NCT01968954

Brief Summary

This study is a multicenter, randomized study in subjects with high cholesterol receiving highly effective statins to assess the efficacy, safety and tolerability of Bococizumab (PF-04950615;RN316) to lower LDL-C.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
711

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Oct 2013

Geographic Reach
9 countries

103 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2013

Completed
20 days until next milestone

First Submitted

Initial submission to the registry

October 21, 2013

Completed
3 days until next milestone

First Posted

Study publicly available on registry

October 24, 2013

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2016

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

May 17, 2017

Completed
Last Updated

May 17, 2017

Status Verified

March 1, 2017

Enrollment Period

2.5 years

First QC Date

October 21, 2013

Results QC Date

April 6, 2017

Last Update Submit

April 6, 2017

Conditions

Keywords

mixed dyslipidemiahigh risk of cardiovascular events

Outcome Measures

Primary Outcomes (1)

  • Percent Change From Baseline in Low Density Lipoprotein-Cholesterol (LDL-C) at Week 12

    Baseline, Week 12

Secondary Outcomes (27)

  • Percent Change From Baseline in Total Cholesterol (TC) at Week 12, 24 and 52

    Baseline, Week 12, 24, 52

  • Percent Change From Baseline in Non- High Density Lipoprotein-Cholesterol (Non HDL-C) at Week 12, 24 and 52

    Baseline, Week 12, 24, 52

  • Percent Change From Baseline in Apolipoprotein B (ApoB) at Week 12, 24 and 52

    Baseline, Week 12, 24, 52

  • Percent Change From Baseline in Lipoprotein(a) at Week 12, 24 and 52

    Baseline, Week 12, 24, 52

  • Percent Change From Baseline in High Density Lipoprotein-Cholesterol (HDL-C) at Week 12, 24 and 52

    Baseline, Week 12, 24, 52

  • +22 more secondary outcomes

Other Outcomes (3)

  • Absolute Change From Baseline in Triglyceride (TG) at Week 12, 24 and 52

    Baseline, Week 12, 24, 52

  • Absolute Change From Baseline in ApolipoproteinA-I (ApoA-I) at Week 12, 24 and 52

    Baseline, Week 12, 24, 52

  • Absolute Change From Baseline in ApolipoproteinA-II (ApoA-II) at Week 12, 24 and 52

    Baseline, Week 12, 24, 52

Study Arms (2)

Bococizumab (PF-04950615;RN316)

EXPERIMENTAL
Drug: Bococizumab (PF-04950615;RN316)

Placebo

PLACEBO COMPARATOR
Other: Placebo

Interventions

150 mg every 2 weeks, subcutaneous injection, 12 months

Also known as: RN316
Bococizumab (PF-04950615;RN316)
PlaceboOTHER

subcutaneous injection, every 2 weeks for 12 months

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Treated with a statin.
  • Fasting LDL-C \> 70 mg/dL and triglyceride \<=400 mg/dL.
  • High or very high risk of incurring a cardiovascular event.

You may not qualify if:

  • Pregnant or breastfeeding females.
  • Cardiovascular or cerebrovascular event of procedures during the past 30 days.
  • Congestive heart failure NYHA class IV.
  • Poorly controlled hypertension.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (103)

Achieve Clinical Research, LLC

Birmingham, Alabama, 35216, United States

Location

Cardiovascular Associates of the Southeast, LLC

Birmingham, Alabama, 35243, United States

Location

Southwest Heart Group

Tucson, Arizona, 85710, United States

Location

ARA-Arizona Research Associates

Tucson, Arizona, 85712, United States

Location

Diagnamics, Inc.

Encinitas, California, 92024, United States

Location

Encompass Clinical Research North Coast

Encinitas, California, 92024, United States

Location

MD Studies, Inc.

Fountain Valley, California, 92708, United States

Location

Alliance Research Centers

Laguna Hills, California, 92653, United States

Location

Prime Care Clinical Research

Laguna Hills, California, 92653, United States

Location

Providence Clinical Research

North Hollywood, California, 91606, United States

Location

San Diego Family Care

San Diego, California, 92111, United States

Location

St. Joseph's Medical Associates

Stockton, California, 95204, United States

Location

Orange County Research Center

Tustin, California, 92780, United States

Location

Clinical Research Advantage, Inc./Cassidy Medical Group - Vista

Vista, California, 92083, United States

Location

Elite Clinical Trials

Wildomar, California, 92595, United States

Location

Expresscare Clinical Research

Colorado Springs, Colorado, 80909, United States

Location

Soundview Medical Associates

Norwalk, Connecticut, 06851, United States

Location

Eastern Research, Inc.

Hialeah, Florida, 33013, United States

Location

East Coast Institute for Research, LLC at Northeast Florida Endocrine & Diabetes Associates

Jacksonville, Florida, 32204, United States

Location

Care Partners Clinical Research, LLC

Jacksonville, Florida, 32277, United States

Location

Prestige Clinical Research Center Inc

Miami, Florida, 33133, United States

Location

Edgewater Medical Research

New Smyrna Beach, Florida, 32169, United States

Location

Gulfcoast Medical Research Center, LLC

Tampa, Florida, 33607, United States

Location

Fellows Research Alliance, Inc.

Savannah, Georgia, 31406, United States

Location

SouthCoast Medical Group

Savannah, Georgia, 31406, United States

Location

Evanston Premier Healthcare Research LLC

Evanston, Illinois, 60201, United States

Location

Comunity Clinical Research Center

Anderson, Indiana, 46011, United States

Location

American Health Network of Indiana, LLC

Avon, Indiana, 46123, United States

Location

Midwest Institute for Clinical Research

Indianapolis, Indiana, 46260, United States

Location

Horizon Research Group of Opelousas, LLC

Eunice, Louisiana, 70535, United States

Location

Internal Medicine Associates

Eunice, Louisiana, 70535, United States

Location

Beacon Clinical Research, LLC

Quincy, Massachusetts, 02169, United States

Location

Allina Health System, dba Abbott Northwestern Hospital

Minneapolis, Minnesota, 55407, United States

Location

Minneapolis Heart Institute Foundation

Minneapolis, Minnesota, 55407, United States

Location

University of MN, Lillehei Clinical Trials Unit

Minneapolis, Minnesota, 55455, United States

Location

Montana Medical Research Inc.

Missoula, Montana, 59808, United States

Location

PMG Research of Raleigh, LLC d/b/a PMG Research of Cary

Cary, North Carolina, 27518, United States

Location

Clinical Trials of America, Inc.

Winston-Salem, North Carolina, 27103, United States

Location

Radiant Research, Inc

Akron, Ohio, 44311, United States

Location

Rapid Medical Research, Inc.

Cleveland, Ohio, 44122, United States

Location

The Office of Daniel G. Williams, MD

Perrysburg, Ohio, 43551, United States

Location

Great Lakes Medical Research, LLC

Willoughby, Ohio, 44094, United States

Location

South Oklahoma Heart Research LLC

Oklahoma City, Oklahoma, 73135, United States

Location

Integrated Medical Research, PC

Ashland, Oregon, 97520, United States

Location

Columbia Research Group, Inc.

Portland, Oregon, 97239, United States

Location

Harleysville Medical Associates

Harleysville, Pennsylvania, 19438, United States

Location

Perelman Center for Advanced Medicine Heart & Vascular Center

Philadelphia, Pennsylvania, 19104, United States

Location

Berks Cardiologists, Ltd.

Wyomissing, Pennsylvania, 19610, United States

Location

Medical Research South,LLC

Charleston, South Carolina, 29407, United States

Location

Berkeley Family Practice

Moncks Corner, South Carolina, 29461, United States

Location

Internal Medicine and Pediatric Associates of Bristol, PC

Bristol, Tennessee, 37620, United States

Location

3 rd Coast Research Associates

Corpus Christi, Texas, 78413, United States

Location

Texas Center For Drug Development, Inc.

Houston, Texas, 77081, United States

Location

Pioneer Research Solutions, Inc.

Houston, Texas, 77099, United States

Location

Protenium Clinical Research

Hurst, Texas, 76054, United States

Location

Utah Cardiology, P.C.

Layton, Utah, 84041, United States

Location

National Clinical Research - Norfolk, Inc.

Norfolk, Virginia, 23502, United States

Location

Premier Clinical Research

Spokane, Washington, 99202, United States

Location

Australian Clinical Research Network

Maroubra, New South Wales, 2035, Australia

Location

Core Research Group Pty Ltd

Milton, Queensland, 4064, Australia

Location

The Avenue Cardiovascular Centre

St Kilda East, Victoria, 3183, Australia

Location

Ecogene-21

Chicoutimi, Quebec, G7H 7K9, Canada

Location

Montreal Heart Institute

Montreal, Quebec, H1T 1C8, Canada

Location

Diex Research Montreal Inc.

Montreal, Quebec, H4N 3C5, Canada

Location

ALPHA Recherche Clinique

Québec, Quebec, G3K 2P8, Canada

Location

Centre Hospitalier Universitaire de Sherbrooke (CHUS)

Sherbrooke, Quebec, J1H 5N4, Canada

Location

Medexa Recherche

Victoriaville, Quebec, G6P 6P6, Canada

Location

Fakultni nemocnice Hradec Kralove

Hradec Králové, 500 05, Czechia

Location

Kardiologie a interni lekarstvi

Prague, 158 00, Czechia

Location

Lekarsky dum Ormiga

Zlín, 760 01, Czechia

Location

Klinische Forschung Berlin-Mitte GmbH

Berlin, 10117, Germany

Location

Klinische Forschung Hannover - Mitte GmbH

Hanover, 30159, Germany

Location

Klinikum der Stadt Ludwigshafen am Rhein gGmbH

Ludwigshafen, 67063, Germany

Location

Klinische Forschung Schwerin GmbH

Schwerin, 19055, Germany

Location

The Chinese University of Hong Kong

Shatin, Hong Kong

Location

Department of Medicine & Therapeutics-The Chinese University of Hong Kong

Shatin, NT, Hong Kong

Location

IRCCS Ospedale San Raffaele

Milan, MI, 20132, Italy

Location

IRCCS Centro Cardiologico Fondazione Monzino

Milan, MI, 20138, Italy

Location

IRCCS Istituto Auxologico Italiano

Milan, MI, 20145, Italy

Location

Azienda Ospedaliera Universitaria Policlinico "Paolo Giaccone"

Palermo, PA, 90127, Italy

Location

Dipartimento di Medicina Interna e Specialita Mediche Policlinico Umberto I

Roma, RM, 00161, Italy

Location

SYNEXUS Polska Sp. z o.o. Oddzial w Katowicach

Katowice, Masovian Voivodeship, 40-040, Poland

Location

NZOZ Terapia Optima

Katowice, Silesian Voivodeship, 40-752, Poland

Location

Synexus Polska Sp. z o.o. Oddzial w Gdyni

Gdynia, 81-384, Poland

Location

Niepubliczny Zaklad Opieki Zdrowotnej CEREO-MED Sp. z o.o.

Lodz, 92-003, Poland

Location

Medicus w Opolu Sp z o.o.

Opole, 45-706, Poland

Location

Medicome Sp. z o.o.

Oświęcim, 32-600, Poland

Location

Synexus Polska Sp. z o.o Oddzial w Poznaniu

Poznan, 60-702, Poland

Location

Centrum Medyczne Ogrodowa Sp. z o.o.

Skierniewice, 96-100, Poland

Location

Centrum Medyczne "SOPMED" Sp. z o.o.

Sopot, 81-756, Poland

Location

Synexus Polska Sp. z o.o. Oddzial w Warszawie

Warsaw, 01-192, Poland

Location

Centrum Medyczne AMED

Warsaw, 01-518, Poland

Location

CSK MSW w Warszawie, Klinika Kardiologii Zachowawczej i Nadcisnienia Tetniczego

Warsaw, 02-507, Poland

Location

Synexus Polska Sp. z o.o. Oddzial we Wroclawiu

Wroclaw, 50-088, Poland

Location

The Catholic University of Korea, Uijeongbu St. Mary's Hospital

Uijeongbu-si, Gyeonggi-do, 480-717, South Korea

Location

Yonsei University Wonju Severance Christian Hospital

Gangwon-Do, 220-701, South Korea

Location

Chonnam National University Hospital

Gwangju, 501-757, South Korea

Location

Seoul National University Hospital

Seoul, 110-744, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 120-752, South Korea

Location

Gangnam Sevrance Hospital, Yeonsei University Health System

Seoul, 135-720, South Korea

Location

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, 137-701, South Korea

Location

Ajou University Hospital

Suwon, 443-380, South Korea

Location

Ulsan University Hospital

Ulsan, 682-714, South Korea

Location

Related Publications (6)

  • Wang EQ, Kaila N, Plowchalk D, Gibiansky L, Yunis C, Sweeney K. Population PK/PD modeling of low-density lipoprotein cholesterol response in hypercholesterolemic participants following administration of bococizumab, a potent anti-PCSK9 monoclonal antibody. CPT Pharmacometrics Syst Pharmacol. 2023 Dec;12(12):2013-2026. doi: 10.1002/psp4.13050. Epub 2023 Nov 22.

  • McCush F, Wang E, Yunis C, Schwartz P, Baltrukonis D. Anti-drug Antibody Magnitude and Clinical Relevance Using Signal to Noise (S/N): Bococizumab Case Study. AAPS J. 2023 Sep 2;25(5):85. doi: 10.1208/s12248-023-00846-x.

  • Chasman DI, Hyde CL, Giulianini F, Danning RD, Wang EQ, Hickling T, Ridker PM, Loomis AK. Genome-wide pharmacogenetics of anti-drug antibody response to bococizumab highlights key residues in HLA DRB1 and DQB1. Sci Rep. 2022 Mar 11;12(1):4266. doi: 10.1038/s41598-022-07997-5.

  • Wang EQ, Bukowski JF, Yunis C, Shear CL, Ridker PM, Schwartz PF, Baltrukonis D. Assessing the Potential Risk of Cross-Reactivity Between Anti-Bococizumab Antibodies and Other Anti-PCSK9 Monoclonal Antibodies. BioDrugs. 2019 Oct;33(5):571-579. doi: 10.1007/s40259-019-00375-0.

  • Ridker PM, Rose LM, Kastelein JJP, Santos RD, Wei C, Revkin J, Yunis C, Tardif JC, Shear CL; Studies of PCSK9 Inhibition and the Reduction of vascular Events (SPIRE) Investigators. Cardiovascular event reduction with PCSK9 inhibition among 1578 patients with familial hypercholesterolemia: Results from the SPIRE randomized trials of bococizumab. J Clin Lipidol. 2018 Jul-Aug;12(4):958-965. doi: 10.1016/j.jacl.2018.03.088. Epub 2018 Apr 3.

  • Ridker PM, Tardif JC, Amarenco P, Duggan W, Glynn RJ, Jukema JW, Kastelein JJP, Kim AM, Koenig W, Nissen S, Revkin J, Rose LM, Santos RD, Schwartz PF, Shear CL, Yunis C; SPIRE Investigators. Lipid-Reduction Variability and Antidrug-Antibody Formation with Bococizumab. N Engl J Med. 2017 Apr 20;376(16):1517-1526. doi: 10.1056/NEJMoa1614062. Epub 2017 Mar 17.

Related Links

MeSH Terms

Conditions

Hyperlipidemias

Interventions

bococizumab

Condition Hierarchy (Ancestors)

DyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 21, 2013

First Posted

October 24, 2013

Study Start

October 1, 2013

Primary Completion

April 1, 2016

Study Completion

April 1, 2016

Last Updated

May 17, 2017

Results First Posted

May 17, 2017

Record last verified: 2017-03

Locations