NCT02603887

Brief Summary

This pilot early phase I trial studies pembrolizumab in treating patients with slow growing (smoldering) multiple myeloma with intermediate or high-risk of spreading. Immunotherapy with monoclonal antibodies, such as pembrolizumab, may help the body's immune system attack the cancer, and may interfere with the ability of tumor cells to grow and spread.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
20

participants targeted

Target at P25-P50 for early_phase_1

Timeline
20mo left

Started Jul 2016

Longer than P75 for early_phase_1

Geographic Reach
1 country

1 active site

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress86%
Jul 2016Dec 2027

First Submitted

Initial submission to the registry

November 11, 2015

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 13, 2015

Completed
8 months until next milestone

Study Start

First participant enrolled

July 20, 2016

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 30, 2017

Completed
2.2 years until next milestone

Results Posted

Study results publicly available

March 20, 2020

Completed
7.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2027

Expected
Last Updated

January 29, 2026

Status Verified

January 1, 2026

Enrollment Period

1.4 years

First QC Date

November 11, 2015

Results QC Date

February 7, 2020

Last Update Submit

January 13, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate (ORR)

    Overall response rate is defined as patients who have achieved partial response or higher as described per IMWG criteria for multiple myeloma after 8 cycles of therapy with pembrolizumab. Will be measured according to International Myeloma Working Group Criteria (IMWG) criteria. Response rate will be estimated accordingly. Each cycle has a duration of 21 days.

    From cycle 1 to cycle 8, up to 168 days

Secondary Outcomes (3)

  • Number of Participants That Had Progression to Multiple Myeloma

    At 30 months from study entry

  • Clinical Benefit Rate

    From cycle 1 to cycle 8, up to 168 days

  • Overall Survival

    Time of start of treatment to death from any cause up to 2 years and 6 months

Study Arms (1)

Treatment (pembrolizumab)

EXPERIMENTAL

Patients receive pembrolizumab IV over 30 minutes on day 1. Treatment repeats every 21 days for up to 24 courses in the absence of disease progression or unacceptable toxicity.

Other: Laboratory Biomarker AnalysisBiological: Pembrolizumab

Interventions

PembrolizumabBIOLOGICAL

Given IV

Also known as: Keytruda, Lambrolizumab, MK-3475, SCH 900475
Treatment (pembrolizumab)

Correlative studies

Treatment (pembrolizumab)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may not qualify if:

  • Patients must have histologically confirmed SMM based on the following criteria:
  • (A) Mayo clinic criteria (patient must have at least 2 risk factors present):
  • \. Bone marrow core biopsy plasma cell involvement by cluster of differentiation (CD)138 immunohistochemistry \>= 10%
  • \. Monoclonal spike \>= 3 g/dL
  • \. Free light chain ratio in serum \< 0.125 or \> 8; \*2 of 3 risk factors: intermediate risk for progression at a rate of 51% at 5 years, \*3 of 3 risk factors: high risk for progression at a rate of 76% at 5 years
  • OR (B) Programa para el Tratamiento de Hemopatias Malignas (PETHEMA) criteria (patient must have at least 1 risk factor present)
  • \. \>= 95% abnormal plasma cells/total plasma cells in bone marrow compartment
  • \. Immunoparesis \*1 of 2 risk factors: intermediate risk for progression at a rate of 46% at 5 years, \*2 of 2 risk factors: high risk for progression at a rate of 72% at 5 years
  • OR (C) Southwestern Oncology Group (SWOG) criteria (patient must have 2 risk factors present or one risk factor if this risk factor is a 70-gene signature (GEP70) score of \> 37.2)
  • \. Monoclonal spike \>= 3 g/dL
  • \. Involved free light chain \>= 25 mg/dL
  • \. GEP70 risk score \> 37.2 \*\>= 2 risk factors: high risk of progression at a rate of 70% at 2 years\*; we would also include patients with 1 risk factor as long as this risk factor is GEP70 risk score \> 37.2 since patients with this risk factor have an intermediate risk of progression at a rate of 50% at 2 years
  • Creatinine clearance \>= 50 ml/min; creatinine clearance (CrCl) will be calculated by Cockcroft-Gault method
  • Eastern Cooperative Oncology Group (ECOG) performance status 0-1
  • Absolute neutrophil count (ANC) \>= 1.0 x 10\^9 /L
  • +35 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

M D Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Related Publications (1)

  • Manasanch EE, Han G, Mathur R, Qing Y, Zhang Z, Lee H, Weber DM, Amini B, Berkova Z, Eterovic K, Zhang S, Zhang J, Song X, Mao X, Morgan M, Feng L, Baladandayuthapani V, Futreal A, Wang L, Neelapu SS, Orlowski RZ. A pilot study of pembrolizumab in smoldering myeloma: report of the clinical, immune, and genomic analysis. Blood Adv. 2019 Aug 13;3(15):2400-2408. doi: 10.1182/bloodadvances.2019000300.

Related Links

MeSH Terms

Conditions

Smoldering Multiple Myeloma

Interventions

pembrolizumab

Condition Hierarchy (Ancestors)

Precancerous ConditionsNeoplasmsHypergammaglobulinemiaBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesParaproteinemiasImmunoproliferative DisordersImmune System Diseases

Results Point of Contact

Title
Dr. Elisabet Manasanch/ Assistant Professor, Lymphoma-Myeloma
Organization
UT MD Anderson Cancer Center

Study Officials

  • Neeraj Saini, MD

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
early phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 11, 2015

First Posted

November 13, 2015

Study Start

July 20, 2016

Primary Completion

December 30, 2017

Study Completion (Estimated)

December 31, 2027

Last Updated

January 29, 2026

Results First Posted

March 20, 2020

Record last verified: 2026-01

Locations