NCT02097524

Brief Summary

The main purposes of this study are to describe the pharmacodynamic effects, safety and pharmacokinetics of a single dose of sarilumab.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
105

participants targeted

Target at P75+ for phase_1 rheumatoid-arthritis

Timeline
Completed

Started Mar 2014

Geographic Reach
1 country

19 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2014

Completed
2 days until next milestone

First Submitted

Initial submission to the registry

March 3, 2014

Completed
24 days until next milestone

First Posted

Study publicly available on registry

March 27, 2014

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2015

Completed
Last Updated

May 5, 2015

Status Verified

May 1, 2015

Enrollment Period

1.1 years

First QC Date

March 3, 2014

Last Update Submit

May 4, 2015

Conditions

Outcome Measures

Primary Outcomes (1)

  • PD parameters

    Pharmacodynamic (PD) parameters, what a drug does to the body, will be collected from baseline through week 4: * the time to nadir (or peak) * change from baseline * area under the curve (AUC)

    baseline through week 4

Secondary Outcomes (2)

  • Percentage of TEAEs

    baseline through week 6

  • PK parameters

    baseline through week 4

Study Arms (4)

Sarilumab - dose 1

EXPERIMENTAL

Single subcutaneous (SC) injection of Sarilumab, dose 1, plus methotrexate background treatment (dispensed and dosed according to local practice)

Drug: Sarilumab

Sarilumab - dose 2

EXPERIMENTAL

Single SC injection of Sarilumab, dose 2, plus methotrexate background treatment (dispensed and dosed according to local practice)

Drug: Sarilumab

Tocilizumab - dose 1

ACTIVE COMPARATOR

Single intravenous (IV) administration of Tocilizumab, dose 1, plus methotrexate background treatment (dispensed and dosed according to local practice)

Drug: Tocilizumab

Tocilizumab - dose 2

ACTIVE COMPARATOR

Single IV administration of Tocilizumab, dose 2, plus methotrexate background treatment (dispensed and dosed according to local practice)

Drug: Tocilizumab

Interventions

Also known as: REGN88, SAR153191
Sarilumab - dose 1Sarilumab - dose 2
Tocilizumab - dose 1Tocilizumab - dose 2

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with RA as defined by the 2010 revised American College of Rheumatology (ACR)
  • ACR Class I-III functional status, based on the 1991 revised criteria
  • Treated for a minimum of 12 weeks with Methotrexate with a stable dose of MTX for at least 8 weeks prior to screening visit

You may not qualify if:

  • Patients less than 18 years of age or minimum legal age
  • Prior treatment with any biologic anti-Interleukin 6 (IL-6) or IL-6 Receptor (IL-6R) antagonists
  • Use of parenteral corticosteroids or intra-articular corticosteroids within 4 weeks prior to screening
  • Use of oral corticosteroids in a dose higher than prednisone 10 mg or equivalent per day, or a change in dosage within 4 weeks prior to randomization
  • Participation in any clinical research study that evaluated an investigational drug or therapy within 5 half-lives or 60 days of the screening visit, whichever is longer
  • Treatment with oral/ biologic DMARDs (disease-modifying antirheumatic drugs), other than MTX, within a certain amount of time prior to screening visit
  • Active or suspected TB or at high risk of contracting TB
  • Fever, or chronic, persistent, or recurring infections requiring active treatment
  • HIV positive

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (19)

Unknown Facility

Birmingham, Alabama, United States

Location

Unknown Facility

Orange, California, United States

Location

Unknown Facility

DeLand, Florida, United States

Location

Unknown Facility

Edgewater, Florida, United States

Location

Unknown Facility

Miami, Florida, United States

Location

Unknown Facility

Miami Lakes, Florida, United States

Location

Unknown Facility

Granger, Indiana, United States

Location

Unknown Facility

Grand Blanc, Michigan, United States

Location

Unknown Facility

Charlotte, North Carolina, United States

Location

Unknown Facility

Cinicinnati, Ohio, United States

Location

Unknown Facility

Memphis, Tennessee, United States

Location

Unknown Facility

Austin, Texas, United States

Location

Unknown Facility

Carrollton, Texas, United States

Location

Unknown Facility

Channelview, Texas, United States

Location

Unknown Facility

Dallas, Texas, United States

Location

Unknown Facility

Houston, Texas, United States

Location

Unknown Facility

Mesquite, Texas, United States

Location

Unknown Facility

Plano, Texas, United States

Location

Unknown Facility

San Antonio, Texas, United States

Location

Related Publications (2)

  • Kovalenko P, Paccaly A, Boyapati A, Xu C, St John G, Nivens MC, Davis JD, Rippley R, DiCioccio AT. Population Pharmacodynamic Model of Neutrophil Margination and Tolerance to Describe Effect of Sarilumab on Absolute Neutrophil Count in Patients with Rheumatoid Arthritis. CPT Pharmacometrics Syst Pharmacol. 2020 Jul;9(7):405-416. doi: 10.1002/psp4.12534. Epub 2020 Jun 20.

  • Emery P, Rondon J, Parrino J, Lin Y, Pena-Rossi C, van Hoogstraten H, Graham NMH, Liu N, Paccaly A, Wu R, Spindler A. Safety and tolerability of subcutaneous sarilumab and intravenous tocilizumab in patients with rheumatoid arthritis. Rheumatology (Oxford). 2019 May 1;58(5):849-858. doi: 10.1093/rheumatology/key361.

MeSH Terms

Conditions

Arthritis, Rheumatoid

Interventions

sarilumabtocilizumab

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Clinical Trial Management

    Regeneron Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
BASIC SCIENCE
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 3, 2014

First Posted

March 27, 2014

Study Start

March 1, 2014

Primary Completion

April 1, 2015

Study Completion

April 1, 2015

Last Updated

May 5, 2015

Record last verified: 2015-05

Locations