NCT02354859

Brief Summary

The purpose of this study is to assess the efficacy of IV gallium to improve pulmonary function as measured by a 5% or greater relative improvement in forced expiratory volume in one second (FEV1) from baseline to Day 28. Funding Source - FDA OOPD

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
119

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Mar 2016

Geographic Reach
1 country

23 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 30, 2014

Completed
6 months until next milestone

First Posted

Study publicly available on registry

February 3, 2015

Completed
1.1 years until next milestone

Study Start

First participant enrolled

March 1, 2016

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2018

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

March 21, 2019

Completed
Last Updated

March 21, 2019

Status Verified

March 1, 2019

Enrollment Period

1.9 years

First QC Date

July 30, 2014

Results QC Date

January 28, 2019

Last Update Submit

March 20, 2019

Conditions

Keywords

Cystic FibrosisGallium NitrateIV GalliumPseudomonas aeruginosa

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With 5% or Greater Relative Change in FEV1 (Liters) From Baseline to Day 28

    Difference between treatment groups in the proportion of subjects with 5% or greater relative change in FEV1 (liters) from baseline to Day 28.

    Baseline to Day 28

Secondary Outcomes (5)

  • Incidence of Adverse Events (AEs) and Serious Adverse Events (SAEs)

    Day 1 to Day 56

  • Rate of Adverse Events (AEs) and Serious Adverse Events (SAEs)

    Day 1 to Day 56

  • Relative Change in FEV1 (Liters) From Baseline to Day 56

    Day 1 to Day 56

  • Absolute Change in P. Aeruginosa Sputum Density (log10 (CFU)) From Baseline to Day 56

    Day 1 to Day 56

  • Absolute Change in Respiratory Symptoms, as Measured by the CF Respiratory Symptoms Diary-Chronic Respiratory Infection Symptom Severity Score (CFRSD-CRISS), From Baseline to Day 56

    Day 1 to Day 56

Study Arms (2)

5 day of infusion of gallium nitrate

ACTIVE COMPARATOR

Gallium nitrate will be infused continuously over 5 days at 200 mg/m2/day. Study drug will be administered via a peripheral IV catheter, a peripherally inserted central catheter (PICC) line, midline catheter, or a chronic indwelling vascular access device () using an ambulatory infusion pump infused over 24 hours for 5 sequential days.

Drug: Gallium nitrate

5 day of infusion of normal saline

PLACEBO COMPARATOR

Placebo with be dispensed as 1,000 milliliters of 0.9% sodium chloride to match the reconstitution volume of the IV Ga

Drug: Normal Saline

Interventions

Study subjects will receive an infusion of either placebo or gallium nitrate.

Also known as: Ga, GaN3O9
5 day of infusion of gallium nitrate

Study subjects will receive an infusion of either placebo (normal saline) or gallium nitrate.

Also known as: Sodium Chloride, NS
5 day of infusion of normal saline

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Greater than or equal to 18 years of age at Screening
  • Documented chronic colonization with P. aeruginosa defined as dentification in two sputum or oropharyngeal cultures within the year prior to Day 1
  • Documentation of a CF diagnosis as evidenced by one or more clinical features consistent with the CF phenotype and one or more of the following criteria:
  • sweat chloride ≥ 60 mEq/liter by quantitative pilocarpine iontophoresis test (QPIT)
  • two well-characterized mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene
  • Abnormal nasal potential difference (NPD; change in NPD in response to a low chloride solution and isoproteronol of less than -5 mV)
  • FEV1 ≥ 25 % of predicted value at Screening
  • Able to expectorate sputum
  • Serum liver function tests ≤ 2.5 x upper limit of normal at Screening
  • Serum urea nitrogen (BUN) ≤ 1.5 x upper limit of normal at Screening
  • Serum creatinine ≤ 2.0 mg/dl and ≤ 1.5 x upper limit of normal at Screening
  • Hemoglobin ≥ 9 g/dl, platelets ≥ 100,000/mm3, and white blood cells (WBC)
  • ≥ 4,500/mm3 at Screening
  • Ionized calcium ≥ lower limit of normal at Screening
  • Written informed consent obtained from subject or subject's legal representative
  • +5 more criteria

You may not qualify if:

  • Use of inhaled antibiotics within seven days prior to Day 1
  • Unable or unwilling to withhold use of chronic inhaled antibiotics through Day 28
  • Use of intravenous, inhaled, or oral antibiotics for an acute indication within 14 days prior to Day 1
  • Use of bisphosphonates within seven days prior to Day 1
  • History of osteoporosis (defined as the most recent dexa scan with a T-score ≤ -2.5 with the dexa scan performed within the five years prior to Screening)
  • Lactating female
  • Known sensitivity to gallium

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

AL Adult Birmingham / The Children's Hospital Atlanta

Birmingham, Alabama, 35233, United States

Location

UC San Diego Medical Center

La Jolla, California, 92037, United States

Location

Denver Adult / National Jewish Health

Denver, Colorado, 80206, United States

Location

Shands Hospital

Gainesville, Florida, 32610, United States

Location

Jackson Memorial Hospital; University of Miami Hospital; University of Miami Hospital and Clinics

Miami, Florida, 33136, United States

Location

Atlanta Emory Adult / Emory University Hospital

Atlanta, Georgia, 30322, United States

Location

Chicago Northwestern Adult / Northwestern Memorial Hospital

Chicago, Illinois, 60611, United States

Location

Iowa City University of Iowa Adult / University of Iowa Hospitals & Clinics

Iowa City, Iowa, 52242, United States

Location

Lexington, KY Adult / University of Kentucky Chandler Medical Center

Lexington, Kentucky, 40506-9983, United States

Location

Portland, ME Adult

Portland, Maine, 04102, United States

Location

Baltimore Hopkins Adult / John Hopkins Hospital

Baltimore, Maryland, 21205, United States

Location

Boston CHB Adult / Boston Children's Hospital (BCH)

Boston, Massachusetts, 02115, United States

Location

Minneapolis CC and Adult / University of Minnesota Medical Center, Fairview

Minneapolis, Minnesota, 55455, United States

Location

Omaha Adult / The Nebraska Medical Center

Omaha, Nebraska, 68198-5300, United States

Location

Lebanon, NH Dartmouth-Hitchcock CC and Adult / Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

Cleveland CC and Peds, Hospital of Cleveland

Cleveland, Ohio, 44106, United States

Location

Columbus CC and Peds / Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

Location

Toledo, OH CC and Peds / The Toledo Hospital; Toledo Children's Hospital

Toledo, Ohio, 43606, United States

Location

Oklahoma City Adult / Presbyterian Hospital at OU Medical Center

Oklahoma City, Oklahoma, 73104, United States

Location

Pittsburgh Adult, Children's Hospital of Pittsburgh UPMC

Pittsburgh, Pennsylvania, 15224, United States

Location

SC CC and Adult Charleston / MUSC

Charleston, South Carolina, 29425, United States

Location

Salt Lake City Adult, Intermountain Cystic Fibrosis Center

Salt Lake City, Utah, 84132, United States

Location

Seattle UW Adult / University of Washington Medical Center

Seattle, Washington, 98195, United States

Location

MeSH Terms

Conditions

Cystic FibrosisPseudomonas Infections

Interventions

gallium nitrateSaline SolutionSodium Chloride

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, DiseasesGram-Negative Bacterial InfectionsBacterial InfectionsBacterial Infections and MycosesInfections

Intervention Hierarchy (Ancestors)

Crystalloid SolutionsIsotonic SolutionsSolutionsPharmaceutical PreparationsChloridesHydrochloric AcidChlorine CompoundsInorganic ChemicalsSodium Compounds

Results Point of Contact

Title
Christopher H. Goss, Professor of Medicine and Pediatrics
Organization
University of Washington

Study Officials

  • Christopher H Goss, MD

    University of Washington

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor, Medicine/Pulmonary & Critical Care Medicine

Study Record Dates

First Submitted

July 30, 2014

First Posted

February 3, 2015

Study Start

March 1, 2016

Primary Completion

February 1, 2018

Study Completion

February 1, 2018

Last Updated

March 21, 2019

Results First Posted

March 21, 2019

Record last verified: 2019-03

Data Sharing

IPD Sharing
Will share

Once the study is complete and the primary paper is published, de-identified data will be available from the Cystic Fibrosis Therapeutics Development Network Coordinating Center upon approval of a formal data request.

Locations