NCT02000622

Brief Summary

This open label, randomised, controlled, multi-centre phase III study will assess the efficacy and safety of single agent olaparib vs standard of care based on physician's choice of capecitabine, vinorelbine or eribulin in metastatic breast cancer patients with gBRCA 1/2 mutations.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
302

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Mar 2014

Longer than P75 for phase_3

Geographic Reach
19 countries

171 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 18, 2013

Completed
16 days until next milestone

First Posted

Study publicly available on registry

December 4, 2013

Completed
4 months until next milestone

Study Start

First participant enrolled

March 27, 2014

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 9, 2016

Completed
1 year until next milestone

Results Posted

Study results publicly available

December 22, 2017

Completed
8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 23, 2025

Completed
Last Updated

February 13, 2026

Status Verified

January 1, 2026

Enrollment Period

2.7 years

First QC Date

November 18, 2013

Results QC Date

November 28, 2017

Last Update Submit

January 27, 2026

Conditions

Keywords

Breast CancerMetastaticOlaparibBRCAPARP inhibitorHER2chemotherapy

Outcome Measures

Primary Outcomes (1)

  • Progression-free Survival (PFS) Using Blinded Independent Central Review (BICR) According to Modified Response Evaluation Criteria In Solid Tumours (RECIST v1.1)

    Time from randomisation to the earliest of objective radiological progression or death by any cause in the absence of objective progression. Objective radiological progression is defined using Response Evaluation Criteria In Solid Tumours (RECIST v1.1), as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions.

    Radiological scans performed at baseline then every ~6 weeks up to 24 weeks, then every ~ 12 weeks thereafter until objective radiological disease progression. Assessed up to a maximum of 30 months.

Secondary Outcomes (7)

  • Time to Second Progression or Death (PFS2)

    Second progression status reviewed every 8 weeks following the first objective radiological progression as per investigator assessment. Assessed up to a maximum of 30 months.

  • Overall Survival (OS)

    Survival status reviewed every 3 weeks until treatment discontinued, then every 8 weeks. Assessed up to a maximum of 30 months.

  • Objective Response Rate (ORR) Using Blinded Independent Central Review (BICR) Data Assessed by Modified Response Evaluation Criteria In Solid Tumours (RECIST v1.1)

    Radiological scans performed at baseline then every ~6 weeks up to 24 weeks, then every ~ 12 weeks thereafter until objective radiological disease progression. Assessed up to a maximum of 30 months.

  • Adjusted Mean Change in Global Health Status/Quality of Life (QoL) Score From the European Organisation for Research and Treatment of Cancer - Quality of Life Questionnaire (EORTC QLQ-C30)

    EORTC QLQ-C30 assessments performed at baseline then every ~6 weeks until objective radiological disease progression. Assessed up to a maximum of 30 months.

  • Progression-free Survival (PFS) Using Blinded Independent Central Review (BICR) According to Modified Response Evaluation Criteria In Solid Tumours (RECIST v1.1) in Patients Confirmed as Myriad CDx gBRCAm

    Radiological scans performed at baseline then every ~6 weeks up to 24 weeks, then every ~ 12 weeks thereafter until objective radiological disease progression. Assessed up to a maximum of 30 months.

  • +2 more secondary outcomes

Other Outcomes (4)

  • Time to First Subsequent Cancer Therapy or Death (TFST)

    Subsequent cancer therapy status reviewed every 8 weeks following study treatment discontinuation. Assessed up to a maximum of 30 months.

  • Time to Second Subsequent Cancer Therapy or Death (TSST)

    Subsequent cancer therapy status reviewed every 8 weeks following study treatment discontinuation. Assessed up to a maximum of 30 months.

  • Time to First Subsequent Cancer Therapy or Death (TFST) at Extended OS

    Subsequent cancer therapy status reviewed every 8 weeks following study treatment discontinuation until Sep 2017 (final OS DCO), then every 3 months. Assessed up to a maximum of 64 months.

  • +1 more other outcomes

Study Arms (2)

Olaparib

EXPERIMENTAL

Olaparib tablet 300mg bd po

Drug: Olaparib

Physician's choice chemotherapy

ACTIVE COMPARATOR

Capecitabine 2500 mg/m2 d1-14 q 21, or Vinorelbine 30 mg/m2 d1,8 q 21, or Eribulin 1.4 mg/m2 d1,8 q 21

Drug: Physician's choice chemotherapy

Interventions

Patients will be administered olaparib orally twice daily (bid) at 300 mg. Two (2) x 150 mg olaparib tablets should be taken at the same times each morning and evening of each day, approximately 12 hours apart with approximately 240 mL of water.

Olaparib

Investigators will declare one of the following regimens: * Capecitabine 2500 mg/m2 po daily (divided in 2 doses) x 14 days, repeat every 21 days * Vinorelbine 30 mg/m2 IV Day 1 and Day 8, repeat every 21 days * Eribulin 1.4 mg/m2 IV Day 1 and Day 8, repeat every 21 days

Physician's choice chemotherapy

Eligibility Criteria

Age18 Years - 99 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Germline mutation in BRCA1 or BRCA2 that is predicted to be deleterious or suspected deleterious.
  • Histologically or cytologically confirmed breast cancer with evidence of metastatic disease.
  • Prior therapy with an anthracycline and a taxane in either an adjuvant or metastatic setting.
  • Prior platinum allowed as long as no breast cancer progression occurred on treatment or if given in adjuvant/neoadjuvant setting at least 12 months from last dose to study entry elapsed.
  • ER/PR breast cancer positive patients must have received and progressed on at least one endocrine therapy (adjuvant or metastatic), or have disease that the treating physician believes to be inappropriate for endocrine therapy.
  • ECOG performance status 0-1.
  • Adequate bone marrow, kidney and liver function.

You may not qualify if:

  • Prior treatment with PARP inhibitor.
  • Patients with HER2 positive disease.
  • More than 2 prior lines of chemotherapy for metastatic breast cancer.
  • Untreated and/or uncontrolled brain metastases.
  • Prior malignancy unless curatively treated and disease-free for \> 5 years prior to study entry. Prior adequately treated non-melanoma skin cancer, in situ cancer of the cervix, DCIS or stage I grade 1 endometrial cancer allowed.
  • Known HIV (Human Immunodeficiency Virus) infection.
  • Pregnant or breast-feeding women.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (171)

Research Site

San Diego, California, 92123, United States

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Santa Rosa, California, 95403, United States

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Whittier, California, 90602, United States

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Denver, Colorado, 80204, United States

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New Haven, Connecticut, 06510, United States

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Washington D.C., District of Columbia, 20007, United States

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Jacksonville, Florida, 32224, United States

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Orlando, Florida, 32804, United States

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Plantation, Florida, 33324, United States

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Columbus, Georgia, 31904, United States

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Marietta, Georgia, 30060, United States

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Chicago, Illinois, 60612, United States

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Niles, Illinois, 60714, United States

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Wichita, Kansas, 67214, United States

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Lafayette, Louisiana, 70506, United States

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Boston, Massachusetts, 02114, United States

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Boston, Massachusetts, 02118, United States

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Boston, Massachusetts, 02215, United States

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Detroit, Michigan, 48201, United States

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Grand Rapids, Michigan, 49503, United States

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Rochester, Minnesota, 55905-0001, United States

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Saint Louis Park, Minnesota, 55416, United States

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Jackson, Mississippi, 39202, United States

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Columbia, Missouri, 65212, United States

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St Louis, Missouri, 63131, United States

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Lebanon, New Hampshire, 03756, United States

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Commack, New York, 11725, United States

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Harrison, New York, 10604, United States

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New York, New York, 10021, United States

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New York, New York, 10065, United States

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Rockville Centre, New York, 11570, United States

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Syracuse, New York, 13210, United States

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Cincinnati, Ohio, 45267, United States

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Cleveland, Ohio, 44106, United States

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Cleveland, Ohio, 44195, United States

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Portland, Oregon, 97213, United States

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Philadelphia, Pennsylvania, 19104, United States

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Sayre, Pennsylvania, 18840, United States

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Germantown, Tennessee, 38138, United States

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Houston, Texas, 77030, United States

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Tyler, Texas, 75701, United States

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Burlington, Vermont, 05401, United States

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Plovdiv, 4000, Bulgaria

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Plovdiv, 4004, Bulgaria

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Sofia, 1233, Bulgaria

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Sofia, 1303, Bulgaria

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Sofia, 1330, Bulgaria

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Sofia, 1504, Bulgaria

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Varna, 9010, Bulgaria

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Vratsa, 3000, Bulgaria

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Beijing, 100006, China

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Beijing, 100021, China

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Beijing, 100142, China

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Changchun, 130061, China

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Changsha, 410013, China

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Chengdu, 610041, China

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Dalian, 116011, China

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Guangzhou, 510060, China

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Hangzhou, 310022, China

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Harbin, 150081, China

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Nanjing, 210009, China

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Shanghai, 200025, China

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Shanghai, 200032, China

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Shenyang, 110016, China

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Tianjin, 300060, China

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Brno, 656 53, Czechia

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Olomouc, 775 20, Czechia

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Prague, 128 08, Czechia

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Caen, 14076, France

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Montpellier, 34298, France

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Rouen, 76038, France

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Strasbourg, 67065, France

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Villejuif, 94800, France

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Budapest, 1032, Hungary

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Budapest, 1083, Hungary

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Budapest, 1115, Hungary

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Budapest, 1122, Hungary

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Budapest, 1145, Hungary

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Nyíregyháza, 4400, Hungary

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Veszprém, 8200, Hungary

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Bologna, 40138, Italy

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Naples, 80131, Italy

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Padua, 35128, Italy

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Roma, 00144, Italy

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Roma, 00168, Italy

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Rozzano, 20089, Italy

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Chūōku, 104-0045, Japan

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Chūōku, 104-8560, Japan

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Fukuoka, 811-1395, Japan

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Kagoshima, 892-0833, Japan

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Nagoya, 464-8681, Japan

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Osaka, 540-0006, Japan

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Sapporo, 003-0804, Japan

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Shinagawa-ku, 142-8666, Japan

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Suita, 565-0871, Japan

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Estado de México, 50080, Mexico

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Mérida, 97000, Mexico

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Mérida, 97070, Mexico

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Mérida, 97133, Mexico

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México, 6760, Mexico

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San Juan del Río, 76800, Mexico

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Cusco, CUSCO 01, Peru

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Lima, LIMA 01, Peru

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Lima, Lima 18, Peru

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Lima, LIMA 27, Peru

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Lima, LIMA 34, Peru

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Lima, LIMA 41, Peru

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San Borja, LIMA 41, Peru

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Elblag, 82-300, Poland

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Gdansk, 80-952, Poland

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Grzepnica, 72-003, Poland

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Lodz, 93-513, Poland

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Tarnobrzeg, 39-400, Poland

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Warsaw, 01-748, Poland

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Warsaw, 03-291, Poland

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Bucharest, 011171, Romania

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Bucharest, 013811, Romania

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Bucharest, 030171, Romania

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Cluj-Napoca, 400015, Romania

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Arkhangelsk, 163045, Russia

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Ivanovo, 153040, Russia

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Moscow, 115478, Russia

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Omsk, 644013, Russia

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Saint Petersburg, 191014, Russia

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Saint Petersburg, 195257, Russia

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Saint Petersburg, 195271, Russia

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Saint Petersburg, 197022, Russia

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Saint Petersburg, 197758, Russia

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Saransk, 430005, Russia

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Yaroslavl, 150054, Russia

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Cheongju-si, 28644, South Korea

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Daegu, 41404, South Korea

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Incheon, 21565, South Korea

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Seongnam-si, 13620, South Korea

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Seoul, 03080, South Korea

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Seoul, 03722, South Korea

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Seoul, 158-710, South Korea

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Seoul, 6351, South Korea

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Barcelona, 08003, Spain

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Córdoba, 14004, Spain

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Granada, 18014, Spain

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Madrid, 28034, Spain

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Majadahonda, 28222, Spain

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Oviedo, 33011, Spain

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Seville, 41013, Spain

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Valencia, 46026, Spain

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Zaragoza, 50009, Spain

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Bern, CH-3010, Switzerland

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Lausanne, CH-1011, Switzerland

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Zurich, 8063, Switzerland

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Kaohsiung City, 80756, Taiwan

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Taichung, 407, Taiwan

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Taipei, 10048, Taiwan

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Taipei, 10449, Taiwan

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Taipei, 11217, Taiwan

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Taoyuan District, 333, Taiwan

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Adana, 1260, Turkey (Türkiye)

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Ankara, 06230, Turkey (Türkiye)

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Edirne, 22030, Turkey (Türkiye)

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Gaziantep, 27310, Turkey (Türkiye)

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Istanbul, 34390, Turkey (Türkiye)

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Izmir, 35100, Turkey (Türkiye)

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Kayseri, 38039, Turkey (Türkiye)

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Konya, 42080, Turkey (Türkiye)

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Mersin, 33110, Turkey (Türkiye)

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Aberdeen, AB25 2ZN, United Kingdom

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Colchester, CO4 5JL, United Kingdom

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Coventry, CV2 2DX, United Kingdom

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London, W6 8RF, United Kingdom

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Manchester, M20 4BX, United Kingdom

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Plymouth, PL6 8DH., United Kingdom

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Related Publications (1)

  • Robson M, Im SA, Senkus E, Xu B, Domchek SM, Masuda N, Delaloge S, Li W, Tung N, Armstrong A, Wu W, Goessl C, Runswick S, Conte P. Olaparib for Metastatic Breast Cancer in Patients with a Germline BRCA Mutation. N Engl J Med. 2017 Aug 10;377(6):523-533. doi: 10.1056/NEJMoa1706450. Epub 2017 Jun 4.

Related Links

MeSH Terms

Conditions

Breast NeoplasmsNeoplasm Metastasis

Interventions

olaparib

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Medical Science Director
Organization
AstraZeneca

Study Officials

  • Mark Robson, MD

    Memorial Sloan-Kettering Cancer Center, New York

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 18, 2013

First Posted

December 4, 2013

Study Start

March 27, 2014

Primary Completion

December 9, 2016

Study Completion

December 23, 2025

Last Updated

February 13, 2026

Results First Posted

December 22, 2017

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure
More information

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