NCT02573363

Brief Summary

This phase I trial studies the side effects and the best dose of selinexor when give together with standard chemotherapy, high dose cytarabine and mitoxantrone hydrochloride, in treating patients with acute myeloid leukemia. Selinexor may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. Drugs used in chemotherapy, such as cytarabine and mitoxantrone hydrochloride, work in different ways to stop the growth of cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Giving selinexor together with standard chemotherapy may be a better treatment for patients with acute myeloid leukemia.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
25

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Oct 2015

Typical duration for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 5, 2015

Completed
2 days until next milestone

Study Start

First participant enrolled

October 7, 2015

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 9, 2015

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2018

Completed
1.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 3, 2019

Completed
Last Updated

April 8, 2020

Status Verified

April 1, 2020

Enrollment Period

2.2 years

First QC Date

October 5, 2015

Last Update Submit

April 6, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • MTD of selinexor based on the dose-limiting toxicity graded according to the National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) version 4.03

    56 days

Secondary Outcomes (5)

  • Allo-SCT success rate

    After completion of induction therapy (6 months to a year)

  • Incidence of adverse events graded according to NCI CTCAE version 4.03

    Up to 30 days post-treatment

  • Incidence of non-relapse mortality

    Up to 1 year

  • Overall survival (OS) rates

    Date induction chemotherapy to the date of disease relapse or death, assessed up to 1 year

  • Progression-free survival (PFS) rates

    Date induction chemotherapy to the date of disease relapse or death, assessed up to 1 year

Other Outcomes (1)

  • MRD status as measured by WT1 transcript levels using quantitative real time-PCR

    Up to 1 year

Study Arms (1)

selinexor, cytarabine, and mitoxantrone

EXPERIMENTAL

INDUCTION CHEMOTHERAPY: Patients receive high-dose cytarabine and mitoxantrone hydrochloride per standard of care on days 1 and 5, and selinexor PO on days 2, 4, 9, and 11. CONSOLIDATION CHEMOTHERAPY: Patients receive high-dose cytarabine per standard of care on days 1, 3, and 5, and selinexor PO on days 2, 4, 9, and 11. Treatment repeats every 28 days for up to 4 courses in the absence of disease progression or unacceptable toxicity. MAINTENANCE CHEMOTHERAPY: Patients achieving at least stable disease after consolidation chemotherapy may receive selinexor PO on days 1, 8, 15, and 22 at the discretion of principal investigator.

Drug: CytarabineDrug: Mitoxantrone HydrochlorideDrug: Selinexor

Interventions

Given per standard of care

Also known as: Ara-C
selinexor, cytarabine, and mitoxantrone

Given per standard of care

Also known as: Mitroxone
selinexor, cytarabine, and mitoxantrone

Given PO

Also known as: KPT-330
selinexor, cytarabine, and mitoxantrone

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Signed, written informed consent in accordance with federal, local, and institutional guidelines
  • Patients with newly diagnosed or relapsed/refractory AML, except acute promyelocytic leukemia (APL), requiring intensive induction chemotherapy
  • Eastern Cooperative Oncology Group (ECOG) performance status of =\< 2
  • Creatinine clearance \> 30 cc/min calculated using the Cockcroft and Gault (1976) formula or measured
  • Total bilirubin =\< 2 mg/dl unless high indirect bilirubin is due to a congenital disorder
  • Transaminases (aspartate aminotransferase \[AST\] or alanine aminotransferase \[ALT\]) =\< 3.0 x upper limit of normal (ULN) unless due to leukemia infiltration
  • Prothrombin time (PT) and partial thromboplastin time (PTT) =\< 2 x ULN
  • Willingness and ability to comply with scheduled visits, treatment plans, laboratory tests and other study procedures
  • It is important patients understand the need to use birth control while on this study; female patients of child-bearing potential must agree to use dual methods of contraception and have a negative serum pregnancy test at screening (\< 3 days prior to first dose), male patients with partners of childbearing potential must agree to use effective contraception during the study period and a period of 3 months after the last dose of study drug; for both male and female patients, effective methods of contraception must be used throughout the study and for three months following the last dose

You may not qualify if:

  • Treatment with any investigational agent within two weeks prior to first dose in this study; hydroxyurea is allowed to control the AML prior to treatment on the study
  • AML central nervous system (CNS) involvement
  • Major surgery within 2 weeks of first dose of study drug; patients must have recovered from the effects of any surgery performed greater than 2 weeks previously
  • Patient has a concurrent advantage active malignancy under treatment
  • Unstable cardiovascular function:
  • Symptomatic ischemia, or
  • Uncontrolled clinically significant conduction abnormalities (i.e., ventricular tachycardia on antiarrhythmic agents are excluded; 1st degree atrioventricular \[AV\] block or asymptomatic left anterior fascicular block/right bundle branch block \[left anterior fascicular block (LAFB)/right bundle branch block (RBBB)\] will not be excluded), or
  • Congestive heart failure (CHF) New York Heart Association (NYHA) class \>= 3, or
  • Myocardial infarction (MI) within 3 months
  • Uncontrolled infection requiring parenteral antibiotics, antivirals, or antifungals within one week prior to first dose; infections controlled on concurrent anti-microbial agents are acceptable, and anti-microbial prophylaxis per institutional guidelines is acceptable
  • Known active hepatitis B virus (HBV) or C virus (HCV) infection; or known to be positive for HCV ribonucleic acid (RNA) or HBsAg (HBV surface antigen)
  • Known human immunodeficiency virus (HIV) infection
  • Any medical condition which, in the investigator's opinion, could compromise the patient's safety
  • Patients unable to swallow tablets or patients with malabsorption syndrome, or any other disease significantly affecting gastrointestinal function
  • Seizure or cerebrovascular accident (CVA) in the last year

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

University of Chicago Comprehensive Cancer Center

Chicago, Illinois, 60637, United States

Location

Related Publications (1)

  • Wang AY, Weiner H, Green M, Chang H, Fulton N, Larson RA, Odenike O, Artz AS, Bishop MR, Godley LA, Thirman MJ, Kosuri S, Churpek JE, Curran E, Pettit K, Stock W, Liu H. A phase I study of selinexor in combination with high-dose cytarabine and mitoxantrone for remission induction in patients with acute myeloid leukemia. J Hematol Oncol. 2018 Jan 5;11(1):4. doi: 10.1186/s13045-017-0550-8.

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

CytarabineMitoxantroneselinexor

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

CytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsArabinonucleosidesNucleosidesNucleic Acids, Nucleotides, and NucleosidesAnthraquinonesAnthronesAnthracenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsQuinonesPolycyclic Compounds

Study Officials

  • Hongtao Liu

    University of Chicago Comprehensive Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 5, 2015

First Posted

October 9, 2015

Study Start

October 7, 2015

Primary Completion

January 1, 2018

Study Completion

May 3, 2019

Last Updated

April 8, 2020

Record last verified: 2020-04

Locations