NCT02704403

Brief Summary

The primary objectives of this study are to evaluate the effect of Elafibranor treatment compared to placebo on 1) histological improvement and 2) all-cause mortality and liver-related outcomes in patients with nonalcoholic steatohepatitis (NASH) and fibrosis.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
2,157

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Mar 2016

Longer than P75 for phase_3

Geographic Reach
25 countries

326 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 16, 2016

Completed
14 days until next milestone

Study Start

First participant enrolled

March 1, 2016

Completed
9 days until next milestone

First Posted

Study publicly available on registry

March 10, 2016

Completed
4.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 28, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 28, 2020

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

March 23, 2022

Completed
Last Updated

March 23, 2022

Status Verified

February 1, 2022

Enrollment Period

4.7 years

First QC Date

February 16, 2016

Results QC Date

January 7, 2022

Last Update Submit

February 25, 2022

Conditions

Keywords

ElafibranorNASHNonalcoholic steatohepatitisFatty liver diseaseFibrosis

Outcome Measures

Primary Outcomes (2)

  • Number of Elafibranor-treated Participants Relative to Placebo Achieving Resolution of Nonalcoholic Steatohepatitis Without Worsening of Fibrosis

    To evaluate the effect of Elafibranor compared to placebo on liver histology in nonalcoholic steatohepatitis (NASH) participants with fibrosis by assessing the following endpoint: The number of Elafibranor-treated participants relative to placebo achieving NASH resolution without worsening of fibrosis. This outcome measure is for the surrogate endpoint analysis.

    Measurement at 72 weeks

  • Time to Long-term Outcome Composed of All-cause Mortality, Cirrhosis, and Liver-related Clinical Outcomes

    Composite long-term outcome measured by the number of participants with the onset of any of the adjudicated events, composed of death due to any cause, histological liver cirrhosis, and the full list of portal hypertension/cirrhosis related events as follows: liver transplantation; model for end stage liver disease (MELD) score greater than or equal to 15 for participants with baseline score less than or equal to 12, and onset of variceal bleeding requiring hospitalization, hepatic encephalopathy with West Haven/Conn score greater than or equal to 2 and requiring hospitalization, spontaneous bacterial peritonitis, and ascites requiring treatment. The MELD scale ranges from 6 to 40, showing how much a participant needs a liver transplant: higher number is more urgent. The West Haven/Conn scale is 5-point (0 to 4) grading severity of hepatic encephalopathy: higher score means worse hepatic encephalopathy. This outcome measure is for the long-term endpoint analysis.

    From first randomization up to early termination of the study corresponding to 54 months (54 months being the longest duration for any given participant)

Secondary Outcomes (7)

  • Number of Elafibranor-treated Participants Relative to Placebo Achieving Improvement of Fibrosis of at Least 1 Stage

    Measurements at 72 weeks

  • Change From Baseline of Hemoglobin A1c (HbA1c) in Diabetic Participants After 72 Weeks of Treatment in Elafibranor-treated Participants Relative to Placebo

    Measurements after 72 weeks of treatment and up to study termination

  • Change From Baseline of High-density Lipoprotein (HDL) Cholesterol After 72 Weeks of Treatment in Elafibranor-treated Participants Relative to Placebo

    Measurements after 72 weeks of treatment and up to study termination

  • Change From Baseline of Low-density Lipoprotein (LDL) Cholesterol After 72 Weeks of Treatment in Elafibranor-treated Participants Relative to Placebo

    Measurements after 72 weeks of treatment and up to study termination

  • Change From Baseline of Homeostatic Model Assessment-IR (HOMA-IR) After 72 Weeks of Treatment in Elafibranor-treated Participants Relative to Placebo in Non-diabetic Participants

    Measurements after 72 weeks of treatment and up to study termination

  • +2 more secondary outcomes

Study Arms (2)

120 mg Elafibranor

EXPERIMENTAL

Coated tablets dosed at 120mg Elafibranor; oral administration; one tablet per day before breakfast with a glass of water

Drug: Elafibranor

Placebo

PLACEBO COMPARATOR

Coated placebo tablets; oral administration; one tablet per day before breakfast with a glass of water

Drug: Placebo

Interventions

Also known as: GFT505
120 mg Elafibranor
Placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males or females aged from 18 to 75 years inclusive at first screening visit.
  • Must provide signed written informed consent and agree to comply with the study protocol.
  • Females participating in this study must be of nonchildbearing potential or using highly efficient contraception for the full duration of the study and for 1 month after the end of treatment, as described below:
  • Cessation of menses for at least 12 months due to ovarian failure,
  • Surgical sterilization such as bilateral oopherectomy, hysterectomy, or medically documented ovarian failure
  • If requested by local IRB regulations and/or National laws, sexual abstinence may be considered adequate (the reliability of sexual abstinence needs to be evaluated in relation to the duration of the clinical trial and the preferred and usual lifestyle of the patient)
  • Using a highly effective nonhormonal method of contraception (bilateral tubal occlusion, vasectomized partner, or intra-uterine device)
  • Double contraception with barrier AND highly effective hormonal method of contraception (oral, intravaginal, or transdermal combined estrogen and progestogen hormonal contraception associated with inhibition of ovulation; oral, injectable, or implantable progestogen-only hormonal contraception associated with inhibition of ovulation; or intrauterine hormone-releasing system). The hormonal contraception must be started at least 1 month prior to Randomization.
  • Histological confirmation of steatohepatitis on a diagnostic liver biopsy by central reading of the slides (biopsy obtained within 6 months prior to randomization or during the screening period) with at least 1 in each component of the NAS score (steatosis scored 0-3, ballooning degeneration scored 0-2, and lobular inflammation scored 0-3).
  • NAS score ≥4.
  • Fibrosis stage of 1 or greater and below 4, according to the NASH CRN fibrosis staging system.
  • Stable dose of vitamin E, polyunsaturated fatty acids, or ursodeoxycholic acid from at least 6 months prior to diagnostic liver biopsy
  • For participants with type 2 diabetes, glycemia must be controlled. If glycemia is controlled by antidiabetic drugs, change in anti-diabetic therapy must follow these requirements:
  • No qualitative change 6 months prior to diagnostic liver biopsy up to Randomization (i.e., implementation of a new anti-diabetic therapy) for participants treated with metformin, gliptins, sulfonylureas, sodium/glucose cotransporter (SGLT) 2 inhibitors, glucagon-like peptide (GLP)-1 agonists, or insulin. Dose changes of these medications are allowed in the 6 months prior to diagnostic liver biopsy, except for GLP-1 agonists, which must remain on stable dose in the 6 months prior to diagnostic liver biopsy.
  • No implementation of GLP-1 agonists and SGLT2 inhibitors up to 72 weeks of treatment (Visit 7).
  • +1 more criteria

You may not qualify if:

  • Known heart failure (Grade I to IV of New York Heart Association classification).
  • History of efficient bariatric surgery within 5 years prior to screening.
  • Uncontrolled hypertension during the Screening Period despite optimal antihypertensive therapy
  • Type 1 diabetes participants .
  • Participants with decompensated diabetes (HbA1c\>9%).
  • Participants with a history of clinically significant acute cardiac event within 6 months prior to screening
  • Weight loss of more than 5% within 6 months prior to randomization
  • Compensated and decompensated cirrhosis
  • Current or recent history (\<5 years) of significant alcohol consumption
  • Pregnant or lactating females or females planning to become pregnant during the study period.
  • Other well documented causes of chronic liver disease according to standard diagnostic procedures
  • Participants with previous exposure to Elafibranor
  • Prohibited concomitant medication
  • Any medical conditions that may diminish life expectancy to less than 2 years including known cancers.
  • Evidence of any other unstable or untreated clinically significant immunological, endocrine, hematological, gastrointestinal, neurological, neoplastic or psychiatric disease.
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (326)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Digestive Health Specialists of the Southeast

Dothan, Alabama, 36305, United States

Location

The Institute for Liver Health

Chandler, Arizona, 85224, United States

Location

The Institute for Liver Health

Glendale, Arizona, 85306, United States

Location

Banner University Medical Center Phoenix

Phoenix, Arizona, 85006, United States

Location

Dignity Health St. Joseph's Hospital

Phoenix, Arizona, 85013, United States

Location

Mayo Clinic Hospital

Phoenix, Arizona, 85054, United States

Location

Institute for Liver Health

Tucson, Arizona, 85711, United States

Location

Adobe Clinical Research, LLC

Tucson, Arizona, 85712, United States

Location

The University of Arizona College of Medicine Liver Research Institute

Tucson, Arizona, 85724-0001, United States

Location

Liver Wellness Center

Little Rock, Arkansas, 72205, United States

Location

GW Research, Inc.

Chula Vista, California, 91910, United States

Location

Southern California Research Center

Coronado, California, 92118, United States

Location

University of California, San Francisco, Fresno Community Regional Medical Center

Fresno, California, 93701-2302, United States

Location

Fresno Clinical Research Center

Fresno, California, 93720, United States

Location

University of California, San Francisco, Fresno Community Regional Medical Center

Fresno, California, 93721, United States

Location

Scripps Clinic Torrey Pines

La Jolla, California, 92037, United States

Location

University of California - San Diego

La Jolla, California, 92037, United States

Location

Loma Linda University Medical Center - Transplantation Insitute

Loma Linda, California, 92354, United States

Location

VA Long Beach Healthcare System

Long Beach, California, 90822, United States

Location

Keck Hospital of USC

Los Angeles, California, 90033, United States

Location

Ruane Clinical Research Group Inc.

Los Angeles, California, 90036, United States

Location

Cedars Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Gastrointestinal Biosciences Clinical Trials LLC

Los Angeles, California, 90067, United States

Location

Veterans Affaires Greater Los Angeles Healthcare System, West LA VA Medical Center

Los Angeles, California, 90073, United States

Location

Veterans Affairs Greater Los Angeles Healthcare System

Los Angeles, California, 90073, United States

Location

Alliance Clinical Research

Oceanside, California, 92056, United States

Location

National Research Institute

Panorama City, California, 91402, United States

Location

Alliance Clinical Research

Poway, California, 92064, United States

Location

University of California, Davis Medical Center

Sacramento, California, 95817, United States

Location

University of California, San Diego Airway Research and Clinical Trials Center

San Diego, California, 92103, United States

Location

Medical Associates Research Group, Inc.

San Diego, California, 92123, United States

Location

VA San Diego HealthCare System

San Diego, California, 92161, United States

Location

Quest Clinical Research

San Francisco, California, 94115, United States

Location

Sutter West Bay Hospitals dba California Pacific Medical Center

San Francisco, California, 94115, United States

Location

University of California, San Francisco, Medical Center at Parnassus

San Francisco, California, 94143, United States

Location

Ventura Clinical Trials

Ventura, California, 93003, United States

Location

South Denver Gastroenterology

Englewood, Colorado, 80113, United States

Location

Yale University School of Medicine, Section of Digestive Diseases

New Haven, Connecticut, 65200, United States

Location

Georgetown University Hospitals

Washington D.C., District of Columbia, 20007, United States

Location

Sibley Memorial Hospital

Washington D.C., District of Columbia, 20016, United States

Location

Excel Medical Clinical Trials LLC

Boca Raton, Florida, 33434, United States

Location

Integrity Clinical Research LLC

Doral, Florida, 33166, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

Nature Coast Clinical Research

Inverness, Florida, 34452, United States

Location

Mayo Clinic Hospital

Jacksonville, Florida, 32224, United States

Location

Florida Digestive Health Specialists, LLP

Lakewood Rch, Florida, 34211-4930, United States

Location

Atlantic Gastroenterology Associates, LLC

Lakewood Rch, Florida, 34211, United States

Location

Miami VA Healthcare System

Miami, Florida, 33125-1624, United States

Location

University of Miami - Miller School of Medicine

Miami, Florida, 33136, United States

Location

University of Miami - Schiff Center for Liver Diseases

Miami, Florida, 33136, United States

Location

South Florida Center of Gastroenterology, PA

Wellington, Florida, 33414, United States

Location

Florida Medical Clinic, PA

Zephyrhills, Florida, 33542, United States

Location

Summit Clinical Research

Athens, Georgia, 30607, United States

Location

Emory University Hospital Midtown

Atlanta, Georgia, 30308, United States

Location

Piedmont Atlanta Hospital

Atlanta, Georgia, 30309, United States

Location

Atlanta Medical Center, Inc.

Atlanta, Georgia, 30312, United States

Location

Gastrointestinal Specialists of Georgia, PC

Marietta, Georgia, 30060-8949, United States

Location

The Queen's Medical Center

Honolulu, Hawaii, 96813, United States

Location

Northwestern Memorial Hospital - Arkes Family Pavilion

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60637, United States

Location

The University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Loyola University Chicago

Maywood, Illinois, 60153, United States

Location

Gastroenterology Associates of Hazard

Hazard, Kentucky, 41701, United States

Location

University of Kentucky Chandler Medical Center

Lexington, Kentucky, 40536, United States

Location

University of Louisville Medical / Dental Complex

Louisville, Kentucky, 40202, United States

Location

Tulane University School of Medicine

New Orleans, Louisiana, 70112, United States

Location

Louisiana Research Center, LLC

Shreveport, Louisiana, 71105, United States

Location

Johns Hopkins Hospital

Baltimore, Maryland, 21205, United States

Location

Walter Reed National Military Medical Center

Bethesda, Maryland, 20889, United States

Location

Kaiser Permanente Shady Grove Medical Center

Rockville, Maryland, 20850, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Beth Israel Deaconess Medical Center (BIDMC)

Boston, Massachusetts, 02215, United States

Location

University of Massachusetts Memorial Medical Center

Worcester, Massachusetts, 06155, United States

Location

Henry Ford Health System, Division of Gastroenterology & Hepatology

Detroit, Michigan, 48202, United States

Location

Gastrointestinal Associates & Endoscopy Center

Flowood, Mississippi, 39232, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

St. Luke's Liver Transplant & Specialist

Kansas City, Missouri, 64111, United States

Location

Kansas City VA Medical Center

Kansas City, Missouri, 64128, United States

Location

Kansas City Research Institute

Kansas City, Missouri, 64131, United States

Location

Saint Louis University School of Medicine

St Louis, Missouri, 63104, United States

Location

Rutgers, Robert Wood Johnson Medical School

New Brunswick, New Jersey, 89030, United States

Location

Rutgers, New Jersey Medical School

Newark, New Jersey, 07103, United States

Location

Southwest Gastroenterology Associates

Albuquerque, New Mexico, 87109, United States

Location

University at Buffalo, Clinical and Translational Research Center

Buffalo, New York, 14203, United States

Location

Hofstra Northwell School of Medicine

Manhasset, New York, 11030, United States

Location

Concorde Medical Group

New York, New York, 10016, United States

Location

New York University Langone Medical Center

New York, New York, 10016, United States

Location

Weill Medical College of Cornell University

New York, New York, 10021, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

New York-Presbyterian Hospital - Columbia University Medical Center

New York, New York, 10032, United States

Location

Beth Israel Medical Center

New York, New York, 45267, United States

Location

Premier Medical Group

Poughkeepsie, New York, 12601, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467, United States

Location

Asheville Gastroenterology Associates

Asheville, North Carolina, 28801, United States

Location

UNC Health Care System

Chapel Hill, North Carolina, 27599, United States

Location

Carolinas Medical Center

Charlotte, North Carolina, 28204, United States

Location

Duke Gastroenterology

Durham, North Carolina, 22710, United States

Location

Cumberland Research Associates, LLC

Fayetteville, North Carolina, 28304, United States

Location

Carolinas Center for Liver Disease, Carolinas HealthCare System/Atrium Health

Huntersville, North Carolina, 28078, United States

Location

Diabetes & Endocrinology Consultants

Morehead City, North Carolina, 28557, United States

Location

Wake Research Associates

Raleigh, North Carolina, 27612, United States

Location

Piedmont Healthcare

Statesville, North Carolina, 28677, United States

Location

Trial Management Associates

Wilmington, North Carolina, 28403, United States

Location

Consultants for Clinical Research

Cincinnati, Ohio, 45249, United States

Location

Ohio Gastroenterology & Liver Institute

Cincinnati, Ohio, 45249, United States

Location

University of Cincinnati Physicians Company , LLC

Cincinnati, Ohio, 45267, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

The Ohio State University Wexner Medical Center

Columbus, Ohio, 43210, United States

Location

Options Health Research, LLC

Tulsa, Oklahoma, 74104-4017, United States

Location

Drexel University, College of Medicine

Philadelphia, Pennsylvania, 19102, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

Temple University Health System

Philadelphia, Pennsylvania, 19140, United States

Location

Albert Einstein Medical Center

Philadelphia, Pennsylvania, 19141, United States

Location

UPMC Montefiore

Pittsburgh, Pennsylvania, 15213, United States

Location

Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

Ralph H. Johnson VA Medical Center

Charleston, South Carolina, 29401, United States

Location

Medical University of South Carolina (MUSC)

Charleston, South Carolina, 29425, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Associates in Gastroenterology, PLC

Hermitage, Tennessee, 37076, United States

Location

Methodist University Hospital

Memphis, Tennessee, 38103, United States

Location

Quality Medical Research, PLLC

Nashville, Tennessee, 37211, United States

Location

Texas Clinical Research Institute

Arlington, Texas, 76012, United States

Location

Methodist Dallas Medical Center

Dallas, Texas, 75203, United States

Location

Liver Center of Texas

Dallas, Texas, 75234, United States

Location

Baylor All Saints Medical Center - Baylor Research Institute

Fort Worth, Texas, 76104, United States

Location

DHAT Research Institute

Garland, Texas, 75044, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Liver Associates of Texas, P.A.

Houston, Texas, 77030, United States

Location

Research Specialists of Texas

Houston, Texas, 77030, United States

Location

Centex Studies Inc.

Houston, Texas, 77058, United States

Location

Gulf Coast Research Group LLC

Houston, Texas, 77098, United States

Location

Brooke Army Medical Center

Houston, Texas, 78234, United States

Location

Gastroenterology Consultants of San Antonio

Live Oak, Texas, 78233, United States

Location

Centex Studies Inc

McAllen, Texas, 78504, United States

Location

Pinnacle Clinical Research, PLLC

Rollingwood, Texas, 78746, United States

Location

The Texas Liver Institute, Inc.

San Antonio, Texas, 78215, United States

Location

Pinnacle Clinical Research, PLLC

San Antonio, Texas, 78229, United States

Location

Texas Digestive Consultants (TDDC)

Southlake, Texas, 76092-9167, United States

Location

Victoria Gastroenterology

Victoria, Texas, 77904, United States

Location

University of Utah School of Medicine

Salt Lake City, Utah, 84132, United States

Location

University of Virginia Health System

Charlottesville, Virginia, 22908, United States

Location

University of Virginia

Charlottesville, Virginia, 22908, United States

Location

Inova Fairfax Medical Campus - Center for Liver Disease

Falls Church, Virginia, 22042, United States

Location

Bon Secours Liver Institute of Virginia - Newport News

Newport News, Virginia, 23602, United States

Location

Bon Secours Liver Institute of Virginia - Richmond

Richmond, Virginia, 23226, United States

Location

Hunter Holmes McGuire VA Medical Center

Richmond, Virginia, 23249, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Kaiser Permanente Springfield Medical Center

Springfield, Virginia, 22150, United States

Location

Harborview Medical Center

Seattle, Washington, 98104-2420, United States

Location

Swedish Organ Transplant and Liver Center

Seattle, Washington, 98104, United States

Location

Sanatorio Güemes

Caba, Buenos Aires, 1180AAX, Argentina

Location

Axismed S.R.L

CABA, Buenos Aires, C1430CKE, Argentina

Location

Instituto de Investigaciones Clinicas San Nicolas SRL

San Nicolás de los Arroyos, Buenos Aires, 2900, Argentina

Location

Hospital Alemán

Buenos Aires, 1118, Argentina

Location

Centro de Investigación y Prevención Cardiovascular SA (CIPREC)

Buenos Aires, 1119, Argentina

Location

Fundación Sanatorio Güemes

Buenos Aires, 1180, Argentina

Location

Hospital Italiano de Buenos Aires

Buenos Aires, 1181, Argentina

Location

Hospital Británico de Buenos Aires

Buenos Aires, 1280, Argentina

Location

CCBR Clinical Research

Buenos Aires, 1430, Argentina

Location

Centro De Hepatologia Ciudad de La Plata

La Plata, 1704, Argentina

Location

Hospital Universitario Austral

Pilar, 1629, Argentina

Location

Dim Clinica Privada

Ramos Mejía, 1704, Argentina

Location

Hospital Provincial del Centenario

Rosario, 2000, Argentina

Location

Instituto Medico Alas

Salta, A4400ERH, Argentina

Location

Flinders Medical Centre

Bedford Park, 5042, Australia

Location

Box Hill Hospital

Box Hill, 3128, Australia

Location

Monash Medical Centre Clayton

Clayton, 3168, Australia

Location

Concord Repatriation General Hospital

Concord, 2139, Australia

Location

St. Vincent's Hospital Melbourne

Fitzroy, 3065, Australia

Location

Austin Hospital

Heidelberg, 3084, Australia

Location

Nepean Hospital

Kingswood, 2747, Australia

Location

The St George Hospital

Kogarah, 2217, Australia

Location

The Alfred Hospital

Melbourne, 3004, Australia

Location

Fiona Stanley Hospital

Murdoch, 6150, Australia

Location

Sir Charles Gairdner Hospital (SCGH)

Nedlands, 6009, Australia

Location

Westmead Hospital

Westmead, 2145, Australia

Location

Hôpital Erasme

Brussels, 1070, Belgium

Location

Universitair Ziekenhuis Brussel

Brussels, 1090, Belgium

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

Universitair Ziekenhuis Antwerpen

Edegem, 2650, Belgium

Location

Universitair Ziekenhuis Gent

Ghent, 9000, Belgium

Location

Universitair Ziekenhuis Leuven

Leuven, 3000, Belgium

Location

Centre Hospitalier de Wallonie Picardie (CHWAPI)

Tournai, 7500, Belgium

Location

LAIR Centre

Vancouver, British Columbia, V5Z 1H2, Canada

Location

Vancouver General Hospital (VGH) - Gordon and Leslie Diamond Health Care Centre

Vancouver, British Columbia, V5Z 1M9, Canada

Location

Toronto General Hospital

Toronto, Ontario, M5G 2C4, Canada

Location

Toronto Western Hospital

Toronto, Ontario, M5G 2C4, Canada

Location

Toronto Liver Centre

Toronto, Ontario, M6H 3M1, Canada

Location

Monteregie Centre de Recherche

Greenfield Park, Quebec, J4V 2H1, Canada

Location

The Montreal Chest Institute

Montreal, Quebec, H4A 3J1, Canada

Location

University of Calgary, Cumming School of Medicine

Calgary, AB, T2N 4Z6, Canada

Location

Queen Elizabeth II Health Sciences Centre, Nova Scotia Health Authority

Halifax, B3H 1V7, Canada

Location

Mc Gill University Health Centre (MUHC)

Montreal, H4A 3J1, Canada

Location

University of Manitoba

Winnipeg, MB, R3E 3P4, Canada

Location

Hospital de La Serena

La Serena, 1710209, Chile

Location

Alta Salud

Los Ángeles, 4430035, Chile

Location

Hospital Clínico UC

Santiago, 8330024, Chile

Location

Hospital Clínico Universidad de Chile

Santiago, 8380456, Chile

Location

Centro de Estudios Clinicos Barros Luco SPA (Patients seen, Fibroscan stored and Drug Shipment)

Santiago, 8910108, Chile

Location

Clínica Reñaca

Viña del Mar, 2540488, Chile

Location

Solano&Terront Servicios Médicos LTDA - Unidad Integral de Endocrinologia UNIENDO

Bogotá, Bogota D.C., 110221, Colombia

Location

Fundación Cardio Infantil - Instituto de Cardiología

Bogotá, 04073-5820, Colombia

Location

Fundación Valle del Lili

Cali, 760032, Colombia

Location

Centro Medico Imbanaco

Cali, 760042, Colombia

Location

Fundacion Hospitalaria San Vicente de Paul

Medellín, 050010, Colombia

Location

Hospital Universitario San Vicente de Paul Fundación

Medellín, 50010, Colombia

Location

Hospital Pablo Tobon Uribe

Medellín, 50034, Colombia

Location

Fakultní Nemocnice Brno

Brno, 625 00, Czechia

Location

Research Site S.R.O.

Pilsen, 30100, Czechia

Location

Research Site, s.r.o

Pilsen, 30100, Czechia

Location

KlinMed s.r.o.

Prague, 120 00, Czechia

Location

Aarhus University Hospital

Aarhus, 8000, Denmark

Location

Helsinki University Central Hospital

Helsinki, 00029, Finland

Location

CHU Amiens Picardie

Amiens, 80054, France

Location

CHU Angers

Angers, 49933, France

Location

Hôpital Antoine-Béclère

Clamart, 92140, France

Location

Hôpital Beaujon

Clichy, 92110, France

Location

Hôpital Henri Mondor

Créteil, 94000, France

Location

CHU Limoges - Hôpital Dupuytren

Limoges, 87042, France

Location

Hôpital de la Croix-Rousse

Lyon, 69004, France

Location

Hôpital Saint Joseph

Marseille, 13285, France

Location

CHRU Montpellier- Hôpital Saint Eloi

Montpellier, 34295, France

Location

CHU de Nantes - Hôpital Laennec

Nantes, 44093, France

Location

CHU de Nice- Hôpital de l'Archet II

Nice, 06202, France

Location

Hôpital Saint-Antoine

Paris, 75012, France

Location

Hopital Pitie-Salpetriere

Paris, 75013, France

Location

Hôpital Cochin

Paris, 75014, France

Location

Hôpital Haut-Lévêque

Pessac, 33604, France

Location

CHU Toulouse - Hôpital Purpan

Toulouse, 31059, France

Location

CHU Nancy - Hôpital Brabois

Vandœuvre-lès-Nancy, 54511, France

Location

Hôpital Paul Brousse

Villejuif, 94800, France

Location

Universitätsklinikum Köln

Cologne, Northwest, 50937, Germany

Location

Universitätsklinikum RWTH Aachen

Aachen, 52074, Germany

Location

Liver Center

Berlin, 10969, Germany

Location

Gastroenterologie am Bayerischen Platz/ Gastro-Studien

Berlin, Germany

Location

Universitätsklinikum Bonn

Bonn, 53127, Germany

Location

Universitätsklinikum Köln

Cologne, 50937, Germany

Location

Universitätsklinikum Essen

Essen, 45147, Germany

Location

Universitätsklinikum Frankfurt - Goethe Universität

Frankfurt, 60590, Germany

Location

Universitätsklinikum Freiburg

Freiburg im Breisgau, 79106, Germany

Location

Asklepios Klinik St. Georg

Hamburg, 20099, Germany

Location

Universitätsklinikum Hamburg-Eppendorf (UKE)

Hamburg, 20246, Germany

Location

Medizinische Hochschule Hannover (MHH)

Hanover, 30625, Germany

Location

Universitätsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

EUGASTRO GmbH

Leipzig, 04103, Germany

Location

Universitätsklinikum Leipzig

Leipzig, 04103, Germany

Location

Universitätsklinikum Magdeburg

Magdeburg, 39120, Germany

Location

Universitätsmedizin der Johannes Gutenberg-Universität Mainz

Mainz, 55131, Germany

Location

Universitätsklinikum Würzburg

Würzburg, 97080, Germany

Location

Azienda Ospedaliero-Universitaria di Bologna Policlinico S. Orsola-Malpighi

Bologna, 40138, Italy

Location

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico

Milan, 20122, Italy

Location

Azienda Ospedaliera di Rilievo Nazionale "A. Cardarelli"

Napoli, 80131, Italy

Location

Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone

Palermo, 90127, Italy

Location

Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone

Palermo, 90141, Italy

Location

Policlinico Tor Vergata

Roma, 00133, Italy

Location

Fondazione Policlinico Universitario Agostino Gemelli

Roma, 00168, Italy

Location

Ospedale Casa Sollievo della Sofferenza I.R.C.C.S.

San Giovanni Rotondo, 71013, Italy

Location

Azienda Ospedaliera Universitaria Citta della Salute e della Scienza di Torino - Ospedale Molinette

Torino, 10126, Italy

Location

Hospital Angeles Clinica Londres

México, DIF, 6700, Mexico

Location

Centro de Investigación Clínica del Pacífico, S.A de C.V.

Acapulco, 39670, Mexico

Location

Hospital Maria Auxiliadora

Guadalajara, Mexico

Location

Médica Sur

Mexico City, 14050, Mexico

Location

Consultorio Medico

Mexico City, Mexico

Location

Accelerium S de RL de C.V.

Monterrey, Mexico

Location

Vrije Universiteit Medical Center

Amsterdam, 1081 HZ, Netherlands

Location

Academisch Medisch Centrum

Amsterdam, 1105 AZ, Netherlands

Location

Maastricht UMC+

Maastricht, 6229 HX, Netherlands

Location

Radboud UMC

Nijmegen, 6525 GA, Netherlands

Location

Centro Hospitalar e Universitário de Coimbra, EPE - Hospitais da Universidade de Coimbra

Coimbra, 3000-075, Portugal

Location

Centro Hospitalar Lisboa Central, EPE - Hospital Santo António dos Capuchos

Lisbon, 1169-050, Portugal

Location

Centro Hospitalar de Lisboa Norte, EPE - Hospital Santa Maria

Lisbon, 1649-035, Portugal

Location

Centro Hospitalar de São João, EPE - Hospital de São João

Porto, 4200-319, Portugal

Location

Centro Hospitalar de São João

Porto, 4200-319, Portugal

Location

Centro Hospita de Tras-os-Montes e Alto Douro, EPE

Vila Real, 5000-508, Portugal

Location

Caparra Internal Medicine Research Center

Río Grande, 00745, Puerto Rico

Location

Klinical Investigations Group, LLC

San Juan, 00909, Puerto Rico

Location

Fundacion de Investigacion de Diego

San Juan, 00927, Puerto Rico

Location

Fundación de Investigación

San Juan, 909, Puerto Rico

Location

Institutul National de Boli Infectioase "Prof. Dr. Matei Bals"

Bucharest, 021105, Romania

Location

Institutul Clinic Fundeni

Bucharest, 022328, Romania

Location

SC Cabinet Particular Policlinic Algomed SRL

Timișoara, 300002, Romania

Location

Spitalul Clinic Judetean de Urgenta "Pius Brinzeu" Timisoara

Timișoara, 300736, Romania

Location

FSBRI "Federal Research Center of nutrition and biotechnology

Moscow, 109240, Russia

Location

I. M. Sechenov - First Moscow State Medical University

Moscow, 119991, Russia

Location

M. F. Vladimirsky - Clinical Research Institution of Moscow Region

Moscow, 129110, Russia

Location

Military medical academy n. a. S.M. Kirov

Saint Petersburg, 194044, Russia

Location

City Clinical Hospital No. 31

Saint Petersburg, 197110, Russia

Location

St Petersburg State Budgetary Healthcare Institution City Clinical Hospital N°31

Saint Petersburg, 197110, Russia

Location

Tiervlei Trial Centre

Cape Town, 7530, South Africa

Location

Mediclinic Constantiaberg

Cape Town, 7800, South Africa

Location

Phoenix Pharma (Pty) Ltd

Port Elizabeth, 6001, South Africa

Location

Hospital de la Santa Creu i Sant Pau

Barcelona, 8025, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, 8035, Spain

Location

Hospital Clinic i Provincial

Barcelona, 8036, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 128041, Spain

Location

Hospital Universitario Puerta de Hierro

Majadahonda, 28222, Spain

Location

Hospital Universitario Virgen de la Victoria

Málaga, 29010, Spain

Location

Complexo Hospitalario Universitario de Pontevedra

Pontevedra, 36071, Spain

Location

Hospital Universitario Marqués de Valdecilla

Santander, 39008, Spain

Location

Campus Hospital Universitario Virgen del Rocío - Instituto de Biomedicina de Sevilla (IBIS)

Seville, 41014, Spain

Location

Karolinska Universitetssjukhuset Huddinge

Stockholm, 14186, Sweden

Location

INSELSPITAL, University Hospital Bern

Bern, 3010, Switzerland

Location

Centre Hospitalier Universitaire Vaudois (CHUV)

Lausanne, 1011, Switzerland

Location

Kantonsspital St. Gallen

Sankt Gallen, 9007, Switzerland

Location

UniversitätsSpital Zürich

Zurich, 8091, Switzerland

Location

Ankara Üniversitesi Tıp Fakültesi

Ankara, 6100, Turkey (Türkiye)

Location

Istanbul Universitesi Istanbul Tip Fakultesi

Çapa, 34093, Turkey (Türkiye)

Location

Bezmiâlem Vakıf Üniversitesi

Fatih, 34093, Turkey (Türkiye)

Location

Sağlık Bilimleri Üniversitesi Ümraniye Eğitim ve Araştırma Hastanesi

Istanbul, 34766, Turkey (Türkiye)

Location

Ege Üniversitesi

Izmir, 35040, Turkey (Türkiye)

Location

Marmara Üniversitesi Eğitim ve Araştırma Hastanesi

Pendik, 34890, Turkey (Türkiye)

Location

University Hospitals Birmingham NHS foundation Trust

Birmingham, B15 2TT, United Kingdom

Location

Addenbrooke's Hospital

Cambridge, CB2 0QQ, United Kingdom

Location

Frimley Park Hospital NHS Foundation Trust

Frimley, GU16 7UJ, United Kingdom

Location

Hull and East Yorkshire Hospitals NHS Trust - Hull Royal Infirmary

Hull, HU3 2JZ, United Kingdom

Location

Bart Health NHS Trust- Royal London Hospital

London, E1 1BB, United Kingdom

Location

The Royal Free London NHS Foundation Trust - The Royal Free Hospital

London, NW3 2QG, United Kingdom

Location

Guy's and St Thomas' NHS Foundation Trust - St Thomas' Hospital

London, SE1 7EH, United Kingdom

Location

St George's University Hospitals NHS Foundation Trust - St George's Hospital

London, SW170QT, United Kingdom

Location

The Newcastle upon Tyne Hospitals NHS Foundation Trust - Freeman Hospital

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Nottingham University Hospitals NHS FoundationTrust - Queen's Medical Centre

Nottingham, NG7 2UH, United Kingdom

Location

Plymouth Hospitals NHS Trust - Derriford Hospital

Plymouth, PL6 8DH, United Kingdom

Location

Portsmouth Hospitals NHS Trust - Queen Alexandra Hospital

Portsmouth, PO6 3LY, United Kingdom

Location

MeSH Terms

Conditions

Non-alcoholic Fatty Liver DiseaseFibrosis

Interventions

2-(2,6-dimethyl-4-(3-(4-(methylthio)phenyl)-3-oxo-1-propenyl)phenoxyl)-2-methylpropanoic acid

Condition Hierarchy (Ancestors)

Fatty LiverLiver DiseasesDigestive System DiseasesPathologic ProcessesPathological Conditions, Signs and Symptoms

Limitations and Caveats

The study was prematurely terminated based upon limited efficacy at time of the interim analysis, not due to safety concerns, and the conclusion that there would be limited benefit for participants to continue in the trial. Therefore, the results for efficacy endpoints other than the primary and key secondary endpoints are not presented in the disclosure of these results.

Results Point of Contact

Title
Carol Addy, MD MMSc
Organization
GENFIT

Study Officials

  • Carol Addy, MD MMSc

    Genfit

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 16, 2016

First Posted

March 10, 2016

Study Start

March 1, 2016

Primary Completion

October 28, 2020

Study Completion

October 28, 2020

Last Updated

March 23, 2022

Results First Posted

March 23, 2022

Record last verified: 2022-02

Locations