NCT02412878

Brief Summary

The purpose of the study is to compare the progression-free survival (PFS) of once-weekly carfilzomib dosing in combination with dexamethasone to twice-weekly carfilzomib dosing in combination with dexamethasone in adults with relapsed and refractory multiple myeloma, previously treated with bortezomib and an immunomodulatory agent (IMiD).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
478

participants targeted

Target at P50-P75 for phase_3 multiple-myeloma

Timeline
Completed

Started Sep 2015

Shorter than P25 for phase_3 multiple-myeloma

Geographic Reach
20 countries

140 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 6, 2015

Completed
3 days until next milestone

First Posted

Study publicly available on registry

April 9, 2015

Completed
5 months until next milestone

Study Start

First participant enrolled

September 9, 2015

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 15, 2017

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

December 13, 2018

Completed
25 days until next milestone

Study Completion

Last participant's last visit for all outcomes

January 7, 2019

Completed
Last Updated

September 23, 2022

Status Verified

September 1, 2022

Enrollment Period

1.8 years

First QC Date

April 6, 2015

Results QC Date

October 24, 2018

Last Update Submit

September 9, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival

    Progression-free survival (PFS) was defined as the time from randomization to the earlier of disease progression or death due to any cause. Disease status was assessed at a central laboratory with serum and urine protein electrophoresis, immunofixation, serum-free light chain (SFLC) assay, bone marrow sample evaluation, serum calcium, plasmacytoma evaluation, and skeletal survey. Response and disease progression were determined using a validated computer algorithm based on the International Myeloma Working Group-Uniform Response Criteria (IMWG-URC). Median PFS was derived using the Kaplan-Meier method; participants still alive with no disease progression were censored at the time of their last disease assessment.

    From randomization until the data cut-off date of 15 June 2017; median (minimum, maximum) follow-up time for PFS was 12.0 (0, 20) and 12.6 (0, 19) months in each treatment group respectively.

Secondary Outcomes (4)

  • Overall Response Rate

    Disease response was assessed every 28 days until progressive disease, up to the data cut-off date of 15 June 2017; median time on follow-up was 12.0 and 12.6 months in each treatment group respectively.

  • Overall Survival

    From randomization until the data cut-off date of 15 June 2017; median (minimum, maximum) follow-up time for OS was 12.6 (0, 20) and 13.2 (0, 19) months in each treatment group respectively.

  • Number of Participants With Adverse Events (AEs)

    From first dose of study drug up to 30 days after last dose, up to the end of study; median (minimum, maximum) duration of treatment was 29.1 (0.1, 156.3) weeks and 38.0 (0.1, 158.3) weeks in each treatment group respectively.

  • Plasma Carfilzomib Concentration During Cycle 2

    Cycle 2 day 1 predose, 15 minutes after the start of infusion (once-weekly carfilzomib only), end of infusion, and 30 minutes after the end of infusion

Study Arms (2)

Once-weekly Carfilzomib 20/70 mg/m² + Dexamethasone

EXPERIMENTAL

Participants received carfilzomib administered by intravenous (IV) infusion on days 1, 8, and 15 of each 28-day cycle (20 mg/m² on day 1 of cycle 1 and 70 mg/m² thereafter). Participants also received 40 mg dexamethasone IV or orally on days 1, 8, 15 and 22 for the first 8 cycles; starting with cycle 9, dexamethasone was administered only on days 1, 8, and 15.

Drug: CarfilzomibDrug: Dexamethasone

Twice-weekly Carfilzomib 20/27 mg/m² + Dexamethasone

EXPERIMENTAL

Participants received carfilzomib administered by IV infusion on days 1, 2, 8, 9, 15, and 16 of each 28-day cycle (20 mg/m² on days 1 and 2 of cycle 1 and 27 mg/m² thereafter). Participants also received 40 mg dexamethasone IV or orally on days 1, 8, 15 and 22 for the first 8 cycles; starting with cycle 9, dexamethasone was administered only on days 1, 8, and 15.

Drug: CarfilzomibDrug: Dexamethasone

Interventions

Carfilzomib was administered as an IV infusion

Also known as: PR-171, PR171, Kyprolis® (carfilzomib) for Injection
Once-weekly Carfilzomib 20/70 mg/m² + DexamethasoneTwice-weekly Carfilzomib 20/27 mg/m² + Dexamethasone

Commercially available dexamethasone was obtained by the investigational site.

Once-weekly Carfilzomib 20/70 mg/m² + DexamethasoneTwice-weekly Carfilzomib 20/27 mg/m² + Dexamethasone

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Relapsed multiple myeloma
  • Refractory multiple myeloma defined as meeting 1 or more of the following:
  • Nonresponsive to most recent therapy (stable disease only or PD while on treatment), or
  • Disease progression within 60 days of discontinuation from most recent therapy
  • At least 2 but no more than 3 prior therapies for multiple myeloma
  • Prior exposure to an immunomodulatory agent (IMiD)
  • Prior exposure to a proteasome inhibitor (PI)
  • Documented response of at least partial response (PR) to 1 line of prior therapy
  • Measurable disease with at least 1 of the following assessed within the 21 days prior to randomization:
  • Serum M-protein ≥ 0.5 g/dL
  • Urine M-protein ≥ 200 mg/24 hours
  • In subjects without detectable serum or urine M-protein, serum free light chain (SFLC) \> 100 mg/L (involved light chain) and an abnormal serum kappa lambda ratio
  • Eastern Cooperative Oncology Group Performance Status (ECOG PS) of 0 or 1
  • Left ventricular ejection fraction (LVEF) ≥ 40% within the 21 days prior to randomization
  • Adequate organ and bone marrow function within the 21 days prior to randomization defined by:
  • +6 more criteria

You may not qualify if:

  • Waldenström macroglobulinemia
  • Multiple myeloma of Immunoglobin M (IgM) subtype
  • POEMS syndrome (polyneuropathy, organomegaly, endocrinopathy, monoclonal protein, and skin changes)
  • Plasma cell leukemia (\> 2.0 × 10⁹/L circulating plasma cells by standard differential)
  • Myelodysplastic syndrome
  • Second malignancy within the past 5 years except:
  • Adequately treated basal cell or squamous cell skin cancer
  • Carcinoma in situ of the cervix
  • Prostate cancer \< Gleason score 6 with stable prostate-specific antigen (PSA) over 12 months
  • Ductal breast carcinoma in situ with full surgical resection (i.e., negative margins)
  • Treated medullary or papillary thyroid cancer
  • Similar condition with an expectation of \> 95% five-year disease-free survival
  • History of or current amyloidosis
  • Cytotoxic chemotherapy within the 28 days prior to randomization
  • Immunotherapy within the 21 days prior to randomization
  • +15 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (140)

Research Site

Scottsdale, Arizona, 85259-5499, United States

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Mayo Clinic

Scottsdale, Arizona, United States

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Bethesda, Maryland, 20817, United States

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Center for Cancer and Blood Disorders

Bethesda, Maryland, United States

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Rockville, Maryland, 20850, United States

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Maryland Oncology Hematology, P.A

Rockville, Maryland, United States

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Hackensack, New Jersey, 07601, United States

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John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, United States

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New York, New York, 10021, United States

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Pittsburgh, Pennsylvania, 15224, United States

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Tyler, Texas, 75701, United States

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Blood and Cancer Center of East Texas

Tyler, Texas, United States

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Darlinghurst, New South Wales, 2010, Australia

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Tweed Heads, New South Wales, 2485, Australia

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Waratah, New South Wales, 2298, Australia

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Box Hill, Victoria, 3128, Australia

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Antwerp, 2060, Belgium

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Bruges, 8000, Belgium

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Brussels, 1090, Belgium

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Brussels, 1200, Belgium

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Ghent, 9000, Belgium

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Leuven, 3000, Belgium

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Calgary, Alberta, T2N 2T9, Canada

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Kelowna, British Columbia, V1Y 5L3, Canada

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Vancouver, British Columbia, V5Z 1M9, Canada

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St. John's, Newfoundland and Labrador, A1B 3V6, Canada

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Halifax, Nova Scotia, B3H 2Y9, Canada

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Ottawa, Ontario, K1H 8L6, Canada

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Toronto, Ontario, M5G 2M9, Canada

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Montreal, Quebec, H4J 1C5, Canada

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Québec, Quebec, G1J 1Z4, Canada

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Brno, 625 00, Czechia

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Hradec Králové, 500 05, Czechia

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Olomouc, 775 20, Czechia

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Ostrava-Poruba, 708 52, Czechia

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Prague, 100 34, Czechia

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Prague, 128 08, Czechia

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Aalborg, 9000, Denmark

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Copenhagen, 2100, Denmark

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Odense C, 5000, Denmark

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Vejle, 7100, Denmark

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Helsinki, 00290, Finland

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Tampere, 33521, Finland

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Turku, 20520, Finland

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Bayonne, 64109, France

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Brest, 29609, France

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Dijon, 21000, France

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Nantes, 44093, France

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Nîmes, 30029, France

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Paris, 75012, France

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Pierre-Bénite, 69495, France

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Rennes, 35033, France

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Tours, 37044, France

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Cologne, 50937, Germany

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Leipzig, 04103, Germany

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München, 81241, Germany

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Rostock, 18057, Germany

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Tübingen, 72076, Germany

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Athens, 10676, Greece

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Athens, 11528, Greece

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Pátrai, 26504, Greece

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Budapest, 1097, Hungary

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Debrecen, 4032, Hungary

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Gyula, 5700, Hungary

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Kaposvár, 7400, Hungary

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Ancona, 60126, Italy

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Bologna, 40138, Italy

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Brescia, 25123, Italy

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Cagliari, 09121, Italy

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Catania, 95124, Italy

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Florence, 50134, Italy

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Genova, 16132, Italy

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Napoli, 80131, Italy

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Pavia, 27100, Italy

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Piacenza, 29100, Italy

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Pisa, 56100, Italy

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Roma, 00161, Italy

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Roma, 00168, Italy

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Torino, 10126, Italy

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Toyohashi, Aichi-ken, 441-8570, Japan

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Fukuoka, Fukuoka, 812-8582, Japan

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Ogaki-shi, Gifu, 503-8502, Japan

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Maebashi, Gunma, 371-8511, Japan

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Shibukawa-shi, Gunma, 377-8511, Japan

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Sapporo, Hokkaido, 060-8543, Japan

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Isehara-shi, Kanagawa, 259-1193, Japan

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Kyoto, Kyoto, 602-8566, Japan

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Sendai, Miyagi, 980-8574, Japan

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Okayama, Okayama-ken, 701-1192, Japan

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Suita-shi, Osaka, 565-0871, Japan

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Kawagoe-shi, Saitama, 350-8550, Japan

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Utsunomiya, Tochigi, 320-0834, Japan

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Chuo-ku, Tokyo, 104-0045, Japan

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Koto-ku, Tokyo, 135-8550, Japan

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Shibuya-ku, Tokyo, 150-8935, Japan

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Tachikawa-shi, Tokyo, 190-0014, Japan

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Fukuoka, 811-1395, Japan

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Nagoya, 467-8602, Japan

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Niigata, 951-8566, Japan

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Tokushima, 770-8539, Japan

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Christchurch, 8011, New Zealand

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Otahuhu, Auckland, 1640, New Zealand

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Oslo, 0372, Norway

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Trondheim, 7006, Norway

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Brzozów, 36-200, Poland

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Chorzów, 41-500, Poland

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Katowice, 40-032, Poland

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Krakow, 31-501, Poland

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Lodz, 93-510, Poland

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Olsztyn, 10-228, Poland

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Poznan, 60-569, Poland

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Torun, 87-100, Poland

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Warsaw, 02-106, Poland

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Wroclaw, 50-367, Poland

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Brasov, 500152, Romania

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Bucharest, 022328, Romania

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Seville, Andalusia, 41013, Spain

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Zaragoza, Aragon, 50012, Spain

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Palma de Mallorca, Balearic Islands, 07010, Spain

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Salamanca, Castille and León, 37007, Spain

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Badalona, Catalonia, 08916, Spain

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Barcelona, Catalonia, 08036, Spain

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Girona, Catalonia, 17007, Spain

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Pamplona, Navarre, 31008, Spain

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Madrid, 28034, Spain

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Madrid, 28040, Spain

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Madrid, 28041, Spain

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Gothenburg, 413 45, Sweden

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Helsingborg, 251 87, Sweden

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Lund, 221 85, Sweden

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Stockholm, 141 86, Sweden

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Stockholm, 171 76, Sweden

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Uddevalla, 451 80, Sweden

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Bournemouth, BH7 7DW, United Kingdom

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London, EC1A 7BE, United Kingdom

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London, NW1 2PG, United Kingdom

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Manchester, M13 9WL, United Kingdom

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Nottingham, NG5 1PB, United Kingdom

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Sheffield, S10 2JF, United Kingdom

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Wolverhampton, WV10 0QP, United Kingdom

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Related Publications (7)

  • Moreau P, Mateos MV, Berenson JR, Weisel K, Lazzaro A, Song K, Dimopoulos MA, Huang M, Zahlten-Kumeli A, Stewart AK. Once weekly versus twice weekly carfilzomib dosing in patients with relapsed and refractory multiple myeloma (A.R.R.O.W.): interim analysis results of a randomised, phase 3 study. Lancet Oncol. 2018 Jul;19(7):953-964. doi: 10.1016/S1470-2045(18)30354-1. Epub 2018 Jun 1.

    PMID: 29866475BACKGROUND
  • Facon T, Niesvizky R, Mateos MV, Siegel D, Rosenbaum C, Bringhen S, Weisel K, Ho PJ, Ludwig H, Kumar S, Wang K, Obreja M, Yang Z, Klippel Z, Mezzi K, Goldrick A, Tekle C, Dimopoulos MA. Efficacy and safety of carfilzomib-based regimens in frail patients with relapsed and/or refractory multiple myeloma. Blood Adv. 2020 Nov 10;4(21):5449-5459. doi: 10.1182/bloodadvances.2020001965.

    PMID: 33166401BACKGROUND
  • Dimopoulos MA, Niesvizky R, Weisel K, Siegel DS, Hajek R, Mateos MV, Cavo M, Huang M, Zahlten-Kumeli A, Moreau P. Once- versus twice-weekly carfilzomib in relapsed and refractory multiple myeloma by select patient characteristics: phase 3 A.R.R.O.W. study subgroup analysis. Blood Cancer J. 2020 Mar 9;10(3):35. doi: 10.1038/s41408-020-0300-y.

    PMID: 32152297BACKGROUND
  • Moreau P, Stewart KA, Dimopoulos M, Siegel D, Facon T, Berenson J, Raje N, Berdeja JG, Orlowski RZ, Yang H, Ma H, Klippel Z, Zahlten-Kumeli A, Mezzi K, Iskander K, Mateos MV. Once-weekly (70 mg/m2 ) vs twice-weekly (56 mg/m2 ) dosing of carfilzomib in patients with relapsed or refractory multiple myeloma: A post hoc analysis of the ENDEAVOR, A.R.R.O.W., and CHAMPION-1 trials. Cancer Med. 2020 May;9(9):2989-2996. doi: 10.1002/cam4.2945. Epub 2020 Feb 28.

    PMID: 32108443BACKGROUND
  • Moreau P, Kumar S, Boccia R, Iida S, Goldschmidt H, Cocks K, Trigg A, Zahlten-Kumeli A, Yucel E, Panjabi SS, Dimopoulos M. Convenience, satisfaction, health-related quality of life of once-weekly 70 mg/m2 vs. twice-weekly 27 mg/m2 carfilzomib (randomized A.R.R.O.W. study). Leukemia. 2019 Dec;33(12):2934-2946. doi: 10.1038/s41375-019-0480-2. Epub 2019 May 15.

    PMID: 31092895BACKGROUND
  • Kumar SK, Majer I, Panjabi S, Medhekar R, Campioni M, Dimopoulos MA. Cost-effectiveness of once weekly carfilzomib 70 mg/m2 plus dexamethasone in patients with relapsed and refractory multiple myeloma in the United States. Expert Rev Hematol. 2020 Jun;13(6):687-696. doi: 10.1080/17474086.2020.1746639. Epub 2020 Apr 6.

    PMID: 32249621BACKGROUND
  • Dimopoulos MA, Moreau P, Iida S, Huang SY, Takezako N, Chng WJ, Zahlten-Kumeli A, Sersch MA, Li J, Huang M, Lee JH. Outcomes for Asian patients with multiple myeloma receiving once- or twice-weekly carfilzomib-based therapy: a subgroup analysis of the randomized phase 3 ENDEAVOR and A.R.R.O.W. Trials. Int J Hematol. 2019 Oct;110(4):466-473. doi: 10.1007/s12185-019-02704-z. Epub 2019 Aug 6.

Related Links

MeSH Terms

Conditions

Multiple Myeloma

Interventions

carfilzomibWW Domain-Containing OxidoreductaseDexamethasone

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Short Chain Dehydrogenase-ReductasesNAD (+) and NADP (+) Dependent Alcohol OxidoreductasesAlcohol OxidoreductasesOxidoreductasesEnzymesEnzymes and CoenzymesTumor Suppressor ProteinsNeoplasm ProteinsProteinsAmino Acids, Peptides, and ProteinsPregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, Fluorinated

Results Point of Contact

Title
Study Director
Organization
Amgen Inc.

Study Officials

  • MD

    Amgen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 6, 2015

First Posted

April 9, 2015

Study Start

September 9, 2015

Primary Completion

June 15, 2017

Study Completion

January 7, 2019

Last Updated

September 23, 2022

Results First Posted

December 13, 2018

Record last verified: 2022-09

Locations