NCT02580591

Brief Summary

The study will investigate the efficacy, safety, tolerability and Pharmacokinetic(PK) of 3 doses of empagliflozin compared with placebo over 26 weeks in 960 patients with type 1 diabetes mellitus as adjunctive therapy to insulin

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
977

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Dec 2015

Geographic Reach
24 countries

189 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 19, 2015

Completed
1 day until next milestone

First Posted

Study publicly available on registry

October 20, 2015

Completed
2 months until next milestone

Study Start

First participant enrolled

December 22, 2015

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 12, 2017

Completed
8 days until next milestone

Study Completion

Last participant's last visit for all outcomes

September 20, 2017

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

November 2, 2018

Completed
Last Updated

November 2, 2018

Status Verified

October 1, 2018

Enrollment Period

1.7 years

First QC Date

October 19, 2015

Results QC Date

September 20, 2018

Last Update Submit

October 31, 2018

Conditions

Outcome Measures

Primary Outcomes (2)

  • Change From Baseline in Glycated Hemoglobin (HbA1c) at Week 26 for Full Analysis Set (FAS) (Observed Cases [OC])

    Change from baseline in Glycated hemoglobin (HbA1c) for full analysis set (FAS) (observed cases \[OC\]) is presented. With regards to efficacy and safety endpoints, the term 'baseline' referred to the last observed measurement prior to administration of any randomized trial medication. Least squares mean is adjusted mean change from baseline.

    Baseline to week 26

  • Change From Baseline in Glycated Hemoglobin (HbA1c) at Week 26 for Modified Intention-to-treat Population Set (mITT) (Observed Case (OC) - All Data (AD) (OC-AD))

    Change from baseline in Glycated hemoglobin (HbA1c) for modified intention-to-treat population set (mITT) (observed case - all data \[OC-AD\]) is presented. With regards to efficacy and safety endpoints, the term 'baseline' referred to the last observed measurement prior to administration of any randomized trial medication. Least squares mean is adjusted mean change from baseline.

    Baseline to week 26

Secondary Outcomes (4)

  • Rate Per Patient-year of Investigator-reported Symptomatic Hypoglycemic Adverse Events (AEs) With Confirmed Plasma Glucose (PG)

    Week 5 to Week 26, Week 1 to Week 26

  • Change From Baseline in Body Weight at Week 26

    Baseline to week 26

  • Change From Baseline in Total Daily Insulin Dose (TDID) at Week 26

    Baseline to week 26

  • Change From Baseline in Systolic Blood Pressure (SBP) and Diastolic Blood Pressure (DBP) at Week 26

    Baseline to week 26

Study Arms (4)

Empagliflozin low dose

EXPERIMENTAL
Drug: EmpagliflozinDrug: Placebo

Empagliflozin high dose

EXPERIMENTAL
Drug: EmpagliflozinDrug: Placebo

Empagliflozin medium dose

EXPERIMENTAL
Drug: EmpagliflozinDrug: Placebo

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

Empagliflozin high doseEmpagliflozin low doseEmpagliflozin medium dose

For blinding purposes

Empagliflozin high doseEmpagliflozin low doseEmpagliflozin medium dosePlacebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Signed and dated written informed consent
  • Male or female patient receiving insulin for the treatment of documented diagnosis of type 1 diabetes mellitus (T1DM) \> 1 year
  • C-peptide value of \< 0.7 ng/mL
  • Use of Multiple Daily Injections (MDI) of insulin or insulin pump user with total daily insulin \>= 0.3 and \<= 1.5 U/kg
  • Glycated haemoglobin (HbA1c) \>= 7.5% and \<= 10.0%
  • Good understanding of T1DM
  • Age \>= 18 years
  • Body Mass Index (BMI) \>= 18.5 kg/m2
  • Estimated glomerular filtration rate \>= 30 mL/min/1.73 m2
  • Women of child-bearing potential must use highly effective methods of birth control

You may not qualify if:

  • History of type 2 diabetes mellitus, maturity onset diabetes of the young (MODY), pancreatic surgery or chronic pancreatitis
  • Pancreas, pancreatic islet cells or renal transplant recipient
  • T1DM treatment with any other antihyperglycaemic drug except subcutaneous basal and bolus insulin within last 3 months
  • Occurrence of severe hypoglycaemia within last 3 months and until randomisation
  • Occurence of diabetic ketoacidosis within 3 months prior to Visit 1 and until Visit 6
  • Irregular sleep/wake cycle
  • Acute coronary syndrome, stroke or Transient Ischaemic Attack (TIA) within last 3 months
  • Severe gastroparesis
  • Brittle diabetes
  • Liver disease
  • Eating disorders
  • Treatment with anti-obesity drugs, weight-loss surgery or aggressive diet regimen
  • Treatment with systemic corticosteroids
  • Change in dose of thyroid hormones within last 6 weeks and until randomisation
  • Cancer or treatment for cancer in the last five years
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (189)

Healthscan Clinical Trials LLC

Montgomery, Alabama, 36106, United States

Location

John Muir Physician Network Clinical Research Center

Concord, California, 94520, United States

Location

Valley Research

Fresno, California, 93720, United States

Location

Marin Endocrine Care and Research

Greenbrae, California, 94904, United States

Location

Pacific Research Partners, LLC

Oakland, California, 94607, United States

Location

NorCal Endocrinology and Internal Medicine

San Ramon, California, 94583, United States

Location

William Sansum Diabetes Center

Santa Barbara, California, 93105, United States

Location

University of Colorado Denver

Aurora, Colorado, 80045, United States

Location

International Research Associates, LLC

Hialeah, Florida, 33012, United States

Location

Solutions Through Advanced Research, Inc.

Jacksonville, Florida, 32225, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Suncoast Clinical Research, Inc.

New Port Richey, Florida, 34652, United States

Location

Atlanta Diabetes Associates

Atlanta, Georgia, 30318, United States

Location

Physicians Research Associates, LLC

Lawrenceville, Georgia, 30046, United States

Location

Sestron Clinical Research

Marietta, Georgia, 30060, United States

Location

Eagle's Landing Diabetes and Endocrinology

Stockbridge, Georgia, 30281, United States

Location

Northwest Endo Diabetes Research, LLC

Arlington Heights, Illinois, 60005, United States

Location

Kentucky Diabetes Endocrinology Center

Lexington, Kentucky, 40503, United States

Location

University of Maryland School of Medicine

Baltimore, Maryland, 21201, United States

Location

MODEL Clinical Research

Baltimore, Maryland, 21204, United States

Location

Clinical Research Consultants, LLC

Kansas City, Missouri, 64111, United States

Location

Desert Endocrinology Clinical Research Center

Henderson, Nevada, 89052, United States

Location

Palm Research Center

Las Vegas, Nevada, 89128, United States

Location

Endocrine-Diabetes Care and Resource Center

Rochester, New York, 14607, United States

Location

Endocrine Associates of Long Island, PC

Smithtown, New York, 11787, United States

Location

Diabetes Endocrinology Research Center of Western New York

Williamsville, New York, 14221, United States

Location

Diabetes and Endocrinology Consultants, PC

Morehead City, North Carolina, 28557, United States

Location

Holzer Clinic LLC

Gallipolis, Ohio, 45631, United States

Location

COR Clinical Research, LLC

Oklahoma City, Oklahoma, 73103, United States

Location

Strand Physician Specialists dba Carolina Health Specialists

Myrtle Beach, South Carolina, 29572, United States

Location

AM Diabetes and Endocrinology Center

Bartlett, Tennessee, 38133, United States

Location

Holston Medical Group

Bristol, Tennessee, 37620, United States

Location

University Diabetes and Endocrine Consultants

Chattanooga, Tennessee, 37411, United States

Location

Texas Diabetes & Endocrinology PA

Austin, Texas, 78749, United States

Location

Texas Health Physicians Group

Dallas, Texas, 75218, United States

Location

Dallas Diabetes and Endocrine Center

Dallas, Texas, 75230, United States

Location

Research Institute of Dallas

Dallas, Texas, 75231, United States

Location

Endeavor Clinical Trials, PA

San Antonio, Texas, 78229, United States

Location

Virginia Endocrinology Research

Chesapeake, Virginia, 23321, United States

Location

Coffs Endocrine & Diabetes Services

Coffs Harbour, New South Wales, 2450, Australia

Location

Lyell McEwin Hospital

Elizabeth Vale, South Australia, 5112, Australia

Location

SA Endocrine Research P/L

Keswick, South Australia, 5035, Australia

Location

Eastern Clinical Research Unit

East Ringwood, Victoria, 3135, Australia

Location

Richmond Road and Diagnostic Treatment Centre

Calgary, Alberta, T2T 5C7, Canada

Location

The Bailey Clinic

Red Deer, Alberta, T4N 6V7, Canada

Location

Eastern Health (MUN)

St. John's, Newfoundland and Labrador, A1B 3V6, Canada

Location

Centre for Studies in Family Medicine

London, Ontario, N6G 2M1, Canada

Location

St. Michael's Hospital

Toronto, Ontario, M5B 1W8, Canada

Location

Omnispec Recherche Clinique Inc.

Mirabel, Quebec, J7J 2K8, Canada

Location

Applied Medical Informatics Research INC.

Westmount, Quebec, H3Z 1E5, Canada

Location

Clinique des maladies Lipidiques de Quebec

Québec, G1V 4M6, Canada

Location

University Hospital Brno

Brno, 625 00, Czechia

Location

Diahaza s.r.o.Intern.Med.Outpat.Clin.Dep.Diabetology,Holesov

Holešov, 769 01, Czechia

Location

AIDIN VK s.r.o.,Department Diabetology, Hranice

Hranice, 753 01, Czechia

Location

Univ. Hospital Kralovske Vinohrady

Prague, 100 42, Czechia

Location

DiaGolfova s.r.o., Department Diabetology, Prague

Prague, 102 00, Czechia

Location

Milan Kvapil s.r.o.,Diabetology ambulance,Prague

Prague, 149 00, Czechia

Location

ResTrial s.r.o.Diabetology Ambulance,Prague

Prague, 18100, Czechia

Location

HUS, Lihavuustutkimusyksikkö Biomedicum Helsinki

Helsinki, 00290, Finland

Location

Mehiläinen Jyväskylä

Jyväskylä, 40100, Finland

Location

Satakunnan Diabetesasema, Pori

Pori, 28100, Finland

Location

FinnMedi Oy, Tampere

Tampere, 33520, Finland

Location

TYKS

Turku, FI-20520, Finland

Location

HOP Jean Minjoz

Besançon, 25030, France

Location

HOP Le Creusot

Le Creusot, 71200, France

Location

HOP Paris Saint-Joseph

Paris, 75014, France

Location

HOP Bichat

Paris, 75018, France

Location

HOP de Poitiers

Poitiers, 86021, France

Location

HOP Civil

Strasbourg, 67091, France

Location

HOP Rangueil

Toulouse Cédex 04, 31059, France

Location

Diabetes-Klinik Bad Mergentheim GmbH & Co. KG

Bad Mergentheim, 97980, Germany

Location

Diabetologische Schwerpunktpraxis, Bosenheim

Bosenheim, 55545, Germany

Location

Praxis Dr. Busch, Dortmund

Dortmund, 44137, Germany

Location

GWT-TUD GmbH

Dresden, 01307, Germany

Location

ZKS Südbrandenburg GmbH

Elsterwerda, 04910, Germany

Location

InnoDiab Forschung GmbH

Essen, 45136, Germany

Location

Praxis Dr. Kaiser, Frankfurt

Frankfurt, 60388, Germany

Location

Institut für Diabetesforschung Münster GmbH

Münster, 48145, Germany

Location

Diabetologische Schwerpunktpraxis

Münster, 48153, Germany

Location

Praxis Dr. Behnke, Neuwied

Neuwied, 56564, Germany

Location

Praxis Dr. Hilgenberg

Rehburg-Loccum, 31547, Germany

Location

"Korgialeneio-Benakeio" Hellenic Red Cross Hospital

Athens, 115 26, Greece

Location

General Hospital of Athens "Laiko"

Athens, 11527, Greece

Location

Univ. Gen. Hosp. of Ioannina

Ioannina, 45500, Greece

Location

General Hospital of Nikaia

Nikaia, 18484, Greece

Location

General Hopsital of Thessaloniki "Ippokrateio"

Thessaloniki, 54642, Greece

Location

General Hospital of Thessaloniki "G. Papanikolaou"

Thessaloniki, 57010, Greece

Location

Clinexpert Kft.

Budapest, 1033, Hungary

Location

Synexus Magyarorszag Kft.

Budapest, 1036, Hungary

Location

University Debrecen Hospital

Debrecen, 4032, Hungary

Location

CRU Hungary Ltd, Private Practice, Miskolc

Miskolc, 3529, Hungary

Location

Clinfan SMO Ltd.

Szekszárd, 7100, Hungary

Location

Csongrad Country Dr Bugyi Istvan Hosp.

Szentes, 6600, Hungary

Location

Zala Country Hospital, Diabetic Outpatient Clinic

Zalaegerszeg, 8900, Hungary

Location

Mater Misericordiae University Hospital

Dublin, 7, Ireland

Location

Inrca-Irccs

Ancona, 60124, Italy

Location

A.O. Spedali Civili di Brescia

Brescia, 25123, Italy

Location

Osp. Campo di Marte

Lucca, 55100, Italy

Location

Azienda Ospedaliera Universitaria "Federico II"

Napoli, 80131, Italy

Location

Policlinico Gemelli

Roma, 00168, Italy

Location

Osp. S. Giovanni Calibita Fatebenefratelli

Roma, 00186, Italy

Location

IRCCS Gruppo Multimedica

Sesto San Giovanni (MI), 20099, Italy

Location

A.O.U. Senese Policlinico Santa Maria alle Scotte

Siena, 53100, Italy

Location

Ospedale Molinette, AO Città della Salute e della

Torino, 10126, Italy

Location

Zemgales Center of diabetes, Jelgava

Jelgava, 3001, Latvia

Location

A. Lucenko's Internist & Endocrinologist Doctor's Practice

Liepāja, 3401, Latvia

Location

Dace Teterovska Doctor's Practice in Endocrinology,Ogre

Ogre, 5001, Latvia

Location

P. Stradins Clinical University Hospital, Riga

Riga, 1002, Latvia

Location

Riga Health Center, Private Practice

Riga, 1002, Latvia

Location

Sigulda Hospital, Outpatient department

Sigulda, 2150, Latvia

Location

VSV Centrs, Stalte Private Practice, Talsi

Talsi, 3201, Latvia

Location

Clínica EndocrInol en Diabetes Obesidad y Tiroides (DOT)

Aguascalientes, 20129, Mexico

Location

Hospital Cardiologica Aguascalientes

Aguascalientes, 20230, Mexico

Location

Unidad de Investigacion Clinica Cardiometabolica de Occident

Guadalajara, 44150, Mexico

Location

Instituto Jaliscience de Inv. en Diabetes y Obesidad, S.C.

Guadalajara, 44600, Mexico

Location

Unidad de Patologia Clinica

Guadalajara, CP 44650, Mexico

Location

Noordwest Ziekenhuisgroep

Alkmaar, 1815 JD, Netherlands

Location

Ziekenhuisgroep Twente locatie Almelo

Almelo, 7609 PP, Netherlands

Location

Meander Medisch Centrum

Amersfoort, 3813 TZ, Netherlands

Location

Gelre Ziekenhuizen Apeldoorn

Apeldoorn, 7334 DZ, Netherlands

Location

EB Utrecht Research

Utrecht, 3511 NH, Netherlands

Location

Universitair Medisch Centrum Utrecht

Utrecht, 3584 CX, Netherlands

Location

South Pacific Clinical Trials

Auckland, New Zealand, 0610, New Zealand

Location

Lipid and Diabetes Research Group

Christchurch, 8011, New Zealand

Location

M3 Helse AS

Hamar, N-2317, Norway

Location

Oslo Universitetssykehus HF, Lipidklinikken

Oslo, N-0027, Norway

Location

Stavanger Helseforskning

Stavanger, N-4068, Norway

Location

Universitetssykehuset Nord-Norge, Tromsø

Tromsø, N-9038, Norway

Location

DiabSerwis S.C., Chorzow

Chorzów, 41-500, Poland

Location

Medical Centre Pratia Gdynia

Gdynia, 81-338, Poland

Location

Medical Centre Pratia Katowice I

Katowice, 40-954, Poland

Location

Medical Centre Pratia Krakow

Krakow, 30-002, Poland

Location

University Hospital in Krakow

Krakow, 31-501, Poland

Location

Independent Public Clin.Hosp.no1Lublin,Dep.Internal Diseases

Lublin, 20-081, Poland

Location

Witold Chodzko Institute Rural Medic,Dep.Diabetology,Lublin

Lublin, 20-090, Poland

Location

Reg.Spec.Hosp.Olsztyn,Clin,Endocrinology,Diabetics.&Int.Med.

Olsztyn, 10-561, Poland

Location

Clinical Research Center Medicome, Oswiecim

Oświęcim, 32-600, Poland

Location

Omedica Medical Centre, Poznan

Poznan, 60-111, Poland

Location

Medical Centre Pratia Warszawa

Warsaw, 01-868, Poland

Location

NZOZ Med-Art.Specialist Clinics, Zory

Żory, 44-240, Poland

Location

Hospital de Braga-Escala Braga

Braga, 4710-243, Portugal

Location

Centro Hospitalar da Cova da Beira Hospital Pêro da Covilhã

Covilha, 6200-251, Portugal

Location

APDP - Associação Protectora dos Diabéticos de Portugal

Lisbon, 1250-189, Portugal

Location

H. Santo António - Centro Hospitalar do Porto

Porto, 4099-001, Portugal

Location

Centro Hospitalar São João,EPE

Porto, 4200-319, Portugal

Location

ULSAM, EPE - Hospital de Santa Luzia

Viana do Castelo, 4901-858, Portugal

Location

Centro Hospitalar de Vila Nova de Gaia

Vila Nova de Gaia, 4400-129, Portugal

Location

Nicodiab SRL, Bucharest

Bucharest, 010507, Romania

Location

Milit. Cent. Emerg. Univ. Hosp. Dr. Davila, Met. Dis. Dept.

Bucharest, 010825, Romania

Location

SC Medical Centre "Sanatatea Ta" SRL, Bucharest

Bucharest, 020603, Romania

Location

SC Pelican Impex SRL, Cabinet Nr. 201, Diabetes Dept.

Oradea, Bihor County, 410469, Romania

Location

Centrul Medical Dr Negrisanu SRL

Timișoara, 300456, Romania

Location

City Clinical Hospital no. 67, Moscow

Moscow, 123423, Russia

Location

CJSC"Polyclinic complex",Dep.Endocrinology,St.Petersburg

Saint Petersburg, 190013, Russia

Location

City Outpatient dep.no.107;clinc.pharmacology,st.petersburg

Saint Petersburg, 195030, Russia

Location

Medical Academy named after I. Mechnikov, St. Petersburg

Saint Petersburg, 195067, Russia

Location

City Hospital Saint Elizaveta, Dept. Endocrinology

Saint Petersburg, 195257, Russia

Location

Policlinic No. 1 of Russian Academy of Sciences, St. Petersburg

Saint Petersburg, 199034, Russia

Location

LCS Clinical Research Unit

Bryanston, 2021, South Africa

Location

TREAD Research

Cape Town, 7530, South Africa

Location

Dr Hilton Kaplan

Cape Town, 7708, South Africa

Location

Dr. L. A.Distiller

Johannesburg, 2198, South Africa

Location

VX Pharma (Pty) Ltd Pretoria

Pretoria, 0087, South Africa

Location

Diabetes Care Centre

Pretoria, 0181, South Africa

Location

Hospital A Coruña

A Coruña, 15006, Spain

Location

CM Avances Médicos

Granada, 18003, Spain

Location

Hospital de la Inmaculada Concepción

Granada, 18004, Spain

Location

Hospital General Universitario Gregorio Marañón

Madrid, 28007, Spain

Location

Hospital Universitario Infanta Leonor

Madrid, 28031, Spain

Location

Endo-Diabesidad-Clínica Durán & Asociados

Seville, 41018, Spain

Location

Hospital Virgen Macarena

Seville, 41071, Spain

Location

Hospital Clínico de Valencia

Valencia, 46010, Spain

Location

Ängelholms Sjukhus

Ängelholm, 262 81, Sweden

Location

CTC Sahlgrenska Universitetssjukhuset

Gothenburg, 413 45, Sweden

Location

Karlskoga lasarett

Karlskoga, 691 81, Sweden

Location

Skånes universitetssjukhus, Lund

Lund, 221 85, Sweden

Location

S3 Clinical Research Centers

Vällingby, 162 68, Sweden

Location

Royal Bournemouth and Christchurch Hospital

Bournemouth, BH7 7DW, United Kingdom

Location

Bradford Royal Infirmary

Bradford, BD9 6RJ, United Kingdom

Location

Hull Royal Infirmary

Hull, HU3 2RW, United Kingdom

Location

Ipswich Hospital

Ipswich, IP4 5PD, United Kingdom

Location

Leicester General Hospital

Leicester, LE5 4PW, United Kingdom

Location

Guy's Hospital

London, SE1 9RT, United Kingdom

Location

King's College Hospital

London, SE5 9RJ, United Kingdom

Location

St Mary's Hospital

London, W2 1NY, United Kingdom

Location

James Cook University Hospital

Middlesbrough, TS4 3BW, United Kingdom

Location

Royal Victoria Infirmary

Newcastle upon Tyne, NE1 4LP, United Kingdom

Location

Queen's Medical Centre

Nottingham, NG7 2UH, United Kingdom

Location

George Eliot Hospital

Nuneaton, CV10 7DJ, United Kingdom

Location

Related Publications (2)

  • Song C, Dhaliwal S, Bapat P, Scarr D, Bakhsh A, Budhram D, Verhoeff NJ, Weisman A, Fralick M, Ivers NM, Cherney DZI, Tomlinson G, Lovblom LE, Mumford D, Perkins BA. Point-of-Care Capillary Blood Ketone Measurements and the Prediction of Future Ketoacidosis Risk in Type 1 Diabetes. Diabetes Care. 2023 Nov 1;46(11):1973-1977. doi: 10.2337/dc23-0840.

  • Rosenstock J, Marquard J, Laffel LM, Neubacher D, Kaspers S, Cherney DZ, Zinman B, Skyler JS, George J, Soleymanlou N, Perkins BA. Empagliflozin as Adjunctive to Insulin Therapy in Type 1 Diabetes: The EASE Trials. Diabetes Care. 2018 Dec;41(12):2560-2569. doi: 10.2337/dc18-1749. Epub 2018 Oct 4.

MeSH Terms

Conditions

Diabetes Mellitus, Type 1

Interventions

empagliflozin

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Boehringer Ingelheim, Call Center
Organization
Boehringer Ingelheim

Study Officials

  • Boehringer Ingelheim

    Boehringer Ingelheim

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 19, 2015

First Posted

October 20, 2015

Study Start

December 22, 2015

Primary Completion

September 12, 2017

Study Completion

September 20, 2017

Last Updated

November 2, 2018

Results First Posted

November 2, 2018

Record last verified: 2018-10

Locations