NCT02319837

Brief Summary

The purpose of this study is to assess enzalutamide plus leuprolide in patients with high-risk nonmetastatic prostate cancer progressing after radical prostatectomy or radiotherapy or both. The randomized / blinded portion of the study is now completed following primary endpoint analyses. The study remains ongoing in open label format.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,068

participants targeted

Target at P75+ for phase_3

Timeline
4mo left

Started Dec 2014

Longer than P75 for phase_3

Geographic Reach
16 countries

221 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress97%
Dec 2014Sep 2026

First Submitted

Initial submission to the registry

December 14, 2014

Completed
3 days until next milestone

Study Start

First participant enrolled

December 17, 2014

Completed
1 day until next milestone

First Posted

Study publicly available on registry

December 18, 2014

Completed
8.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 31, 2023

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

March 25, 2024

Completed
2.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 19, 2026

Expected
Last Updated

July 8, 2025

Status Verified

July 1, 2025

Enrollment Period

8.1 years

First QC Date

December 14, 2014

Results QC Date

January 31, 2024

Last Update Submit

July 3, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Metastasis-free Survival (MFS) Compared Between Enzalutamide Plus Leuprolide and Placebo Plus Leuprolide

    MFS was defined as the duration of time in months between randomization and the earliest objective evidence of radiographic progression by central imaging or death without radiographic progression, whichever occurred first. Radiographic progression for soft tissue disease was defined by Response Evaluation Criteria in Solid Tumors, version 1.1 (RECIST 1.1). Radiographic progression for bone disease was defined as the appearance of 1 or more metastatic lesions on bone scan (a bone scan assesses 5 regions of the skeleton, including skull, thorax, spine, pelvis, and extremities). Confirmation with a second imaging modality (plain film, computed tomography \[CT\], or magnetic resonance imaging \[MRI\]) was to be required when bone lesions were found in a single region on the bone scan. Appearance of metastatic lesions in 2 or more of the 5 regions on a bone scan was not to require confirmation with a second imaging modality.

    From randomization until radiographic progression or death without radiographic progression, whichever occurred first (up to Month 98 when at least 197 MFS events occurred among the 3 treatment groups)

Secondary Outcomes (22)

  • Metastasis-free Survival (MFS) Compared Between Enzalutamide Monotherapy and Placebo Plus Leuprolide

    From randomization until radiographic progression or death without radiographic progression, whichever occurred first (up to Month 98 when at least 197 MFS events occurred among the 3 treatment groups)

  • Time to Prostate-specific Antigen (PSA) Progression

    From randomization until first PSA progression (up to Month 98)

  • Time to First Use of New Antineoplastic Therapy

    From randomization until first use of new antineoplastic therapy (up to Month 98)

  • Overall Survival (OS)

    From randomization until death due to any cause (up to Month 98 when at least 197 MFS events occurred among the 3 treatment groups)

  • Time to Distant Metastasis

    From randomization until the earliest objective evidence of distant soft tissue metastases or metastatic bone disease (up to Month 98)

  • +17 more secondary outcomes

Study Arms (3)

Enzalutamide plus leuprolide

EXPERIMENTAL

Enzalutamide (160 mg) administered as four 40-mg capsules by mouth once daily in combination with leuprolide administered as as a single intramuscular or subcutaneous injection once every 12 weeks

Drug: EnzalutamideDrug: Leuprolide Open Label

Enzalutamide monotherapy

EXPERIMENTAL

Enzalutamide (160 mg) administered as four 40-mg capsules by mouth once daily

Drug: Enzalutamide

Leuprolide plus placebo

ACTIVE COMPARATOR

Enzalutamide placebo (placebo) capsules (identical in appearance to enzalutamide) administered as 4 capsules by mouth once daily in combination with leuprolide administered as a single intramuscular or subcutaneous injection once every 12 weeks. The randomized blinded portion of the study has concluded following primary endpoint analyses. In the Open Label Period the placebo is no longer applicable in this study arm, and patients continue to receive leuprolide alone.

Drug: Placebo (No longer applicable in Open Label study period)

Interventions

Also known as: MDV3100, Xtandi
Enzalutamide monotherapyEnzalutamide plus leuprolide

Sugar pill to mimic enzalutamide

Leuprolide plus placebo
Also known as: Eligard, Leuprolide Acetate, Leuprorelin, Lupron
Enzalutamide plus leuprolide

Eligibility Criteria

Age18 Years+
Sexmale(Gender-based eligibility)
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed adenocarcinoma of the prostate at initial biopsy, without neuroendocrine differentiation, signet cell, or small cell features;
  • Prostate cancer initially treated by radical prostatectomy or radiotherapy (including brachytherapy) or both, with curative intent;
  • PSA doubling time ≤ 9 months;
  • Screening PSA by the central laboratory ≥ 1 ng/mL for patients who had radical prostatectomy (with or without radiotherapy) as primary treatment for prostate cancer and at least 2 ng/mL above the nadir for patients who had radiotherapy only as primary treatment for prostate cancer;
  • Serum testosterone ≥ 150 ng/dL (5.2 nmol/L).

You may not qualify if:

  • Prior or present evidence of distant metastatic disease as assessed by radiographic imaging;
  • Prior hormonal therapy. Neoadjuvant/adjuvant therapy to treat prostate cancer ≤ 36 months in duration and ≥ 9 months before randomization, or a single dose or a short course (≤ 6 months) of hormonal therapy given for rising PSA ≥ 9 months before randomization is allowed.;
  • Prior cytotoxic chemotherapy, aminoglutethimide, ketoconazole, abiraterone acetate, or enzalutamide for prostate cancer;
  • Prior systemic biologic therapy, including immunotherapy, for prostate cancer;
  • Major surgery within 4 weeks before randomization;
  • Treatment with 5-α reductase inhibitors (finasteride, dutasteride) within 4 weeks of randomization;
  • Known or suspected brain metastasis or active leptomeningeal disease;
  • History of another invasive cancer within 3 years before screening, with the exception of fully treated cancers with a remote probability of recurrence

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (247)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

University of Alabama at Birmingham, IDS Pharmacy

Birmingham, Alabama, 35249, United States

Location

University of Alabama at Birmingham

Birmingham, Alabama, 35249, United States

Location

Alaska Urological Institute dba Alaska Clinical Research Center

Anchorage, Alaska, 99503, United States

Location

Urological Associates of Southern Arizona, PC

Tucson, Arizona, 85741, United States

Location

Tower Hematology Oncology Medical Group

Beverly Hills, California, 90211, United States

Location

Cedars-Senai OCC Pharmacy

Los Angeles, California, 90048, United States

Location

Cedars-Sinai Medical Center, Samuel Oschin Comprehensive Cancer Institute

Los Angeles, California, 90048, United States

Location

University of California, Irvine Medical Center

Orange, California, 92868, United States

Location

Sutter Medical Group, Vascular & Varicose Vein Center

Roseville, California, 95661, United States

Location

Sutter Medical Group

Roseville, California, 95661, United States

Location

UC Davis Comprehensive Cancer Center

Sacramento, California, 95817, United States

Location

University of California Davis Medical Center

Sacramento, California, 95817, United States

Location

University of California, Davis, School of Medicine

Sacramento, California, 95817, United States

Location

The Urology Center of Colorado

Denver, Colorado, 80211, United States

Location

Foothills Urology, P.C.

Golden, Colorado, 80401, United States

Location

Eastern Connecticut Hematology Oncology Associates

Norwich, Connecticut, 06360, United States

Location

Lakeland Regional Health Hollis Cancer Center

Lakeland, Florida, 33805, United States

Location

Emory University Hospital

Atlanta, Georgia, 30322, United States

Location

Winship Cancer Institute, Emory University

Atlanta, Georgia, 30322, United States

Location

Northwestern Medical Group

Chicago, Illinois, 60611, United States

Location

Northwestern Memorial Hospital

Chicago, Illinois, 60611, United States

Location

First Urology, PSC

Jeffersonville, Indiana, 47130, United States

Location

The University of Kansas Hospital

Kansas City, Kansas, 66160, United States

Location

Kansas City Urology Care, PA

Overland Park, Kansas, 66211, United States

Location

The University of Kansas Cancer Center and Medical Pavilion

Westwood, Kansas, 66205, United States

Location

GU Research Network/Wichita Urology Group

Wichita, Kansas, 67226, United States

Location

John Hopkins University Hospital

Baltimore, Maryland, 21287, United States

Location

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

Baltimore, Maryland, 21287, United States

Location

The Sidney Kimmel Cancer Center at Johns Hopkins Hospital- Oncology Investigational Drug Services

Baltimore, Maryland, 21287, United States

Location

Chesapeake Urology Research Associates

Towson, Maryland, 21204, United States

Location

Comprehensive Urology - Macomb Office

Macomb, Michigan, 48044, United States

Location

Comprehensive Urology - Royal Oak (Stephenson) office

Royal Oak, Michigan, 48067, United States

Location

GU Research Network, LLC / Urology Cancer Center

Omaha, Nebraska, 68130, United States

Location

VA Lahontan Valley Outpatient Clinic

Fallon, Nevada, 89406, United States

Location

Memorial Sloan Kettering Cancer Center Basking Ridge

Basking Ridge, New Jersey, 07920, United States

Location

Memorial Sloan Kettering Cancer Center Commack

Commack, New York, 11725, United States

Location

Memorial Sloan Kettering Cancer Center Westchester

Harrison, New York, 10604, United States

Location

Memorial Hospital

New York, New York, 10065, United States

Location

Sidney Kimmel Center for Prostate and Urologic Cancers

New York, New York, 10065, United States

Location

Premier Medical Group of the Hudson Valley PC

Poughkeepsie, New York, 12603, United States

Location

Memorial Sloan Kettering Cancer Center Rockville Centre

Rockville Centre, New York, 11570, United States

Location

Associated Medical Professionals of New York, PLLC

Syracuse, New York, 13210, United States

Location

Memorial Sloan Kettering Cancer Center Nassau

Uniondale, New York, 11553, United States

Location

Duke Investigational Chemotherapy Services

Durham, North Carolina, 27710, United States

Location

Duke Nuclear Medicine

Durham, North Carolina, 27710, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Alliance Urology Specialists, PA

Greensboro, North Carolina, 27403, United States

Location

TriState Urologic Services PSC Inc., dba The Urology Group

Cincinnati, Ohio, 45212, United States

Location

Mercy Health Jewish Hospital

Cincinnati, Ohio, 45236, United States

Location

Clinical Research Solutions

Middleburg Heights, Ohio, 44130, United States

Location

Southwest Urology

Middleburg Heights, Ohio, 44130, United States

Location

Stephenson Cancer Center

Oklahoma City, Oklahoma, 73104, United States

Location

Oregon Imaging Center

Eugene, Oregon, 97401, United States

Location

Oregon Urology Institute

Springfield, Oregon, 97477, United States

Location

Urologic Consultants of SE PA

Bala-Cynwyd, Pennsylvania, 19004, United States

Location

Keystone Urology Specialists

Lancaster, Pennsylvania, 17604, United States

Location

Thomas Jefferson University, Sidney Kimmel Cancer Center, Clinical Research Organization

Philadelphia, Pennsylvania, 19083, United States

Location

Honickman Centre

Philadelphia, Pennsylvania, 19107, United States

Location

Thomas Jefferson University Hospital, Bodine Buiding

Philadelphia, Pennsylvania, 19107, United States

Location

Thomas Jefferson University, Medical Oncology

Philadelphia, Pennsylvania, 19107, United States

Location

Thomas Jefferson University, Sidney Kimmel Cancer Center

Philadelphia, Pennsylvania, 19107, United States

Location

Carolina Urologic Research Center

Myrtle Beach, South Carolina, 29572, United States

Location

Vanderbilt Unversity Medical Center, Dept. of Urologic Surgery

Nashville, Tennessee, 37232, United States

Location

Vanderbilt Unversity Medical Center, The Urology Clinic

Nashville, Tennessee, 37232, United States

Location

Urology Clinics of North Texas, PLLC

Dallas, Texas, 75231, United States

Location

Houston Metro Urology

Houston, Texas, 77027, United States

Location

Urology San Antonio Research

San Antonio, Texas, 78229, United States

Location

Henrico Doctor's Hospital

Henrico, Virginia, 23229, United States

Location

Virginia Urology

Richmond, Virginia, 23235, United States

Location

Urology of Virginia, PLLC.

Virginia Beach, Virginia, 23462, United States

Location

Genesis Cancer Care NSW

Gateshead, New South Wales, 2290, Australia

Location

Lismore Base hospital

Lismore, New South Wales, 2480, Australia

Location

Liverpool Hospital

Liverpool, New South Wales, 2170, Australia

Location

Macquarie University

North Ryde, New South Wales, 2109, Australia

Location

Genesis Cancer Care

North Sydney, New South Wales, 2060, Australia

Location

Port Macquarie Base Hospital

Port Macquarie, New South Wales, 2444, Australia

Location

GenesisCare North Shore

St Leonards, New South Wales, 2065, Australia

Location

The Tweed Hospital

Tweed Heads, New South Wales, 2485, Australia

Location

Australian Clinical Trials Pty Ltd

Wahroonga, New South Wales, 2076, Australia

Location

Sydney Adventist Hospital

Wahroonga, New South Wales, 2076, Australia

Location

Calvary Mater Newcastle

Waratah, New South Wales, 2298, Australia

Location

Westmead Hospital

Westmead, New South Wales, 2145, Australia

Location

Illawarra Cancer Care Centre

Wollongong, New South Wales, 2500, Australia

Location

Crown Princess Mary Cancer Centre

Westmead, NEW, 2145, Australia

Location

Icon Cancer Care Wesley

Auchenflower, Queensland, 4066, Australia

Location

Icon Cancer Care Chermside

Chermside, Queensland, 4032, Australia

Location

Icon Cancer Care South Brisbane

South Brisbane, Queensland, 4101, Australia

Location

Icon Cancer Foundation

South Brisbane, Queensland, 4101, Australia

Location

Icon Cancer Centre Southport

Southport, Queensland, 4215, Australia

Location

Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Box Hill Hospital

Box Hill, Victoria, 3128, Australia

Location

Monash Medical Centre

Clayton, Victoria, 3168, Australia

Location

Austin Health

Heidelberg, Victoria, 3084, Australia

Location

Australian Urology Associates

Malvern, Victoria, 3144, Australia

Location

Sunshine Hospital

St Albans, Victoria, 3021, Australia

Location

Fiona Stanley Hospital

Murdoch, Western Australia, 6150, Australia

Location

Hospital Barmherzige Schwestern Linz

Linz, Upper Austria, 4010, Austria

Location

Hospital Barmherzige Schwestern Linz, Department of Urology

Linz, 4010, Austria

Location

Ordensklinikum Linz GmbH

Linz, 4020, Austria

Location

Department of Nuclear Medicine and Endocrinology, University Hospital Salzburg, Austria

Salzburg, 5020, Austria

Location

Department of Radiology, University Hospital Salzburg, Austria

Salzburg, 5020, Austria

Location

Department of Urology,Paracelsus Medical University Salzburg

Salzburg, 5020, Austria

Location

AKH - Medizinische Universität Wien

Vienna, 1090, Austria

Location

Department of Internal Medicine I, Medical university Vienna

Vienna, 1090, Austria

Location

Hospital São Rafael S.A

Salvador, Estado de Bahia, 41253-190, Brazil

Location

Liga Paranaense de Combate ao Cancer - Hospital Erasto Gaertner

Curitiba, Paraná, 81520-060, Brazil

Location

CITO - Centro Integrado de Terapia Onco-Hematologica - Hospital de Clinicas de Passo Fundo

Passo Fundo, Rio Grande do Sul, 99010-260, Brazil

Location

Hospital de Clinicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, 90035-903, Brazil

Location

CLINIONCO - Clinica de Oncologia de Porto Alegre Ltda.

Porto Alegre, Rio Grande do Sul, 90430-090, Brazil

Location

Hospital Sao Lucas da PUCRS

Porto Alegre, Rio Grande do Sul, 90610-0000, Brazil

Location

Fundacao Pio XII - Hospital de Cancer de Barretos

Barretos, São Paulo, 14784-400, Brazil

Location

Hospital das Clinicas da Faculdade de Ciencias Medicas da UNICAMP

Campinas, São Paulo, 13083-970, Brazil

Location

Centro de Estudos e Pesquisas de Hematologia e Oncologia - Faculdade de Medicina do ABC

Santo André, São Paulo, 09060-650, Brazil

Location

Oncosite - Centro de Pesquisa Clinica em Oncologia Ltda

Ijuí/RS, 98700-000, Brazil

Location

Prostate Cancer Centre

Calgary, Alberta, T2V 1P9, Canada

Location

Cross Cancer Institute

Edmonton, Alberta, T6G 1Z2, Canada

Location

Vancouver Prostate Centre

Vancouver, British Columbia, V5Z 1M9, Canada

Location

Manitoba Prostate Centre CancerCare Manitoba

Winnipeg, Manitoba, R3E 0V9, Canada

Location

Nova Scotia Health Authority

Halifax, Nova Scotia, B3H 2Y9, Canada

Location

The Male/Female Health and Research Centre, Royal Court Medical Centre

Barrie, Ontario, L4M 7G1, Canada

Location

Kingston General Hospital

Kingston, Ontario, K7L 2V7, Canada

Location

Centre for Applied Urological Research

Kingston, Ontario, K7L 3J7, Canada

Location

Hotel Dieu Hospital

Kingston, Ontario, K7L 5G2, Canada

Location

Urology Associates/ Urologic Medical Research

Kitchener, Ontario, N2N 2B9, Canada

Location

London Health Sciences Centre - Victoria Hospital

London, Ontario, N6A 5W9, Canada

Location

Sunnybrook Health Sciences Centre

Toronto, Ontario, M4N 3M5, Canada

Location

University Health Network - Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Urology South Shore Research

Greenfield Park, Quebec, J4V 2H3, Canada

Location

Centre Hospitalier de l'Universite de Montreal

Montreal, Quebec, H2X 3E4, Canada

Location

McGill University Health Centre

Montreal, Quebec, H4A 3J1, Canada

Location

Ultra-Med Inc.

Pointe-Claire, Quebec, H9R 4S3, Canada

Location

CHU de Quebec - L'Hotel-Dieu de Quebec

Québec, Quebec, G1R 2J6, Canada

Location

CHU de Quebec - L'Hotel-Dieu de Quebec - CRCEO

Québec, Quebec, G1R 3S1, Canada

Location

Rigshospitalet - Copenhagen University Hospital

Copenhagen N, Copenhagen N, 2200, Denmark

Location

Aarhus University Hospital

Arhus N, 8200, Denmark

Location

Rigshospitalet - Copenhagen University Hospital

Copenhagen, 2100, Denmark

Location

Rigshospitalet, Dept of Radiology

Copenhagen, 2100, Denmark

Location

Odense University Hospital

Odense C, 5000, Denmark

Location

Vejle Sygehus

Vejle, 7100, Denmark

Location

Helsingin yliopistollinen keskussairaala

Helsinki, 00290, Finland

Location

Oulun yliopistollinen sairaala

Oulu, 90220, Finland

Location

Satakunnan Keskussairaala

Pori, 28500, Finland

Location

Seinaejoen Keskussairaala

Seinäjoki, 60220, Finland

Location

Tampereen yliopistollinen sairaala

Tampere, 33520, Finland

Location

ICO- site Paul Papin

Angers, 49933, France

Location

Clinique Pasteur - Lanroze Service Pharmacie

Brest, 29200, France

Location

Clinique Pasteur - Lanroze

Brest, 29200, France

Location

CHD Vendée

La Roche-sur-Yon, 85925, France

Location

CHRU de Lille - Hopital Claude Huriez

Lille, 59037, France

Location

ICM Val d'Aurelle

Montpellier, 34298, France

Location

CHU de Nantes - Hotel Dieu

Nantes, 44000, France

Location

Hopital Saint-Louis

Paris, 75475, France

Location

Institut Mutualiste Montsouris

Paris, 75674, France

Location

CHP Saint-Gregoire

Saint-Grégoire, 35760, France

Location

ICO - site Rene Gauducheau

Saint-Herblain, 44805, France

Location

Hia Begin

Saint-Mandé, 94160, France

Location

Hopital Foch

Suresnes, 92151, France

Location

Institut Gustave Roussy

Villejuif, 94800, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Farmacia, Azienda Socio Sanitaria Territoriale di Cremona

Cremona, 26100, Italy

Location

Struttura Complessa di Oncologia, Azienda Socio Sanitaria Territoriale di Cremona

Cremona, 26100, Italy

Location

UO di Radiologia, Azienda Socio Sanitaria Territoriale di Cremona

Cremona, 26100, Italy

Location

UO di Oncologia,Ospedale Civile degli Infermi

Faenza RA, 48018, Italy

Location

UO di Radiologia, Ospedale Civile degli Infermi

Faenza RA, 48018, Italy

Location

UO di Oncologia, Ospedale Civile Umberto I

Lugo RA, 48022, Italy

Location

Uo di Radiologia, Ospedale Civile Umberto I

Lugo RA, 48022, Italy

Location

Laboratorio Farmaci Antiblastici, IRCCS Istituto

Meldola (FC), 47014, Italy

Location

U.O. Oncologia Medica, IRCCS Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori

Meldola (FC), 47014, Italy

Location

UO Radiologia,IRCCS Istituto Scientifico Romagnolo Per lO Studio e la Cura dei Tumori (IRST)

Meldola (FC), 47014, Italy

Location

Istituto Nazionale Tumori Fondazione G. Pascale/Oncologia Medica A

Napoli, 80131, Italy

Location

S.C.D.U. Oncologia Medica, A.O.U. San Luigi Gonzaga

Orbassano (TO), 10043, Italy

Location

S.C.D.U. Radiodiagnostica, A.O.U. San Luigi Gonzaga

Orbassano (TO), 10043, Italy

Location

Servizio di Farmacia, Ospedale Santa Maria delle Croci

Ravenna, 48121, Italy

Location

Servizio di Radiologia, Ospedale Santa Maria Delle Croci

Ravenna, 48121, Italy

Location

UO di Oncologia Medica, Ospedale Santa Maria delle Croci

Ravenna, 48121, Italy

Location

Farmacia Interna, Ospedale degli Infermi

Rimini, 47923, Italy

Location

UO Oncologia, Ospedale degli Infermi

Rimini, 47923, Italy

Location

Azienda Ospedaliera S, Camillo Forlanini, UOC per il governo clinico in Oncologia Medica,pad,Flajani

Roma, 00152, Italy

Location

U.O. di Oncologia Medica, Ospedale Santa Chiara

Trento, 38122, Italy

Location

U.O. Medicina Nucleare, Ospedale Santa Chiara

Trento, 38122, Italy

Location

U.O. Radiologia, Ospedale Santa Chiara

Trento, 38122, Italy

Location

VU Medical Centrum, Department of Urology

Amsterdam, 1081 HV, Netherlands

Location

Academisch Medisch Centrum

Amsterdam, 1105AZ, Netherlands

Location

Gelderse Vallei Ziekenhuis

Ede, 6710 HN, Netherlands

Location

Catharina Ziekenhuis Eindhoven

Eindhoven, 5623 EJ, Netherlands

Location

University Medical Centrum Groningen, Department Urologie

Groningen, 9713 GZ, Netherlands

Location

Medisch Centrum Leeuwarden

Leeuwarden, 8934 AD, Netherlands

Location

Maastricht University Medical Center, Department of Urology

Maastricht, 6229 HX, Netherlands

Location

Antonius Ziekenhuis

Sneek, 8601 ZK, Netherlands

Location

Uniwersyteckie Centrum Kliniczne Klinika Onkologii i Radioterapii

Gdansk, 80-952, Poland

Location

Wojewodzki Szpital Specjalistyczny im. Janusza Korczaka w Slupsku Sp. z o. o.

Słupsk, 76-200, Poland

Location

Wojewodzki Szpital Specjalistyczny im. Janusza Korczaka w Slupsku Sp. z o.o., Oddzial Urologiczny

Słupsk, 76-200, Poland

Location

Kujawsko-Pomorskie Centrum Urologicznw Sp z o.o

Torun, 87-100, Poland

Location

Centrum Medyczne Melita Medical

Wroclaw, 50-449, Poland

Location

EMC Instytut Medyczny Spolka Akcyjna

Wroclaw, 54-144, Poland

Location

Fakultna nemocnica s poliklinikou F.D.Roosevelta

Banská Bystrica, 975 17, Slovakia

Location

CUIMED, s.r.o., Urologicka ambulancia

Bratislava, 851 05, Slovakia

Location

Vychodoslovensky onkologicky ustav, a.s.

Košice, 041 91, Slovakia

Location

Univerzitna nemocnica Martin

Martin, 036 59, Slovakia

Location

UROEXAM, spol. s r.o.

Nitra, 949 01, Slovakia

Location

MILAB

Prešov, 080 81, Slovakia

Location

Fakultna nemocnica s poliklinikou Zilina

Žilina, 012 07, Slovakia

Location

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, 13620, South Korea

Location

Pusan National University Yangsan Hospital

Yangsan, Gyeongsangnam-do, 50612, South Korea

Location

Chonnam National University Hwasun Hospital

Hwasun-gun, Jeollanam-do, 58128, South Korea

Location

Gachon University Gil Medical Center

Incheon, 21565, South Korea

Location

Severance Hospital. Yonsei University Health System

Seoul, 03722, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Gangnam Severance Hospital, Yonsei University Health System

Seoul, 06273, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Hospital Universitari Son Espases

Palma de Mallorca, Balearic Islands, 07010, Spain

Location

Althaia, Xarxa Assistencial Universitària de Manresa

Manresa, Barcelona, 08243, Spain

Location

Complejo Hospitalario Universitario de Santiago

Santiago de Compostela, LA Coruna, 15706, Spain

Location

Hospital del Mar

Barcelona, 08003, Spain

Location

Hospital Clinic i Provincial de Barcelona, Dr. Antonio Alcaraz Asensio

Barcelona, 08036, Spain

Location

Hospital Universitario Puerta del Mar

Cadiz, 11009, Spain

Location

ICO Girona; Hospital Universitari de Girona Dr. Josep Trueta. Servicio de Oncologia

Girona, 17007, Spain

Location

Hospital Universitario de La Princesa

Madrid, 28006, Spain

Location

Hospital General Universitario Gregorio Maranon. Servicio de Oncologia.

Madrid, 28007, Spain

Location

Centro Oncologico MD Anderson International Espana

Madrid, 28033, Spain

Location

Hospital Universitario Ramon Y Cajal

Madrid, 28034, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Complejo Hospitalario Universitario de Orense

Ourense, 32005, Spain

Location

Corporacio Sanitaria Parc Tauli

Sabadell, 08208, Spain

Location

Hospital Clinico Universitario de Salamanca

Salamanca, 37007, Spain

Location

Instituto Valenciano de Oncologia IVO

Valencia, 46009, Spain

Location

Sahlgrenska Universitetssjukhuset, Sahlgrenska

Gothenburg, 413 45, Sweden

Location

Skanes Universitetssjukhus

Malmo, 205 02, Sweden

Location

Universitetssjukhuset Orebro

Örebro, 70 185, Sweden

Location

Sodersjukhuset AB

Stockholm, 118 83, Sweden

Location

Karolinska Universitetssjukhuset Solna

Stockholm, 17176, Sweden

Location

Norrlands Universitetssjukhus

Umeå, 90 185, Sweden

Location

Norrlands Universitetssjukhus

Umeå, 90185, Sweden

Location

Akademiska Sjukhuset

Uppsala, 751 85, Sweden

Location

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, 807, Taiwan

Location

China Medical University Hospital

Taichung, 40447, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 40705, Taiwan

Location

National Taiwan University Hospital

Taipei, 10002, Taiwan

Location

Chang Gung Memorial Hospital, Linkou

Taoyuan District, 333, Taiwan

Location

Ross Hall Hospital

Glasgow, CITY of Glasgow, G52 3NQ, United Kingdom

Location

Royal Devon & Exeter Hospital

Wonford, Devon, EX2 5DW, United Kingdom

Location

Royal Free Hospital

London, Greater London, NW3 2QG, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Cancer Centre, Queen Elizabeth Hospital

Birmingham, WEST Midlands, B15 2TH, United Kingdom

Location

University Hospitals Bristol NHS Foundation Trust

Bristol, BS2 8ED, United Kingdom

Location

Beatson West of Scotland Cancer Centre

Glasgow, G12 OYN, United Kingdom

Location

Related Publications (8)

  • Shore ND, Gleave M, De Giorgi U, Rannikko A, Pieczonka CM, Sridharan S, Brasso K, Woo HH, Gomez Caamano A, Saranchuk JW, Nordquist LT, Ferreira U, Tang Y, Rosbrook B, Haas GP, Rosales M, Zohren F, Tarazi J, Freedland SJ. Treatment of High-Risk Biochemically Recurrent Prostate Cancer With Enzalutamide in Combination With Leuprolide: Secondary Endpoints From the EMBARK Trial. J Urol. 2025 Dec 9:101097JU0000000000004890. doi: 10.1097/JU.0000000000004890. Online ahead of print.

  • Shore ND, De Giorgi U, Tutrone RF, Bailen JL, Roos EPM, Kliment J, Marx G, Karsh LI, Ramirez-Backhaus M, Uchio EM, Supiot S, Tang Y, Rosbrook B, Haas GP, Rosales M, Zohren F, Tarazi J, Freedland SJ. Enzalutamide Monotherapy for the Treatment of Prostate Cancer With High-Risk Biochemical Recurrence: EMBARK Secondary End Points. J Urol. 2025 Dec 17:101097JU0000000000004879. doi: 10.1097/JU.0000000000004879. Online ahead of print.

  • Shore ND, Luz MA, De Giorgi U, Gleave M, Gotto GT, Pieczonka CM, Haas GP, Kim CS, Ramirez-Backhaus M, Rannikko A, Kalac M, Sridharan S, Rosales M, Tang Y, Tutrone RF Jr, Venugopal B, Villers A, Woo HH, Wang F, Freedland SJ. Improved Survival with Enzalutamide in Biochemically Recurrent Prostate Cancer. N Engl J Med. 2025 Oct 19. doi: 10.1056/NEJMoa2510310. Online ahead of print.

  • De Giorgi U, Freedland SJ, Rannikko A, Ramirez-Backhaus M, Villers A, Tarazi J, Tang Y, Haas GP, Rosales M, Shore ND. Enzalutamide in patients with high-risk biochemically recurrent prostate cancer according to the European Association of Urology definition: a post hoc analysis of EMBARK. Prostate Cancer Prostatic Dis. 2025 Mar 26. doi: 10.1038/s41391-025-00959-8. Online ahead of print.

  • Freedland SJ, Gleave M, De Giorgi U, Rannikko A, Pieczonka CM, Tutrone RF, Venugopal B, Woo HH, Ramirez-Backhaus M, Supiot S, Lantz A, Ganguli A, Ivanova J, Kral P, Huang SP, Saad F, Shore ND. Enzalutamide and Quality of Life in Biochemically Recurrent Prostate Cancer. NEJM Evid. 2023 Dec;2(12):EVIDoa2300251. doi: 10.1056/EVIDoa2300251. Epub 2023 Oct 22.

  • Freedland SJ, de Almeida Luz M, De Giorgi U, Gleave M, Gotto GT, Pieczonka CM, Haas GP, Kim CS, Ramirez-Backhaus M, Rannikko A, Tarazi J, Sridharan S, Sugg J, Tang Y, Tutrone RF Jr, Venugopal B, Villers A, Woo HH, Zohren F, Shore ND; EMBARK Study. Improved Outcomes with Enzalutamide in Biochemically Recurrent Prostate Cancer. N Engl J Med. 2023 Oct 19;389(16):1453-1465. doi: 10.1056/NEJMoa2303974.

  • LBA02-09 EMBARK: A Phase 3 Randomized Study of Enzalutamide or Placebo Plus Leuprolide Acetate and Enzalutamide Monotherapy in High-risk Biochemically Recurrent Prostate Cancer. J Urol. 2023 Jul;210(1):224-226. doi: 10.1097/JU.0000000000003518. Epub 2023 May 2.

  • Freedland SJ, De Giorgi U, Gleave M, Rosbrook B, Shen Q, Sugg J, Haas GP, Shore ND. A phase 3 randomised study of enzalutamide plus leuprolide and enzalutamide monotherapy in high-risk non-metastatic hormone-sensitive prostate cancer with rising PSA after local therapy: EMBARK study design. BMJ Open. 2021 Aug 12;11(8):e046588. doi: 10.1136/bmjopen-2020-046588.

MeSH Terms

Conditions

Prostatic Neoplasms

Interventions

enzalutamideluprolide acetate gel depotLeuprolide

Condition Hierarchy (Ancestors)

Genital Neoplasms, MaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesProstatic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

Gonadotropin-Releasing HormonePituitary Hormone-Releasing HormonesHypothalamic HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsNeuropeptidesPeptidesAmino Acids, Peptides, and ProteinsOligopeptidesNerve Tissue ProteinsProteins

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Masking Details
The randomized blinded portion of the study has concluded. The study is now being conducted open label manner.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 14, 2014

First Posted

December 18, 2014

Study Start

December 17, 2014

Primary Completion

January 31, 2023

Study Completion (Estimated)

September 19, 2026

Last Updated

July 8, 2025

Results First Posted

March 25, 2024

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations