NCT02433158

Brief Summary

This is an open label extension study in subjects with Sickle Cell Disease (SCD) who have completed the double blind Phase 3 study (B5201002).

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
154

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Dec 2015

Typical duration for phase_3

Geographic Reach
2 countries

97 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 29, 2015

Completed
5 days until next milestone

First Posted

Study publicly available on registry

May 4, 2015

Completed
8 months until next milestone

Study Start

First participant enrolled

December 16, 2015

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 15, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 15, 2019

Completed
Last Updated

February 10, 2021

Status Verified

February 1, 2021

Enrollment Period

3.9 years

First QC Date

April 29, 2015

Last Update Submit

February 8, 2021

Conditions

Keywords

RivipanselGMI-1070Selectin InhibitorSCDVOC

Outcome Measures

Primary Outcomes (4)

  • Number (%) of subjects with treatment emergent adverse events (TEAEs) over the study.

    Number (%) of subjects with treatment emergent adverse events (TEAEs) over the study, number of TEAEs over the study and rate of TEAEs per subject per Vaso-Occlusive Crisis (VOC) will be summarized overall, by system organ class and by preferred term.

    18 months

  • Number (%) of subjects with adjudicated Acute Chest Syndrome (ACS) over the study.

    Number (%) of subjects with adjudicated Acute Chest Syndrome (ACS) over the study, number of events of adjudicated ACS and the rates of these events per subject per Vaso-Occlusive Crisis (VOC) will be summarized.

    18 months

  • Number (%) of subjects with adjudicated severe and/or generalized cutaneous manifestations over the study

    Number (%) of subjects with adjudicated severe and/or generalized cutaneous manifestations over the study, number of events of adjudicated severe and/or generalized cutaneous manifestations and the rates of these events per subject per Vaso-Occlusive Crisis (VOC) will be summarized.

    18 months

  • Number (%) of subjects with serious adverse events (SAEs) over the study.

    Number (%) of subjects with serious adverse events (SAEs) over the study, number of SAEs over the study and rate of SAEs per subject per VOC will be summarized overall, by system organ class and by preferred term.

    18 months

Secondary Outcomes (1)

  • Subject re hospitalization

    18 months

Study Arms (2)

Cohort 1

EXPERIMENTAL

Includes one adult stratum (\>18 years old) and one pediatric stratum (12-17 years old). Subjects aged 12 and over who weigh \>40 kg, will receive a loading dose of 1680 mg followed by a maintenance dose of 840 mg.

Drug: Rivipansel

Cohort 2

EXPERIMENTAL

Includes one pediatric stratum (6-11 years old). Subjects 6 to 11 years of age or subjects who weigh 40 kg, will receive a loading dose of 40 mg/kg (maximum of 1680 mg) followed by a maintenance dose of 20 mg/kg (maximum of 840 mg).

Drug: Rivipansel

Interventions

Rivipansel will be infused intravenously every 12 hours up to a maximum of 15 doses.

Also known as: GMI-1070
Cohort 1Cohort 2

Eligibility Criteria

Age6 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Completion of Study B5201002.
  • Documented diagnosis of SCD.
  • At least 6 years of age.
  • Male and female subjects of childbearing potential and at risk for pregnancy must agree to use a highly effective method of contraception throughout the study.
  • Diagnosis of VOC necessitating IV opioids and admission to the hospital.
  • Able to receive the first dose of rivipansel within 24 hours from administration of the first dose of IV opioids for this hospitalization.

You may not qualify if:

  • Non-compliance with study procedures in the double blind study (B5201002).
  • Occurrence of any severe and/or generalized cutaneous manifestation or any other adverse event during participation in Study B5201002 that was related to study drug and which would therefore make it inappropriate for the subject to receive rivipansel in the current study.
  • Other severe acute or chronic medical or psychiatric condition or laboratory abnormality that may increase the risk associated with study participation or study drug administration or may interfere with the interpretation of study results.
  • Clinically significant deterioration in renal function in Study B5201002.
  • Pregnant female subjects, breastfeeding female subjects and male and female subjects of childbearing potential who are unwilling or unable to use a highly effective method of contraception.
  • Active use of illicit drugs and/or alcohol dependence.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (97)

University of South Alabama Women's and Children's Hospital

Mobile, Alabama, 36604, United States

Location

Arkansas Children's Hospital Research Pharmacy

Little Rock, Arkansas, 72202, United States

Location

Arkansas Children's Hospital

Little Rock, Arkansas, 72202, United States

Location

UC Davis Medical Center Main Hospital

Sacramento, California, 95817, United States

Location

University of California Davis Medical Center

Sacramento, California, 95817, United States

Location

Howard University Center for Sickle Cell disease

Washington D.C., District of Columbia, 20001, United States

Location

MedStar Health Research Institute

Washington D.C., District of Columbia, 20010, United States

Location

Howard University Hospital

Washington D.C., District of Columbia, 20060, United States

Location

Golisano Childrens Hospital of Southwest Florida

Fort Myers, Florida, 33908, United States

Location

Jackson Memorial Hospital

Miami, Florida, 33136, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

St. Mary's Medical Center

West Palm Beach, Florida, 33407, United States

Location

Children's Healthcare of Atlanta Aflac Cancer and Blood Disorders Center:

Atlanta, Georgia, 30303, United States

Location

Grady Health System

Atlanta, Georgia, 30303, United States

Location

Children's Healthcare of Atlanta Aflac Cancer and Blood Disorders Center:

Atlanta, Georgia, 30322, United States

Location

Emory Children's Center

Atlanta, Georgia, 30322, United States

Location

Children's Healthcare of Atlanta Aflac Cancer and Blood Disorders Center/

Atlanta, Georgia, 30342, United States

Location

Children's Healthcare of Atlanta: Scottish Rite Campus

Atlanta, Georgia, 30342, United States

Location

Memorial Family Medicine Center

Savannah, Georgia, 31404, United States

Location

Memorial Health University Medical Center

Savannah, Georgia, 31404, United States

Location

The University of Chicago/Comer Children's Hospital

Chicago, Illinois, 60637, United States

Location

University of Chicago, Investigational Drug Service Pharmacy

Chicago, Illinois, 60637, United States

Location

University of Maryland Medical System Investigational Pharmacy

Baltimore, Maryland, 21201, United States

Location

University of Maryland Medical System

Baltimore, Maryland, 21201, United States

Location

Johns Hopkins Department of Medicine Clinical Trials Unit

Baltimore, Maryland, 21205, United States

Location

The Johns Hopkins University School of Medicine

Baltimore, Maryland, 21205, United States

Location

The Johns Hopkins Hospital Department of Pharmacy Services

Baltimore, Maryland, 21287-6180, United States

Location

Johns Hopkins Medicine

Baltimore, Maryland, 21287, United States

Location

Boston Children's Hospital

Boston, Massachusetts, 02115, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Center for Clinical Investigation, Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Investigational Drug Services

Boston, Massachusetts, 02115, United States

Location

Children's Hospital of Michigan

Detroit, Michigan, 48201, United States

Location

University of Mississippi Medical Center - Outpatient Clinical Research Unit

Jackson, Mississippi, 39216, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Center for Outpatient Health

St Louis, Missouri, 63108, United States

Location

Barnes-Jewish Hospital Department of Pharmacy

St Louis, Missouri, 63110, United States

Location

Barnes-Jewish Hospital

St Louis, Missouri, 63110, United States

Location

Center for Advanced Medicine

St Louis, Missouri, 63110, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Bristol Myers Squibb Children's Hospital at Robert Wood Johnson University Hospital

New Brunswick, New Jersey, 08901, United States

Location

Rutgers-Robert Wood Johnson Medical School

New Brunswick, New Jersey, 08901, United States

Location

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08903, United States

Location

Kings County Hospital Center

Brooklyn, New York, 11203, United States

Location

State University of New York (SUNY) Downstate Medical Center

Brooklyn, New York, 11203, United States

Location

SUNY Downstate Medical Center University Hospital of Brooklyn

Brooklyn, New York, 11203, United States

Location

Columbia University Medical Center Research Pharmacy

New York, New York, 10032, United States

Location

MS CHONY Pediatric Emergency Department

New York, New York, 10032, United States

Location

MS CHONY Pediatric Hematology/Oncology Unit

New York, New York, 10032, United States

Location

Jacobi Medical Center

The Bronx, New York, 10461, United States

Location

Duke University Hospital, Investigational Drug Service

Durham, North Carolina, 27710, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

East Carolina University Brody School of Medicine

Greenville, North Carolina, 27834, United States

Location

East Carolina University, Brody School of Medicine

Greenville, North Carolina, 27834, United States

Location

Leo W. Jenkins Cancer Center

Greenville, North Carolina, 27834, United States

Location

Vidant Medical Center

Greenville, North Carolina, 27834, United States

Location

University of Cincinnati - Hoxworth Building

Cincinnati, Ohio, 45219, United States

Location

University of Cincinnati Medical Center / Investigational Pharmacy

Cincinnati, Ohio, 45219, United States

Location

University of Cincinnati Medical Center / Research Office

Cincinnati, Ohio, 45219, United States

Location

University of Cincinnati Medical Center

Cincinnati, Ohio, 45219, United States

Location

University of Cincinnati Physicians Company LLC

Cincinnati, Ohio, 45219, United States

Location

UC Health Ridgeway Hospital

Cincinnati, Ohio, 45229, United States

Location

The Ohio State University Investigational Drug Services

Columbus, Ohio, 43203, United States

Location

The Ohio State University Wexner Center East

Columbus, Ohio, 43203, United States

Location

The Ohio State University James Comprehensive Cancer Hospital & Solove Research Institute

Columbus, Ohio, 43210, United States

Location

The Ohio State University Wexner Medical Center

Columbus, Ohio, 43210, United States

Location

UPMC Presbyterian

Pittsburgh, Pennsylvania, 15213, United States

Location

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

Hasbro Children's Hospital

Providence, Rhode Island, 02903, United States

Location

Rhode Island Hospital-Pharmacy Service

Providence, Rhode Island, 02903, United States

Location

Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

The Miriam Hospital

Providence, Rhode Island, 02906, United States

Location

Medical University of South Carolina Lifespan Comprehensive Sickle Cell Center

Charleston, South Carolina, 29425, United States

Location

Medical University of South Carolina-Hospital

Charleston, South Carolina, 29425, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

MUSC Investigational Drug Services

Charleston, South Carolina, 29425, United States

Location

Cook Children's Hematology and Oncology Center

Fort Worth, Texas, 76104, United States

Location

Cook Children's Medical Center

Fort Worth, Texas, 76104, United States

Location

Cook Children's Hematology and Oncology Center-Grapevine

Grapevine, Texas, 76051, United States

Location

University of Texas Medical School

Houston, Texas, 77030, United States

Location

Primary Children's Hospital Laboratory

Salt Lake City, Utah, 84113, United States

Location

Primary Children's Hospital

Salt Lake City, Utah, 84113, United States

Location

Main Hospital-VCU

Richmond, Virginia, 23298, United States

Location

Virginia Commonwealth University - Investigational Drug Services

Richmond, Virginia, 23298, United States

Location

Virginia Commonwealth University- Clinical Research Services Unit

Richmond, Virginia, 23298, United States

Location

Royal Alexandra Hospital

Edmonton, Alberta, T5H 3V9, Canada

Location

Miseracordia Community Hospital

Edmonton, Alberta, T5R 4H5, Canada

Location

Kaye Edmonton Clinic 3C

Edmonton, Alberta, T6G 1Z1, Canada

Location

University of Alberta Hospital, Pharmacy Services

Edmonton, Alberta, T6G 1Z1, Canada

Location

Stollery Children's Hospital

Edmonton, Alberta, T6G 2B7, Canada

Location

University of Alberta Hospital

Edmonton, Alberta, T6G 2B7, Canada

Location

Research transition Facility

Edmonton, Alberta, T6G 2V2, Canada

Location

Grey Nuns Community Hospital

Edmonton, Alberta, T6L 5X8, Canada

Location

Children's Hospital of Eastern Ontario

Ottawa, Ontario, K1H 8L1, Canada

Location

The Hospital for Sick Children

Toronto, Ontario, M5G 1X8, Canada

Location

Centre Hospitalier Universitaire Sainte-Justine

Montreal, Quebec, H3T 1C5, Canada

Location

The Montreal Children's Hospital / McGill University Health Centre

Montreal, Quebec, H4A3J1, Canada

Location

Related Publications (1)

  • Dampier CD, Telen MJ, Wun T, Brown RC, Desai P, El Rassi F, Fuh B, Kanter J, Pastore Y, Rothman J, Taylor JG, Readett D, Sivamurthy KM, Tammara B, Tseng LJ, Lozier JN, Thackray H, Magnani JL, Hassell KL; RESET Investigators. A randomized clinical trial of the efficacy and safety of rivipansel for sickle cell vaso-occlusive crisis. Blood. 2023 Jan 12;141(2):168-179. doi: 10.1182/blood.2022015797.

MeSH Terms

Conditions

Anemia, Sickle CellVaso-Occlusive Crises

Interventions

rivipansel

Condition Hierarchy (Ancestors)

Anemia, Hemolytic, CongenitalAnemia, HemolyticAnemiaHematologic DiseasesHemic and Lymphatic DiseasesHemoglobinopathiesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 29, 2015

First Posted

May 4, 2015

Study Start

December 16, 2015

Primary Completion

November 15, 2019

Study Completion

November 15, 2019

Last Updated

February 10, 2021

Record last verified: 2021-02

Data Sharing

IPD Sharing
Will not share

Locations