NCT02477839

Brief Summary

The purpose of this trial is to assess the efficacy, safety and tolerability of lacosamide administered as add-on therapy with 1 to 3 anti-seizure medications. This trial is for children aged 1 month to less than 4 years with epilepsy who currently have uncontrolled partial-onset seizures.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
255

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jun 2015

Longer than P75 for phase_3

Geographic Reach
26 countries

88 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 13, 2015

Completed
23 days until next milestone

Study Start

First participant enrolled

June 5, 2015

Completed
18 days until next milestone

First Posted

Study publicly available on registry

June 23, 2015

Completed
4.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 28, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 28, 2020

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

July 1, 2021

Completed
Last Updated

July 1, 2021

Status Verified

June 1, 2021

Enrollment Period

5 years

First QC Date

May 13, 2015

Results QC Date

May 27, 2021

Last Update Submit

June 30, 2021

Conditions

Keywords

Epilepsychildrenpartial-onset seizureslacosamideLCMpediatric

Outcome Measures

Primary Outcomes (3)

  • Change in Average Daily Frequency (ADF) of Electrographic Partial-onset Seizures From End-of-Baseline (EOB) Period Video-EEG to End-of-Maintenance (EOM) Period Video-EEG

    The change in ADF of electrographic partial-onset seizures as measured on the End-of-Maintenance Period video-electroencephalogram (EEG) compared to the End-of-Baseline Period video-EEG. Seizure frequency was analyzed using an analysis of covariance (ANCOVA) with terms for treatment, pooled randomized age stratum, pooled center, and Baseline seizure ADF. Seizure ADF was log transformed using the transformation of ln(X+1), where X is the seizure ADF. Baseline seizure ADF was log transformed. Least squares means were based on log-transformed data of the full ANCOVA model.

    End-of-Baseline Period (Day -3 to Day 1) to End-of-Maintenance Period (Day 24 to Day 27)

  • Participant Withdrawals Due to Adverse Events (AEs) During the Study

    An adverse event (AE) is any untoward medical occurrence in a patient or clinical study participant, temporally associated with the use of study medication, whether or not considered related to the study medication. An AE could, therefore, be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of study medication.

    From the Baseline Period (Day -7) to the End of Study Visit (up to 93 days)

  • Percentage of Participants With Adverse Events Reported Spontaneously by the Participant's Parent(s) and/or Legal Representative(s)/Caregiver(s) (in Accordance With Local Regulation) or Observed by the Investigator

    An adverse event (AE) is any untoward medical occurrence in a patient or clinical study participant, temporally associated with the use of study medication, whether or not considered related to the study medication. An AE could, therefore, be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of study medication.

    From the Baseline Period (Day -7) to the End of Study Visit (up to 93 days)

Secondary Outcomes (9)

  • Absolute Change in Average Daily Frequency (ADF) of Electrographic Partial-onset Seizures From End-of-Baseline (EOB) Period Video-EEG to End-of-Maintenance (EOM) Period Video-EEG

    End-of-Baseline Period (Day -3 to Day 1) to End-of-Maintenance Period (Day 24 to Day 27)

  • Percent Change in Average Daily Frequency (ADF) of Electrographic Partial-onset Seizures From End-of-Baseline (EOB) Period Video-EEG to End-of-Maintenance (EOM) Period Video-EEG

    End-of-Baseline Period (Day -3 to Day 1) to End-of-Maintenance Period (Day 24 to Day 27)

  • Percentage of Participants Who Achieved 'Seizure-free' Status From All Seizure Types During the End-of-Maintenance (EOM) Period Video-EEG

    During the End-of-Maintenance Period (Day 24 to Day 27)

  • Percentage of Participants Who Achieved 'Seizure-free' Status From Partial-onset Seizure Types Only During the End-of-Maintenance (EOM) Period Video-EEG

    During the End-of-Maintenance Period (Day 24 to Day 27)

  • Percentage of Participants Experiencing a >=25% to <50% Reduction in Average Daily Frequency (ADF) of Electrographic Partial-onset Seizures From End-of-Baseline (EOB) Period Video-EEG to End-of-Maintenance (EOM) Period Video-EEG

    End-of-Baseline Period (Day -3 to Day 1) to End-of-Maintenance Period (Day 24 to Day 27)

  • +4 more secondary outcomes

Study Arms (2)

Lacosamide

EXPERIMENTAL

Lacosamide syrup 8 mg/kg/day to 12 mg/kg/day

Drug: Lacosamide

Placebo

PLACEBO COMPARATOR

Matching placebo syrup

Other: Placebo

Interventions

Active Substance: Lacosamide Pharmaceutical Form: Syrup Concentration: 10 mg/mL Route of Administration: oral

Also known as: Vimpat, UCB Code: SPM 927, Abbreviated name: LCM
Lacosamide
PlaceboOTHER

Active Substance: Placebo Pharmaceutical Form: Syrup Concentration: N/A Route of Administration: oral

Also known as: PBO
Placebo

Eligibility Criteria

Age1 Month - 47 Months
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Subject is male or female from \>=1 month (ie, 4 weeks after full term \[37 weeks gestational age\]) to \<4 years of age
  • Subject has a diagnosis of epilepsy with partial-onset seizures. The results of \>=1 prior EEG and \>=1 magnetic resonance imaging/computerized tomography scan should be consistent with this diagnosis
  • Subject weighs \>=4 kg to \<30 kg at Visit 1
  • Subject has experienced \>=2 partial-onset seizures with or without secondary generalization during each consecutive 7-day period during the 2 weeks prior to Visit 1
  • Subject has \>=2 partial-onset seizures with or without secondary generalization during the End-of-Baseline video-EEG. Electrographic seizures are defined as recognizable ictal patterns on an EEG involving \>=2 contiguous electrodes. The seizures are initiated as a unilateral or strongly asymmetric abnormal epileptiform discharge lasting a total of \>10 seconds
  • Subject is on a stable (concurrently or sequentially) dosage regimen of 1 to 3 AEDs. The dosage regimen of concomitant AED therapy must be kept constant for a period of \>=2 weeks prior to Visit 1. A stable daily dosage regimen of a concomitant benzodiazepine (BZD) will be considered as a concomitant AED
  • Vagus nerve stimulation (VNS) is allowed and will not be counted as a concomitant AED. The VNS device must have been implanted for \>=6 months prior to Visit 1; device settings must be kept stable for \>=2 weeks prior to Visit 1 and kept stable during the Baseline, Treatment, and Transition Periods. Use of the VNS device magnet is allowed
  • Subject is an acceptable candidate for venipuncture

You may not qualify if:

  • Subject is on a ketogenic diet that has either changed within the 4 weeks prior to Visit 1 or is expected to change during the study
  • Subject has creatinine clearance \<30 mL/minute
  • Subject has a clinically relevant ECG abnormality, in the opinion of the investigator (eg, second or third degree heart block at rest or a corrected QT interval \[QTc\] \>=450 ms)
  • Subject has a hemodynamically significant congenital heart disease
  • Subject has an arrhythmic heart condition requiring medical therapy
  • Subject has a known history of severe anaphylactic reaction secondary to medication intake or serious blood dyscrasias
  • Subject has a current diagnosis of Lennox-Gastaut syndrome, epilepsia partialis continua, primary generalized epilepsy, Dravet Syndrome, or seizures that are not of partial-onset origin
  • Subject has a history of generalized convulsive status epilepticus \<=2 months prior to Screening (Visit 1)
  • Subject has been treated with felbamate and has experienced any serious toxicity issues (defined as liver failure, aplastic anemia) with this treatment. Subjects treated with felbamate for \<12 months are excluded. Subjects treated with felbamate for \>=12 months prior to Visit 1 and who have not experienced serious toxicity issues are eligible
  • Subject has an acute or subacutely progressive central nervous system disease. Subject has epilepsy secondary to a progressing cerebral disease or any other progressively neurodegenerative disease (malignant brain tumor or Rasmussen Syndrome)
  • Subject has a known cardiac sodium channelopathy, such as Brugada syndrome

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (88)

Sp0967 638

Birmingham, Alabama, 35233, United States

Location

Sp0967 117

Tampa, Florida, 33609, United States

Location

Sp0967 115

Henderson, Nevada, 89052, United States

Location

Sp0967 120

Lebanon, New Hampshire, 03756, United States

Location

Sp0967 129

Dallas, Texas, 75235, United States

Location

Sp0967 630

San Antonio, Texas, 78207, United States

Location

Sp0967 643

San Antonio, Texas, 78249, United States

Location

Sp0967 142

Córdoba, Argentina

Location

Sp0967 158

Passo Fundo, Brazil

Location

Sp0967 152

Porto Alegre, Brazil

Location

Sp0967 150

São Paulo, Brazil

Location

Sp0967 154

São Paulo, Brazil

Location

Sp0967 310

Plovdiv, Bulgaria

Location

Sp0967 530

Beijing, China

Location

Sp0967 535

Changchun, China

Location

Sp0967 532

Chongqing, China

Location

Sp0967 536

Nanchang, China

Location

Sp0967 531

Shanghai, China

Location

Sp0967 537

Shenzhen, China

Location

Sp0967 613

Osijek, Croatia

Location

Sp0967 610

Rijeka, Croatia

Location

Sp0967 612

Zagreb, Croatia

Location

Sp0967 320

Ostrava-Poruba, Czechia

Location

Sp0967 349

Marseille, France

Location

Sp0967 346

Rennes, France

Location

Sp0967 344

Strasbourg, France

Location

Sp0967 620

Tbilisi, Georgia

Location

Sp0967 621

Tbilisi, Georgia

Location

Sp0967 622

Tbilisi, Georgia

Location

Sp0967 623

Tbilisi, Georgia

Location

Sp0967 542

Athens, Greece

Location

Sp0967 361

Budapest, Hungary

Location

Sp0967 362

Budapest, Hungary

Location

Sp0967 363

Budapest, Hungary

Location

Sp0967 364

Budapest, Hungary

Location

Sp0967 368

Budapest, Hungary

Location

Sp0967 374

Petah Tikva, Israel

Location

Sp0967 397

Genova, Italy

Location

Sp0967 398

Messina, Italy

Location

Sp0967 381

Milan, Italy

Location

Sp0967 700

Napoli, Italy

Location

Sp0967 383

Roma, Italy

Location

Sp0967 395

Roma, Italy

Location

Sp0967 694

Aguascalientes, Mexico

Location

Sp0967 561

Chihuahua City, Mexico

Location

Sp0967 569

Culiacán, Mexico

Location

Sp0967 693

Culiacán, Mexico

Location

Sp0967 563

Guadalajara, Mexico

Location

Sp0967 564

México, Mexico

Location

Sp0967 568

Monterrey, Mexico

Location

Sp0967 692

Monterrey, Mexico

Location

Sp0967 650

Chisinau, Moldova

Location

Sp0967 720

Cebu, Philippines

Location

Sp0967 724

Cebu, Philippines

Location

Sp0967 721

Manila, Philippines

Location

Sp0967 723

Manila, Philippines

Location

Sp0967 727

Quezon City, Philippines

Location

Sp0967 422

Krakow, Poland

Location

Sp0967 750

Lisbon, Portugal

Location

Sp0967 581

Bucharest, Romania

Location

Sp0967 582

Iași, Romania

Location

Sp0967 573

Sibiu, Romania

Location

Sp0967 577

Timișoara, Romania

Location

Sp0967 454

Kemerovo, Russia

Location

Sp0967 456

Nizhny Novgorod, Russia

Location

Sp0967 452

Novosibirsk, Russia

Location

Sp0967 453

Omsk, Russia

Location

Sp0967 455

Perm, Russia

Location

Sp0967 730

Smolensk, Russia

Location

Sp0967 458

Tomsk, Russia

Location

Sp0967 459

Ulyanovsk, Russia

Location

Sp0967 450

Yekaterinburg, Russia

Location

Sp0967 461

Belgrade, Serbia

Location

Sp0967 464

Belgrade, Serbia

Location

Sp0967 463

Novi Sad, Serbia

Location

Sp0967 474

Bratislava, Slovakia

Location

Sp0967 212

Seoul, South Korea

Location

Sp0967 215

Seoul, South Korea

Location

Sp0967 224

Taipei, Taiwan

Location

Sp0967 237

Bangkok, Thailand

Location

Sp0967 235

Pathum Wan, Thailand

Location

Sp0967 602

Dnipro, Ukraine

Location

Sp0967 609

Dnipro, Ukraine

Location

Sp0967 681

Ivano-Frankivsk, Ukraine

Location

Sp0967 600

Kiev, Ukraine

Location

Sp0967 606

Kiev, Ukraine

Location

Sp0967 682

Uzhhorod, Ukraine

Location

Sp0967 603

Vinnytsia, Ukraine

Location

MeSH Terms

Conditions

Epilepsy

Interventions

Lacosamide

Condition Hierarchy (Ancestors)

Brain DiseasesCentral Nervous System DiseasesNervous System Diseases

Intervention Hierarchy (Ancestors)

AcetamidesAmidesOrganic ChemicalsAcetatesAcids, AcyclicCarboxylic Acids

Results Point of Contact

Title
UCB
Organization
Cares

Study Officials

  • UCB Cares

    +1 877 822 9493 (UCB)

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

May 13, 2015

First Posted

June 23, 2015

Study Start

June 5, 2015

Primary Completion

May 28, 2020

Study Completion

May 28, 2020

Last Updated

July 1, 2021

Results First Posted

July 1, 2021

Record last verified: 2021-06

Locations