NCT02253173

Brief Summary

This study will assess the safety and efficacy of a new formulation of vaginal estradiol for the treatment of symptoms of vulvar and vaginal atrophy in postmenopausal women.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
764

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Sep 2014

Shorter than P25 for phase_3

Geographic Reach
2 countries

105 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2014

Completed
25 days until next milestone

First Submitted

Initial submission to the registry

September 26, 2014

Completed
5 days until next milestone

First Posted

Study publicly available on registry

October 1, 2014

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2015

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

May 25, 2017

Completed
Last Updated

May 25, 2017

Status Verified

April 1, 2017

Enrollment Period

1.1 years

First QC Date

September 26, 2014

Results QC Date

August 8, 2016

Last Update Submit

April 20, 2017

Conditions

Keywords

VVAPainful SexPostmenopausal

Outcome Measures

Primary Outcomes (4)

  • Co-Primary Efficacy Endpoint - Vaginal Superficial Cells

    • Change from Baseline to Week 12 in the percentage of vaginal superficial cells (by vaginal cytologic smear) compared to placebo

    Baseline and 12 Weeks

  • Co-Primary Efficacy Endpoint - Vaginal Parabasal Cells

    • Change from Baseline to Week 12 in the percentage of vaginal parabasal cells (by vaginal cytologic smear) compared to placebo

    Baseline and 12 Weeks

  • Co-Primary Efficacy Endpoint - Vaginal pH

    • Change from Baseline to Week 12 in vaginal pH as compared to placebo

    Baseline and 12 Weeks

  • Co-Primary Efficacy Endpoint - Severity of Most Bothersome Symptom (Dyspareunia)

    • Change from Baseline to Week 12 on the severity of the MBS of dyspareunia (vaginal pain associated with sexual activity) associated with VVA as compared to placebo VVA Symptoms Self-Assessment Questionnaire Severity Scale: 0 = None, 1 = Mild, 2 = Moderate, 3 = Severe. Subjects assessed severity at Baseline and Week 12

    Baseline and Week 12

Secondary Outcomes (43)

  • Secondary Efficacy Endpoints - Vaginal Superficial Cells

    Baseline and Week 2

  • Secondary Efficacy Endpoints- Vaginal Superficial Cells

    Baseline and Week 6

  • Secondary Efficacy Endpoints - Vaginal Superficial Cells

    Baseline and Week 8

  • Secondary Efficacy Endpoints - Vaginal Parabasal Cells

    Baseline and Week 2

  • Secondary Efficacy Endpoints - Vaginal Parabasal Cells

    Baseline and Week 6

  • +38 more secondary outcomes

Other Outcomes (1)

  • PK Substudy - Hormone Concentration Assessments (Serum Estradiol, Estrone and Estrone Conjugates; SHBG)

    Pre-treatment, Day 2, Weeks 2 and 12

Study Arms (4)

Estradiol 4mcg Vaginal Softgel Capsule

EXPERIMENTAL

Estradiol 4mcg Vaginal Softgel Capsule

Drug: Estradiol

Estradiol 10mcg Vaginal Softgel Capsule

EXPERIMENTAL

Estradiol 10mcg Vaginal Softgel Capsule

Drug: Estradiol

Estradiol 25mcg Vaginal Softgel Capsule

EXPERIMENTAL

Estradiol 25mcg Vaginal Softgel Capsule

Drug: Estradiol

Placebo Vaginal Softgel Capsule

PLACEBO COMPARATOR

Placebo Vaginal Softgel Capsule

Drug: Placebo

Interventions

Estradiol 10mcg Vaginal Softgel CapsuleEstradiol 25mcg Vaginal Softgel CapsuleEstradiol 4mcg Vaginal Softgel Capsule
Placebo Vaginal Softgel Capsule

Eligibility Criteria

Age40 Years - 75 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Postmenopausal female subjects between the ages of 40 and 75 years (at the time of randomization) with at least:
  • months of spontaneous amenorrhea (women \<55 years of age with a history of hysterectomy without bilateral oophorectomy prior to natural menopause must have follicle stimulating hormone (FSH) levels \> 40 mIU/mL), OR
  • months of spontaneous amenorrhea with follicle stimulating hormone (FSH) levels \> 40mlU/mL OR
  • At least 6 weeks postsurgical bilateral oophorectomy.
  • ≤5% superficial cells on vaginal cytological smear
  • Vaginal pH \> 5.0
  • Moderate to severe symptom of vaginal pain associated with sexual activity considered the most bothersome vaginal symptom by the subject at screening visit 1A.
  • Moderate to severe symptom of vaginal pain associated with sexual activity at screening visit 1B.
  • Onset of moderate to severe dyspareunia in the postmenopausal years.
  • Subjects should be sexually active (i.e. have sexual activity with vaginal penetration within approximately 1 month of screening visit 1A).
  • Subjects should anticipate having sexual activity (with vaginal penetration) during the conduct of the trial.
  • For subjects with an intact uterus: Subjects must have an acceptable result from an evaluable screening endometrial biopsy.
  • Subjects who have a Body Mass Index (BMI) less than or equal to 38 kg/m2. BMI values should be rounded to the nearest integer (ex. 32.4 rounds down to 32, while 26.5 rounds up to 27).
  • In the opinion of the investigator, the subject will comply with the protocol and has a high probability of completing the study.

You may not qualify if:

  • Use of the following:
  • Oral estrogen-, progestin-, androgen-, or SERM-containing drug products within 8 weeks before screening visit 1A (can enter washout);
  • Use of transdermal hormone products within 4 weeks before screening visit 1A (can enter washout);
  • Use of vaginal hormone products (rings, creams, gels) within 4 weeks before screening visit1A (can enter washout);
  • Use of intrauterine progestins within 8 weeks before screening visit 1A (can enter washout);
  • Use of progestin implants/injectables or estrogen pellets/injectables within 6 months before screening visit 1A (cannot enter washout);
  • Use of vaginal lubricants or moisturizers within 7 days before the screening visit 1B vaginal pH assessment.
  • A history or active presence of clinically important medical disease that might confound the study or be detrimental to the subject, examples include:
  • Hypersensitivity to estrogens;
  • Endometrial hyperplasia;
  • Undiagnosed vaginal bleeding;
  • Have a history of a chronic liver or kidney dysfunction/disorder (e.g., Hepatitis C or chronic renal failure);
  • Thrombophlebitis, thrombosis or thromboembolic disorders;
  • Cerebrovascular accident, stroke, or transient ischemic attack;
  • Myocardial infarction or ischemic heart disease;
  • +27 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (105)

Medical Affiliated Research Center

Huntsville, Alabama, 35801, United States

Location

Montogomery Women's Health

Montgomery, Alabama, 36117, United States

Location

Cactus Clinical Research

Mesa, Arizona, 85209, United States

Location

Arizona Wellness Center for Women

Phoenix, Arizona, 85032, United States

Location

Radiant Research

Scottsdale, Arizona, 85251, United States

Location

Visions Clinical Research - Tucson

Tucson, Arizona, 85712, United States

Location

Sutter East Bay Medical Foundation

Berkeley, California, 94705, United States

Location

Torrance Clinical Research Institute Inc

Lomita, California, 90717, United States

Location

Futura Research

Norwalk, California, 90650, United States

Location

Northern California Research

Sacramento, California, 95821, United States

Location

Medical Center for Clinical Research

San Diego, California, 92108, United States

Location

San Diego Sexual Medicine

San Diego, California, 92120, United States

Location

Women's Health Care Research Corp.

San Diego, California, 92123, United States

Location

Lynn Institute of the Rockies

Colorado Springs, Colorado, 80909, United States

Location

Downtown Women's Health Care

Denver, Colorado, 80209, United States

Location

Horizons Clinical Research Center

Denver, Colorado, 80220, United States

Location

Red Rocks OB/Gyn

Lakewood, Colorado, 80228, United States

Location

Clinical Research Consulting

Milford, Connecticut, 06460, United States

Location

Coastal Connecticut Research, LLC

New London, Connecticut, 06320, United States

Location

James A. Simon, Women's Health & Research Consultants

Washington D.C., District of Columbia, 20036, United States

Location

South Florida Medical Research

Aventura, Florida, 33180, United States

Location

Nature Coast Clinical Research

Crystal River, Florida, 34429, United States

Location

Avail Clinical Research

DeLand, Florida, 32720, United States

Location

Clinical Physiology Associates

Fort Myers, Florida, 33916, United States

Location

UF Health Physicians Women's & REI Springhill

Gainesville, Florida, 32606, United States

Location

UF College of Medicine-Jacksonville, Dept. of Obstetrics and Gynecology

Jacksonville, Florida, 32207, United States

Location

Jacksonville Center for Clinical Research

Jacksonville, Florida, 32216, United States

Location

South Florida Wellness & Clinical Research Institute

Margate, Florida, 33063, United States

Location

New Age Medical Research Corporation

Miami, Florida, 33186, United States

Location

Suncoast Clinical Research, Inc.

New Port Richey, Florida, 34652, United States

Location

Healthcare Clinical Data

North Miami, Florida, 33161, United States

Location

Ideal Clinical Research

North Miami Beach, Florida, 33162, United States

Location

Radiant Research

Pinellas Park, Florida, 33781, United States

Location

All Women's Healthcare of West Broward

Plantation, Florida, 33324, United States

Location

Physician Care Clinical Research

Sarasota, Florida, 34239, United States

Location

Comprehensive Clinical Trials

West Palm Beach, Florida, 33409, United States

Location

Women's Health Associates

Atlanta, Georgia, 30342, United States

Location

Masters of Clinical Research, Inc.

Augusta, Georgia, 30909, United States

Location

Soapstone Center for Clinical Research

Decatur, Georgia, 30034, United States

Location

WR-Mount Vernon Clinical Research

Sandy Springs, Georgia, 30328, United States

Location

Fellows Research Alliance, Inc.

Savannah, Georgia, 31046, United States

Location

Advanced Clinical Research

Boise, Idaho, 83642, United States

Location

Women's Healthcare Associates P.A.

Idaho Falls, Idaho, 83404, United States

Location

Radiant Research

Chicago, Illinois, 60654, United States

Location

American Health Network of Indiana, LLC

Avon, Indiana, 46123, United States

Location

Lafayette Clinical Research Group

Lafayette, Indiana, 47905, United States

Location

Cypress Medical Research Center

Wichita, Kansas, 67226, United States

Location

Central Kentucky Research Associates, Inc.

Lexington, Kentucky, 40509, United States

Location

Bluegrass Clinical Research, Inc.

Louisville, Kentucky, 40291, United States

Location

Horizon Research Group of Opelousas

Eunice, Louisiana, 70535, United States

Location

Capital Women's Care

Frederick, Maryland, 21702, United States

Location

Maryland Center for Sexual Health

Lutherville, Maryland, 21093, United States

Location

ClinSite, LLC

Ann Arbor, Michigan, 48106, United States

Location

Beyer Research

Kalamazoo, Michigan, 49009, United States

Location

Saginaw Valley Medical Research Group, L.L.C.

Saginaw, Michigan, 48604, United States

Location

Montana Health

Billings, Montana, 59102, United States

Location

Women's Clinic of Lincoln

Lincoln, Nebraska, 68510, United States

Location

Office of Edmond E. Pack, MD

Las Vegas, Nevada, 89113, United States

Location

Office of R. Garn Mabey, MD

Las Vegas, Nevada, 89128, United States

Location

Lawrence OB-GYN Clinical Research, LLC

Lawrenceville, New Jersey, 08648, United States

Location

Rutgers-Robert Wood Johnson Medical School

New Brunswick, New Jersey, 08901, United States

Location

Women's Health Research Center

Plainsboro, New Jersey, 08536, United States

Location

Bosque Women's Care

Albuquerque, New Mexico, 87109, United States

Location

Southwest Clinical Research

Albuquerque, New Mexico, 87109, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Suffolk OB/GYN

Port Jefferson, New York, 08536, United States

Location

Women's Wellness Clinic

Durham, North Carolina, 27713, United States

Location

Pinewest OB-GYN, Inc.

High Point, North Carolina, 27262, United States

Location

Wake Research Associates

Raleigh, North Carolina, 27612, United States

Location

Hawthorne Research

Winston-Salem, North Carolina, 27103, United States

Location

Lyndhurst Clinical Research

Winston-Salem, North Carolina, 27103, United States

Location

Lillestol Research

Fargo, North Dakota, 58103, United States

Location

Radiant Research

Akron, Ohio, 44311, United States

Location

University of Cincinnati Physicians Company

Cincinnati, Ohio, 45267-0457, United States

Location

Rapid Medical Research

Cleveland, Ohio, 44122, United States

Location

Columbus Center for Women's Health Research

Columbus, Ohio, 43213, United States

Location

HWC Women's Research Center

Englewood, Ohio, 45322, United States

Location

Landerbrook Health Center

Mayfield Heights, Ohio, 44124, United States

Location

Sunstone Medical Research

Medford, Oregon, 97504, United States

Location

The Clinical Trial Center

Jenkintown, Pennsylvania, 19046, United States

Location

Clinical Research of Philadelphia

Philadelphia, Pennsylvania, 19114, United States

Location

Clinical Trials Research Services

Pittsburgh, Pennsylvania, 15206, United States

Location

Fellows Research Alliance, Inc.

Bluffton, South Carolina, 29910, United States

Location

Vista Clinical Research

Columbia, South Carolina, 29201, United States

Location

Coastal Carolina Research Center

Mt. Pleasant, South Carolina, 29464, United States

Location

Chattanooga Medical Research

Chattanooga, Tennessee, 37404, United States

Location

Advanced Research Associates

Corpus Christi, Texas, 78414, United States

Location

Research Across America

Dallas, Texas, 75234, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390-9032, United States

Location

Advances in Health

Houston, Texas, 77030, United States

Location

Hwca, Pllc

Houston, Texas, 77054, United States

Location

TMC Life Research

Houston, Texas, 77054, United States

Location

Stone Oak, LLC dba Discovery Clinical Trials

San Antonio, Texas, 78258, United States

Location

National Clinical Research-Norfolk

Norfolk, Virginia, 23502, United States

Location

Clinical Research Center, EVMS

Norfolk, Virginia, 23507, United States

Location

Virginia Women's Center, Inc.

Richmond, Virginia, 23233, United States

Location

National Clinical Research-Richmond, Inc

Richmond, Virginia, 23294, United States

Location

Tidewater Clinical Research

Virginia Beach, Virginia, 23456, United States

Location

Seattle Women's Health, Research, and Gynecology

Seattle, Washington, 98105, United States

Location

North Spokane Women's Health

Spokane, Washington, 99207, United States

Location

Diex Research Montreal Inc.

Montreal, Quebec, H4N 3C5, Canada

Location

Center for Research Saint-Louis

Québec, Quebec, G1W4R4, Canada

Location

Manna Research Inc

Saint Romuald, Quebec, G6W 5M6, Canada

Location

Diex Research Sherbrooke Inc.

Sherbrooke, Quebec, J1H 1Z1, Canada

Location

Clinique RSF Inc.

Québec, G1S 2L6, Canada

Location

Related Publications (5)

  • Lara LA, Cartagena-Ramos D, Figueiredo JB, Rosa-E-Silva ACJ, Ferriani RA, Martins WP, Fuentealba-Torres M. Hormone therapy for sexual function in perimenopausal and postmenopausal women. Cochrane Database Syst Rev. 2023 Aug 24;8(8):CD009672. doi: 10.1002/14651858.CD009672.pub3.

  • Mirkin S, Simon JA, Liu JH, Archer DF, Castro PD, Graham S, Bernick B, Komm B. Evaluation of endometrial progesterone receptor expression after 12 weeks of exposure to a low-dose vaginal estradiol insert. Menopause. 2021 May 28;28(9):998-1003. doi: 10.1097/GME.0000000000001801.

  • Constantine G, Millheiser LS, Kaunitz AM, Parish SJ, Graham S, Bernick B, Mirkin S. Early onset of action with a 17beta-estradiol, softgel, vaginal insert for treating vulvar and vaginal atrophy and moderate to severe dyspareunia. Menopause. 2019 Nov;26(11):1259-1264. doi: 10.1097/GME.0000000000001394.

  • Constantine GD, Simon JA, Pickar JH, Archer DF, Bernick B, Graham S, Mirkin S. Estradiol vaginal inserts (4 microg and 10 microg) for treating moderate to severe vulvar and vaginal atrophy: a review of phase 3 safety, efficacy and pharmacokinetic data. Curr Med Res Opin. 2018 Dec;34(12):2131-2136. doi: 10.1080/03007995.2018.1527578. Epub 2018 Sep 28.

  • Constantine GD, Bouchard C, Pickar JH, Archer DF, Graham S, Bernick B, Mirkin S. Consistency of Effect with a Low-Dose, Estradiol Vaginal Capsule (TX-004HR): Evaluating Improvement in Vaginal Physiology and Moderate-to-Severe Dyspareunia in Subgroups of Postmenopausal Women. J Womens Health (Larchmt). 2017 Jun;26(6):616-623. doi: 10.1089/jwh.2016.6187. Epub 2017 Mar 29.

MeSH Terms

Conditions

Dyspareunia

Interventions

Estradiol

Condition Hierarchy (Ancestors)

Genital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesGenital Diseases, MaleSexual Dysfunction, PhysiologicalMale Urogenital DiseasesSexual Dysfunctions, PsychologicalMental Disorders

Intervention Hierarchy (Ancestors)

EstrenesEstranesSteroidsFused-Ring CompoundsPolycyclic CompoundsEstradiol CongenersGonadal Steroid HormonesGonadal HormonesHormonesHormones, Hormone Substitutes, and Hormone Antagonists

Results Point of Contact

Title
Sebastian Mirkin, MD, Chief Medical Officer
Organization
TherapeuticsMD

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 26, 2014

First Posted

October 1, 2014

Study Start

September 1, 2014

Primary Completion

October 1, 2015

Study Completion

October 1, 2015

Last Updated

May 25, 2017

Results First Posted

May 25, 2017

Record last verified: 2017-04

Locations