argentina

Location

Atencion Integral en Reumatologia (AIR)

Ciudad Autonoma Buenos Aires, 1426, Argentina

Location

Organizacion Medica de Investigacion (OMI)

Ciudad Autonoma Buenos Aires, C1015ABO, Argentina

Location

APRILLUS

Ciudad Autonoma Buenos Aires, C1046AAQ, Argentina

Location

Instituto Centenario

Ciudad Autonoma Buenos Aires, C1204AAD, Argentina

Location

Hospital Privado Centro Medico de Cordoba S.A

Córdoba, 5016, Argentina

Location

Centro Polivalente de Asistencia e Inv. Clinica CER

San Juan, 5400, Argentina

Location

HUWC - UFC - Hospital Universitário Walter Cantídio - Universidade Federal do Ceará

Fortaleza, Ceará, 60430-370, Brazil

Location

CEDOES - Diagnóstico e Pesquisa

Vitória, Espírito Santo, 29055450, Brazil

Location

CIP - Centro Internacional de Pesquisa

Goiânia, Goiás, 74110-120, Brazil

Location

CMiP - Centro Mineiro de Pesquisa

Juiz de Fora, Minas Gerais, 36010-570, Brazil

Location

CETI - Centro de Estudos em Terapias Inovadoras Ltda.

Curitiba, Paraná, 80030-110, Brazil

Location

Hospital Bruno Born

Lajeado, Rio Grande do Sul, 95900-010, Brazil

Location

LMK Serviços Médicos S/S Ltda

Porto Alegre, Rio Grande do Sul, 90480-000, Brazil

Location

Faculdade de Medicina do ABC

Santo André, São Paulo, 09060-650, Brazil

Location

Centro Multidisciplinar de Estudos Clínicos - CEMEC

São Bernardo do Campo, São Paulo, 09715-090, Brazil

Location

Clínica de Neoplasias Litoral Ltda.

Santa Catarina, 88301-215, Brazil

Location

CPCLIN - Centro de Pesquisas Clínicas Ltda.

São Paulo, 01228-200, Brazil

Location

Associação de Assistência à Criança Deficiente - AACD

São Paulo, 04032-060, Brazil

Location

Centro de Reumatologia y Ortopedia SAS

Barranquilla, 80020, Colombia

Location

Centro de Investigacion en Reumatologia y Especialidades Medicas SAS. CIREEM

Bogotá, 110221, Colombia

Location

Medicity S.A.S.

Bucaramanga, 680003, Colombia

Location

Clinica de Artritis Temprana S.A.

Cali, 76001, Colombia

Location

Revmatologie MUDr. Klara Sirova s.r.o.

Ostrava - Moravska Ostrava, 70200, Czechia

Location

CCR Czech, a.s.

Pardubice, 53002, Czechia

Location

MEDICAL PLUS s.r.o.

Uherské Hradiště, 68601, Czechia

Location

PV - Medical, s.r.o.

Zlín, 760 01, Czechia

Location

Kerckhoff-Klinik gGmbH

Bad Nauheim, Hesse, 61231, Germany

Location

SMO.MD GmbH

Magdeburg, Saxony-Anhalt, 39120, Germany

Location

HRF Hamburger Rheuma Forschungszentrum

Hamburg, 20095, Germany

Location

Clinexpert Egeszsegugyi Szolg. es Ker. Kft.

Budapest, 1033, Hungary

Location

Obudai Egeszsegugyi Centrum

Budapest, 1036, Hungary

Location

MAV Korhaz és Rendelointezet

Szolnok, 5000, Hungary

Location

Vital Medical Center

Veszprém, 8200, Hungary

Location

Clinica de Investigacion en Reumatologia y Obesidad S.C.

Guadalajara, Jalisco, 44650, Mexico

Location

Centro de Estudios de Investigacion Basica y Clinica SC

Guadalajara, Jalisco, 44690, Mexico

Location

Centro de Investigacion Clínica GRAMEL S.C

Mexico City, Mexico City, 03720, Mexico

Location

Clinstile, S.A. de C.V.

Mexico City, Mexico City, 06700, Mexico

Location

Accelerium S. de R.L. de C.V.

Monterrey, Nuevo León, 64000, Mexico

Location

Universidad Autonoma de Nuevo Leon, Hospital Universitario Dr. Jose Eleuterio Gonzalez

Monterrey, Nuevo León, 64460, Mexico

Location

Centro de Alta Especialidad en Reumatología e Investigación del Potosí, S.C.

San Luis Potosí City, San Luis Potos, 78213, Mexico

Location

Investigacion y Biomedicina de Chihuahua, S.C.

Chihuahua City, 31000, Mexico

Location

Szpital Uniwersytecki nr 2 im.dr J. Biziela

Bydgoszcz, 85-168, Poland

Location

McBk S.C.

Grodzisk Mazowiecki, 05-825, Poland

Location

Centrum Medyczne AMED

Lodz, 91-363, Poland

Location

Szpital Wojewodzki im. Prymasa Kardynala Stefana Wyszynskiego

Sieradz, 98-200, Poland

Location

Samodzielny Publiczny ZOZ Tomaszow Lubelski

Tomaszów Lubelski, 22-600, Poland

Location

McM Polimedica

Warsaw, 02-777, Poland

Location

State Budgetary Healthcare Institution "City Clinical Hospital # 15 n.a O.M. Filatov" of Moscow Healtheare Department

Moscow, Moscow Oblast, 111539, Russia

Location

City Clinical Hospital #1

Novosibirsk, Novosibirsk Oblast, 630099, Russia

Location

Diagnostic Center Ultramed

Omsk, Omsk Oblast, 644024, Russia

Location

SBHI of the Republic of Karelia "Republican Hospital named after V.A.Baranov"

Petrozavodsk, Republic of Karelia, 185019, Russia

Location

Rostov State Medical Unversity

Rostov-on-Don, Rostov Oblast, 344022, Russia

Location

SBHI of Stavropol Region "Stavropol Regional Clinical Hospital"

Stavropol, Stavropol Kray, 355030, Russia

Location

Regional Clinical Hospital

Vladimir, Vladimirskaya Oblast’, 600023, Russia

Location

FSBSI "Scientific Research Institute of Rheumatology n.a. V.A. Nasonova"

Moscow, 115522, Russia

Location

Ajou University Hospital

Suwon, Gyeonggi-do, 443-380, South Korea

Location

Chonnam National University Hospital

Gwangju, 61469, South Korea

Location

Hallym University Sacred Heart Hospital

Gyeonggi-do, 431-796, South Korea

Location

Severance Hospital, Yonsei University

Seoul, 3722, South Korea

Location

Related Publications (1)

  • Feist E, Fatenejad S, Grishin S, Korneva E, Luggen ME, Nasonov E, Samsonov M, Smolen JS, Fleischmann RM. Olokizumab, a monoclonal antibody against interleukin-6, in combination with methotrexate in patients with rheumatoid arthritis inadequately controlled by tumour necrosis factor inhibitor therapy: efficacy and safety results of a randomised controlled phase III study. Ann Rheum Dis. 2022 Dec;81(12):1661-1668. doi: 10.1136/ard-2022-222630. Epub 2022 Sep 15.

MeSH Terms

Conditions

Arthritis, Rheumatoid

Interventions

olokizumab

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Maria Lemak, Scientific Advisor
Organization
R-Pharm

Study Officials

  • Mikhail Samsonov

    R-Pharm

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 29, 2016

First Posted

May 3, 2016

Study Start

January 25, 2017

Primary Completion

September 12, 2019

Study Completion

October 1, 2019

Last Updated

September 21, 2023

Results First Posted

July 21, 2021

Record last verified: 2023-09

Locations